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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

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C12N2310/31of the backbone

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Patents Grantslast 30 patents

Information Patent Grant
Compositions, systems, and methods for regulation of hepatitis b vi...
- Patent number 12,221,608
- Issue date Feb 11, 2025
- TUNE THERAPEUTICS, INC.
- Brian Cosgrove
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of diacyglycerol acyltransferase 2 (DGAT2)
- Patent number 12,215,321
- Issue date Feb 4, 2025
- Ionis Pharmaceuticals, Inc.
- Eric E. Swayze
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for RNA-directed target DNA modification a...
- Patent number 12,215,343
- Issue date Feb 4, 2025
- The Regents of the University of California
- Jennifer A. Doudna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Aptamer-based CAR T-cell switch
- Patent number 12,209,243
- Issue date Jan 28, 2025
- Alaya.bio Inc.
- Anna Miodek
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Multiplexed analysis of materials for tissue delivery
- Patent number 12,201,696
- Issue date Jan 21, 2025
- Georgia Tech Research Corporation
- James Dahlman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotide agonists targeting progranulin
- Patent number 12,203,071
- Issue date Jan 21, 2025
- HOFFMANN-LA ROCHE INC.
- Ravi Jagasia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CCR7 aptamers and uses thereof
- Patent number 12,194,056
- Issue date Jan 14, 2025
- City of Hope
- John J. Rossi
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting gene expression of alpha-1...
- Patent number 12,188,017
- Issue date Jan 7, 2025
- Arrowhead Pharmaceuticals, Inc.
- Christine I Wooddell
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for reducing Ataxin-2 expression
- Patent number 12,188,020
- Issue date Jan 7, 2025
- Ionis Pharmaceuticals, Inc.
- Frank Rigo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides for the treatment of Stargardt disease
- Patent number 12,180,471
- Issue date Dec 31, 2024
- ProQR Therapeutics II B.V.
- Aliye Seda Yilmaz-Elis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating ATXN1
- Patent number 12,180,479
- Issue date Dec 31, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dynamic pharmacokinetic-modifying anchors
- Patent number 12,180,477
- Issue date Dec 31, 2024
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for RNA-directed target DNA modification a...
- Patent number 12,180,503
- Issue date Dec 31, 2024
- The Regents of the University of California
- Jennifer A. Doudna
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Methods and compositions for RNA-directed target DNA modification a...
- Patent number 12,180,504
- Issue date Dec 31, 2024
- The Regents of the University of California
- Jennifer A. Doudna
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Chiral design
- Patent number 12,180,472
- Issue date Dec 31, 2024
- WAVE LIFE SCIENCES LTD.
- Meena Meena
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides targeting alpha-synuclein and uses thereof
- Patent number 12,180,478
- Issue date Dec 31, 2024
- Bristol-Myers Squibb Company
- Richard E. Olson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for improving strand biased
- Patent number 12,173,287
- Issue date Dec 24, 2024
- Alnylam Pharmaceuticals, Inc.
- Rubina G. Parmar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Peptide nucleic acid conjugates
- Patent number 12,173,031
- Issue date Dec 24, 2024
- Ventana Medical Systems, Inc.
- Rui Hong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA-editing oligonucleotides and uses thereof
- Patent number 12,173,285
- Issue date Dec 24, 2024
- Korro Bio, Inc.
- Andrew W. Fraley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Fully stabilized asymmetric siRNA
- Patent number 12,173,286
- Issue date Dec 24, 2024
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Unnatural base pair compositions and methods of use
- Patent number 12,173,291
- Issue date Dec 24, 2024
- The Scripps Research Institute
- Floyd E. Romesberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified guide RNAs
- Patent number 12,173,284
- Issue date Dec 24, 2024
- Intellia Therapeutics, Inc.
- Amy Madison Rhoden Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified double-stranded RNA agents
- Patent number 12,168,767
- Issue date Dec 17, 2024
- Alnylam Pharmaceuticals, Inc.
- Martin Maier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR-CAS9 modified CD34+ human hematopoietic stem and progenitor...
- Patent number 12,161,674
- Issue date Dec 10, 2024
- Vertex Pharmaceuticals Incorporated
- Ewelina Morawa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...
- Patent number 12,163,132
- Issue date Dec 10, 2024
- Children's National Medical Center
- Yi-Wen Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for the treatment of expanded repeat-assoc...
- Patent number 12,161,658
- Issue date Dec 10, 2024
- UNIVERSITY OF MASSACHUSETTS
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides to restore dysferlin protein expression...
- Patent number 12,163,129
- Issue date Dec 10, 2024
- University of Massachusetts
- Robert H. Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating neuronal excitability and m...
- Patent number 12,163,130
- Issue date Dec 10, 2024
- Icahn School of Medicine at Mount Sinai
- Anne Schaefer
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Oligonucleotides for modulating Tau expression
- Patent number 12,163,131
