Nucleic acids or oligonucleotides having modified sugars

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A61K31/712

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K31/00Medicinal preparations containing organic active ingredients

Current Industry

A61K31/712Nucleic acids or oligonucleotides having modified sugars

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Patents Grantslast 30 patents

Information Patent Grant
Compounds and compositions including phosphorothioated oligodeoxynu...
- Patent number 12,227,745
- Issue date Feb 18, 2025
- City of Hope
- Marcin Tomasz Kortylewski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
PSMD9 inhibitors for the treatment of hepatic lipid dysregulation
- Patent number 12,221,491
- Issue date Feb 11, 2025
- Baker Heart and Diabetes Institute
- Anna Christine Drew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense antibacterial compounds and methods
- Patent number 12,209,240
- Issue date Jan 28, 2025
- Board of Regents, The University of Texas System
- David Greenberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating myelodysplastic syndrome
- Patent number 12,201,645
- Issue date Jan 21, 2025
- Geron Corporation
- Jacqueline Cirillo Bussolari
- G01 - MEASURING TESTING
Information Patent Grant
Compositions for stimulation of mammalian innate immune resistance...
- Patent number 12,201,684
- Issue date Jan 21, 2025
- The Board of Regents, The University of Texas System
- Burton Dickey
- Y02 - TECHNOLOGIES OR APPLICATIONS FOR MITIGATION OR ADAPTATION AGAINST CLIMA...
Information Patent Grant
Compounds and methods for modulating ATXN1
- Patent number 12,180,479
- Issue date Dec 31, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating myelodysplastic syndrome
- Patent number 12,171,778
- Issue date Dec 24, 2024
- Geron Corporation
- Aleksandra Rizo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA-editing oligonucleotides and uses thereof
- Patent number 12,173,285
- Issue date Dec 24, 2024
- Korro Bio, Inc.
- Andrew W. Fraley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for the treatment of expanded repeat-assoc...
- Patent number 12,161,658
- Issue date Dec 10, 2024
- UNIVERSITY OF MASSACHUSETTS
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleoside-modified RNA for inducing an adaptive immune response
- Patent number 12,138,305
- Issue date Nov 12, 2024
- The Trustees of the University of Pennsylvania
- Drew Weissman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Coronavirus vaccine
- Patent number 12,133,899
- Issue date Nov 5, 2024
- BIONTECH SE
- Ugur Sahin
- B82 - NANO-TECHNOLOGY
Information Patent Grant
Non-liposomal systems for nucleic acid delivery
- Patent number 12,129,467
- Issue date Oct 29, 2024
- ARBUTUS BIOPHARMA CORPORATION
- Ed Yaworski
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Modified antisense oligomers for exon inclusion in spinal muscular...
- Patent number 12,121,532
- Issue date Oct 22, 2024
- Sarepta Therapeutics, Inc.
- Marco A. Passini
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
TREM compositions and uses thereof
- Patent number 12,121,531
- Issue date Oct 22, 2024
- FLAGSHIP PIONEERING INNOVATIONS VI, LLC
- Theonie Anastassiadis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antiviral agents for treatment of coronaviruses
- Patent number 12,121,533
- Issue date Oct 22, 2024
- Meharry Medical College
- Donald J. Alcendor
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
GLP-1 receptor ligand moiety conjugated oligonucleotides and uses t...
- Patent number 12,115,225
- Issue date Oct 15, 2024
- Astrazeneca AB
- Brett P. Monia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for synthesizing 5′-capped RNAs
- Patent number 12,103,944
- Issue date Oct 1, 2024
- TriLink Biotechnologies, LLC
- Richard I. Hogrefe
- A23 - FOODS OR FOODSTUFFS THEIR TREATMENT, NOT COVERED BY OTHER CLASSES
Information Patent Grant
Antisense oligonucleic acid
- Patent number 12,104,154
- Issue date Oct 1, 2024
- Osaka University
- Satoshi Obika
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating facioscapulohumeral muscular d...
- Patent number 12,104,156
- Issue date Oct 1, 2024
- AVIDITY BIOSCIENCES, INC.
- Barbora Malecova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
P-ethoxy nucleic acids for liposomal formulation
- Patent number 12,097,214
- Issue date Sep 24, 2024
- BIO-PATH HOLDINGS, INC.
- Peter Nielsen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating PNPLA3 expression
- Patent number 12,084,662
- Issue date Sep 10, 2024
- Dicerna Pharmaceuticals, Inc.
- Utsav Saxena
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified oligonucleotides and methods of use
- Patent number 12,077,757
- Issue date Sep 3, 2024
- JANSSEN PHARMACEUTICA NV
- Sergei Gryaznov
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Anti-transferrin receptor antibody-PMO conjugates for inducing DMD...
- Patent number 12,071,621
- Issue date Aug 27, 2024
- AVIDITY BIOSCIENCES, INC.
- Beatrice Diana Darimont
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
SERPINA1 iRNA compositions and methods of use thereof
- Patent number 12,071,619
- Issue date Aug 27, 2024
- Alnylam Pharmaceuticals, Inc.
- Alfica Sehgal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Splice-switching oligonucleotides and methods of use
- Patent number 12,071,626
- Issue date Aug 27, 2024
- Duke University
- Jennifer Freedman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for treating cancers and enhancing therape...
- Patent number 12,064,446
- Issue date Aug 20, 2024
- Thomas Jefferson University
- David W. Andrews
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense nucleic acids
- Patent number 12,060,556
- Issue date Aug 13, 2024
- Nippon Shinyaku Co., Ltd.
- Naoki Watanabe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeted nanocarriers for targeted drug delivery of gene therapeutics
- Patent number 12,059,475
- Issue date Aug 13, 2024
- SOLMIC BIOTECH GMBH
- Marcus Furch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating Facioscapulohumeral muscular d...
- Patent number 12,049,629
- Issue date Jul 30, 2024
- AVIDITY BIOSCIENCES, INC.
- Barbora Malecova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense compounds targeting genes associated with cystic fibrosis
- Patent number 12,042,508
- Issue date Jul 23, 2024
- Rosalind Franklin University of Medicine and Science
- Michelle L. Hastings
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING

