Antisense

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CPC
C12N2310/11

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

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C12N2310/11Antisense

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Patents Grantslast 30 patents

Information Patent Grant
Intron fragments
- Patent number 12,173,304
- Issue date Dec 24, 2024
- NEURACLE GENETICS INC.
- Hoon Young Kong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective inhibition of T follicular helper cells for treatment of...
- Patent number 12,168,003
- Issue date Dec 17, 2024
- New York University
- Preeyam S. Patel
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Trimeric peptides for antisense delivery
- Patent number 12,168,059
- Issue date Dec 17, 2024
- Sarepta Therapeutics, Inc.
- Justin Wolfe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating PACS1 and PACS2 syndromes
- Patent number 12,161,639
- Issue date Dec 10, 2024
- University of Pittsburgh of the Commonwealth System of Higher Education
- Gary Thomas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Ferrochelatase inhibitors and methods of use
- Patent number 12,161,642
- Issue date Dec 10, 2024
- Indiana University Research and Technology Corporation
- Timothy W. Corson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...
- Patent number 12,163,132
- Issue date Dec 10, 2024
- Children's National Medical Center
- Yi-Wen Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and uses for treatment thereof
- Patent number 12,163,128
- Issue date Dec 10, 2024
- Board of Supervisors of Louisiana State University and Agricultural and Mecha...
- Edward L. Grabczyk
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides to restore dysferlin protein expression...
- Patent number 12,163,129
- Issue date Dec 10, 2024
- University of Massachusetts
- Robert H. Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides for modulating Tau expression
- Patent number 12,163,131
- Issue date Dec 10, 2024
- HOFFMANN-LA ROCHE INC.
- Peter Hagedorn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulating the cellular stress response
- Patent number 12,157,888
- Issue date Dec 3, 2024
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of uveitis with endoplasmic reticulum aminopeptidase 1 (E...
- Patent number 12,157,891
- Issue date Dec 3, 2024
- REGENERON PHARMACEUTICALS, INC.
- Sahar Gelfman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of MALAT1 expression
- Patent number 12,157,890
- Issue date Dec 3, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective antisense compounds and uses thereof
- Patent number 12,152,244
- Issue date Nov 26, 2024
- Ionis Pharmaceuticals, Inc.
- Michael Oestergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeting human satellite II (HSATII)
- Patent number 12,152,241
- Issue date Nov 26, 2024
- The General Hospital Corporation
- David T. Ting
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compositions for treating pain via multiple targets
- Patent number 12,152,243
- Issue date Nov 26, 2024
- QUELLTX, INC.
- Graham T. Dempsey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment and diagnosis of inflammatory disorders
- Patent number 12,146,138
- Issue date Nov 19, 2024
- Zhenglun Zhu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotide interference treatments of prostate cancer
- Patent number 12,146,139
- Issue date Nov 19, 2024
- The Board of Regents of the University of Oklahoma
- Maria Jesus Ruiz Echevarria
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for preventing ischemia reperfusion injury in an organ with...
- Patent number 12,145,984
- Issue date Nov 19, 2024
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- André Herbelin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of modulating RNA translation
- Patent number 12,139,710
- Issue date Nov 12, 2024
- The Regents of the University of California
- Eugene Yeo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Direct and selective inhibition of MDM4 for treatment of cancer
- Patent number 12,139,712
- Issue date Nov 12, 2024
- VIB VZW
- Jean-Christophe Marine
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compounds for red blood cell-mediated delivery of an ac...
- Patent number 12,139,713
- Issue date Nov 12, 2024
- K2B Therapeutics, Inc.
- HoWon J. Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides for the treatment of Leber congenital am...
- Patent number 12,139,711
- Issue date Nov 12, 2024
- STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM
- Robert Wilhelmus Johanna Collin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for upregulating immune responses using combinations of ant...
- Patent number 12,139,535
- Issue date Nov 12, 2024
- Dana-Farber Cancer Institute, Inc.
- Gordon J. Freeman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cell-penetrating peptides for antisense delivery
- Patent number 12,138,312
- Issue date Nov 12, 2024
- Sarepta Therapeutics, Inc.
- Justin M. Wolfe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligomers and methods of using the same for treating dise...
- Patent number 12,139,709
- Issue date Nov 12, 2024
- Sarepta Therapeutics, Inc.
- Frederick Joseph Schnell
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for organ specific delivery of nucleic acids
- Patent number 12,133,924
- Issue date Nov 5, 2024
- The Board of Regents of the University of Texas System
- Qiang Cheng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Increasing gene expression
- Patent number 12,134,772
- Issue date Nov 5, 2024
- Advantage Therapeutics, Inc.
- Ci-Di Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Structural domains of antisense RNA molecules up-regulating transla...
- Patent number 12,134,768
- Issue date Nov 5, 2024
- Fondazione Istituto Italiano di Tecnologia
- Stefano Gustincich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for targeting pain directed at metabolic pathways
- Patent number 12,128,062
- Issue date Oct 29, 2024
- University of Maryland, Baltimore
- Ohannes Kevork Melemedjian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
