Morpholino-type ring

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CPC
C12N2310/3233

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

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C12N2310/3233Morpholino-type ring

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Oligonucleotides targeting frataxin and related methods
- Patent number 12,312,585
- Issue date May 27, 2025
- UNIVERSITY OF MASSACHUSETTS
- Feng Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Phosphorodiamidate morpholino oligomers
- Patent number 12,297,219
- Issue date May 13, 2025
- Sarepta Therapeutics, Inc.
- Baozhong Cai
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dual-acting siRNA based modulation of C9orf72
- Patent number 12,297,429
- Issue date May 13, 2025
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment methods for muscular dystrophy
- Patent number 12,286,630
- Issue date Apr 29, 2025
- Sarepta Therapeutics, Inc.
- Huadong Sun
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Muscle-targeting complexes comprising an anti-transferrin receptor...
- Patent number 12,263,225
- Issue date Apr 1, 2025
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic oligonucleotides
- Patent number 12,234,455
- Issue date Feb 25, 2025
- IFOM Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d′Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Pharmaceutical composition for treatment of diseases associated wit...
- Patent number 12,227,743
- Issue date Feb 18, 2025
- Osaka University
- Fumihiro Sanada
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense antibacterial compounds and methods
- Patent number 12,209,240
- Issue date Jan 28, 2025
- Board of Regents, The University of Texas System
- David Greenberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for reducing Ataxin-2 expression
- Patent number 12,188,020
- Issue date Jan 7, 2025
- Ionis Pharmaceuticals, Inc.
- Frank Rigo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Trimeric peptides for antisense delivery
- Patent number 12,168,059
- Issue date Dec 17, 2024
- Sarepta Therapeutics, Inc.
- Justin Wolfe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for the treatment of expanded repeat-assoc...
- Patent number 12,161,658
- Issue date Dec 10, 2024
- UNIVERSITY OF MASSACHUSETTS
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...
- Patent number 12,163,132
- Issue date Dec 10, 2024
- Children's National Medical Center
- Yi-Wen Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides to restore dysferlin protein expression...
- Patent number 12,163,129
- Issue date Dec 10, 2024
- University of Massachusetts
- Robert H. Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulating the cellular stress response
- Patent number 12,157,888
- Issue date Dec 3, 2024
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment and diagnosis of inflammatory disorders
- Patent number 12,146,138
- Issue date Nov 19, 2024
- Zhenglun Zhu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Direct and selective inhibition of MDM4 for treatment of cancer
- Patent number 12,139,712
- Issue date Nov 12, 2024
- VIB VZW
- Jean-Christophe Marine
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligomers and methods of using the same for treating dise...
- Patent number 12,139,709
- Issue date Nov 12, 2024
- Sarepta Therapeutics, Inc.
- Frederick Joseph Schnell
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified antisense oligomers for exon inclusion in spinal muscular...
- Patent number 12,121,532
- Issue date Oct 22, 2024
- Sarepta Therapeutics, Inc.
- Marco A. Passini
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating cancer having an active Wnt/β-catenin pathway
- Patent number 12,109,212
- Issue date Oct 8, 2024
- Dana-Farber Cancer Institute, Inc.
- William C. Hahn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Polynucleotides containing a morpholino linker
- Patent number 12,071,620
- Issue date Aug 27, 2024
- ModernaTX, Inc.
- Gabor Butora
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Anti-transferrin receptor antibody-PMO conjugates for inducing DMD...
- Patent number 12,071,621
- Issue date Aug 27, 2024
- AVIDITY BIOSCIENCES, INC.
- Beatrice Diana Darimont
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and methods of inducing exon...
- Patent number 12,064,483
- Issue date Aug 20, 2024
- AVIDITY BIOSCIENCES, INC.
- Arthur A. Levin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for inhibiting detoxification response
- Patent number 12,065,648
- Issue date Aug 20, 2024
- The General Hospital Corporation
- Gary Ruvkun
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense nucleic acids
- Patent number 12,060,556
- Issue date Aug 13, 2024
- Nippon Shinyaku Co., Ltd.
- Naoki Watanabe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for reducing pathogenic isoforms
- Patent number 12,043,832
- Issue date Jul 23, 2024
- Washington University
- Andrew Findlay
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Antisense compounds targeting genes associated with cystic fibrosis
- Patent number 12,042,508
- Issue date Jul 23, 2024
- Rosalind Franklin University of Medicine and Science
- Michelle L. Hastings
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Muscle targeting complexes and uses thereof for treating dystrophin...
- Patent number 12,005,124
- Issue date Jun 11, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Antisense nucleic acids
- Patent number 11,981,894
- Issue date May 14, 2024
- Nippon Shinyaku Co., Ltd.
- Yukiko Enya
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Antisense oligonucleotide and composition for prevention or treatme...
