cell type or tissue specific enhancer/promoter combination

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C12N2830/008

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

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C12N2830/008cell type or tissue specific enhancer/promoter combination

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Liver-specific viral promoters and methods of using the same
- Patent number 12,319,924
- Issue date Jun 3, 2025
- Uniqure IP B.V.
- Jacek Lubelski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid constructs for VA RNA transcription
- Patent number 12,312,606
- Issue date May 27, 2025
- HOFFMANN-LA ROCHE INC.
- Ulrich Goepfert
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Non-human animals expressing exogenous terminal deoxynucleotidyltra...
- Patent number 12,295,354
- Issue date May 13, 2025
- REGENERON PHARMACEUTICALS, INC.
- Lynn Macdonald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for juvenile Batten disease
- Patent number 12,297,447
- Issue date May 13, 2025
- BOARD OF REGENTS OF THE UNIVERSITY OF NEBRASKA
- Tammy Kielian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transcription regulatory elements and uses thereof
- Patent number 12,296,026
- Issue date May 13, 2025
- Astellas Gene Therapies, Inc.
- John T. Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Frataxin expression constructs having engineered promoters and meth...
- Patent number 12,281,321
- Issue date Apr 22, 2025
- VOYAGER THERAPEUTICS, INC.
- Holger Patzke
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression in cone cells
- Patent number 12,275,959
- Issue date Apr 15, 2025
- Adverum Biotechnologies, Inc.
- Thomas W. Chalberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
High-transducing HSV vectors
- Patent number 12,275,949
- Issue date Apr 15, 2025
- Periphagen, Inc.
- David M. Krisky
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized CLN5 genes and expression cassettes and their use
- Patent number 12,275,948
- Issue date Apr 15, 2025
- The University of North Carolina at Chapel Hill
- Steven James Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating non-age-associated hearing im...
- Patent number 12,264,317
- Issue date Apr 1, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimized mini-dystrophin genes and expression cassettes and their use
- Patent number 12,257,321
- Issue date Mar 25, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Recombinant constructs and transgenic fluorescent ornamental fish t...
- Patent number 12,256,719
- Issue date Mar 25, 2025
- GLOFISH LLC
- Alan Blake
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimised coding sequence and promoter
- Patent number 12,257,319
- Issue date Mar 25, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for transducing lymphocytes and regulating...
- Patent number 12,258,574
- Issue date Mar 25, 2025
- Exuma Biotech Corp.
- Gregory Ian Frost
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Adeno-associated virus vector delivery of alpha-sarcoglycan and the...
- Patent number 12,258,573
- Issue date Mar 25, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Treatment of mucopolysaccharidosis IVA
- Patent number 12,247,213
- Issue date Mar 11, 2025
- The Nemours Foundation
- Shunji Tomatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
DNA vector for targeted gene therapy
- Patent number 12,246,073
- Issue date Mar 11, 2025
- GENETIC DIAGNOSTICS AND THERAPY 21 LTD
- Anton Gamolski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus factor VIII vectors
- Patent number 12,239,692
- Issue date Mar 4, 2025
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Replication-defective arenavirus vectors
- Patent number 12,227,755
- Issue date Feb 18, 2025
- Universitat Zurich
- Daniel D. Pinschewer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Factor IX encoding nucleotides
- Patent number 12,209,262
- Issue date Jan 28, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Hybrid regulatory elements
- Patent number 12,171,843
- Issue date Dec 24, 2024
- Genethon
- Federico Mingozzi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for delivering RNA to neurons to treat herpes infections
- Patent number 12,156,919
- Issue date Dec 3, 2024
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR therapy
- Patent number 12,152,242
- Issue date Nov 26, 2024
- The Curators of the University of Missouri
- Dongsheng Duan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric protein and related genic transfer technology
- Patent number 12,138,319
- Issue date Nov 12, 2024
- Lucio Pastore
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Rescuing voltage-gated sodium channel function in inhibitory neurons
- Patent number 12,121,563
- Issue date Oct 22, 2024
- Allen Institute
- John K. Mich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and materials for GALGT2 gene therapy
- Patent number 12,121,595
- Issue date Oct 22, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vectors for treatment of Rett syndrome
- Patent number 12,104,163
- Issue date Oct 1, 2024
- Sarepta Therapeutics, Inc.
- Colin O'Banion
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating solid or lymphatic tumors by combination therapy
- Patent number 12,090,183
- Issue date Sep 17, 2024
- CG ONCOLOGY, INC.
- Alex Wah Hin Yeung
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods for using transcription-dependent directed evolution of AAV...
- Patent number 12,084,654
- Issue date Sep 10, 2024
- Oregon Health & Science University
- Hiroyuki Nakai
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING AND/OR PREVENTING GLYCOGEN ST...
