cell type or tissue specific enhancer/promoter combination

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C12N2830/008

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

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C12N2830/008cell type or tissue specific enhancer/promoter combination

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Thermal control of T-cell immunotherapy through molecular and physi...
- Patent number 12,359,208
- Issue date Jul 15, 2025
- California Institute of Technology
- Mohamad H. Abedi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating laminopathies
- Patent number 12,357,707
- Issue date Jul 15, 2025
- Encoded Therapeutics, Inc.
- Sirika Wood
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Liver-specific viral promoters and methods of using the same
- Patent number 12,319,924
- Issue date Jun 3, 2025
- Uniqure IP B.V.
- Jacek Lubelski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid constructs for VA RNA transcription
- Patent number 12,312,606
- Issue date May 27, 2025
- HOFFMANN-LA ROCHE INC.
- Ulrich Goepfert
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Non-human animals expressing exogenous terminal deoxynucleotidyltra...
- Patent number 12,295,354
- Issue date May 13, 2025
- REGENERON PHARMACEUTICALS, INC.
- Lynn Macdonald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for juvenile Batten disease
- Patent number 12,297,447
- Issue date May 13, 2025
- BOARD OF REGENTS OF THE UNIVERSITY OF NEBRASKA
- Tammy Kielian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transcription regulatory elements and uses thereof
- Patent number 12,296,026
- Issue date May 13, 2025
- Astellas Gene Therapies, Inc.
- John T. Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Frataxin expression constructs having engineered promoters and meth...
- Patent number 12,281,321
- Issue date Apr 22, 2025
- VOYAGER THERAPEUTICS, INC.
- Holger Patzke
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression in cone cells
- Patent number 12,275,959
- Issue date Apr 15, 2025
- Adverum Biotechnologies, Inc.
- Thomas W. Chalberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
High-transducing HSV vectors
- Patent number 12,275,949
- Issue date Apr 15, 2025
- Periphagen, Inc.
- David M. Krisky
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized CLN5 genes and expression cassettes and their use
- Patent number 12,275,948
- Issue date Apr 15, 2025
- The University of North Carolina at Chapel Hill
- Steven James Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating non-age-associated hearing im...
- Patent number 12,264,317
- Issue date Apr 1, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Recombinant constructs and transgenic fluorescent ornamental fish t...
- Patent number 12,256,719
- Issue date Mar 25, 2025
- GLOFISH LLC
- Alan Blake
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimized mini-dystrophin genes and expression cassettes and their use
- Patent number 12,257,321
- Issue date Mar 25, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimised coding sequence and promoter
- Patent number 12,257,319
- Issue date Mar 25, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for transducing lymphocytes and regulating...
- Patent number 12,258,574
- Issue date Mar 25, 2025
- Exuma Biotech Corp.
- Gregory Ian Frost
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Adeno-associated virus vector delivery of alpha-sarcoglycan and the...
- Patent number 12,258,573
- Issue date Mar 25, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Treatment of mucopolysaccharidosis IVA
- Patent number 12,247,213
- Issue date Mar 11, 2025
- The Nemours Foundation
- Shunji Tomatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
DNA vector for targeted gene therapy
- Patent number 12,246,073
- Issue date Mar 11, 2025
- GENETIC DIAGNOSTICS AND THERAPY 21 LTD
- Anton Gamolski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus factor VIII vectors
- Patent number 12,239,692
- Issue date Mar 4, 2025
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Replication-defective arenavirus vectors
- Patent number 12,227,755
- Issue date Feb 18, 2025
- Universitat Zurich
- Daniel D. Pinschewer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Factor IX encoding nucleotides
- Patent number 12,209,262
- Issue date Jan 28, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Hybrid regulatory elements
- Patent number 12,171,843
- Issue date Dec 24, 2024
- Genethon
- Federico Mingozzi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for delivering RNA to neurons to treat herpes infections
- Patent number 12,156,919
- Issue date Dec 3, 2024
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR therapy
- Patent number 12,152,242
- Issue date Nov 26, 2024
- The Curators of the University of Missouri
- Dongsheng Duan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric protein and related genic transfer technology
- Patent number 12,138,319
- Issue date Nov 12, 2024
- Lucio Pastore
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Rescuing voltage-gated sodium channel function in inhibitory neurons
- Patent number 12,121,563
- Issue date Oct 22, 2024
- Allen Institute
- John K. Mich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and materials for GALGT2 gene therapy
- Patent number 12,121,595
- Issue date Oct 22, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vectors for treatment of Rett syndrome
- Patent number 12,104,163
- Issue date Oct 1, 2024
- Sarepta Therapeutics, Inc.
- Colin O'Banion