Patents Applicationslast 30 patents

Information Patent Application
MICRORNA-BASED PARTICLE FOR THE TREATMENT OF DYSREGULATED IMMUNE RE...
- Publication number 20250049837
- Publication date Feb 13, 2025
- UNITY HEALTH TORONTO
- CLAUDIA CHIMISSO DOS SANTOS
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATING GLYCOGEN SYNTHASE 1
- Publication number 20250051781
- Publication date Feb 13, 2025
- Ionis Pharmaceuticals, Inc.
- Huynh-Hoa Bui
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Compounds Targeting Genes Associated with Cystic Fibrosis
- Publication number 20250049838
- Publication date Feb 13, 2025
- ROSALIND FRANKLIN UNIVERSITY OF MEDICINE AND SCIENCE
- Michelle L. Hastings
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Application
NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY
- Publication number 20250034571
- Publication date Jan 30, 2025
- ARBUTUS BIOPHARMA CORPORATION
- Ed Yaworski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC NUCLEIC ACIDS AND METHODS OF USE THEREOF
- Publication number 20250025487
- Publication date Jan 23, 2025
- Cedars-Sinai Medical Center
- Eduardo Marbán
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods and Compositions for Treating Cancers and Enhancing Therape...
- Publication number 20250009781
- Publication date Jan 9, 2025
- Thomas Jefferson University
- David W. Andrews
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TOLL-LIKE RECEPTOR THERAPY COMBINATIONS WITH CBL-B INHIBITOR COMPOUNDS
- Publication number 20250009731
- Publication date Jan 9, 2025
- Nurix Therapeutics, Inc.
- Marilena GALLOTTA
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TREM COMPOSITIONS AND USES THEREOF
- Publication number 20250000890
- Publication date Jan 2, 2025
- Flagship Pioneering Innovations VI, LLC.
- Theonie Anastassiadis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PARN AS A BIOMARKER AND THERAPEUTIC TARGET
- Publication number 20240425866
- Publication date Dec 26, 2024
- The Regents of the University of Colorado, a Body Corporate
- Roy R. Parker
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MICRORNA-BASED PARTICLE FOR THE TREATMENT OF DYSREGULATED IMMUNE RE...
- Publication number 20240415867
- Publication date Dec 19, 2024
- UNITY HEALTH TORONTO
- CLAUDIA CHIMISSO DOS SANTOS
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
- Publication number 20240417721
- Publication date Dec 19, 2024
- ProQR Therapeutics II B.V.
- Janne Juha TURUNEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTAGONIST OF THE MIRNA-106B-5P TO TREAT OR PREVENT THE CARDIOTOXIC...
- Publication number 20240417727
- Publication date Dec 19, 2024
- Universidad De Murcia
- Domingo Andrés PASCUAL FIGAL
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING PNPLA3 EXPRESSION
- Publication number 20240401059
- Publication date Dec 5, 2024
- Dicerna Pharmaceuticals, Inc.
- Utsav SAXENA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC AGENTS FOR THE TREATMENT OF DISEASES ASSOCIATED WITH UN...
- Publication number 20240400667
- Publication date Dec 5, 2024
- FUNDACIO PRIVADA INSTITUCIO CATALANA DE RECERCA I ESTUDIS AVANCATS (ICREA)
- Joan SEOANE SUÁREZ
- G01 - MEASURING TESTING
Information Patent Application
