Membership
Tour
Register
Log in
characterised by an aspect of the 'active' part of the composition delivered
Follow
Industry
CPC
A61K48/005
This industry / category may be too specific. Please go to a parent level for more data
Parent Industries
A
HUMAN NECESSITIES
A61
Medical science
A61K
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
A61K48/00
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy
Current Industry
A61K48/005
characterised by an aspect of the 'active' part of the composition delivered
Industries
Overview
Organizations
People
Information
Impact
Please log in for detailed analytics
Patents Grants
last 30 patents
Information
Patent Grant
Optimized promoter sequences, intron-free expression constructs and...
Patent number
12,290,574
Issue date
May 6, 2025
SPARK THERAPEUTICS, INC.
Xavier Anguela
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Heterologous targeting peptide grafted AAVs
Patent number
12,291,719
Issue date
May 6, 2025
UNIVERSITY OF MASSACHUSETTS
Miguel Sena Esteves
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Genome editing methods and constructs
Patent number
12,285,495
Issue date
Apr 29, 2025
FONDAZIONE TELETHON ETS
Alberto Auricchio
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Means and methods for AAV gene therapy in humans
Patent number
12,285,451
Issue date
Apr 29, 2025
Uniqure IP B.V.
Bart Antonius Nijmeijer
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Riboswitch modulated gene therapy for retinal diseases
Patent number
12,286,631
Issue date
Apr 29, 2025
The Medical College of Wisconsin, Inc.
Daniel M. Lipinski
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Frataxin expression constructs having engineered promoters and meth...
Patent number
12,281,321
Issue date
Apr 22, 2025
VOYAGER THERAPEUTICS, INC.
Holger Patzke
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
5′-cap-trinucleotide- or higher oligonucleotide compounds and their...
Patent number
12,281,138
Issue date
Apr 22, 2025
BIONTECH RNA PHARMACEUTICALS GMBH
Andreas Kuhn
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Methods of reducing FUS/TLS- or TDP-43-mediated neuronal cytotoxici...
Patent number
12,275,764
Issue date
Apr 15, 2025
Brandeis University
Greg Petsko
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Recombinant adeno-associated viruses encoding serpin peptides and u...
Patent number
12,274,757
Issue date
Apr 15, 2025
University of Florida Research Foundation, Incorporated
Alexandra Rose Lucas
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
AAV-mediated delivery of therapeutic antibodies to the inner ear
Patent number
12,275,960
Issue date
Apr 15, 2025
Akouos, Inc.
Emmanuel John Simons
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Methods of treating and diagnosing epilepsy
Patent number
12,274,756
Issue date
Apr 15, 2025
Yale University
Angelique Bordey
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Compositions and methods comprising engineered chimeric antigen rec...
Patent number
12,269,860
Issue date
Apr 8, 2025
AUTOLUS LIMITED
Martin Pulé
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Composition and methods for treatment of ornithine transcarbamylase...
Patent number
12,268,754
Issue date
Apr 8, 2025
Translate Bio, Inc.
Kim Askew
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Allele-specific inactivation of mutant HTT via gene editing at codi...
Patent number
12,268,755
Issue date
Apr 8, 2025
UNIVERSITY OF MASSACHUSETTS
Michael Harry Brodsky
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Induction of osteogenesis by delivering BMP encoding RNA
Patent number
12,263,229
Issue date
Apr 1, 2025
ethris GmbH
Elizabeth Balmayor
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Gene therapy for limb-girdle muscular dystrophy type 2C
Patent number
12,263,230
Issue date
Apr 1, 2025
Research Institute at Nationwide Children's Hospital
Louise R. Rodino-Klapac
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Adeno-associated virus virions for treatment of epilepsy
Patent number
12,263,231
Issue date
Apr 1, 2025
Jichi Medical University
Shin-ichi Muramatsu
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Composition for regulating production of proteins
Patent number
12,263,232
Issue date
Apr 1, 2025
Wyvern Pharmaceuticals Inc.
Jill L. Thompson
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Systems, methods and compositions for sequence manipulation with op...
Patent number
12,258,595
Issue date
Mar 25, 2025
The Broad Institute, Inc.
Silvana Konermann
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Adeno-associated virus vector delivery of a fragment of micro-dystr...
