characterised by an aspect of the administration regime

Industry

CPC
A61K48/0083

This industry / category may be too specific. Please go to a parent level for more data

Parent Industries

AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

Current Industry

A61K48/0083characterised by an aspect of the administration regime

Industries

Patents Grantslast 30 patents

Information Patent Grant
Gene therapy for ciliopathies
- Patent number 12,171,794
- Issue date Dec 24, 2024
- UCL BUSINESS LTD
- Philip Beales
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Apparatus for efficient genetic modification of cells
- Patent number 12,139,697
- Issue date Nov 12, 2024
- The Charles Stark Draper Laboratory, Inc.
- Kenneth T. Kotz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunostimulating vector system
- Patent number 12,133,898
- Issue date Nov 5, 2024
- Provecs Medical GmbH
- Frank Schnieders
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for efficient delivery of therapeutic molecules in vitro an...
- Patent number 12,102,691
- Issue date Oct 1, 2024
- Massachusetts Eye and Ear Infirmary
- Zheng-Yi Chen
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Gene therapy of hemophilia a using viral vectors encoding recombina...
- Patent number 12,091,675
- Issue date Sep 17, 2024
- Takeda Pharmaceutical Company Limited
- Hanspeter Rottensteiner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transgene cassettes, AAV vectors and AAV viral vectors for the expr...
- Patent number 12,077,772
- Issue date Sep 3, 2024
- The Board of Regents of the University of Texas System
- Steven J. Gray
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Nucleic acid-polypeptide compositions and methods of inducing exon...
- Patent number 12,064,483
- Issue date Aug 20, 2024
- AVIDITY BIOSCIENCES, INC.
- Arthur A. Levin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treating metastatic cancer and model systems for metastatic disease
- Patent number 12,059,480
- Issue date Aug 13, 2024
- Memorial Sloan Kettering Cancer Center
- Karuna Ganesh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Tunable endogenous protein degradation with heterobifunctional comp...
- Patent number 12,023,385
- Issue date Jul 2, 2024
- Dana-Farber Cancer Institute, Inc.
- Dennis Buckley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapies for lysosomal disorders
- Patent number 11,999,974
- Issue date Jun 4, 2024
- Prevail Therapeutics, Inc.
- Asa Abeliovich
- G01 - MEASURING TESTING
Information Patent Grant
Use of bacterial voltage gated ion channels for human therapies
- Patent number 11,980,671
- Issue date May 14, 2024
- Duke University
- Nenad Bursac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,913,001
- Issue date Feb 27, 2024
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,905,514
- Issue date Feb 20, 2024
- GlaxoSmithKline Biological S.A.
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV9-mediated gene therapy for treating mucopolysaccharidosis type I
- Patent number 11,890,329
- Issue date Feb 6, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunization of large mammals with low doses of RNA
- Patent number 11,891,608
- Issue date Feb 6, 2024
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for AADC deficiency
- Patent number 11,865,188
- Issue date Jan 9, 2024
- NATIONAL TAIWAN UNIVERSITY
- Mark Pykett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,851,660
- Issue date Dec 26, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,845,925
- Issue date Dec 19, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
In vivo therapeutic delivery procedure and device
- Patent number 11,839,761
- Issue date Dec 12, 2023
- Wisconsin Alumni Research Foundation
- Susan Hagness
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Codon optimized GLA genes and uses thereof
- Patent number 11,802,278
- Issue date Oct 31, 2023
- David H. Kirn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for the treatment of malignancies
- Patent number 11,801,312
- Issue date Oct 31, 2023
- University of South Florida
- Richard Heller
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods for selective kinase inhibition by endogenously produced an...
- Patent number 11,793,889
- Issue date Oct 24, 2023
- KINASE PHARMA INC.
- Bradley G Thompson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunization of large mammals with low doses of RNA
- Patent number 11,773,395
- Issue date Oct 3, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,739,334
- Issue date Aug 29, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Microbubble nucleic acid delivery platform
- Patent number 11,737,971
- Issue date Aug 29, 2023
- University of Pittsburgh of the Commonwealth System of Higher Education
- Flordeliza Villanueva
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Immunisation of large mammals with low doses of RNA
- Patent number 11,655,475
- Issue date May 23, 2023
- GlaxoSmithKline Biologicals SA
- Andrew Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method and system for optogenetics experiments
- Patent number 11,633,620
- Issue date Apr 25, 2023
- THE HONG KONG POLYTECHNIC UNIVERSITY SHENZHEN RESEARCH INSTITUTE
- Puxiang Lai
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Apparatus for efficient genetic modification of cells
- Patent number 11,584,908
- Issue date Feb 21, 2023
- The Charles Stark Draper Laboratory, Inc.
- Kenneth T. Kotz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunomodulating gene therapy
- Patent number 11,547,717
- Issue date Jan 10, 2023
- Duke University
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
ATP-binding cassette family coding polyribonucleotides and formulat...
- Patent number 11,479,768
- Issue date Oct 25, 2022
- ethris GmbH
- Christian Plank
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
BAG3 COMPOSITIONS AND METHODS
- Publication number 20250001014
- Publication date Jan 2, 2025
- Temple University - Of The Commonwealth System of Higher Education
- Arthur M. FELDMAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA
- Publication number 20240417740
- Publication date Dec 19, 2024
- GlaxoSmithKline Biologicals S.A.
- Andrew GEALL
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANELLOVECTORS FOR DELIVERY OF EFFECTORS TO THE CENTRAL NERVOUS SYSTEM
- Publication number 20240415978
- Publication date Dec 19, 2024
- FLAGSHIP PIONEERING INNOVATIONS V, INC.
- Roger Joseph Hajjar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF HEREDITARY ANGIOEDEMA WITH AAV GENE THERAPY VECTORS AN...
- Publication number 20240408240
- Publication date Dec 12, 2024
- BioMarin Pharmaceutical Inc.
- Peter COLOSI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD AND PHARMACEUTICAL COMPOSITION FOR TREATING A CARTILAGE DAMA...
- Publication number 20240408237
- Publication date Dec 12, 2024
- Far Eastern Memorial Hospital
- Hsiu-Jung LIAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METH...
- Publication number 20240390516
- Publication date Nov 28, 2024
- Jaguar Gene Therapy, LLC
- Michael Hughes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSGENE CASSETTES, AAV VECTORS AND AAV VIRAL VECTORS FOR THE EXPR...
- Publication number 20240376498
- Publication date Nov 14, 2024
- The Board of Regents of the University of Texas System
- Steven J. GRAY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR IMPROVED TREATMENT OF X-LINKED MYOTUBU...
- Publication number 20240366785
- Publication date Nov 7, 2024
- Audentes Therapeutics, Inc.
- Weston MILLER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...
- Publication number 20240358736
- Publication date Oct 31, 2024
- Avidity Biosciences, Inc.
- Arthur A. LEVIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS AND METHODS FOR NUCLEIC ACID EXPRESSION IN VIVO
- Publication number 20240350662
- Publication date Oct 24, 2024
- DNARx
- Robert James Debs
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Method of Enhancing Gene Therapy by Targeting cGAS-STING Pathway
- Publication number 20240350667
- Publication date Oct 24, 2024
- Spark Therapeutics, Inc.
- Xavier Anguel
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IGK SIG...
- Publication number 20240342313
- Publication date Oct 17, 2024
- PHARMA CINQ, LLC
- Tianci LUO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
JUNCTOPHILIN-2 (JPH2) GENE THERAPY USING AAV VECTOR
- Publication number 20240335565
- Publication date Oct 10, 2024
- Spacecraft Seven, LLC
- Christopher Dean HERZOG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATING DISEASES AND IMPROVING NUCLEIC ACID DELIVERY
- Publication number 20240325570
- Publication date Oct 3, 2024
- Mayo Foundation for Medical Education and Research
- Michael A. Barry
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCL...
- Publication number 20240316217
- Publication date Sep 26, 2024
- Regents of the University of Minnesota
- R. Scott McIvor
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV9-MEDIATED GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I
- Publication number 20240307511
- Publication date Sep 19, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
THERAPEUTIC GENE SILENCING WITH CRISPR-CAS13
- Publication number 20240307557
- Publication date Sep 19, 2024
- THE BOARD OF TRUSTEES OF THE UNIVERSITY OF ILLINOIS
- THOMAS GAJ
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR ADMINISTERING OTOFERLIN DUAL VECTOR SY...
- Publication number 20240309399
- Publication date Sep 19, 2024
- Decibel Therapeutics, Inc.
- Qi-Ying HU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
APOE AND APOB MODIFIED LIPID NANOPARTICLE COMPOSITIONS AND USES THE...
- Publication number 20240299580
- Publication date Sep 12, 2024
- GENERATION BIO CO.
- Michelle LeBlanc
- B82 - NANO-TECHNOLOGY
Information Patent Application
GENE THERAPIES FOR LYSOSOMAL DISORDERS
- Publication number 20240287471
- Publication date Aug 29, 2024
- Prevail Therapeutics, Inc.
- Asa ABELIOVICH
- G01 - MEASURING TESTING
Information Patent Application
CENTRAL NERVOUS SYSTEM TARGETING POLYNUCLEOTIDES
- Publication number 20240285667
- Publication date Aug 29, 2024
- VOYAGER THERAPEUTICS, INC.
- Gregory Robert Stewart
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR DEPLETING ANTIBODIES
- Publication number 20240271115
- Publication date Aug 15, 2024
- The University of North Carolina at Chapel Hill
- Haiyan Fu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRODUCTS AND METHODS FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20240261434
- Publication date Aug 8, 2024
- Research Institute at Nationwide Children's Hospital
- Kevin Flanigan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ELECTROPORATION GENE THERAPY FOR TISSUE BARRIERS
- Publication number 20240238450
- Publication date Jul 18, 2024
- COCHLEAR LIMITED
- Wolfram Frederik DUECK
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TREATMENT METHOD OF LEFT VENTRICULAR DYSFUNCTION FOLLOWING AN ACUTE...
- Publication number 20240238449
- Publication date Jul 18, 2024
- Universidad De Murcia
- Domingo Andrés PASCUAL FIGAL
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Application
GENE THERAPY FOR ARRHYTHMOGENIC RIGHT VENTRICULAR CARDIOMYOPATHY
- Publication number 20240216541
- Publication date Jul 4, 2024
- The Regents of the University of California
- Farah Sheikh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING OCULAR DISEASES USING AAV2 VARIANTS ENCODING AF...
- Publication number 20240197915
- Publication date Jun 20, 2024
- Adverum Biotechnologies, Inc.
- Julie CLARK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VIRAL VECTORS WITH REDUCED IMMUNOGENICITY
- Publication number 20240182922
- Publication date Jun 6, 2024
- Cornell University
- Shaoyi JIANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING OSMIDROSIS
- Publication number 20240167028
- Publication date May 23, 2024
- Roger L. Kaspar
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Conjugated Antisense Compounds for Use in Therapy
- Publication number 20240165146
- Publication date May 23, 2024
- Ionis Pharmaceuticals, Inc.
- Nicholas J. Viney
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the administration regime