- Patent number 11,963,974
- Issue date Apr 23, 2024
- National Center for Child Health and Development
- Go Tajima
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides targeting SCN2A for the treatment of SCN...
- Patent number 11,939,582
- Issue date Mar 26, 2024
- RogCon, Inc.
- Steven Petrou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
METHODS OF TREATING OSMIDROSIS
- Publication number 20250188461
- Publication date Jun 12, 2025
- Roger L. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20250186605
- Publication date Jun 12, 2025
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS
- Publication number 20250188474
- Publication date Jun 12, 2025
- Zhenglun Zhu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTIVIRAL ANTISENSE OLIGOMER
- Publication number 20250188469
- Publication date Jun 12, 2025
- Nippon Shinyaku Co., Ltd.
- Shinichiro Nakagawa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLIOBLASTOMA BY INHIB...
- Publication number 20250188457
- Publication date Jun 12, 2025
- Northwestern University
- Peiwen CHEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Nucleic Acids
- Publication number 20250188459
- Publication date Jun 12, 2025
- NIPPON SHINYAKU CO., LTD.
- Naoki Watanabe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREA...
- Publication number 20250179485
- Publication date Jun 5, 2025
- AptamiR Therapeutics, Inc.
- Marc Thibonnier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING GLAUCOMA
- Publication number 20250179490
- Publication date Jun 5, 2025
- PYC Therapeutics Limited
- Janya Grainok
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE
- Publication number 20250177543
- Publication date Jun 5, 2025
- Oxford University Innovation Limited
- Matthew WOOD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
- Publication number 20250179487
- Publication date Jun 5, 2025
- Sarepta Therapeutics, Inc.
- Frederick Joseph SCHNELL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED REPEAT-ASSOC...
- Publication number 20250177431
- Publication date Jun 5, 2025
- University of Massachusetts
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TRE...
- Publication number 20250179495
- Publication date Jun 5, 2025
- The University of Chicago
- Elizabeth McNally
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...
- Publication number 20250170260
- Publication date May 29, 2025
- Avidity Biosciences, Inc.
- Arthur A. LEVIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE-INDUCED EXON2 INCLUSION IN ACID ALPHA-GLUCOSIDASE
- Publication number 20250171783
- Publication date May 29, 2025
- Sarepta Therapeutics, Inc.
- Stephen Donald WILTON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20250170261
- Publication date May 29, 2025
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGOMERS AND METHODS OF USING THE SAME FOR TREATING DISE...
- Publication number 20250171779
- Publication date May 29, 2025
- Sarepta Therapeutics, Inc.
- Frederick Joseph Schnell
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRIMERIC PEPTIDES FOR ANTISENSE DELIVERY
- Publication number 20250161469
- Publication date May 22, 2025
- Sarepta Therapeutics, Inc.
- Justin Wolfe
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...
- Publication number 20250161344
- Publication date May 22, 2025
- Avidity Biosciences, Inc.
- Arthur A. LEVIN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS O...
- Publication number 20250163414
- Publication date May 22, 2025
- THE UNIVERSITY OF WESTERN AUSTRALIA
- Stephen Donald Wilton
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
- Publication number 20250154507
- Publication date May 15, 2025
- Sarepta Therapeutics, Inc.
- Peter SAZANI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250145991
- Publication date May 8, 2025
- Sarepta Therapeutics, Inc.
- Richard K. BESTWICK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Nucleic Acids
- Publication number 20250145997
- Publication date May 8, 2025
- Nippon Shinyaku co., Ltd.
- Tatsushi Wakayama
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES
- Publication number 20250145996
- Publication date May 8, 2025
- HOFFMANN-LA ROCHE INC.
- Jessica Marine Aurore BASTIEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT FOR SOD1 ASSOCIATED DISEASE
- Publication number 20250136993
- Publication date May 1, 2025
- Black Swan Pharmaceuticals, Inc.
- Stephen Donald Wilton
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR SKIPPING EXON 44 IN DUCHENNE MUSCULAR DYS...
- Publication number 20250129365
- Publication date Apr 24, 2025
- Entrada Therapeutics, Inc.
- Xiang Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRE-MRNA SLICE MODULATING PEPTIDE-CONJUGATED ANTISENSE THERAPEUTICS...
- Publication number 20250114464
- Publication date Apr 10, 2025
- The Governors of the University of Alberta
- Toshifumi YOKOTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEAS...
- Publication number 20250114368
- Publication date Apr 10, 2025
- Ann and Robert H. Lurie Children's Hospital of Chicago
- Yongchao C. MA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATING THE CELLULAR STRESS RESPONSE
- Publication number 20250115910
- Publication date Apr 10, 2025
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTION OR TREATME...
- Publication number 20250101431
- Publication date Mar 27, 2025
- NATIONAL CENTER FOR CHILD HEALTH AND DEVELOPMENT
- Go Tajima
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATMENT OF NEURODEGE...
- Publication number 20250092392
- Publication date Mar 20, 2025
- Eisai R&D Management Co., Ltd.
- Vinod VATHIPADIEKAL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Morpholino-type ring