LIPOCATIONIC DENDRIMERS AND USES THEREOF
- Publication number 20240391869
- Publication date Nov 28, 2024
- The Board of Regents of the University of Texas System
- Daniel J. SIEGWART
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RNA CONSTRUCTS AND USES THEREOF
- Publication number 20240390524
- Publication date Nov 28, 2024
- BIONTECH SE
- Ugur Sahin
- B82 - NANO-TECHNOLOGY
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN
- Publication number 20240376469
- Publication date Nov 14, 2024
- Ionis Pharmaceuticals, Inc.
- Bethany Fitzsimmons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTI-TRANSFERRIN RECEPTOR ANTIBODY-PMO CONJUGATES FOR INDUCING DMD...
- Publication number 20240368598
- Publication date Nov 7, 2024
- Avidity Biosciences, Inc.
- Beatrice Diana DARIMONT
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Nucleic Acids
- Publication number 20240368597
- Publication date Nov 7, 2024
- NIPPON SHINYAKU CO., LTD.
- Yukiko ENYA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATING SCN1A EXPRESSION
- Publication number 20240360449
- Publication date Oct 31, 2024
- Ionis Pharmaceuticals, Inc.
- Paymaan Jafar-nejad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compounds and Methods for Reducing LRRK2 Expression
- Publication number 20240360453
- Publication date Oct 31, 2024
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CA...
- Publication number 20240352462
- Publication date Oct 24, 2024
- Dana-Farber Cancer Institute, Inc.
- Nikhil C. Munshi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS
- Publication number 20240344072
- Publication date Oct 17, 2024
- UCL Business LTD
- Haiyan Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DNAZYMES TARGETING CELL WALL SYNTHESIS ENZYMES AND USES THEREOF
- Publication number 20240336923
- Publication date Oct 10, 2024
- 1E Therapeutics, Ltd.
- Ido BACHELET
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ALLELE-SELECTIVE COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN EX...
- Publication number 20240325425
- Publication date Oct 3, 2024
- Ionis Pharmaceuticals, Inc.
- Michael OESTERGAARD
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
POLYNUCLEOTIDE AND PHARMACEUTICAL COMPOSITION
- Publication number 20240325426
- Publication date Oct 3, 2024
- KYOWA KIRIN CO., LTD.
- Hiroto Iwai
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NEPHROTOXICITY REDUCING AGENT
- Publication number 20240316093
- Publication date Sep 26, 2024
- Nippon Shinyaku Co., Ltd.
- Takashi HORIUCHI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20240318177
- Publication date Sep 26, 2024
- Dyne Therapeutics, Inc.
- Cody A. Desjardins
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR INCREASING STMN2 EXPRESSION
- Publication number 20240316092
- Publication date Sep 26, 2024
- Ionis Pharmaceuticals, Inc.
- Huynh-Hoa Bui
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR D...
- Publication number 20240309382
- Publication date Sep 19, 2024
- Avidity Biosciences, Inc.
- Barbora MALECOVA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Nucleic acids or oligonucleotides having modified sugars

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compounds and compositions including phosphorothioated oligodeoxynu...