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Gene therapy for ciliopathies

Apparatus for efficient genetic modification of cells

Immunostimulating vector system

Methods for efficient delivery of therapeutic molecules in vitro an...

Gene therapy of hemophilia a using viral vectors encoding recombina...

Transgene cassettes, AAV vectors and AAV viral vectors for the expr...

Nucleic acid-polypeptide compositions and methods of inducing exon...

Treating metastatic cancer and model systems for metastatic disease

Tunable endogenous protein degradation with heterobifunctional comp...

Gene therapies for lysosomal disorders

Use of bacterial voltage gated ion channels for human therapies

Immunisation of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

AAV9-mediated gene therapy for treating mucopolysaccharidosis type I

Immunization of large mammals with low doses of RNA

Gene therapy for AADC deficiency

Immunisation of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

In vivo therapeutic delivery procedure and device

Codon optimized GLA genes and uses thereof

Method for the treatment of malignancies

Methods for selective kinase inhibition by endogenously produced an...

Immunization of large mammals with low doses of RNA

Immunisation of large mammals with low doses of RNA

Microbubble nucleic acid delivery platform

Immunisation of large mammals with low doses of RNA

Method and system for optogenetics experiments

Apparatus for efficient genetic modification of cells

Immunomodulating gene therapy

ATP-binding cassette family coding polyribonucleotides and formulat...

Patents Applicationslast 30 patents

BAG3 COMPOSITIONS AND METHODS

IMMUNISATION OF LARGE MAMMALS WITH LOW DOSES OF RNA

ANELLOVECTORS FOR DELIVERY OF EFFECTORS TO THE CENTRAL NERVOUS SYSTEM

TREATMENT OF HEREDITARY ANGIOEDEMA WITH AAV GENE THERAPY VECTORS AN...

METHOD AND PHARMACEUTICAL COMPOSITION FOR TREATING A CARTILAGE DAMA...

ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METH...

TRANSGENE CASSETTES, AAV VECTORS AND AAV VIRAL VECTORS FOR THE EXPR...

COMPOSITIONS AND METHODS FOR IMPROVED TREATMENT OF X-LINKED MYOTUBU...

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...

SYSTEMS AND METHODS FOR NUCLEIC ACID EXPRESSION IN VIVO

Method of Enhancing Gene Therapy by Targeting cGAS-STING Pathway

VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IGK SIG...

JUNCTOPHILIN-2 (JPH2) GENE THERAPY USING AAV VECTOR

TREATING DISEASES AND IMPROVING NUCLEIC ACID DELIVERY

METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCL...

AAV9-MEDIATED GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I

THERAPEUTIC GENE SILENCING WITH CRISPR-CAS13

METHODS AND COMPOSITIONS FOR ADMINISTERING OTOFERLIN DUAL VECTOR SY...

APOE AND APOB MODIFIED LIPID NANOPARTICLE COMPOSITIONS AND USES THE...

GENE THERAPIES FOR LYSOSOMAL DISORDERS

CENTRAL NERVOUS SYSTEM TARGETING POLYNUCLEOTIDES

METHODS AND COMPOSITIONS FOR DEPLETING ANTIBODIES

PRODUCTS AND METHODS FOR TREATING MUSCULAR DYSTROPHY

ELECTROPORATION GENE THERAPY FOR TISSUE BARRIERS

TREATMENT METHOD OF LEFT VENTRICULAR DYSFUNCTION FOLLOWING AN ACUTE...

GENE THERAPY FOR ARRHYTHMOGENIC RIGHT VENTRICULAR CARDIOMYOPATHY

METHODS OF TREATING OCULAR DISEASES USING AAV2 VARIANTS ENCODING AF...

VIRAL VECTORS WITH REDUCED IMMUNOGENICITY

METHODS OF TREATING OSMIDROSIS

Conjugated Antisense Compounds for Use in Therapy