regulating transport or export of RNA

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C12N2830/48

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

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C12N2830/48regulating transport or export of RNA

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Patents Grantslast 30 patents

Information Patent Grant
Engineered invariant natural killer T (iNKT) cells and methods of m...
- Patent number 12,187,777
- Issue date Jan 7, 2025
- The Regents of the University of California
- Lili Yang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Intron fragments
- Patent number 12,173,304
- Issue date Dec 24, 2024
- NEURACLE GENETICS INC.
- Hoon Young Kong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating or preventing pyruvate kinase deficiency
- Patent number 12,163,151
- Issue date Dec 10, 2024
- CENTRO DE INVESTIGACIONES ENERGETICAS, MEDIOAMBIENTALES Y TECNOLOGICAS O.A, M.P.
- Jose C. Segovia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant lentiviral vector for stem cell- based gene therapy of...
- Patent number 12,139,720
- Issue date Nov 12, 2024
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- Annarita Miccio
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapy
- Patent number 12,121,593
- Issue date Oct 22, 2024
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
WPRE mutant constructs, compositions, and methods thereof
- Patent number 12,123,013
- Issue date Oct 22, 2024
- Immatics US, Inc.
- Melinda Mata
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Vectors for the treatment of Friedreich's ataxia
- Patent number 12,084,673
- Issue date Sep 10, 2024
- FUNDACIÓ INSTITUT D'INVESTIGACIÓ EN CIENCIES DE LA SALUT GERMANS TRIAS I PUJOL
- Antoni Matilla Dueñas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
BCMA chimeric antigen receptors
- Patent number 12,006,369
- Issue date Jun 11, 2024
- 2seventy bio, Inc.
- Richard Morgan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapies for lysosomal disorders
- Patent number 11,993,790
- Issue date May 28, 2024
- Prevail Therapeutics, Inc.
- Asa Abeliovich
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Adeno associated virus vectors for the treatment of hunter disease
- Patent number 11,981,912
- Issue date May 14, 2024
- Takeda Pharma ceutical Company Limited
- Vivian Choi
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Bicistronic AAV vector for RNA interference in ALS
- Patent number 11,872,290
- Issue date Jan 16, 2024
- Ecole Polytechnique Federale de Lausanne (EPFL)
- Julianne Aebischer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adenoviral vectors with two expression cassettes encoding RSV antig...
- Patent number 11,859,199
- Issue date Jan 2, 2024
- GlaxoSmithKline Biologicals SA
- Stefano Colloca
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
WPRE mutant constructs, compositions, and methods thereof
- Patent number 11,851,673
- Issue date Dec 26, 2023
- Immatics US, Inc.
- Melinda Mata
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Neuroreceptor compositions and methods of use
- Patent number 11,760,788
- Issue date Sep 19, 2023
- Pathways Neuro Pharma, Inc.
- Warren C. Lau
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Globin gene therapy for treating hemoglobinopathies
- Patent number 11,717,579
- Issue date Aug 8, 2023
- Memorial Sloan Kettering Cancer Center
- Michel Sadelain
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
DNA vectors and elements for sustained gene expression in eukaryoti...
- Patent number 11,713,468
- Issue date Aug 1, 2023
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lentiviral vectors for delivery of PKLR to treat pyruvate kinase de...
- Patent number 11,642,422
- Issue date May 9, 2023
- Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, O.A,...
- Jose Carlos Segovia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lentiviral vector expressing membrane-anchored or secreted antibody
- Patent number 11,623,950
- Issue date Apr 11, 2023
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- Floriane Fusil
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Method of detecting and/or identifying adeno-associated virus (AAV)...
- Patent number 11,499,167
- Issue date Nov 15, 2022
- The Trustees of the University of Pennsylvania
- Guangping Gao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for the treatment of a retinal degeneration disease
- Patent number 11,400,167
- Issue date Aug 2, 2022
- EyeServ GmbH
- Stylianos Michalakis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus (AAV) serotype 8 sequences, vectors containi...
- Patent number 11,396,663
- Issue date Jul 26, 2022
- The Trustees of the University of Pennsylvania
- Guangping Gao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated virus (AAV) serotype 8 sequences, vectors containi...
- Patent number 11,390,883
- Issue date Jul 19, 2022
- The Trustees of the University of Pennsylvania
- Guangping Gao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Method of detecting and/or identifying adeno-associated virus (AAV)...
- Patent number 11,377,669
- Issue date Jul 5, 2022
- The Trustees of the University of Pennsylvania
- Guangping Gao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated virus (AAV) clades, sequences, vectors containing...
- Patent number 11,357,868
- Issue date Jun 14, 2022
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Adeno-associated virus (AAV) clades, sequences, vectors containing...
- Patent number 11,357,867
- Issue date Jun 14, 2022
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Viral vectors for prophylaxis and therapy of hemoglobinopathies
- Patent number 11,311,632
- Issue date Apr 26, 2022
- Cornell University
- Stefano Rivella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV delivery of nucleobase editors
- Patent number 11,306,324
- Issue date Apr 19, 2022
- President and Fellows of Harvard College
- David R. Liu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods of treating or preventing pyruvate kinase deficiency
- Patent number 11,286,501
- Issue date Mar 29, 2022
- CENTRO DE INVESTIGACIONES ENERGETICAS, MEDIOAMBIENTALES Y TECNOLOGICAS O.A, M.P.
- Jose C. Segovia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Catecholamine enzyme fusions
- Patent number 11,279,954
- Issue date Mar 22, 2022
- Oxford Biomedica (UK) Ltd.
- Kyriacos A. Mitrophanous
- C07 - ORGANIC CHEMISTRY

