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Selective Reduction of Allelic Variants
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Publication number 20250223589
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Publication date Jul 10, 2025
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Ionis Pharmaceuticals, Inc.
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SYF2 ANTISENSE OLIGONUCLEOTIDES
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Publication number 20250223591
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Publication date Jul 10, 2025
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AcuraStem Incorported
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Emily Elizabeth LEE
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IMMUNOSTIMULATORY COMPOSITIONS
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Publication date Jul 3, 2025
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Elanco Animal Health GmbH
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Thomas ILG
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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RNAi Agents of Modulating PLP1
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Publication number 20250197858
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Publication date Jun 19, 2025
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Ionis Pharmaceuticals, Inc.
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Susan M. Freier
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOUNDS AND METHODS FOR MODULATING SMN2
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Publication number 20250179493
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Publication date Jun 5, 2025
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Ionis Pharmaceuticals, Inc.
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Frank Rigo
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
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Publication number 20250154507
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Publication date May 15, 2025
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Sarepta Therapeutics, Inc.
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...