Nucleic acids adapted for tissue specific expression

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A61K48/0058

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

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A61K48/0058Nucleic acids adapted for tissue specific expression

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Patents Grantslast 30 patents

Information Patent Grant
Nucleic acid molecules and uses thereof for non-viral gene therapy
- Patent number 12,364,774
- Issue date Jul 22, 2025
- Bioverativ Therapeutics Inc.
- Tongyao Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating laminopathies
- Patent number 12,357,707
- Issue date Jul 15, 2025
- Encoded Therapeutics, Inc.
- Sirika Wood
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Use of a small native peptide activator of SERCA pump for treatment...
- Patent number 12,351,609
- Issue date Jul 8, 2025
- The Board of Regents of the University of Texas System
- Eric N. Olson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene editing of CAR-T cells for the treatment of T cell malignancie...
- Patent number 12,350,349
- Issue date Jul 8, 2025
- Washington University
- John F. DiPersio
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy constructs for treating Wilson disease
- Patent number 12,338,450
- Issue date Jun 24, 2025
- Ultragenyx Pharmaceutical Inc.
- Christine Livingston
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Treatment of spinal and bulbar muscular atrophy
- Patent number 12,331,101
- Issue date Jun 17, 2025
- Oxford University Innovation Limited
- Carlo Rinaldi
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Capsid variants and methods of using the same
- Patent number 12,331,081
- Issue date Jun 17, 2025
- DYNO THERAPEUTICS, INC.
- Ina Chen
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Capsid variants and methods of using the same
- Patent number 12,331,082
- Issue date Jun 17, 2025
- DYNO THERAPEUTICS, INC.
- Ina Chen
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Recombinant nucleic acid molecule and application thereof in prepar...
- Patent number 12,331,290
- Issue date Jun 17, 2025
- Purecodon (Hong Kong) Biopharma Ltd.
- Zonghao Qiu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Therapeutic agents comprising nucleic acids and CAR-modified immune...
- Patent number 12,329,826
- Issue date Jun 17, 2025
- Hangzhou Converd Co., Ltd.
- Fang Hu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Pharmaceutical compositions for the treatment of cancer
- Patent number 12,310,936
- Issue date May 27, 2025
- Seleq Oy
- Mikael Björnstedt
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
AAV capsid variants and uses thereof
- Patent number 12,296,025
- Issue date May 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transcription regulatory elements and uses thereof
- Patent number 12,296,026
- Issue date May 13, 2025
- Astellas Gene Therapies, Inc.
- John T. Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized promoter sequences, intron-free expression constructs and...
- Patent number 12,290,574
- Issue date May 6, 2025
- SPARK THERAPEUTICS, INC.
- Xavier Anguela
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Heterologous targeting peptide grafted AAVs
- Patent number 12,291,719
- Issue date May 6, 2025
- UNIVERSITY OF MASSACHUSETTS
- Miguel Sena Esteves
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Means and methods for AAV gene therapy in humans
- Patent number 12,285,451
- Issue date Apr 29, 2025
- Uniqure IP B.V.
- Bart Antonius Nijmeijer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Genome editing methods and constructs
- Patent number 12,285,495
- Issue date Apr 29, 2025
- FONDAZIONE TELETHON ETS
- Alberto Auricchio
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus virions for treatment of epilepsy
- Patent number 12,263,231
- Issue date Apr 1, 2025
- Jichi Medical University
- Shin-ichi Muramatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized mini-dystrophin genes and expression cassettes and their use
- Patent number 12,257,321
- Issue date Mar 25, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimised coding sequence and promoter
- Patent number 12,257,319
- Issue date Mar 25, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for NMNAT1-associated retinal degeneration
- Patent number 12,257,320
- Issue date Mar 25, 2025
- Massachusetts Eye and Ear Infirmary
- Eric A. Pierce
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating non-arteritic anterior ischemic optic neuropathy
- Patent number 12,252,518
- Issue date Mar 18, 2025
- Life Biosciences, Inc.
- Michel Wathier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Myosin 15 promoters and uses thereof
- Patent number 12,252,520
- Issue date Mar 18, 2025
- Decibel Therapeutics, Inc.
- Joseph Burns
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for the treatment of CNGB1-linked retinitis pigmentosa
- Patent number 12,246,072
- Issue date Mar 11, 2025
- Stylianos Michalakis
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Treatment of mucopolysaccharidosis IVA
- Patent number 12,247,213
- Issue date Mar 11, 2025
- The Nemours Foundation
- Shunji Tomatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified ligand-gated ion channels and methods of use
- Patent number 12,247,064
- Issue date Mar 11, 2025
- Howard Hughes Medical Institute
- Scott Sternson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
DNA vector for targeted gene therapy
- Patent number 12,246,073
- Issue date Mar 11, 2025
- GENETIC DIAGNOSTICS AND THERAPY 21 LTD
- Anton Gamolski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus factor VIII vectors
- Patent number 12,239,692
- Issue date Mar 4, 2025
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Drug and gene therapy to treat high myopia and other ocular disorde...
- Patent number 12,233,050
- Issue date Feb 25, 2025
- City University of Hong Kong
- Wenjun Xiong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic constructs for treating cancer
