Muscular dystrophy

Industry

CPC
C07K14/4707

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Parent Industries

CCHEMISTRY METALLURGY C07Organic chemistry C07KPEPTIDES C07K14/00Peptides having more than 20 amino acids Gastrins Somatostatins Melanotropins Derivatives thereof

Current Industry

C07K14/4707Muscular dystrophy

Industries

Patents Grantslast 30 patents

Information Patent Grant
Muscle targeting complexes and uses thereof for treating myotonic d...
- Patent number 12,102,687
- Issue date Oct 1, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Antibody-evading virus vectors
- Patent number 12,091,435
- Issue date Sep 17, 2024
- Ginkgo BioWorks, Inc.
- Daniel McCoy
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antibody-evading virus vectors
- Patent number 12,060,390
- Issue date Aug 13, 2024
- Ginkgo BioWorks, Inc.
- Daniel McCoy
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of muscular dystrophies
- Patent number 12,012,439
- Issue date Jun 18, 2024
- Royal Holloway and Bedford New College
- John George Dickson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Muscle targeting complexes and uses thereof for treating facioscapu...
- Patent number 11,969,475
- Issue date Apr 30, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Micro-dystrophins and related methods of use
- Patent number 11,958,888
- Issue date Apr 16, 2024
- University of Washington
- Jeffrey S. Chamberlain
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Muscle targeting complexes and uses thereof for treating facioscapu...
- Patent number 11,844,843
- Issue date Dec 19, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating muscular dystrophy
- Patent number 11,820,972
- Issue date Nov 21, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective gene therapy expression system
- Patent number 11,819,478
- Issue date Nov 21, 2023
- Genethon
- Ana Maria Buj Bello
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Muscle targeting complexes and uses thereof for treating facioscapu...
- Patent number 11,759,525
- Issue date Sep 19, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of muscular dystrophies
- Patent number 11,725,032
- Issue date Aug 15, 2023
- Royal Holloway and Bedford New College
- George Dickson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Muscle targeting complexes and uses thereof for treating facioscapu...
- Patent number 11,679,161
- Issue date Jun 20, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Muscle targeting complexes and uses thereof for treating Facioscapu...
- Patent number 11,638,761
- Issue date May 2, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Synthetic polynucleotides encoding a human FKRP protein
- Patent number 11,596,698
- Issue date Mar 7, 2023
- Genethon
- Isabelle Richard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Exon skipping oligomer conjugates for muscular dystrophy
- Patent number 11,491,238
- Issue date Nov 8, 2022
- Sarepta Therapeutics, Inc.
- Richard K. Bestwick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated virus delivery of alpha-sarcoglycan po...
- Patent number 11,446,396
- Issue date Sep 20, 2022
- Nationwide Children's Hospital, Inc.
- Jerry R. Mendell
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Exon skipping oligomer conjugates for muscular dystrophy
- Patent number 11,338,041
- Issue date May 24, 2022
- Sarepta Therapeutics, Inc.
- Gunnar J. Hanson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Recombinant virus products and methods for inhibition of expression...
- Patent number 11,091,760
- Issue date Aug 17, 2021
- Nationwide Children's Hospital, Inc.
- Scott Quenton Harper
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods of increasing sarcolemmal utrophin
- Patent number 10,968,262
- Issue date Apr 6, 2021
- Acceleron Pharma Inc.
- Jasbir Seehra
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Exon skipping oligomer conjugates for muscular dystrophy
- Patent number 10,765,760
- Issue date Sep 8, 2020
- Sarepta Therapeutics, Inc.
- Gunnar J. Hanson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Exon skipping oligomer conjugates for muscular dystrophy
- Patent number 10,758,629
- Issue date Sep 1, 2020
- Sarepta Therapeutics, Inc.
- Richard K. Bestwick
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Compositions for treating dystroglycanopathy disorders
- Patent number 10,350,305
- Issue date Jul 16, 2019
- The University of North Carolina at Chapel Hill
- Qi Long Lu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Recombinant virus products and methods for inhibition of expression...
- Patent number 10,196,636
- Issue date Feb 5, 2019
- Nationwide Children's Hospital, Inc.
- Scott Quenton Harper
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated virus delivery of alpha-sarcoglycan po...
- Patent number 10,105,453
- Issue date Oct 23, 2018
- Nationwide Children's Hospital, Inc.
- Jerry R. Mendell
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Selective gene therapy expression system
- Patent number 9,981,049
- Issue date May 29, 2018
- Genethon
- Ana Maria Buj Bello
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
WNT7A compositions and method of using the same
- Patent number 9,732,130
- Issue date Aug 15, 2017
- Ottawa Hospital Research Institute
- Michael A. Rudnicki
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
ActRIIB proteins and variants and uses therefore relating to utroph...
- Patent number 9,617,319
- Issue date Apr 11, 2017
- Acceleron Pharma Inc.
- Jasbir Seehra
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Nucleic acids encoding FHL1 mutations associated with novel X-linke...
- Patent number 9,617,320
- Issue date Apr 11, 2017
- Centre for Addiction and Mental Health
- John Vincent
