regulating transport or export of RNA

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Patents Applicationslast 30 patents

  • Information Patent Application

    STABLE REGULATORY T CELLS AND METHODS OF PRODUCTION

    • Publication number 20250186497
    • Publication date Jun 12, 2025
    • Abata Therapeutics, Inc.
    • Stephen SOFEN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    PROCESS FOR PRODUCING CONE PHOTORECEPTOR CELLS

    • Publication number 20250171738
    • Publication date May 29, 2025
    • Centre for Eye Research Australia Ltd.
    • Ching Bong WONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    PROMOTERS FOR SPECIFIC EXPRESSION OF GENES IN CONE PHOTORECEPTORS

    • Publication number 20250171775
    • Publication date May 29, 2025
    • Institute of Molecular and Clinical Ophthalmology Basel (IOB)
    • Botond Miklós Roska
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    IN VITRO AND IN VIVO PROTEIN TRANSLATION VIA IN SITU CIRCULARIZED RNAS

    • Publication number 20250163454
    • Publication date May 22, 2025
    • The Regents of the University of California
    • Prashant Mali
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    INTRON FRAGMENTS

    • Publication number 20250163455
    • Publication date May 22, 2025
    • NEURACLE GENETICS INC.
    • Hoon Young KONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS OF TREATING NEURODEGENERATIVE DISORDERS

    • Publication number 20250152744
    • Publication date May 15, 2025
    • Genzyme Corporation
    • Shyam RAMACHANDRAN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    BASE EDITING AND CRISPR/CAS9 GENE EDITING STRATEGIES TO CORRECT CD3...

    • Publication number 20250144147
    • Publication date May 8, 2025
    • The Regents of the University of California
    • Donald B. KOHN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS FOR USE OF VIRAL VECTOR CONSTRUCTS FOR THE TREATMENT OF FAB...

    • Publication number 20250144240
    • Publication date May 8, 2025
    • Sangamo Therapeutics, Inc.
    • Cristobal PASSALACQUA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT...

    • Publication number 20250136651
    • Publication date May 1, 2025
    • THE UNIVERSITY COURT OF THE UNIVERSITY OF EDINBURGH
    • Stuart Robert Cobb
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF

    • Publication number 20250135040
    • Publication date May 1, 2025
    • Spacecraft Seven, LLC
    • Christopher Dean HERZOG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT VIRUS EXPRESSING TPK AND USE THEREOF IN TREATMENT OF AL...

    • Publication number 20250121095
    • Publication date Apr 17, 2025
    • SHANGHAI RAISING PHARMACEUTICAL CO., LTD.
    • Jingjing WANG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Gene Therapy Methods for Age-Related Diseases and Conditions

    • Publication number 20250122267
    • Publication date Apr 17, 2025
    • President and Fellows of Harvard College
    • Noah Davidsohn
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    LENTIVIRAL GENE THERAPY RESCUES FUNCTION IN A MOUSE MODEL OF USHER 1B

    • Publication number 20250121093
    • Publication date Apr 17, 2025
    • University of Kansas
    • Hinrich STAECKER
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    SCHWANN CELL-SPECIFIC PROMOTER

    • Publication number 20250115906
    • Publication date Apr 10, 2025
    • Toolgen Incorporated
    • Dong Woo SONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    LENTIVIRAL VECTOR FOR OVEREXPRESSING EGF, RECOMBINANT STEM CELL, AN...

    • Publication number 20250114481
    • Publication date Apr 10, 2025
    • Centre for Regenerative Medicine and Health, Hong Kong Institute of Science &...
    • Dajiang QIN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENE THERAPY FOR GENETIC HEARING LOSS

    • Publication number 20250114480
    • Publication date Apr 10, 2025
    • BridgeBio Gene Therapy Research, Inc.
    • Clayton BEARD
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OPTIMIZED AAV-BASED VACCINE

    • Publication number 20250101458
    • Publication date Mar 27, 2025
    • Massachusetts Eye and Ear Infirmary
    • Luc H. Vandenberghe
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    COMPOSITIONS FOR TREATING CANCER

    • Publication number 20250099615
    • Publication date Mar 27, 2025
    • Kelonia Therapeutics, Inc.
    • Kevin M. Friedman
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT LENTIVIRAL VECTOR FOR STEM CELL-BASED GENE THERAPY OF S...

    • Publication number 20250084437
    • Publication date Mar 13, 2025
    • Institut National de la Sante et de la Recherche Medicale (INSERM)
    • Annarita MICCIO
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    WPRE MUTANT CONSTRUCTS, COMPOSITIONS, AND METHODS THEREOF

    • Publication number 20250075230
    • Publication date Mar 6, 2025
    • Immatics US, Inc.
    • Melinda MATA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    THERAPY

    • Publication number 20250064975
    • Publication date Feb 27, 2025
    • The University of Bristol
    • Moin Ahson Saleem-Uddin
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV GENE THERAPY FOR THE KIDNEY

    • Publication number 20250064984
    • Publication date Feb 27, 2025
    • The University of Bristol
    • Moin Ahson Saleem-Uddin
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACI...

    • Publication number 20250049952
    • Publication date Feb 13, 2025
    • The United States of America,as represented by the Secretary,Department of He...
    • Charles P. Venditti
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

    • Publication number 20250049959
    • Publication date Feb 13, 2025
    • Tenaya Therapeutics, Inc.
    • Huanyu ZHOU
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES

    • Publication number 20250049949
    • Publication date Feb 13, 2025
    • The Trustees of the University of Pennsylvania
    • Christian Hinderer
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AADC/GDNF POLYNUCLEOTIDE, AND USE THEREOF IN TREATING PARKINSON'S D...

    • Publication number 20250051750
    • Publication date Feb 13, 2025
    • SHANGHAI REGENELEAD THERAPIES CO., LTD.
    • Jun Jiang
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

    • Publication number 20250041445
    • Publication date Feb 6, 2025
    • The Trustees of the University of Pennsylvania
    • Juliette Hordeaux
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Lentiviral Vectors

    • Publication number 20250034589
    • Publication date Jan 30, 2025
    • OXFORD BIOMEDICA (UK) LIMITED
    • Daniel Farley
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS

    • Publication number 20250034556
    • Publication date Jan 30, 2025
    • THE BROAD INSTITUTE, INC.
    • Binhui Zhao
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    SELF-INACTIVATING LENTIVIRAL VECTOR ENCODING BETA- OR GAMMA-GLOBIN

    • Publication number 20250034591
    • Publication date Jan 30, 2025
    • Children's Hospital Medical Center
    • Punam MALIK
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...