Patents Applicationslast 30 patents

Information Patent Application
GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
- Publication number 20250041445
- Publication date Feb 6, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Lentiviral Vectors
- Publication number 20250034589
- Publication date Jan 30, 2025
- OXFORD BIOMEDICA (UK) LIMITED
- Daniel Farley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS
- Publication number 20250034556
- Publication date Jan 30, 2025
- THE BROAD INSTITUTE, INC.
- Binhui Zhao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SELF-INACTIVATING LENTIVIRAL VECTOR ENCODING BETA- OR GAMMA-GLOBIN
- Publication number 20250034591
- Publication date Jan 30, 2025
- Children's Hospital Medical Center
- Punam MALIK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOCICEPTOR-SPECIFIC GENE REGULATORY ELEMENTS FOR THE TREATMENT OF PAIN
- Publication number 20250009906
- Publication date Jan 9, 2025
- President and Fellows of Harvard College
- William Renthal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RETGC Gene Therapy
- Publication number 20250002936
- Publication date Jan 2, 2025
- MEIRAGTX UK II LIMITED
- Anastasios Georgiadis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL METHODS OF USING ADENO-ASSOCIATED VIRUS 11 (AAV11)
- Publication number 20240424085
- Publication date Dec 26, 2024
- Massachusetts Eye and Ear Infirmary
- Luc H. Vandenberghe
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GA...
- Publication number 20240424141
- Publication date Dec 26, 2024
- CANbridge Pharmaceuticals, Inc.
- Yunxiang Zhu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
BCMA CHIMERIC ANTIGEN RECEPTORS
- Publication number 20240417481
- Publication date Dec 19, 2024
- 2seventy bio, Inc.
- Richard Morgan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
LENTIVIRAL VECTOR FOR EXPRESSION OF HUMAN PAPILLOMAVIRUS (HPV) ANTI...
- Publication number 20240415951
- Publication date Dec 19, 2024
- Theravectys
- Pierre CHARNEAU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INTEGRASES, LANDING PAD ARCHITECTURES, AND ENGINEERED CELLS COMPRIS...
- Publication number 20240409906
- Publication date Dec 12, 2024
- Asimov Inc.
- Michael T. Leonard
- C07 - ORGANIC CHEMISTRY
Information Patent Application
OPTIMIZED CYP4V2 GENE AND APPLICATION THEREOF
- Publication number 20240366794
- Publication date Nov 7, 2024
- SUZHOU NGGT BIOTECHNOLOGY CO.,LTD.
- Qing CAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Erythroid Specific Enhancers
- Publication number 20240366796
- Publication date Nov 7, 2024
- ALTIUS INSTITUTE FOR BIOMEDICAL SCIENCES
- NIKOLETA PSATHA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METH...
- Publication number 20240358856
- Publication date Oct 31, 2024
- Jaguar Gene Therapy, LLC
- Michael Hughes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY BASED ADMINISTRATION OF LENTIVIRUS VECTOR FOR TREATING...
- Publication number 20240350664
- Publication date Oct 24, 2024
- INTAS PHARMACEUTICALS LTD.
- Ajit GUPTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
JUNCTOPHILIN-2 (JPH2) GENE THERAPY USING AAV VECTOR
- Publication number 20240335565
- Publication date Oct 10, 2024
- Spacecraft Seven, LLC
- Christopher Dean HERZOG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TROPONIN C (TNNC1) GENE THERAPY USING AAV VECTOR