Means and Methods for Chronic Wound Healing
- Publication number 20240425857
- Publication date Dec 26, 2024
- VIB VZW
- Kodimangalam Ravichandran
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PARN AS A BIOMARKER AND THERAPEUTIC TARGET
- Publication number 20240425866
- Publication date Dec 26, 2024
- The Regents of the University of Colorado, a Body Corporate
- Roy R. Parker
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV
- Publication number 20240425859
- Publication date Dec 26, 2024
- HOFFMANN-LA ROCHE INC.
- Souphalone LUANGSAY
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PEPTIDE HAVING INDEPENDENTLY STABILIZED HYDROPHOBIC ALPHA HELIX, PE...
- Publication number 20240424134
- Publication date Dec 26, 2024
- UIF (UNIVERSITY INDUSTRY FOUNDATION), YONSEI UNIVERSITY
- Yong-beom LIM
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
POLY-GA PROTEINS IN ALZHEIMER’S DISEASE
- Publication number 20240426844
- Publication date Dec 26, 2024
- University of Florida Research Foundation, Incorporated
- Laura Ranum
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TARGETING SV2 PROTEINS FOR IMMUNE REGU...
- Publication number 20240423953
- Publication date Dec 26, 2024
- The Regents of the University of California
- Ke SHUAI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
POLYMER NANOPARTICLE AND DNA NANOSTRUCTURE COMPOSITIONS AND METHODS...
- Publication number 20240415865
- Publication date Dec 19, 2024
- Battelle Memorial Institute
- Anthony D. DUONG
- B82 - NANO-TECHNOLOGY
Information Patent Application
Methods and Compositions for RNA-Directed Target DNA Modification a...
- Publication number 20240417756
- Publication date Dec 19, 2024
- The Regents of the University of California
- Jennifer A. Doudna
- H01 - BASIC ELECTRIC ELEMENTS
Information Patent Application
TIS-L TARGETING ANTIVIRAL ANTISENSE OLIGONUCLEOTIDE WITH ABILITY TO...
- Publication number 20240417733
- Publication date Dec 19, 2024
- Seoul National University R&DB Foundation
- Daehyun BAEK
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
FOLDING OLIGONUCLEOTIDES
- Publication number 20240417728
- Publication date Dec 19, 2024
- RNA MORPH LTD
- Eitan LEV
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods for Treating Glioblastoma by Targeting Oncomirs
- Publication number 20240417734
- Publication date Dec 19, 2024
- University of Connecticut
- Raman Bahal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING EPILEPSY
- Publication number 20240417737
- Publication date Dec 19, 2024
- UNIQURE FRANCE
- Chenxia HE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR SKIPPING EXON 45 IN DUCHENNE MUSCULAR...
- Publication number 20240417429
- Publication date Dec 19, 2024
- Entrada Therapeutics, Inc.
- Xiang Li
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
- Publication number 20240417721
- Publication date Dec 19, 2024
- ProQR Therapeutics II B.V.
- Janne Juha TURUNEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
THERAPEUTIC TREATMENT FOR FRAGILE X-ASSOCIATED DISORDER
- Publication number 20240417729
- Publication date Dec 19, 2024
- University of Massachusetts
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMMUNOTHERAPIES FOR THE TREATMENT OF CANCER
- Publication number 20240417738
- Publication date Dec 19, 2024
- Ohio State Innovation Foundation
- Chun-Tien KUO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN
- Publication number 20240415857
- Publication date Dec 19, 2024
- Sarepta Therapeutics, Inc.
- Dan V. Mourich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR TARGETING COMPLEMENT C5
- Publication number 20240417725
- Publication date Dec 19, 2024
- Vanqua Bio, Inc.
- Kevin Hunt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF MODULATING RNA TRANSLATION
- Publication number 20240417730
- Publication date Dec 19, 2024
- THE REGENTS OF THE UNIVERSITY OF CALIFORNIA
- Eugene Yeo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUC5B-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR M...
- Publication number 20240409930
- Publication date Dec 12, 2024
- SpliSense Ltd.
- Gili HART
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMBINATION OF OLIGONUCLEOTIDES FOR MODULATING RTEL1 AND FUBP1
- Publication number 20240409939
- Publication date Dec 12, 2024
- HOFFMANN-LA ROCHE INC.
- Konrad BLEICHER
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S...
- Publication number 20240409945
- Publication date Dec 12, 2024
- Ovid Therapeutics Inc.
- Noelle Germain
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS AND METHODS FOR DETERMINING EFFECTS OF THERAPIES AND GENETI...
- Publication number 20240412818
- Publication date Dec 12, 2024
- DEEP GENOMICS INCORPORATED
- Brendan Frey
- G06 - COMPUTING CALCULATING COUNTING
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20240408227
- Publication date Dec 12, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING NLRP3 OR NLRP1 EXPRESSION
- Publication number 20240409931
- Publication date Dec 12, 2024
- Molecular Axiom, LLC
- Lishan CHEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODELS OF TAUOPATHY
- Publication number 20240409891
- Publication date Dec 12, 2024
- Regeneron Pharmaceuticals, Inc.
- Marine Prissette
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Application
INTEGRIN TARGETING LIGANDS FOR OCULAR DELIVERY OF RNAI COMPOUNDS
- Publication number 20240409927
- Publication date Dec 12, 2024
- Alnylam Pharmaceuticals, Inc.
- JAYAPRAKASH K. NAIR
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NOVEL RNA TRANSCRIPT
- Publication number 20240409928
- Publication date Dec 12, 2024
- PTC THERAPEUTICS, INC.
- Anuradha BHATTACHARYYA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi TARGETING HNRNPH2 MISSENSE MUTATIONS FOR TREATMENT OF BAIN SYN...
- Publication number 20240409937
- Publication date Dec 12, 2024
- Ovid Therapeutics Inc.
- Noelle Germain
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PREVENTIVE OR THERAPEUTIC AGENT FOR BENIGN ADULT FAMILIAL MYOCLONIC...
- Publication number 20240409926
- Publication date Dec 12, 2024
- RIKEN
- Haruhisa INOUE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Intron fragments