- Issue date Dec 10, 2024
- HOFFMANN-LA ROCHE INC.
- Peter Hagedorn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
- Publication number 20250051765
- Publication date Feb 13, 2025
- Alnylam Pharmaceuticals, Inc.
- Kevin FITZGERALD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
iRNA Compositions and Methods for Silencing MYLIP
- Publication number 20250051767
- Publication date Feb 13, 2025
- Alnylam Pharmaceuticals, Inc.
- LUCAS WARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Oligonucleotide for Targeting Progranulin
- Publication number 20250051772
- Publication date Feb 13, 2025
- HOFFMANN-LA ROCHE INC.
- Ravi Jagasia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA
- Publication number 20250051769
- Publication date Feb 13, 2025
- Nippon Shinyaku Co., Ltd.
- Takao KAWANO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
- Publication number 20250051778
- Publication date Feb 13, 2025
- WAVE LIFE SCIENCES LTD.
- Michael John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE...
- Publication number 20250051766
- Publication date Feb 13, 2025
- QURALIS CORPORATION
- SANDRA HINCKLEY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
- Publication number 20250051775
- Publication date Feb 13, 2025
- The United States of America, as represented by the Secretary, Department of...
- Pietro Fratta
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATING GLYCOGEN SYNTHASE 1
- Publication number 20250051781
- Publication date Feb 13, 2025
- Ionis Pharmaceuticals, Inc.
- Huynh-Hoa Bui
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS A...
- Publication number 20250051776
- Publication date Feb 13, 2025
- HAYA Therapeutics SA
- Samir OUNZAIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND SAPONIN FOR TH...
- Publication number 20250051770
- Publication date Feb 13, 2025
- Sapreme Technologies B.V.
- Miriam Verena BUJNY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
- Publication number 20250051777
- Publication date Feb 13, 2025
- HOFFMANN-LA ROCHE INC.
- Peter HAGEDORN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS VIA...
- Publication number 20250043283
- Publication date Feb 6, 2025
- Sarepta Therapeutics, Inc.
- Kyle A. Totaro
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
- Publication number 20250043279
- Publication date Feb 6, 2025
- Alnylam Pharmaceuticals, Inc.
- Mark K. Schlegel
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CRISPR-CAS9 Modified CD34+ Human Hematopoietic Stem and Progenitor...
- Publication number 20250041349
- Publication date Feb 6, 2025
- VERTEX PHARMACEUTICALS INCORPORATED
- Ewelina Morawa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF FGG RELATED DISEASES AND DISORDERS
- Publication number 20250043281
- Publication date Feb 6, 2025
- EMPIRICO INC.
- Omri GOTTESMAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRODUCTS AND COMPOSITIONS
- Publication number 20250043288
- Publication date Feb 6, 2025
- Silence Therapeutics GMBH
- Judith HAUPTMANN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
3-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS...
- Publication number 20250043289
- Publication date Feb 6, 2025
- Alnylam Pharmaceuticals, Inc.
- Ho-Chou Tu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE NUCLEIC ACIDS
- Publication number 20250042933
- Publication date Feb 6, 2025
- NIPPON SHINYAKU CO., LTD
- Naoki Watanabe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR SNCA MODULATION
- Publication number 20250043284
- Publication date Feb 6, 2025
- University of Massachusetts
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Double Stranded Oligonucleotide For Modulating JAK1 Expression
- Publication number 20250034576
- Publication date Jan 30, 2025
- HOFFMANN-LA ROCHE INC.
- Philipp Friedrich BERNINGER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLE...
- Publication number 20250032622
- Publication date Jan 30, 2025
- Avidity Biosciences, Inc.
- Cecilia HURTADO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Methods and Compositions for ADAR-Mediated Editing
- Publication number 20250034564
- Publication date Jan 30, 2025
- Korro Bio, Inc.
- Mallikarjuna Reddy Putta
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
- Publication number 20250034566
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Brian Bettencourt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP)...
- Publication number 20250034570
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Kevin Fitzgerald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED DOUBLE-STRANDED RNA AGENTS
- Publication number 20250034572
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Martin MAIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS
- Publication number 20250034575
- Publication date Jan 30, 2025
- University of Massachusetts
- Michael Czech
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GLYCAN CONJUGATE COMPOSITIONS AND METHODS
- Publication number 20250034565
- Publication date Jan 30, 2025
- GanNA Bio, Inc.
- Namita BISARIA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS...
- Publication number 20250034567
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- JEFFREY ZUBER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods and Compositions for ADAR-Mediated Editing
- Publication number 20250034563
- Publication date Jan 30, 2025
- Korro Bio, Inc.
- Mallikarjuna Reddy Putta
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Com...
- Publication number 20250034577
- Publication date Jan 30, 2025
- Arrowhead Pharmaceuticals, Inc.
- Anthony Nicholas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