- Publication number 20240335566
- Publication date Oct 10, 2024
- Spacecraft Seven, LLC
- Christopher Dean HERZOG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS FOR TREATING BIETTI CRYS...
- Publication number 20240309068
- Publication date Sep 19, 2024
- SHANGHAI VITALGEN BIOPHARMA CO., LTD.
- Lu GUO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LENTIVIRAL VECTOR TECHNOLOGY FOR INNER EAR GENE THERAPY
- Publication number 20240299581
- Publication date Sep 12, 2024
- Medizinische Hochschule Hannover
- Axel SCHAMBACH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CONTROL OF MULTI-GENE EXPRESSION USING SYNTHETIC PROMOTERS
- Publication number 20240294938
- Publication date Sep 5, 2024
- AstraZeneca AB
- Yash Dhananjai PATEL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRAL (AAV) VECTORS FOR TISSUE-TARGETED EXPRESSION...
- Publication number 20240285804
- Publication date Aug 29, 2024
- The Brigham & Women's Hospital, Inc.
- Bei Fengfeng
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ENHANCERS AND VECTORS
- Publication number 20240287546
- Publication date Aug 29, 2024
- ImmunoVec, Inc.
- Ryan Lupman Wong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR CELL TYPE-SPECIFIC GENE EXPRESSION IN...
- Publication number 20240285803
- Publication date Aug 29, 2024
- Decibel Therapeutics, Inc.
- Theresa ABELL
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS HAVING VARIANT CAPSID, AND APPLI...
- Publication number 20240252679
- Publication date Aug 1, 2024
- SHANGHAI REGENELEAD THERAPIES CO., LTD.
- Wentao ZHANG
- C07 - ORGANIC CHEMISTRY
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20240254514
- Publication date Aug 1, 2024
- Allen Institute
- Tanya Daigle
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LIPID PARTICLES CONTAINING A TRUNCATED BABOON ENDOGENOUS RETROVIRUS...
- Publication number 20240254168
- Publication date Aug 1, 2024
- Sana Biotechnology, Inc.
- Richard C. Mulligan
- C07 - ORGANIC CHEMISTRY
Information Patent Application
EXPRESSION VECTORS, BACTERIAL SEQUENCE-FREE VECTORS, AND METHODS OF...
- Publication number 20240229071
- Publication date Jul 11, 2024
- Mediphage Bioceuticals, Inc.
- Roderick SLAVCEV
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS ENCODING GENE EDITING SYSTEMS AND USES THEREOF
- Publication number 20240218393
- Publication date Jul 4, 2024
- MAMMOTH BIOSCIENCES, INC.
- Pei-Qi LIU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HIGH EFFICIENCY TRANS-SPLICING FOR REPLACEMENT OF TARGETED RNA SEQU...
- Publication number 20240209366
- Publication date Jun 27, 2024
- Tacit Therapeutics, Inc.
- David Allen Nelles
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IL2 TETHERED TO ITS RECEPTOR IL2RBETA AND PORE-FORMING PROTEINS AS...
- Publication number 20240207405
- Publication date Jun 27, 2024
- The General Hospital Corporation
- Sumei Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

regulating transport or export of RNA

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Engineered invariant natural killer T (iNKT) cells and methods of m...

Intron fragments

Methods of treating or preventing pyruvate kinase deficiency

Optimized expression cassettes for gene therapy

Recombinant lentiviral vector for stem cell- based gene therapy of...