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Survival motor neuron gene (SMN2) mRNA constructs for post-transcri...
- Patent number 9,394,539
- Issue date Jul 19, 2016
- PTC Therapeutics, Inc.
- Sergey V. Paushkin
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Prophylactic or ameliorating agent for genetic diseases
- Patent number 9,241,929
- Issue date Jan 26, 2016
- Masatoshi Hagiwara
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20240408227
- Publication date Dec 12, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20240398968
- Publication date Dec 5, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS TO SPREAD PROTEIN CARGOES ACROSS MULTI-NUC...
- Publication number 20240391969
- Publication date Nov 28, 2024
- University of Florida Research Foundation, Incorporated
- Eric Tzy-Shi Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF MUSCULAR DYSTROPHY
- Publication number 20240350674
- Publication date Oct 24, 2024
- Solid Biosciences Inc.
- Kristy Jean Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
C2 Domain Therapeutics and Uses Thereof
- Publication number 20240294588
- Publication date Sep 5, 2024
- University of Maryland, Baltimore
- Robert J. Bloch
- C07 - ORGANIC CHEMISTRY
Information Patent Application
MODIFIED AAV CAPSIDS AND USES THEREOF
- Publication number 20240261437
- Publication date Aug 8, 2024
- Solid Biosciences Inc.
- Peter Pechan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTS AND METHODS FOR TREATIN...
- Publication number 20240254181
- Publication date Aug 1, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C07 - ORGANIC CHEMISTRY
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MYOTONIC D...
- Publication number 20240238435
- Publication date Jul 18, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR TREATING DYSFERLINOPATHY
- Publication number 20240228564
- Publication date Jul 11, 2024
- UNIVERSITÉ D'AIX-MARSEILLE
- Marc BARTOLI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods of Treating Muscular Dystrophy
- Publication number 20240191250
- Publication date Jun 13, 2024
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C07 - ORGANIC CHEMISTRY
Information Patent Application
SYNTHETIC INTERMEMBRANE PROTEOLYSIS RECEPTORS FOR CUSTOM ANTIGEN-IN...
- Publication number 20240181057
- Publication date Jun 6, 2024
- The Regents of the University of California
- Kole T. Roybal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...
- Publication number 20240066140
- Publication date Feb 29, 2024
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTIBODY-EVADING VIRUS VECTORS
- Publication number 20240059742
- Publication date Feb 22, 2024
- Ginkgo BioWorks, Inc.
- Daniel McCoy
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
- Publication number 20240042049
- Publication date Feb 8, 2024
- Sarepta Therapeutics, Inc.
- Richard K. BESTWICK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Treatment of Muscular Dystrophies
- Publication number 20230391840
- Publication date Dec 7, 2023
- ROYAL HOLLOWAY AND BEDFORD NEW COLLEGE
- John George Dickson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
A HIGH-THROUGHPUT SCREENING METHOD TO DISCOVER OPTIMAL GRNA PAIRS F...
- Publication number 20230349888
- Publication date Nov 2, 2023
- DUKE UNIVERSITY
- Charles A. Gersbach
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...
- Publication number 20230321264
- Publication date Oct 12, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NOVEL POLYNUCLEOTIDES ENCODING A HUMAN FKRP PROTEIN
- Publication number 20230321277
- Publication date Oct 12, 2023
- GENETHON
- Isabelle RICHARD
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...
- Publication number 20230285582
- Publication date Sep 14, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY WITH DYSFERLIN DUAL VECTORS
- Publication number 20230279065
- Publication date Sep 7, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C07 - ORGANIC CHEMISTRY
Information Patent Application
Self-Complementary Adeno-Associated Virus Vector and its Use in Tre...
- Publication number 20230279431
- Publication date Sep 7, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- C07 - ORGANIC CHEMISTRY
Information Patent Application
OPTIMIZED GENE THERAPY FOR TARGETING MUSCLE IN MUSCLE DISEASES
- Publication number 20230227515
- Publication date Jul 20, 2023
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...
- Publication number 20230118799
- Publication date Apr 20, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
- Publication number 20230110479
- Publication date Apr 13, 2023
- Sarepta Therapeutics, Inc.
- Gunnar J. Hanson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...
- Publication number 20230045314
- Publication date Feb 9, 2023
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Recombinant Adeno-Associated Virus Delivery of Alpha-Sarcoglycan Po...
- Publication number 20220370639
- Publication date Nov 24, 2022
- Nationwide Children's Hospital, Inc.
- Jerry R. Mendell
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION...
- Publication number 20220064641
- Publication date Mar 3, 2022
- Nationwide Children's Hospital, Inc.
- Scott Quenton HARPER
- C07 - ORGANIC CHEMISTRY
Information Patent Application
ACTRIIB PROTEINS AND VARIANTS AND USES THEREFORE RELATING TO UTROPH...
- Publication number 20220041670
- Publication date Feb 10, 2022
- Acceleron Pharma Inc.
- Jasbir Seehra
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTIBODY-EVADING VIRUS VECTORS
- Publication number 20210371471
- Publication date Dec 2, 2021
- StrideBio, Inc.
- Daniel McCoy
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL POLYNUCLEOTIDES ENCODING A HUMAN FKRP PROTEIN
- Publication number 20210338837
- Publication date Nov 4, 2021
- Genethon
- Isabelle RICHARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Muscular dystrophy