- Publication number 20250186618
- Publication date Jun 12, 2025
- DUKE UNIVERSITY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...
- Publication number 20250179450
- Publication date Jun 5, 2025
- The Board of Regents of the University of Texas System
- Yu ZHANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SEQUENCE OF ACTIVATED PROTEIN C
- Publication number 20250177571
- Publication date Jun 5, 2025
- Jichi Medical University
- Tsukasa OHMORI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...
- Publication number 20250161490
- Publication date May 22, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SYNTHETIC CANCER-SPECIFIC PROMOTERS
- Publication number 20250161496
- Publication date May 22, 2025
- EARLI Inc.
- Dariusz WODZIAK
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TRANSCRIPTIONAL AND TRANSLATIONAL DUAL REGULATED ONCOLYTIC HERPES S...
- Publication number 20250161384
- Publication date May 22, 2025
- Virogin Biotech (Shanghai) Ltd
- William Wei-Guo Jia
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250163458
- Publication date May 22, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTH...
- Publication number 20250163470
- Publication date May 22, 2025
- UCL Business LTD
- Thomas Voit
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR EGR2-POSITIVE CE...
- Publication number 20250154527
- Publication date May 15, 2025
- FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
- Georg Keller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
REGULATORY ELEMENT FOR CELL TYPE SPECIFIC EXPRESSION OF GENES IN SP...
- Publication number 20250135029
- Publication date May 1, 2025
- THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK
- Hynek WICHTERLE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED CLN5 GENES AND EXPRESSION CASSETTES AND THEIR USE
- Publication number 20250129384
- Publication date Apr 24, 2025
- The University of North Carolina at Chapel Hill
- Steven James Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HYBRID REGULATORY ELEMENTS
- Publication number 20250127930
- Publication date Apr 24, 2025
- GENETHON
- FEDERICO MINGOZZI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS
- Publication number 20250127932
- Publication date Apr 24, 2025
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
REGULATORY NUCLEIC ACID SEQUENCES
- Publication number 20250129381
- Publication date Apr 24, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Jorge Omar YANEZ-CUNA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF ALPHA-SARCOGLYCAN AND THE...
- Publication number 20250122531
- Publication date Apr 17, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTERS, EXPRESSION CASSETTES, VECTORS, KITS, AND METHODS FOR THE...
- Publication number 20250121092
- Publication date Apr 17, 2025
- Beacon Therapeutics Limited
- Guo-jie Ye
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED LIVER-SPECIFIC ENHANCERS AND THEIR APPLICATIONS
- Publication number 20250121096
- Publication date Apr 17, 2025
- Sichuan Real&Best Biotech Co., Ltd.
- Biao Dong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SCHWANN CELL-SPECIFIC PROMOTER
- Publication number 20250115906
- Publication date Apr 10, 2025
- Toolgen Incorporated
- Dong Woo SONG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS FOR TREATING NEUROLOGICAL DISEASE
- Publication number 20250109398
- Publication date Apr 3, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Anna TRETIAKOVA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RIG1 Inhibition and Therapeutic Viral Protein Expression
- Publication number 20250109409
- Publication date Apr 3, 2025
- ImmunityBio, Inc.
- Patrick Soon-Shiong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS AND COMPOSITIONS FOR GENE AUGMENTATION OF CRUMBS COMPLEX HO...
- Publication number 20250108133
- Publication date Apr 3, 2025
- THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK
- Peter M.J. Quinn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR CUX1-POSITIVE CE...
- Publication number 20250092420
- Publication date Mar 20, 2025
- FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
- Georg Keller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Nucleic Acid-Based Compositions and Methods for Treating Small Vess...
- Publication number 20250064977
- Publication date Feb 27, 2025
- The Schepens Eye Research Institute, Inc.
- Joseph F. Arboleda-Velasquez
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV GENE THERAPY FOR THE KIDNEY
- Publication number 20250064984
- Publication date Feb 27, 2025
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250066437
- Publication date Feb 27, 2025
- SHANGHAI MYGT BIOPHARMACEUTICAL LLC
- Mengdi YAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CONSTRUCTS COMPRISING NEURONAL VIABILITY FACTORS AND USES THEREOF
- Publication number 20250059563
- Publication date Feb 20, 2025
- SPARINGVISION
- Thierry LEVEILLARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VIRAL VECTOR CONSTRUCTS FOR DELIVERY OF NUCLEIC ACIDS ENCODING CYTO...
- Publication number 20250059564
- Publication date Feb 20, 2025
- Kriya Therapeutics, Inc.
- Brian FURMANSKI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES
- Publication number 20250049949
- Publication date Feb 13, 2025
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY
- Publication number 20250049959
- Publication date Feb 13, 2025
- Tenaya Therapeutics, Inc.
- Huanyu ZHOU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED MUSCLE TARGETING COMPOSITIONS
- Publication number 20250051800
- Publication date Feb 13, 2025
- THE BROAD INSTITUTE, INC.
- Pardis SABETI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