- Patent number 12,233,135
- Issue date Feb 25, 2025
- PRECISION MOLECULAR INC.
- Christopher Ullman
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
GENE EDITING REPORTER SYSTEM AND GUIDE RNA AND COMPOSITION RELATED...
- Publication number 20250235559
- Publication date Jul 24, 2025
- Incisive Genetics Inc.
- Blair LEAVITT
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ADENO-ASSOCIATED VIRUS POTENCY ASSAY AND USES THEREOF
- Publication number 20250235560
- Publication date Jul 24, 2025
- Astellas Gene Therapies, Inc.
- Yukari MORIYA
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MATERIALS AND METHODS FOR TREATMENT OF HEREDITARY HAEMOCHROMATOSIS
- Publication number 20250235561
- Publication date Jul 24, 2025
- CRISPR Therapeutics AG
- Roman Lvovitch Bogorad
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MULTIPLEX ASSAY
- Publication number 20250230445
- Publication date Jul 17, 2025
- Cairn Biosciences, Inc.
- M. Susana G. DE ABREU RIBEIRO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20250228967
- Publication date Jul 17, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY
- Publication number 20250228973
- Publication date Jul 17, 2025
- PRECISION BIOSCIENCES, INC.
- James Jefferson Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATION OF NEURAL PATHWAYS
- Publication number 20250228974
- Publication date Jul 17, 2025
- EOS NEUROSCIENCE, INC
- Alan Horsager
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...
- Publication number 20250230467
- Publication date Jul 17, 2025
- The Johns Hopkins University
- Ingie Hong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS...
- Publication number 20250228976
- Publication date Jul 17, 2025
- THE BROAD INSTITUTE, INC.
- Benjamin Deverman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES
- Publication number 20250228975
- Publication date Jul 17, 2025
- CRISPR Therapeutics AG
- Sanjay D'SOUZA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treating Striatonigral Degeneration
- Publication number 20250228977
- Publication date Jul 17, 2025
- Texas Scottish Rite Hospital for Children
- Jonathan J. Rios
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TISSUE-SPECIFIC PROMOTER AND USE THEREOF
- Publication number 20250230466
- Publication date Jul 17, 2025
- BEIJING MEIKANG GENO-IMMUNE BIOTECHNOLOGY CO., LTD.
- Lung-Ji Chang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION
- Publication number 20250222139
- Publication date Jul 10, 2025
- Shape Therapeutics Inc.
- Jacob Michael TOME
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENOME EDITING METHODS AND CONSTRUCTS
- Publication number 20250222140
- Publication date Jul 10, 2025
- Fondazione Telethon ETS
- Alberto Auricchio
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SITE-SPECIFIC IN VIVO T CELL ENGINEERING, SYSTEMS, COMPOSITIONS AND...
- Publication number 20250222138
- Publication date Jul 10, 2025
- Ramot at Tel Aviv University Ltd.
- Adi BARZEL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING...
- Publication number 20250222137
- Publication date Jul 10, 2025
- Akouos, Inc.
- Katherine Diane GRIBBLE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR THE TREATMENT OF PARKINSON'S DISEASE
- Publication number 20250222072
- Publication date Jul 10, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Krystof S. BANKIEWICZ
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Cochlear and/or vestibular cell specific promoter and use thereof
- Publication number 20250213728
- Publication date Jul 3, 2025
- Shanghai Emaygene Technology Co.,Ltd.
- Guisheng ZHONG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL ANELLOVIRIDAE FAMILY VECTOR COMPOSITIONS AND METHODS
- Publication number 20250213725
- Publication date Jul 3, 2025
- FLAGSHIP PIONEERING INNOVATIONS V, INC.
- Lianna Swanson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD TO STIMULATE REGENERATION OF RETINAL GANGLION CELLS
- Publication number 20250213729
- Publication date Jul 3, 2025
- University of Washington
- Levi J. Todd
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DOMINANT-NEGATIVE TUMOR NECROSIS FACTOR ALPHA ADENO-ASSOCIATED VIRU...
- Publication number 20250213727
- Publication date Jul 3, 2025
- Regenxbio Inc.
- Danielle SLITER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR DISEASES WITH CNS MANIFESTATIONS
- Publication number 20250213730
- Publication date Jul 3, 2025
- Takeda Pharmaceutical Company Limited
- Rizwana ISLAM
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC AC...
- Publication number 20250213726
- Publication date Jul 3, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Anna TRETIAKOVA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ULTRASOUND-MEDIATED GENE THERAPY FOR DEEP VEIN THROMBOSIS AND POST-...
- Publication number 20250213695
- Publication date Jul 3, 2025
- Cedars-Sinai Medical Center
- Dan Gazit
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF
- Publication number 20250205366
- Publication date Jun 26, 2025
- Huidagene Therapeutics (Singapore) Pte. Ltd.
- Xing Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...
- Publication number 20250205365
- Publication date Jun 26, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED MUSCLE-SPECIFIC PROMOTERS
- Publication number 20250207126
- Publication date Jun 26, 2025
- Regenxbio Inc.
- Ye Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DRUG AND METHOD FOR FORMING GABAERGIC NEURONS
- Publication number 20250205364
- Publication date Jun 26, 2025
- JINAN UNIVERSITY
- Gong CHEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS COMPRISING A MUSCLE ACTIVE PROMOTER AND METHODS OF USI...
- Publication number 20250205367
- Publication date Jun 26, 2025
- DUKE UNIVERSITY
- Dwight Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING TNNT2 RELATED CARDIOMYOPATHY...
- Publication number 20250195694
- Publication date Jun 19, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Nucleic acids adapted for tissue specific expression