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250235550
- Publication date Jul 24, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EX...
- Publication number 20250236886
- Publication date Jul 24, 2025
- Allen Institute
- Lucas T. Graybuck
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TRANSDUCING LYMPHOCYTES AND REGULATING...
- Publication number 20250236889
- Publication date Jul 24, 2025
- Exuma Biotech Corp.
- Gregory Ian FROST
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY
- Publication number 20250228973
- Publication date Jul 17, 2025
- PRECISION BIOSCIENCES, INC.
- James Jefferson Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...
- Publication number 20250230467
- Publication date Jul 17, 2025
- The Johns Hopkins University
- Ingie Hong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TISSUE-SPECIFIC PROMOTER AND USE THEREOF
- Publication number 20250230466
- Publication date Jul 17, 2025
- BEIJING MEIKANG GENO-IMMUNE BIOTECHNOLOGY CO., LTD.
- Lung-Ji Chang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION
- Publication number 20250222139
- Publication date Jul 10, 2025
- Shape Therapeutics Inc.
- Jacob Michael TOME
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING...
- Publication number 20250222137
- Publication date Jul 10, 2025
- Akouos, Inc.
- Katherine Diane GRIBBLE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL-TYPE SPECIFIC REGULATORY ELEMENTS FOR PHOTORECEPTORS
- Publication number 20250222133
- Publication date Jul 10, 2025
- Senti Biosciences, Inc.
- Russell Morrison Gordley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Cochlear and/or vestibular cell specific promoter and use thereof
- Publication number 20250213728
- Publication date Jul 3, 2025
- Shanghai Emaygene Technology Co.,Ltd.
- Guisheng ZHONG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD TO STIMULATE REGENERATION OF RETINAL GANGLION CELLS
- Publication number 20250213729
- Publication date Jul 3, 2025
- University of Washington
- Levi J. Todd
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENETIC TARGETING OF CELLULAR OR NEURONAL SUB-POPULATIONS
- Publication number 20250215455
- Publication date Jul 3, 2025
- Board of Regents, The University of Texas System
- Boris V. ZEMELMAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC AC...
- Publication number 20250213726
- Publication date Jul 3, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Anna TRETIAKOVA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...
- Publication number 20250205365
- Publication date Jun 26, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED MUSCLE-SPECIFIC PROMOTERS
- Publication number 20250207126
- Publication date Jun 26, 2025
- Regenxbio Inc.
- Ye Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Viral Vectors For Treating Neurogenic Detrusor Overactivity
- Publication number 20250197867
- Publication date Jun 19, 2025
- Assistance Publique-Hopitaux de Paris
- François GIULIANO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE AUGMENTATION THERAPIES FOR INHERITED RETINAL DEGENERATION CAUS...
- Publication number 20250195691
- Publication date Jun 19, 2025
- Massachusetts Eye and Ear Infirmary
- Eric A. Pierce
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING AND/OR PREVENTING GLYCOGEN ST...
- Publication number 20250186618
- Publication date Jun 12, 2025
- DUKE UNIVERSITY
- Baodong Sun
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...
- Publication number 20250179450
- Publication date Jun 5, 2025
- The Board of Regents of the University of Texas System
- Yu ZHANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SEQUENCE OF ACTIVATED PROTEIN C
- Publication number 20250177571
- Publication date Jun 5, 2025
- Jichi Medical University
- Tsukasa OHMORI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...
- Publication number 20250161490
- Publication date May 22, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SYNTHETIC CANCER-SPECIFIC PROMOTERS
- Publication number 20250161496
- Publication date May 22, 2025
- EARLI Inc.
- Dariusz WODZIAK
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250163458
- Publication date May 22, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTH...
- Publication number 20250163470
- Publication date May 22, 2025
- UCL Business LTD
- Thomas Voit
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TRANSCRIPTIONAL AND TRANSLATIONAL DUAL REGULATED ONCOLYTIC HERPES S...
- Publication number 20250161384
- Publication date May 22, 2025
- Virogin Biotech (Shanghai) Ltd
- William Wei-Guo Jia
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR EGR2-POSITIVE CE...
- Publication number 20250154527
- Publication date May 15, 2025
- FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
- Georg Keller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
REGULATORY ELEMENT FOR CELL TYPE SPECIFIC EXPRESSION OF GENES IN SP...
- Publication number 20250135029
- Publication date May 1, 2025
- THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK
- Hynek WICHTERLE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED CLN5 GENES AND EXPRESSION CASSETTES AND THEIR USE
- Publication number 20250129384
- Publication date Apr 24, 2025
- The University of North Carolina at Chapel Hill
- Steven James Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HYBRID REGULATORY ELEMENTS
- Publication number 20250127930
- Publication date Apr 24, 2025
- GENETHON
- FEDERICO MINGOZZI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS
- Publication number 20250127932
- Publication date Apr 24, 2025
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