Selective inhibition of T follicular helper cells for treatment of...

Modulators of APOL1 expression

Trimeric peptides for antisense delivery

Methods of treating PACS1 and PACS2 syndromes

Ferrochelatase inhibitors and methods of use

Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...

Compositions and uses for treatment thereof

Antisense oligonucleotides to restore dysferlin protein expression...

Oligonucleotides for modulating Tau expression

Modulating the cellular stress response

Treatment of uveitis with endoplasmic reticulum aminopeptidase 1 (E...

Modulators of MALAT1 expression

Selective antisense compounds and uses thereof

Targeting human satellite II (HSATII)

Therapeutic compositions for treating pain via multiple targets

Treatment and diagnosis of inflammatory disorders

Oligonucleotide interference treatments of prostate cancer

Methods for preventing ischemia reperfusion injury in an organ with...

Methods of modulating RNA translation

Direct and selective inhibition of MDM4 for treatment of cancer

Therapeutic compounds for red blood cell-mediated delivery of an ac...

Antisense oligonucleotides for the treatment of Leber congenital am...

Methods for upregulating immune responses using combinations of ant...

Cell-penetrating peptides for antisense delivery

Antisense oligomers and methods of using the same for treating dise...

Compositions and methods for organ specific delivery of nucleic acids

Increasing gene expression

Structural domains of antisense RNA molecules up-regulating transla...

Methods for targeting pain directed at metabolic pathways

Patents Applicationslast 30 patents

Means and Methods for Chronic Wound Healing

PARN AS A BIOMARKER AND THERAPEUTIC TARGET

PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV

PEPTIDE HAVING INDEPENDENTLY STABILIZED HYDROPHOBIC ALPHA HELIX, PE...

POLY-GA PROTEINS IN ALZHEIMER’S DISEASE

METHODS AND COMPOSITIONS FOR TARGETING SV2 PROTEINS FOR IMMUNE REGU...

POLYMER NANOPARTICLE AND DNA NANOSTRUCTURE COMPOSITIONS AND METHODS...

Methods and Compositions for RNA-Directed Target DNA Modification a...

TIS-L TARGETING ANTIVIRAL ANTISENSE OLIGONUCLEOTIDE WITH ABILITY TO...

FOLDING OLIGONUCLEOTIDES

Methods for Treating Glioblastoma by Targeting Oncomirs

METHODS AND COMPOSITIONS FOR TREATING EPILEPSY

COMPOSITIONS AND METHODS FOR SKIPPING EXON 45 IN DUCHENNE MUSCULAR...

SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES

THERAPEUTIC TREATMENT FOR FRAGILE X-ASSOCIATED DISORDER

IMMUNOTHERAPIES FOR THE TREATMENT OF CANCER

ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN

OLIGONUCLEOTIDES FOR TARGETING COMPLEMENT C5

METHODS OF MODULATING RNA TRANSLATION

MUC5B-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR M...

COMBINATION OF OLIGONUCLEOTIDES FOR MODULATING RTEL1 AND FUBP1

RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S...

SYSTEMS AND METHODS FOR DETERMINING EFFECTS OF THERAPIES AND GENETI...

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

COMPOSITIONS AND METHODS FOR MODULATING NLRP3 OR NLRP1 EXPRESSION

MODELS OF TAUOPATHY

INTEGRIN TARGETING LIGANDS FOR OCULAR DELIVERY OF RNAI COMPOUNDS

NOVEL RNA TRANSCRIPT

RNAi TARGETING HNRNPH2 MISSENSE MUTATIONS FOR TREATMENT OF BAIN SYN...

PREVENTIVE OR THERAPEUTIC AGENT FOR BENIGN ADULT FAMILIAL MYOCLONIC...