characterised by an aspect of the administration regime

Industry

CPC
A61K48/0083

This industry / category may be too specific. Please go to a parent level for more data

Parent Industries

AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

Current Industry

A61K48/0083characterised by an aspect of the administration regime

Industries

Patents Grantslast 30 patents

Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,913,001
- Issue date Feb 27, 2024
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,905,514
- Issue date Feb 20, 2024
- GlaxoSmithKline Biological S.A.
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV9-mediated gene therapy for treating mucopolysaccharidosis type I
- Patent number 11,890,329
- Issue date Feb 6, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunization of large mammals with low doses of RNA
- Patent number 11,891,608
- Issue date Feb 6, 2024
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for AADC deficiency
- Patent number 11,865,188
- Issue date Jan 9, 2024
- NATIONAL TAIWAN UNIVERSITY
- Mark Pykett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,851,660
- Issue date Dec 26, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,845,925
- Issue date Dec 19, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
In vivo therapeutic delivery procedure and device
- Patent number 11,839,761
- Issue date Dec 12, 2023
- Wisconsin Alumni Research Foundation
- Susan Hagness
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Codon optimized GLA genes and uses thereof
- Patent number 11,802,278
- Issue date Oct 31, 2023
- David H. Kirn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for the treatment of malignancies
- Patent number 11,801,312
- Issue date Oct 31, 2023
- University of South Florida
- Richard Heller
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods for selective kinase inhibition by endogenously produced an...
- Patent number 11,793,889
- Issue date Oct 24, 2023
- KINASE PHARMA INC.
- Bradley G Thompson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunization of large mammals with low doses of RNA
- Patent number 11,773,395
- Issue date Oct 3, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,739,334
- Issue date Aug 29, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Microbubble nucleic acid delivery platform
- Patent number 11,737,971
- Issue date Aug 29, 2023
- University of Pittsburgh of the Commonwealth System of Higher Education
- Flordeliza Villanueva
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,655,475
- Issue date May 23, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method and system for optogenetics experiments
- Patent number 11,633,620
- Issue date Apr 25, 2023
- THE HONG KONG POLYTECHNIC UNIVERSITY SHENZHEN RESEARCH INSTITUTE
- Puxiang Lai
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Apparatus for efficient genetic modification of cells
- Patent number 11,584,908
- Issue date Feb 21, 2023
- The Charles Stark Draper Laboratory, Inc.
- Kenneth T. Kotz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunomodulating gene therapy
- Patent number 11,547,717
- Issue date Jan 10, 2023
- Duke University
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
ATP-binding cassette family coding polyribonucleotides and formulat...
- Patent number 11,479,768
- Issue date Oct 25, 2022
- ethris GmbH
- Christian Plank
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treating metastatic cancer and model systems for metastatic disease
- Patent number 11,464,874
- Issue date Oct 11, 2022
- Memorial Sloan Kettering Cancer Center
- Karuna Ganesh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Means and methods for AAV gene therapy in humans
- Patent number 11,452,749
- Issue date Sep 27, 2022
- Uniqure IP B.V.
- Bart Antonius Nijmeijer
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Nucleic acid-polypeptide compositions and methods of inducing exon...
- Patent number 11,400,163
- Issue date Aug 2, 2022
- AVIDITY BIOSCIENCES, INC.
- Arthur A. Levin
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods for treating cancers
- Patent number 11,400,170
- Issue date Aug 2, 2022
- Gradalis, Inc.
- John Nemunaitis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and systems for noninvasive control of brain cells and rela...
- Patent number 11,400,168
- Issue date Aug 2, 2022
- California Institute of Technology
- Mikhail G. Shapiro
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for treating Phenylketonuria
- Patent number 11,382,941
- Issue date Jul 12, 2022
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression of neuropeptides
- Patent number 11,376,337
- Issue date Jul 5, 2022
- California Institute of Technology
- David J Anderson
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Pharmaceutical composition containing a stabilised mRNA optimised f...
- Patent number 11,369,691
- Issue date Jun 28, 2022
- CureVac AG
- Florian Von Der Mülbe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for modulating development and function of photoreceptor cells
- Patent number 11,351,225
- Issue date Jun 7, 2022
- The Schepens Eye Research Institute, Inc.
- Neena B. Haider
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating Leber's hereditary optic neur...
- Patent number 11,352,645
- Issue date Jun 7, 2022
- Wuhan Neurophth Biotechnology Limited Company
- Bin Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and methods of inducing exon...
- Patent number 11,311,627
- Issue date Apr 26, 2022
- AVIDITY BIOSCIENCES LLC
- Arthur A. Levin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
GENE THERAPY FOR DOPAMINE TRANSPORTER DEFICIENCY SYNDROME
- Publication number 20240115737
- Publication date Apr 11, 2024
- UCL Business LTD
- Joanna NG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
- Publication number 20240117347