cell type or tissue specific enhancer/promoter combination

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Liver-specific viral promoters and methods of using the same

Nucleic acid constructs for VA RNA transcription

Non-human animals expressing exogenous terminal deoxynucleotidyltra...

Gene therapy for juvenile Batten disease

Transcription regulatory elements and uses thereof

Frataxin expression constructs having engineered promoters and meth...

Compositions and methods for enhanced gene expression in cone cells

High-transducing HSV vectors

Optimized CLN5 genes and expression cassettes and their use

Compositions and methods for treating non-age-associated hearing im...

Optimized mini-dystrophin genes and expression cassettes and their use

Recombinant constructs and transgenic fluorescent ornamental fish t...

Optimised coding sequence and promoter

Methods and compositions for transducing lymphocytes and regulating...

Adeno-associated virus vector delivery of alpha-sarcoglycan and the...

Treatment of mucopolysaccharidosis IVA

DNA vector for targeted gene therapy

Adeno-associated virus factor VIII vectors

Replication-defective arenavirus vectors

Factor IX encoding nucleotides

Hybrid regulatory elements

Method for delivering RNA to neurons to treat herpes infections

Optimized expression cassettes for gene therapy

CRISPR therapy

Chimeric protein and related genic transfer technology

Rescuing voltage-gated sodium channel function in inhibitory neurons

Methods and materials for GALGT2 gene therapy

Adeno-associated virus vectors for treatment of Rett syndrome

Methods of treating solid or lymphatic tumors by combination therapy

Methods for using transcription-dependent directed evolution of AAV...

Patents Applicationslast 30 patents

COMPOSITIONS AND METHODS FOR TREATING AND/OR PREVENTING GLYCOGEN ST...

CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...

SEQUENCE OF ACTIVATED PROTEIN C

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...

SYNTHETIC CANCER-SPECIFIC PROMOTERS

TRANSCRIPTIONAL AND TRANSLATIONAL DUAL REGULATED ONCOLYTIC HERPES S...

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTH...

PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR EGR2-POSITIVE CE...

REGULATORY ELEMENT FOR CELL TYPE SPECIFIC EXPRESSION OF GENES IN SP...

OPTIMIZED CLN5 GENES AND EXPRESSION CASSETTES AND THEIR USE

HYBRID REGULATORY ELEMENTS

METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS

REGULATORY NUCLEIC ACID SEQUENCES

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF ALPHA-SARCOGLYCAN AND THE...

PROMOTERS, EXPRESSION CASSETTES, VECTORS, KITS, AND METHODS FOR THE...

ENGINEERED LIVER-SPECIFIC ENHANCERS AND THEIR APPLICATIONS

SCHWANN CELL-SPECIFIC PROMOTER

COMPOSITIONS FOR TREATING NEUROLOGICAL DISEASE

RIG1 Inhibition and Therapeutic Viral Protein Expression

VECTORS AND COMPOSITIONS FOR GENE AUGMENTATION OF CRUMBS COMPLEX HO...

PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR CUX1-POSITIVE CE...

Nucleic Acid-Based Compositions and Methods for Treating Small Vess...

AAV GENE THERAPY FOR THE KIDNEY

TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY

CONSTRUCTS COMPRISING NEURONAL VIABILITY FACTORS AND USES THEREOF

VIRAL VECTOR CONSTRUCTS FOR DELIVERY OF NUCLEIC ACIDS ENCODING CYTO...

GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES

OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

ENGINEERED MUSCLE TARGETING COMPOSITIONS