cell type or tissue specific enhancer/promoter combination

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Thermal control of T-cell immunotherapy through molecular and physi...

Compositions and methods for treating laminopathies

Liver-specific viral promoters and methods of using the same

Nucleic acid constructs for VA RNA transcription

Non-human animals expressing exogenous terminal deoxynucleotidyltra...

Gene therapy for juvenile Batten disease

Transcription regulatory elements and uses thereof

Frataxin expression constructs having engineered promoters and meth...

Compositions and methods for enhanced gene expression in cone cells

High-transducing HSV vectors

Optimized CLN5 genes and expression cassettes and their use

Compositions and methods for treating non-age-associated hearing im...

Recombinant constructs and transgenic fluorescent ornamental fish t...

Optimized mini-dystrophin genes and expression cassettes and their use

Optimised coding sequence and promoter

Methods and compositions for transducing lymphocytes and regulating...

Adeno-associated virus vector delivery of alpha-sarcoglycan and the...

Treatment of mucopolysaccharidosis IVA

DNA vector for targeted gene therapy

Adeno-associated virus factor VIII vectors

Replication-defective arenavirus vectors

Factor IX encoding nucleotides

Hybrid regulatory elements

Method for delivering RNA to neurons to treat herpes infections

Optimized expression cassettes for gene therapy

CRISPR therapy

Chimeric protein and related genic transfer technology

Rescuing voltage-gated sodium channel function in inhibitory neurons

Methods and materials for GALGT2 gene therapy

Adeno-associated virus vectors for treatment of Rett syndrome

Patents Applicationslast 30 patents

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EX...

METHODS AND COMPOSITIONS FOR TRANSDUCING LYMPHOCYTES AND REGULATING...

GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY

METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...

TISSUE-SPECIFIC PROMOTER AND USE THEREOF

PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION

GENE THERAPY DELIVERY COMPOSITIONS AND METHODS FOR TREATING HEARING...

CELL-TYPE SPECIFIC REGULATORY ELEMENTS FOR PHOTORECEPTORS

Cochlear and/or vestibular cell specific promoter and use thereof

METHOD TO STIMULATE REGENERATION OF RETINAL GANGLION CELLS

GENETIC TARGETING OF CELLULAR OR NEURONAL SUB-POPULATIONS

THERAPEUTIC ADENO-ASSOCIATED VIRUS USING CODON OPTIMIZED NUCLEIC AC...

METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...

MODIFIED MUSCLE-SPECIFIC PROMOTERS

Viral Vectors For Treating Neurogenic Detrusor Overactivity

GENE AUGMENTATION THERAPIES FOR INHERITED RETINAL DEGENERATION CAUS...

COMPOSITIONS AND METHODS FOR TREATING AND/OR PREVENTING GLYCOGEN ST...

CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...

SEQUENCE OF ACTIVATED PROTEIN C

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...

SYNTHETIC CANCER-SPECIFIC PROMOTERS

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

GENE THERAPY COMPOSITION AND TREATMENT OF RIGHT VENTRICULAR ARRHYTH...

TRANSCRIPTIONAL AND TRANSLATIONAL DUAL REGULATED ONCOLYTIC HERPES S...

PROMOTER FOR THE EXPRESSION OF GENES IN PARTICULAR EGR2-POSITIVE CE...

REGULATORY ELEMENT FOR CELL TYPE SPECIFIC EXPRESSION OF GENES IN SP...

OPTIMIZED CLN5 GENES AND EXPRESSION CASSETTES AND THEIR USE

HYBRID REGULATORY ELEMENTS

METHOD FOR DELIVERING RNA TO NEURONS TO TREAT HERPES INFECTIONS