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Nucleic acid molecules and uses thereof for non-viral gene therapy

Compositions and methods for treating laminopathies

Use of a small native peptide activator of SERCA pump for treatment...

Gene editing of CAR-T cells for the treatment of T cell malignancie...

Gene therapy constructs for treating Wilson disease

Treatment of spinal and bulbar muscular atrophy

Capsid variants and methods of using the same

Capsid variants and methods of using the same

Recombinant nucleic acid molecule and application thereof in prepar...

Therapeutic agents comprising nucleic acids and CAR-modified immune...

Pharmaceutical compositions for the treatment of cancer

AAV capsid variants and uses thereof

Transcription regulatory elements and uses thereof

Optimized promoter sequences, intron-free expression constructs and...

Heterologous targeting peptide grafted AAVs

Means and methods for AAV gene therapy in humans

Genome editing methods and constructs

Adeno-associated virus virions for treatment of epilepsy

Optimized mini-dystrophin genes and expression cassettes and their use

Optimised coding sequence and promoter

Gene therapy for NMNAT1-associated retinal degeneration

Methods of treating non-arteritic anterior ischemic optic neuropathy

Myosin 15 promoters and uses thereof

Gene therapy for the treatment of CNGB1-linked retinitis pigmentosa

Treatment of mucopolysaccharidosis IVA

Modified ligand-gated ion channels and methods of use

DNA vector for targeted gene therapy

Adeno-associated virus factor VIII vectors

Drug and gene therapy to treat high myopia and other ocular disorde...

Therapeutic constructs for treating cancer

Patents Applicationslast 30 patents

GENE EDITING REPORTER SYSTEM AND GUIDE RNA AND COMPOSITION RELATED...

ADENO-ASSOCIATED VIRUS POTENCY ASSAY AND USES THEREOF

MATERIALS AND METHODS FOR TREATMENT OF HEREDITARY HAEMOCHROMATOSIS

MULTIPLEX ASSAY

AAV CAPSID VARIANTS AND USES THEREOF

GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY

MODULATION OF NEURAL PATHWAYS

METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...

AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS...

METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES

Compositions and Methods for Treating Striatonigral Degeneration

TISSUE-SPECIFIC PROMOTER AND USE THEREOF

PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION

GENOME EDITING METHODS AND CONSTRUCTS

SITE-SPECIFIC IN VIVO T CELL ENGINEERING, SYSTEMS, COMPOSITIONS AND...

GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING...

METHODS AND COMPOSITIONS FOR THE TREATMENT OF PARKINSON'S DISEASE

Cochlear and/or vestibular cell specific promoter and use thereof

NOVEL ANELLOVIRIDAE FAMILY VECTOR COMPOSITIONS AND METHODS

METHOD TO STIMULATE REGENERATION OF RETINAL GANGLION CELLS

DOMINANT-NEGATIVE TUMOR NECROSIS FACTOR ALPHA ADENO-ASSOCIATED VIRU...

GENE THERAPY FOR DISEASES WITH CNS MANIFESTATIONS

THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC AC...

ULTRASOUND-MEDIATED GENE THERAPY FOR DEEP VEIN THROMBOSIS AND POST-...

GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF

METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...

MODIFIED MUSCLE-SPECIFIC PROMOTERS

DRUG AND METHOD FOR FORMING GABAERGIC NEURONS

COMPOSITIONS COMPRISING A MUSCLE ACTIVE PROMOTER AND METHODS OF USI...

METHODS AND COMPOSITIONS FOR TREATING TNNT2 RELATED CARDIOMYOPATHY...