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A61K48/005

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

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A61K48/005characterised by an aspect of the 'active' part of the composition delivered

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Patents Grantslast 30 patents

Information Patent Grant
Gene therapy for the treatment of CNGB1-linked retinitis pigmentosa
- Patent number 12,246,072
- Issue date Mar 11, 2025
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of mucopolysaccharidosis IVA
- Patent number 12,247,213
- Issue date Mar 11, 2025
- The Nemours Foundation
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified ligand-gated ion channels and methods of use
- Patent number 12,247,064
- Issue date Mar 11, 2025
- Howard Hughes Medical Institute
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
DNA vector for targeted gene therapy
- Patent number 12,246,073
- Issue date Mar 11, 2025
- GENETIC DIAGNOSTICS AND THERAPY 21 LTD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus factor VIII vectors
- Patent number 12,239,692
- Issue date Mar 4, 2025
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and uses thereof
- Patent number 12,234,290
- Issue date Feb 25, 2025
- AVIDITY BIOSCIENCES, INC.
- Andrew John Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Pharmaceutical composition comprising AIMP2-DX2 for preventing or t...
- Patent number 12,233,134
- Issue date Feb 25, 2025
- GENEROATH CO., LTD
- Jin Woo Choi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Drug and gene therapy to treat high myopia and other ocular disorde...
- Patent number 12,233,050
- Issue date Feb 25, 2025
- City University of Hong Kong
- Wenjun Xiong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic constructs for treating cancer
- Patent number 12,233,135
- Issue date Feb 25, 2025
- PRECISION MOLECULAR INC.
- Christopher Ullman
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Myosin 15 promoters and uses thereof
- Patent number 12,233,136
- Issue date Feb 25, 2025
- Decibel Therapeutics, Inc.
- Joseph Burns
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Plasmid encoding a c-terminal fragment of paraspeckle component 1 f...
- Patent number 12,227,546
- Issue date Feb 18, 2025
- Academia Sinica
- Yuh-Shan Jou
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
RNA encoding a therapeutic protein
- Patent number 12,227,549
- Issue date Feb 18, 2025
- CureVac SE
- Mariola Fotin-Mleczek
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Altering microbial populations and modifying microbiota
- Patent number 12,226,430
- Issue date Feb 18, 2025
- SNIPR TECHNOLOGIES LIMITED
- Jasper Clube
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Pharmaceutical composition for treatment of diseases associated wit...
- Patent number 12,227,743
- Issue date Feb 18, 2025
- Osaka University
- Fumihiro Sanada
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cell-based assay for measuring drug product potency
- Patent number 12,228,571
- Issue date Feb 18, 2025
- Novartis AG
- Brian Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for eosinophilic disorders
- Patent number 12,226,492
- Issue date Feb 18, 2025
- Cornell University
- Ronald G. Crystal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods of treating non-syndromic sensorineural hearing loss
- Patent number 12,226,493
- Issue date Feb 18, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
GLP-1 and use thereof in compositions for treating metabolic diseases
- Patent number 12,221,615
- Issue date Feb 11, 2025
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Sulfamidase (SGSH) variants, vectors, compositions and methods and...
- Patent number 12,221,635
- Issue date Feb 11, 2025
- The Childeren's Hospital of Philadelphia
- Beverly L. Davidson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Using nucleosome interacting protein domains to enhance targeted ge...
- Patent number 12,221,606
- Issue date Feb 11, 2025
- Sigma-Aldrich Co. LLC
- Fuqiang Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lentivirus packaging system comprising a synthetic positive feedbac...
- Patent number 12,215,339
- Issue date Feb 4, 2025
- University of Cincinnati
- Toru Matsuura
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for expressing factor IX
- Patent number 12,214,023
- Issue date Feb 4, 2025
- Intellia Therapeutics, Inc.
- Jonathan Douglas Finn
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Therapeutic targets for the correction of the human dystrophin gene...
- Patent number 12,214,054
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Therapeutic applications of CPF1-based genome editing
- Patent number 12,214,056
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Selective cell death-inducing enzyme system
- Patent number 12,214,011
- Issue date Feb 4, 2025
- Sylvain Tourel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Systems and methods for treating hyper-igm syndrome
- Patent number 12,214,055
- Issue date Feb 4, 2025
- Cecillia Cotta-Ramusino
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Dry powder composition comprising long-chain RNA
- Patent number 12,208,165
- Issue date Jan 28, 2025
- CureVac SE
- Fabian Johannes Eber
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Effective delivery of large genes by dual AAV vectors
- Patent number RE50283
- Issue date Jan 28, 2025
- FONDAZIONE TELETHON ETS
- Alberto Auricchio
Information Patent Grant
Engineered Herpes Simplex Virus-1 (HSV-1) vectors and uses thereof
- Patent number 12,209,250
- Issue date Jan 28, 2025
- Massachusetts Institute of Technology
- Ron Weiss
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized human clotting factor IX gene expression cassettes and th...
- Patent number 12,209,263
- Issue date Jan 28, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
LMNA GENE EXPRESSION FOR TREATMENT OF LAMINOPATHIES
- Publication number 20250073314
- Publication date Mar 6, 2025