Therapy

WPRE mutant constructs, compositions, and methods thereof

Vectors for the treatment of Friedreich's ataxia

BCMA chimeric antigen receptors

Gene therapies for lysosomal disorders

Adeno associated virus vectors for the treatment of hunter disease

Bicistronic AAV vector for RNA interference in ALS

Adenoviral vectors with two expression cassettes encoding RSV antig...

WPRE mutant constructs, compositions, and methods thereof

Neuroreceptor compositions and methods of use

Globin gene therapy for treating hemoglobinopathies

DNA vectors and elements for sustained gene expression in eukaryoti...

Lentiviral vectors for delivery of PKLR to treat pyruvate kinase de...

Lentiviral vector expressing membrane-anchored or secreted antibody

Method of detecting and/or identifying adeno-associated virus (AAV)...

Gene therapy for the treatment of a retinal degeneration disease

Adeno-associated virus (AAV) serotype 8 sequences, vectors containi...

Adeno-associated virus (AAV) serotype 8 sequences, vectors containi...

Method of detecting and/or identifying adeno-associated virus (AAV)...

Adeno-associated virus (AAV) clades, sequences, vectors containing...

Adeno-associated virus (AAV) clades, sequences, vectors containing...

Viral vectors for prophylaxis and therapy of hemoglobinopathies

AAV delivery of nucleobase editors

Methods of treating or preventing pyruvate kinase deficiency

Catecholamine enzyme fusions

Patents Applicationslast 30 patents

GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

Lentiviral Vectors

COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS

SELF-INACTIVATING LENTIVIRAL VECTOR ENCODING BETA- OR GAMMA-GLOBIN

NOCICEPTOR-SPECIFIC GENE REGULATORY ELEMENTS FOR THE TREATMENT OF PAIN

RETGC Gene Therapy

NOVEL METHODS OF USING ADENO-ASSOCIATED VIRUS 11 (AAV11)

AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GA...

BCMA CHIMERIC ANTIGEN RECEPTORS

LENTIVIRAL VECTOR FOR EXPRESSION OF HUMAN PAPILLOMAVIRUS (HPV) ANTI...

INTEGRASES, LANDING PAD ARCHITECTURES, AND ENGINEERED CELLS COMPRIS...

OPTIMIZED CYP4V2 GENE AND APPLICATION THEREOF

Erythroid Specific Enhancers

ADENO-ASSOCIATED VECTORS AND VIRIONS TO TREAT GALACTOSEMIA AND METH...

GENE THERAPY BASED ADMINISTRATION OF LENTIVIRUS VECTOR FOR TREATING...

JUNCTOPHILIN-2 (JPH2) GENE THERAPY USING AAV VECTOR

TROPONIN C (TNNC1) GENE THERAPY USING AAV VECTOR

RECOMBINANT ADENO-ASSOCIATED VIRAL VECTORS FOR TREATING BIETTI CRYS...

LENTIVIRAL VECTOR TECHNOLOGY FOR INNER EAR GENE THERAPY

CONTROL OF MULTI-GENE EXPRESSION USING SYNTHETIC PROMOTERS

ADENO-ASSOCIATED VIRAL (AAV) VECTORS FOR TISSUE-TARGETED EXPRESSION...

ENHANCERS AND VECTORS

COMPOSITIONS AND METHODS FOR CELL TYPE-SPECIFIC GENE EXPRESSION IN...

RECOMBINANT ADENO-ASSOCIATED VIRUS HAVING VARIANT CAPSID, AND APPLI...

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

LIPID PARTICLES CONTAINING A TRUNCATED BABOON ENDOGENOUS RETROVIRUS...

EXPRESSION VECTORS, BACTERIAL SEQUENCE-FREE VECTORS, AND METHODS OF...

VECTORS ENCODING GENE EDITING SYSTEMS AND USES THEREOF

HIGH EFFICIENCY TRANS-SPLICING FOR REPLACEMENT OF TARGETED RNA SEQU...

IL2 TETHERED TO ITS RECEPTOR IL2RBETA AND PORE-FORMING PROTEINS AS...