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Oligonucleotides targeting frataxin and related methods

Phosphorodiamidate morpholino oligomers

Dual-acting siRNA based modulation of C9orf72

Treatment methods for muscular dystrophy

Muscle-targeting complexes comprising an anti-transferrin receptor...

Therapeutic oligonucleotides

Pharmaceutical composition for treatment of diseases associated wit...

Antisense antibacterial compounds and methods

Methods for reducing Ataxin-2 expression

Trimeric peptides for antisense delivery

Compositions and methods for the treatment of expanded repeat-assoc...

Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...

Antisense oligonucleotides to restore dysferlin protein expression...

Modulating the cellular stress response

Treatment and diagnosis of inflammatory disorders

Direct and selective inhibition of MDM4 for treatment of cancer

Antisense oligomers and methods of using the same for treating dise...

Modified antisense oligomers for exon inclusion in spinal muscular...

Methods of treating cancer having an active Wnt/β-catenin pathway

Polynucleotides containing a morpholino linker

Anti-transferrin receptor antibody-PMO conjugates for inducing DMD...

Nucleic acid-polypeptide compositions and methods of inducing exon...

Methods and compositions for inhibiting detoxification response

Antisense nucleic acids

Methods and compositions for reducing pathogenic isoforms

Antisense compounds targeting genes associated with cystic fibrosis

Muscle targeting complexes and uses thereof for treating dystrophin...

Antisense nucleic acids

Antisense oligonucleotide and composition for prevention or treatme...

Antisense oligonucleotides targeting SCN2A for the treatment of SCN...

Patents Applicationslast 30 patents

METHODS OF TREATING OSMIDROSIS

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS

ANTIVIRAL ANTISENSE OLIGOMER

COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLIOBLASTOMA BY INHIB...

Antisense Nucleic Acids

ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREA...

METHODS OF TREATING GLAUCOMA

CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE

EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED REPEAT-ASSOC...

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TRE...

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...

ANTISENSE-INDUCED EXON2 INCLUSION IN ACID ALPHA-GLUCOSIDASE

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

ANTISENSE OLIGOMERS AND METHODS OF USING THE SAME FOR TREATING DISE...

TRIMERIC PEPTIDES FOR ANTISENSE DELIVERY

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND METHODS OF INDUCING EXON...

ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS O...

MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

Antisense Nucleic Acids

OLIGONUCLEOTIDES TARGETING RNA BINDING PROTEIN SITES

TREATMENT FOR SOD1 ASSOCIATED DISEASE

COMPOUNDS AND METHODS FOR SKIPPING EXON 44 IN DUCHENNE MUSCULAR DYS...

PRE-MRNA SLICE MODULATING PEPTIDE-CONJUGATED ANTISENSE THERAPEUTICS...

COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEAS...

MODULATING THE CELLULAR STRESS RESPONSE

ANTISENSE OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTION OR TREATME...

ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR TREATMENT OF NEURODEGE...