Patent number
12,257,317
Issue date
Mar 25, 2025
Newcastle University
Hanns Lochmuller
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Optimized mini-dystrophin genes and expression cassettes and their use
Patent number
12,257,321
Issue date
Mar 25, 2025
The University of North Carolina at Chapel Hill
Xiao Xiao
A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information
Patent Grant
Optimised coding sequence and promoter
Patent number
12,257,319
Issue date
Mar 25, 2025
UCL BUSINESS LTD
Amit Nathwani
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Methods and compositions for therapeutic protein delivery
Patent number
12,258,597
Issue date
Mar 25, 2025
REGENERON PHARMACEUTICALS, INC.
Andrew Baik
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Polynucleotide compositions, related formulations, and methods of u...
Patent number
12,257,318
Issue date
Mar 25, 2025
ReCode Therapeutics, Inc.
Mirko Hennig
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Adeno-associated virus vector delivery of alpha-sarcoglycan and the...
Patent number
12,258,573
Issue date
Mar 25, 2025
Research Institute at Nationwide Children's Hospital
Louise Rodino-Klapac
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Gene therapy for NMNAT1-associated retinal degeneration
Patent number
12,257,320
Issue date
Mar 25, 2025
Massachusetts Eye and Ear Infirmary
Eric A. Pierce
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Methods of treating non-arteritic anterior ischemic optic neuropathy
Patent number
12,252,518
Issue date
Mar 18, 2025
Life Biosciences, Inc.
Michel Wathier
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Myosin 15 promoters and uses thereof
Patent number
12,252,520
Issue date
Mar 18, 2025
Decibel Therapeutics, Inc.
Joseph Burns
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Delivery, use and therapeutic applications of the CRISPR-Cas system...
Patent number
12,251,450
Issue date
Mar 18, 2025
The Broad Institute, Inc.
Sangeeta Bhatia
G06 - COMPUTING CALCULATING COUNTING
Information
Patent Grant
Closed-ended linear duplex DNA for non-viral gene transfer
Patent number
12,252,703
Issue date
Mar 18, 2025
UNIVERSITY OF MASSACHUSETTS
Robert M. Kotin
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Patents Applications
last 30 patents
Information
Patent Application
Materials and Methods for Treatment of Human Genetic Diseases Inclu...
Publication number
20250146004
Publication date
May 8, 2025
VERTEX PHARMACEUTICALS INCORPORATED
Matthew Hebden Porteus
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
DISRUPTION OF THE SECRETION OF INSULIN-LIKE GROWTH FACTOR 2 FOR CAN...
Publication number
20250144242
Publication date
May 8, 2025
THE HONG KONG UNIVERSITY OF SCIENCE AND TECHNOLOGY
Yusong GUO
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
AAV CAPSIDS FOR IMPROVED HEART TRANSDUCTION AND DETARGETING OF LIVER
Publication number
20250144243
Publication date
May 8, 2025
The Trustees of the University of Pennsylvania
Jacob Hoffman
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR MODIFYING A HUMAN DYSTROPHIN GENE
Publication number
20250144246
Publication date
May 8, 2025
MAMMOTH BIOSCIENCES, INC.
Lucas Benjamin HARRINGTON
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
FORMULATIONS TO ENHANCE THE DELIVERY OF GENE THERAPY VECTORS
Publication number
20250144247
Publication date
May 8, 2025
University of Iowa Research Foundation
Ashley Cooney
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR THE TREATMENT OF WILSON'S DISEASE
Publication number
20250144239
Publication date
May 8, 2025
LogicBio Therapeutics, Inc.
Shengwen Zhang
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS FOR USE OF VIRAL VECTOR CONSTRUCTS FOR THE TREATMENT OF FAB...
Publication number
20250144240
Publication date
May 8, 2025
Sangamo Therapeutics, Inc.
Cristobal PASSALACQUA
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS OF TARGETING REPETITIVE RNA IN HUNTINGTON'S DISEASE
Publication number
20250144241
Publication date
May 8, 2025
The Regents of the University of California
Eugene Yeo
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
TREATMENT OF ACQUIRED FOCAL EPILEPSY
Publication number
20250144244
Publication date
May 8, 2025
UCL Business LTD
Matthew Charles WALKER
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR ARRHYTHMOGENIC CARDIOMYOPATHY
Publication number
20250144245
Publication date
May 8, 2025
Ginkgo BioWorks, Inc.