- Publication date Apr 11, 2024
- WAVE LIFE SCIENCES LTD.
- David Charles Donnell Butler
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR AADC DEFICIENCY
- Publication number 20240100186
- Publication date Mar 28, 2024
- National Taiwan University
- Mark Pykett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF MUCOPOLYSACCHARIDOSIS I WITH FULLY-HUMAN GLYCOSYLATED...
- Publication number 20240050537
- Publication date Feb 15, 2024
- Regenxbio Inc.
- Stephen Yoo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF DANON DISEASE
- Publication number 20240033325
- Publication date Feb 1, 2024
- Spacecraft Seven, LLC
- Jose M. TREVEJO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
VIRAL VECTOR DOSING PROTOCOLS
- Publication number 20240024517
- Publication date Jan 25, 2024
- Selecta Biosciences, Inc.
- Takashi Kei Kishimoto
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CODON OPTIMIZED GLA GENES AND USES THEREOF
- Publication number 20240018498
- Publication date Jan 18, 2024
- 4D MOLECULAR THERAPEUTICS INC.
- David H. KIRN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR RESTRICTING BIODISTRIBUTION OF AAV
- Publication number 20240016956
- Publication date Jan 18, 2024
- AFFINIA THERAPEUTICS INC.
- Roberto CALCEDO DEL HOYO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
USE OF IRAK4 MODULATORS FOR GENE THERAPY
- Publication number 20230405151
- Publication date Dec 21, 2023
- Genzyme Corporation
- Sourav Roy CHOUDHURY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS FOR TREATMENT OF GRN-ASSOCIATED...
- Publication number 20230364264
- Publication date Nov 16, 2023
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR NIEMANN-PICK DISEASE TYPE A
- Publication number 20230287366
- Publication date Sep 14, 2023
- Genzyme Corporation
- Marco A. PASSINI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SONOGENETIC STIMULATION OF CELLS EXPRESSING TRPA1
- Publication number 20230263891
- Publication date Aug 24, 2023
- Salk Institute for Biological Studies
- Sreekanth CHALASANI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND THE TRE...
- Publication number 20230241252
- Publication date Aug 3, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR ADMINISTERING RECOMBINANT VIRAL VECTORS
- Publication number 20230242941
- Publication date Aug 3, 2023
- University of Iowa Research Foundation
- Yinghua Tang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION O...
- Publication number 20230241247
- Publication date Aug 3, 2023
- Spark Therapeutics, Inc.
- Sean ARMOUR
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR INCREASING PLATELET COUNT BY INHIBITING BILIVERDIN IXBE...
- Publication number 20230233712
- Publication date Jul 27, 2023
- The Research Foundation for the State University of New York
- Wadie F. BAHOU
- G01 - MEASURING TESTING
Information Patent Application
ADENO-ASSOCIATED VIRUS FOR THERAPEUTIC DELIVERY TO CENTRAL NERVOUS...
- Publication number 20230226225
- Publication date Jul 20, 2023
- Regents of the University of Minnesota
- R. Scott McIvor
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR PREVENTING INDUCTION OF IMMUNE RESPONSES TO THE TRANSDU...
- Publication number 20230190956
- Publication date Jun 22, 2023
- Inserm (institut National de la Sante et de la Recherche Medicale)
- Fisson SYLVAIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CODON OPTIMIZED GLA GENES AND USES THEREOF
- Publication number 20230190964
- Publication date Jun 22, 2023
- 4D MOLECULAR THERAPEUTICS INC.
- David H. Kirn
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITION AND METHODS FOR TREATMENT OF PRIMARY CILIARY DYSKINESIA
- Publication number 20230190954
- Publication date Jun 22, 2023
- Translate Bio, Inc.
- Caroline J. WOO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR TREATING GAIN-OF-FUNCTION DISORDERS COMBINING GENE EDIT...
- Publication number 20230190962
- Publication date Jun 22, 2023
- BLUEALLELE CORPORATION
- Nicholas BALTES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE
- Publication number 20230190963
- Publication date Jun 22, 2023
- Memorial Sloan-Kettering Cancer Center
- Karuna Ganesh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS USEFUL FOR TREATING GM1 GANGLIOSIDOSIS
- Publication number 20230190966
- Publication date Jun 22, 2023
- The Trustees of the University of Pennsylvania
- James M. Wilson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND SYSTEMS FOR NONINVASIVE CONTROL OF BRAIN CELLS AND RELA...
- Publication number 20230158171
- Publication date May 25, 2023
- California Institute of Technology
- Mikhail SHAPIRO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING MACULAR DYSTROPHY
- Publication number 20230149566
- Publication date May 18, 2023
- Oxford University Innovation Limited
- Robert E. Maclaren
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR ATTENUATING ANTI-VIRAL TRANSFER VECTOR...
- Publication number 20230141563
- Publication date May 11, 2023
- Selecta Biosciences, Inc.
- Petr Ilyinskii
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CONDITIONING REGIMENS FOR IN VIVO GENE THERAPY
- Publication number 20230133243
- Publication date May 4, 2023
- Fred Hutchinson Cancer Center
- Andre Lieber
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
IMMUNIZATION OF LARGE MAMMALS WITH LOW DOSES OF RNA
- Publication number 20230136704
- Publication date May 4, 2023
- GlaxoSmithKline Biologicals S.A.
- Andrew GEALL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA
- Publication number 20230123931
- Publication date Apr 20, 2023
- GlaxoSmithKline Biologicals S.A.
- Andrew GEALL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA
- Publication number 20230112809
- Publication date Apr 13, 2023
- GlaxoSmithKline Biologicals S.A.
- Andrew GEALL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the administration regime