PSMD9 inhibitors for the treatment of hepatic lipid dysregulation

Antisense antibacterial compounds and methods

Methods of treating myelodysplastic syndrome

Compositions for stimulation of mammalian innate immune resistance...

Compounds and methods for modulating ATXN1

Methods of treating myelodysplastic syndrome

RNA-editing oligonucleotides and uses thereof

Compositions and methods for the treatment of expanded repeat-assoc...

Nucleoside-modified RNA for inducing an adaptive immune response

Coronavirus vaccine

Non-liposomal systems for nucleic acid delivery

Modified antisense oligomers for exon inclusion in spinal muscular...

TREM compositions and uses thereof

Antiviral agents for treatment of coronaviruses

GLP-1 receptor ligand moiety conjugated oligonucleotides and uses t...

Compositions and methods for synthesizing 5′-capped RNAs

Antisense oligonucleic acid

Compositions and methods of treating facioscapulohumeral muscular d...

P-ethoxy nucleic acids for liposomal formulation

Compositions and methods for modulating PNPLA3 expression

Modified oligonucleotides and methods of use

Anti-transferrin receptor antibody-PMO conjugates for inducing DMD...

SERPINA1 iRNA compositions and methods of use thereof

Splice-switching oligonucleotides and methods of use

Methods and compositions for treating cancers and enhancing therape...

Antisense nucleic acids

Targeted nanocarriers for targeted drug delivery of gene therapeutics

Compositions and methods of treating Facioscapulohumeral muscular d...

Antisense compounds targeting genes associated with cystic fibrosis

Patents Applicationslast 30 patents

MICRORNA-BASED PARTICLE FOR THE TREATMENT OF DYSREGULATED IMMUNE RE...

COMPOUNDS AND METHODS FOR MODULATING GLYCOGEN SYNTHASE 1

Antisense Compounds Targeting Genes Associated with Cystic Fibrosis

NON-LIPOSOMAL SYSTEMS FOR NUCLEIC ACID DELIVERY

THERAPEUTIC NUCLEIC ACIDS AND METHODS OF USE THEREOF

Methods and Compositions for Treating Cancers and Enhancing Therape...

TOLL-LIKE RECEPTOR THERAPY COMBINATIONS WITH CBL-B INHIBITOR COMPOUNDS

TREM COMPOSITIONS AND USES THEREOF

PARN AS A BIOMARKER AND THERAPEUTIC TARGET

MICRORNA-BASED PARTICLE FOR THE TREATMENT OF DYSREGULATED IMMUNE RE...

SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES

ANTAGONIST OF THE MIRNA-106B-5P TO TREAT OR PREVENT THE CARDIOTOXIC...

COMPOSITIONS AND METHODS FOR MODULATING PNPLA3 EXPRESSION

THERAPEUTIC AGENTS FOR THE TREATMENT OF DISEASES ASSOCIATED WITH UN...

LIPOCATIONIC DENDRIMERS AND USES THEREOF

RNA CONSTRUCTS AND USES THEREOF

COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN

ANTI-TRANSFERRIN RECEPTOR ANTIBODY-PMO CONJUGATES FOR INDUCING DMD...

Antisense Nucleic Acids

COMPOUNDS AND METHODS FOR MODULATING SCN1A EXPRESSION

Compounds and Methods for Reducing LRRK2 Expression

ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CA...

TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS

DNAZYMES TARGETING CELL WALL SYNTHESIS ENZYMES AND USES THEREOF

ALLELE-SELECTIVE COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN EX...

POLYNUCLEOTIDE AND PHARMACEUTICAL COMPOSITION

NEPHROTOXICITY REDUCING AGENT

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

COMPOUNDS AND METHODS FOR INCREASING STMN2 EXPRESSION

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR D...