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Muscle targeting complexes and uses thereof for treating myotonic d...

Antibody-evading virus vectors

Antibody-evading virus vectors

Treatment of muscular dystrophies

Muscle targeting complexes and uses thereof for treating facioscapu...

Micro-dystrophins and related methods of use

Muscle targeting complexes and uses thereof for treating facioscapu...

Methods of treating muscular dystrophy

Selective gene therapy expression system

Muscle targeting complexes and uses thereof for treating facioscapu...

Treatment of muscular dystrophies

Muscle targeting complexes and uses thereof for treating facioscapu...

Muscle targeting complexes and uses thereof for treating Facioscapu...

Synthetic polynucleotides encoding a human FKRP protein

Exon skipping oligomer conjugates for muscular dystrophy

Recombinant adeno-associated virus delivery of alpha-sarcoglycan po...

Exon skipping oligomer conjugates for muscular dystrophy

Recombinant virus products and methods for inhibition of expression...

Methods of increasing sarcolemmal utrophin

Exon skipping oligomer conjugates for muscular dystrophy

Exon skipping oligomer conjugates for muscular dystrophy

Compositions for treating dystroglycanopathy disorders

Recombinant virus products and methods for inhibition of expression...

Recombinant adeno-associated virus delivery of alpha-sarcoglycan po...

Selective gene therapy expression system

WNT7A compositions and method of using the same

ActRIIB proteins and variants and uses therefore relating to utroph...

Nucleic acids encoding FHL1 mutations associated with novel X-linke...

Survival motor neuron gene (SMN2) mRNA constructs for post-transcri...

Prophylactic or ameliorating agent for genetic diseases

Patents Applicationslast 30 patents

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

METHODS AND COMPOSITIONS TO SPREAD PROTEIN CARGOES ACROSS MULTI-NUC...

TREATMENT OF MUSCULAR DYSTROPHY

C2 Domain Therapeutics and Uses Thereof

MODIFIED AAV CAPSIDS AND USES THEREOF

RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTS AND METHODS FOR TREATIN...

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MYOTONIC D...

COMPOSITION FOR TREATING DYSFERLINOPATHY

Methods of Treating Muscular Dystrophy

SYNTHETIC INTERMEMBRANE PROTEOLYSIS RECEPTORS FOR CUSTOM ANTIGEN-IN...

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...

ANTIBODY-EVADING VIRUS VECTORS

EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

Treatment of Muscular Dystrophies

A HIGH-THROUGHPUT SCREENING METHOD TO DISCOVER OPTIMAL GRNA PAIRS F...

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...

NOVEL POLYNUCLEOTIDES ENCODING A HUMAN FKRP PROTEIN

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...

GENE THERAPY WITH DYSFERLIN DUAL VECTORS

Self-Complementary Adeno-Associated Virus Vector and its Use in Tre...

OPTIMIZED GENE THERAPY FOR TARGETING MUSCLE IN MUSCLE DISEASES

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...

EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPU...

Recombinant Adeno-Associated Virus Delivery of Alpha-Sarcoglycan Po...

RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION...

ACTRIIB PROTEINS AND VARIANTS AND USES THEREFORE RELATING TO UTROPH...

ANTIBODY-EVADING VIRUS VECTORS

NOVEL POLYNUCLEOTIDES ENCODING A HUMAN FKRP PROTEIN