- Universitatsklinikum Hamburg-Eppendorf
- Thomas ESCHENHAGEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CYSTATIN RNA COMPOSITIONS FOR TISSUE ENGINEERING
- Publication number 20250073322
- Publication date Mar 6, 2025
- University of lowa Research Foundation
- Aliasger K. Salem
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPROVED COMPOSITIONS FOR DELIVERY OF MRNA
- Publication number 20250073351
- Publication date Mar 6, 2025
- Translate Bio, Inc.
- Shrirang KARVE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING G...
- Publication number 20250075178
- Publication date Mar 6, 2025
- The Board of Trustees of the Leland Stanford Junior University
- Zurab Siprashvili
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF FRAGILE X...
- Publication number 20250073352
- Publication date Mar 6, 2025
- PRIME MEDICINE, INC.
- Tyler HARVEY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FACTOR VIII (FVIII) GENE THERAPY METHODS
- Publication number 20250073353
- Publication date Mar 6, 2025
- Spark Therapeutics, Inc.
- Xavier ANGUELA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR DELIVERY OF AGENTS TO INNER EAR
- Publication number 20250073354
- Publication date Mar 6, 2025
- University of Rochester
- Maiken Nedergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DOUBLE-STRANDED RNA HAVING NUCLEOTIDE ANALOG
- Publication number 20250074933
- Publication date Mar 6, 2025
- Rona Bioscience, Limited
- Jinyu Huang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CAPSID VARIANTS AND METHODS OF USING THE SAME
- Publication number 20250066428
- Publication date Feb 27, 2025
- DYNO THERAPEUTICS, INC.
- Ina Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY METHODS FOR TREATMENT OF DIABETES
- Publication number 20250064978
- Publication date Feb 27, 2025
- Jaguar Gene Therapy, LLC
- Michael Hughes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Nucleic Acid-Based Compositions and Methods for Treating Small Vess...
- Publication number 20250064977
- Publication date Feb 27, 2025
- The Schepens Eye Research Institute, Inc.
- Joseph F. Arboleda-Velasquez
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SELF-ASSEMBLING VIRUS-LIKE PARTICLES FOR DELIVERY OF PRIME EDITORS...
- Publication number 20250064979
- Publication date Feb 27, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Materials and Methods for Treatment of Duchenne Muscular Dystrophy
- Publication number 20250064980
- Publication date Feb 27, 2025
- VERTEX PHARMACEUTICALS INCORPORATED
- Ami Meda Kabadi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENDOGENOUS GENE REGULATION TO TREAT NEUROLOGICAL DISORDERS AND DISE...
- Publication number 20250064974
- Publication date Feb 27, 2025
- UCL Business LTD
- Gabriele LIGNANI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPY
- Publication number 20250064975
- Publication date Feb 27, 2025
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED PNMA PROTEINS AND DELIVERY SYSTEMS THEREOF
- Publication number 20250064976
- Publication date Feb 27, 2025
- THE BROAD INSTITUTE, INC.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF
- Publication number 20250064981
- Publication date Feb 27, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CD5 Modified Cells Comprising Chimeric Antigen Receptors (CARs) for...
- Publication number 20250064852
- Publication date Feb 27, 2025
- The Trustees of the University of Pennsylvania
- Marco Ruella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT AAV VECTORS FOR TREATING GLUTARIC ACIDURIA TYPE I
- Publication number 20250064982
- Publication date Feb 27, 2025
- SHANGHAI VITALGEN BIOPHARMA CO., LTD.
- Lu GUO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING A CARDIAC DISEASE
- Publication number 20250064983
- Publication date Feb 27, 2025
- The Children's Medical Center Corporation
- Vassilios J. Bezzerides
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV GENE THERAPY FOR THE KIDNEY
- Publication number 20250064984
- Publication date Feb 27, 2025
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250066437
- Publication date Feb 27, 2025
- SHANGHAI MYGT BIOPHARMACEUTICAL LLC
- Mengdi YAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR REDUCING PAIN AND INFLAMMATION THROUGH...
- Publication number 20250057981
- Publication date Feb 20, 2025
- Navega Therapeutics, Inc.
- Ana Maria MORENO COLLADO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CARDIAC CALCIUM HANDLING MACHINERY REMODELED IN FRIEDREICH'S ATAXIA
- Publication number 20250057979
- Publication date Feb 20, 2025
- University of South Florida
- Bojjibabu Chidipi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Co-Delivery of a Gene Editor Construct and a Donor Template
- Publication number 20250057980
- Publication date Feb 20, 2025
- TOME BIOSCIENCES, INC.
- Jonathan Douglas Finn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR PROMOTING MIGRATION OF ADULT STEM CELLS USING INCRE...
- Publication number 20250057983
- Publication date Feb 20, 2025
- SOONCHUNHYANG UNIVERSITY INDUSTRY ACADEMY COOPERATION FOUNDATION
- Nayoung Suh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
USE OF PCBP1 TO TREAT HYPERPROLIFERATIVE DISEASE
- Publication number 20250057978
- Publication date Feb 20, 2025
- Ibex Biosciences, Inc.
- Norman Zhennan LAI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROTEINS WITH CARDIOPROTECTIVE ACTIVITY
- Publication number 20250057982
- Publication date Feb 20, 2025
- International Centre for Genetic Engineering and Biotechnology (ICGEB)
- Mauro Giacca
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL-TYPE SPECIFIC MEMBRANE FUSION PROTEINS
- Publication number 20250057984
- Publication date Feb 20, 2025
- THE BROAD INSTITUTE, INC.
- Feng ZHANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treatment of Ocular Disease Associated...
- Publication number 20250057987
- Publication date Feb 20, 2025
- 4D MOLECULAR THERAPEUTICS INC.
- Christian BURNS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the 'active' part of the composition delivered

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Gene therapy for the treatment of CNGB1-linked retinitis pigmentosa

Treatment of mucopolysaccharidosis IVA

Modified ligand-gated ion channels and methods of use

DNA vector for targeted gene therapy

Adeno-associated virus factor VIII vectors

Nucleic acid-polypeptide compositions and uses thereof

Pharmaceutical composition comprising AIMP2-DX2 for preventing or t...

Drug and gene therapy to treat high myopia and other ocular disorde...

Therapeutic constructs for treating cancer

Myosin 15 promoters and uses thereof

Plasmid encoding a c-terminal fragment of paraspeckle component 1 f...

RNA encoding a therapeutic protein

Altering microbial populations and modifying microbiota

Pharmaceutical composition for treatment of diseases associated wit...

Cell-based assay for measuring drug product potency

Gene therapy for eosinophilic disorders

Methods of treating non-syndromic sensorineural hearing loss

GLP-1 and use thereof in compositions for treating metabolic diseases

Sulfamidase (SGSH) variants, vectors, compositions and methods and...

Using nucleosome interacting protein domains to enhance targeted ge...

Lentivirus packaging system comprising a synthetic positive feedbac...

Compositions and methods for expressing factor IX

Therapeutic targets for the correction of the human dystrophin gene...

Therapeutic applications of CPF1-based genome editing

Selective cell death-inducing enzyme system

Systems and methods for treating hyper-igm syndrome

Dry powder composition comprising long-chain RNA

Effective delivery of large genes by dual AAV vectors

Engineered Herpes Simplex Virus-1 (HSV-1) vectors and uses thereof

Optimized human clotting factor IX gene expression cassettes and th...

Patents Applicationslast 30 patents

LMNA GENE EXPRESSION FOR TREATMENT OF LAMINOPATHIES

CYSTATIN RNA COMPOSITIONS FOR TISSUE ENGINEERING

IMPROVED COMPOSITIONS FOR DELIVERY OF MRNA

GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING G...

GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF FRAGILE X...

FACTOR VIII (FVIII) GENE THERAPY METHODS

COMPOSITIONS AND METHODS FOR DELIVERY OF AGENTS TO INNER EAR

DOUBLE-STRANDED RNA HAVING NUCLEOTIDE ANALOG

CAPSID VARIANTS AND METHODS OF USING THE SAME

GENE THERAPY METHODS FOR TREATMENT OF DIABETES

Nucleic Acid-Based Compositions and Methods for Treating Small Vess...

SELF-ASSEMBLING VIRUS-LIKE PARTICLES FOR DELIVERY OF PRIME EDITORS...

Materials and Methods for Treatment of Duchenne Muscular Dystrophy

ENDOGENOUS GENE REGULATION TO TREAT NEUROLOGICAL DISORDERS AND DISE...

THERAPY

ENGINEERED PNMA PROTEINS AND DELIVERY SYSTEMS THEREOF

AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF

CD5 Modified Cells Comprising Chimeric Antigen Receptors (CARs) for...

RECOMBINANT AAV VECTORS FOR TREATING GLUTARIC ACIDURIA TYPE I

COMPOSITIONS AND METHODS FOR TREATING A CARDIAC DISEASE

AAV GENE THERAPY FOR THE KIDNEY

TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY

COMPOSITIONS AND METHODS FOR REDUCING PAIN AND INFLAMMATION THROUGH...

CARDIAC CALCIUM HANDLING MACHINERY REMODELED IN FRIEDREICH'S ATAXIA

Co-Delivery of a Gene Editor Construct and a Donor Template

COMPOSITION FOR PROMOTING MIGRATION OF ADULT STEM CELLS USING INCRE...

USE OF PCBP1 TO TREAT HYPERPROLIFERATIVE DISEASE

PROTEINS WITH CARDIOPROTECTIVE ACTIVITY

CELL-TYPE SPECIFIC MEMBRANE FUSION PROTEINS

Compositions and Methods for Treatment of Ocular Disease Associated...