John Graef
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS AND SYSTEMS FOR IMPROVED NUCLEIC ACID DELIVERY VIA ULTRASOUND
Publication number
20250144248
Publication date
May 8, 2025
SonoThera, Inc.
Steven B. FEINSTEIN
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
COMPOSITIONS AND METHODS FOR TREATING SIALIDOSIS
Publication number
20250135033
Publication date
May 1, 2025
University of Massachusetts
Heather Gray-Edwards
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS FOR EDITING MECP2 TRANSCRIPTS AND METHODS THEREOF
Publication number
20250135036
Publication date
May 1, 2025
WAVE LIFE SCIENCES LTD.
Christopher Michael Acker
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT...
Publication number
20250136651
Publication date
May 1, 2025
THE UNIVERSITY COURT OF THE UNIVERSITY OF EDINBURGH
Stuart Robert Cobb
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VEST...
Publication number
20250136673
Publication date
May 1, 2025
Akouos, Inc.
Emmanuel John Simons
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
MRNA REGULON THERAPY FOR THE TREATMENT OF HAPLOINSUFFICIENCY DISORDERS
Publication number
20250135035
Publication date
May 1, 2025
The Johns Hopkins University
Jeffery Coller
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
CRISPR METHODS FOR CORRECTING BAG3 GENE MUTATIONS IN VIVO
Publication number
20250135032
Publication date
May 1, 2025
Temple University - Of The Commonwealth System of Higher Education
Kamel KHALILI
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
CRISPR-MEDIATED MANIPULATION OF APP EXPRESSION AS A THERAPEUTIC APP...
Publication number
20250135034
Publication date
May 1, 2025
THE HONG KONG UNIVERSITY OF SCIENCE AND TECHNOLOGY
Nancy Yuk-Yu Ip
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR IMPROVED TREATMENT OF POMPE DISEASE
Publication number
20250135038
Publication date
May 1, 2025
Astellas Gene Therapies, Inc.
Tahseen MOZAFFAR
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS OF USING TWO-PROMOTER VECTOR FOR TREATMENT...
Publication number
20250137012
Publication date
May 1, 2025
M6P THERAPEUTICS, INC.
Hung DO
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
DEPLETION OF CELLS BY CRISPR NUCLEASES
Publication number
20250135030
Publication date
May 1, 2025
BRAIN BIOTECH AG
Paul SCHOLZ
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
SINGLE-VECTOR GENE CONSTRUCT COMPRISING INSULIN AND GLUCOKINASE GENES
Publication number
20250135031
Publication date
May 1, 2025
UNIVERSITAT AUTONOMA DE BARCELONA
Fatima BOSCH TUBERT
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
INHIBITOR-RESISTANT MGMT MODIFICATIONS AND MODIFICATION OF MGMT-ENC...
Publication number
20250135039
Publication date
May 1, 2025
Ensoma, Inc.
Robert Thomas Peters
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF
Publication number
20250135040
Publication date
May 1, 2025
Spacecraft Seven, LLC
Christopher Dean HERZOG
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
OPTIMIZED SEQUENCES FOR ENHANCED tRNA EXPRESSION OR/AND NONSENSE MU...
Publication number
20250134919
Publication date
May 1, 2025
University of Rochester
John D. Lueck
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
CODON-OPTIMIZED SMAD7 GENE THERAPY TO TREAT AND PREVENT MUSCLE WAST...
Publication number
20250135037
Publication date
May 1, 2025
AAVogen Inc.
Buel D. Rodgers
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
T CELL MODIFYING COMPOUNDS AND USES THEREOF
Publication number
20250129181
Publication date
Apr 24, 2025
Sangamo Therapeutics, Inc.
Philip D. Gregory
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
CODON-OPTIMIZED REDUCED-SIZE ATP7A CDNA AND USES FOR TREATMENT OF C...
Publication number
20250129382
Publication date
Apr 24, 2025
The United States of America, as Represented by the Secretary, Dept. of Healt...
Stephen G. Kaler
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
DUALLY DERIVATIZED CHITOSAN NANOPARTICLES AND METHODS OF MAKING AND...
Publication number
20250127925
Publication date
Apr 24, 2025
ENGENE, INC.
Jun Gao
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
HYBRID REGULATORY ELEMENTS
Publication number
20250127930
Publication date
Apr 24, 2025
GENETHON
FEDERICO MINGOZZI
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...