of the backbone

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compositions, systems, and methods for regulation of hepatitis b vi...

Modulators of diacyglycerol acyltransferase 2 (DGAT2)

Methods and compositions for RNA-directed target DNA modification a...

Aptamer-based CAR T-cell switch

Multiplexed analysis of materials for tissue delivery

Oligonucleotide agonists targeting progranulin

CCR7 aptamers and uses thereof

Compositions and methods for inhibiting gene expression of alpha-1...

Methods for reducing Ataxin-2 expression

Antisense oligonucleotides for the treatment of Stargardt disease

Compounds and methods for modulating ATXN1

Dynamic pharmacokinetic-modifying anchors

Methods and compositions for RNA-directed target DNA modification a...

Methods and compositions for RNA-directed target DNA modification a...

Chiral design

Antisense oligonucleotides targeting alpha-synuclein and uses thereof

Compositions and methods for improving strand biased

Peptide nucleic acid conjugates

RNA-editing oligonucleotides and uses thereof

Fully stabilized asymmetric siRNA

Unnatural base pair compositions and methods of use

Modified guide RNAs

Modulators of APOL1 expression

Modified double-stranded RNA agents

CRISPR-CAS9 modified CD34+ human hematopoietic stem and progenitor...

Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...

Compositions and methods for the treatment of expanded repeat-assoc...

Antisense oligonucleotides to restore dysferlin protein expression...

Compositions and methods for modulating neuronal excitability and m...

Oligonucleotides for modulating Tau expression

Patents Applicationslast 30 patents

APOLIPOPROTEIN C3 (APOC3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

iRNA Compositions and Methods for Silencing MYLIP

Antisense Oligonucleotide for Targeting Progranulin

ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

TREATMENT OF NEUROLOGICAL DISEASES USING MODULATORS OF UNC13A GENE...

THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS

COMPOUNDS AND METHODS FOR MODULATING GLYCOGEN SYNTHASE 1

COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS A...

COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND SAPONIN FOR TH...

OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION

PROCESSES FOR PREPARING PHOSPHORODIAMIDATE MORPHOLINO OLIGOMERS VIA...

SERPINA1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

CRISPR-CAS9 Modified CD34+ Human Hematopoietic Stem and Progenitor...

TREATMENT OF FGG RELATED DISEASES AND DISORDERS

PRODUCTS AND COMPOSITIONS

3-HYDROXY-3-METHYLGLUTARYL-COA REDUCTASE (HMGCR) IRNA COMPOSITIONS...

ANTISENSE NUCLEIC ACIDS

OLIGONUCLEOTIDES FOR SNCA MODULATION

Double Stranded Oligonucleotide For Modulating JAK1 Expression

COMPOSITIONS AND METHODS OF USING PLN-TARGETING ANTIBODY-OLIGONUCLE...

Methods and Compositions for ADAR-Mediated Editing

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP)...

MODIFIED DOUBLE-STRANDED RNA AGENTS

OLIGONUCLEOTIDES FOR DGAT2, FASN, OPN, AND NOX4 MODULATIONS

GLYCAN CONJUGATE COMPOSITIONS AND METHODS

CELL DEATH-INDUCING DFFA-LIKE EFFECTOR B (CIDEB) IRNA COMPOSITIONS...

Methods and Compositions for ADAR-Mediated Editing

RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Com...