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Immunisation of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

AAV9-mediated gene therapy for treating mucopolysaccharidosis type I

Immunization of large mammals with low doses of RNA

Gene therapy for AADC deficiency

Immunisation of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

In vivo therapeutic delivery procedure and device

Codon optimized GLA genes and uses thereof

Method for the treatment of malignancies

Methods for selective kinase inhibition by endogenously produced an...

Immunization of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

Microbubble nucleic acid delivery platform

Immunisation of large mammals with low doses of RNA

Method and system for optogenetics experiments

Apparatus for efficient genetic modification of cells

Immunomodulating gene therapy

ATP-binding cassette family coding polyribonucleotides and formulat...

Treating metastatic cancer and model systems for metastatic disease

Means and methods for AAV gene therapy in humans

Nucleic acid-polypeptide compositions and methods of inducing exon...

Methods for treating cancers

Methods and systems for noninvasive control of brain cells and rela...

Gene therapy for treating Phenylketonuria

Expression of neuropeptides

Pharmaceutical composition containing a stabilised mRNA optimised f...

Methods for modulating development and function of photoreceptor cells

Compositions and methods for treating Leber's hereditary optic neur...

Nucleic acid-polypeptide compositions and methods of inducing exon...

Patents Applicationslast 30 patents

GENE THERAPY FOR DOPAMINE TRANSPORTER DEFICIENCY SYNDROME

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

GENE THERAPY FOR AADC DEFICIENCY

TREATMENT OF MUCOPOLYSACCHARIDOSIS I WITH FULLY-HUMAN GLYCOSYLATED...

TREATMENT OF DANON DISEASE

VIRAL VECTOR DOSING PROTOCOLS

CODON OPTIMIZED GLA GENES AND USES THEREOF

METHODS AND COMPOSITIONS FOR RESTRICTING BIODISTRIBUTION OF AAV

USE OF IRAK4 MODULATORS FOR GENE THERAPY

RECOMBINANT ADENO-ASSOCIATED VIRUS FOR TREATMENT OF GRN-ASSOCIATED...

GENE THERAPY FOR NIEMANN-PICK DISEASE TYPE A

SONOGENETIC STIMULATION OF CELLS EXPRESSING TRPA1

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND THE TRE...

METHODS AND COMPOSITIONS FOR ADMINISTERING RECOMBINANT VIRAL VECTORS

COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION O...

METHODS FOR INCREASING PLATELET COUNT BY INHIBITING BILIVERDIN IXBE...

ADENO-ASSOCIATED VIRUS FOR THERAPEUTIC DELIVERY TO CENTRAL NERVOUS...

METHODS FOR PREVENTING INDUCTION OF IMMUNE RESPONSES TO THE TRANSDU...

CODON OPTIMIZED GLA GENES AND USES THEREOF

COMPOSITION AND METHODS FOR TREATMENT OF PRIMARY CILIARY DYSKINESIA

METHODS FOR TREATING GAIN-OF-FUNCTION DISORDERS COMBINING GENE EDIT...

TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE

COMPOSITIONS USEFUL FOR TREATING GM1 GANGLIOSIDOSIS

METHODS AND SYSTEMS FOR NONINVASIVE CONTROL OF BRAIN CELLS AND RELA...

COMPOSITIONS AND METHODS FOR TREATING MACULAR DYSTROPHY

METHODS AND COMPOSITIONS FOR ATTENUATING ANTI-VIRAL TRANSFER VECTOR...

CONDITIONING REGIMENS FOR IN VIVO GENE THERAPY

IMMUNIZATION OF LARGE MAMMALS WITH LOW DOSES OF RNA

IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA

IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA