regulating transport or export of RNA

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  • Information Patent Application

    ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

    • Publication number 20250235550
    • Publication date Jul 24, 2025
    • Allen Institute
    • Tanya Daigle
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    PRODUCTION OF VIRAL VECTORS

    • Publication number 20250230468
    • Publication date Jul 17, 2025
    • Revvity Gene Delivery GmbH
    • Michael Otto SALOMON
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLYCOGEN STORAGE DISO...

    • Publication number 20250222134
    • Publication date Jul 10, 2025
    • University of Connecticut
    • Youngmok Lee
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ENGINEERED INVARIANT NATURAL KILLER T (INKT) CELLS AND METHODS OF M...

    • Publication number 20250223333
    • Publication date Jul 10, 2025
    • The Regents of the University of California
    • Lili Yang
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Cochlear and/or vestibular cell specific promoter and use thereof

    • Publication number 20250213728
    • Publication date Jul 3, 2025
    • Shanghai Emaygene Technology Co.,Ltd.
    • Guisheng ZHONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENETIC TARGETING OF CELLULAR OR NEURONAL SUB-POPULATIONS

    • Publication number 20250215455
    • Publication date Jul 3, 2025
    • Board of Regents, The University of Texas System
    • Boris V. ZEMELMAN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS OF TREATING OR PREVENTING PYRUVATE KINASE DEFICIENCY

    • Publication number 20250215454
    • Publication date Jul 3, 2025
    • Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, O.A,...
    • Jose C. SEGOVIA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF

    • Publication number 20250205366
    • Publication date Jun 26, 2025
    • Huidagene Therapeutics (Singapore) Pte. Ltd.
    • Xing Wang
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    STABLE REGULATORY T CELLS AND METHODS OF PRODUCTION

    • Publication number 20250186497
    • Publication date Jun 12, 2025
    • Abata Therapeutics, Inc.
    • Stephen SOFEN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    PROCESS FOR PRODUCING CONE PHOTORECEPTOR CELLS

    • Publication number 20250171738
    • Publication date May 29, 2025
    • Centre for Eye Research Australia Ltd.
    • Ching Bong WONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    PROMOTERS FOR SPECIFIC EXPRESSION OF GENES IN CONE PHOTORECEPTORS

    • Publication number 20250171775
    • Publication date May 29, 2025
    • Institute of Molecular and Clinical Ophthalmology Basel (IOB)
    • Botond Miklós Roska
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    IN VITRO AND IN VIVO PROTEIN TRANSLATION VIA IN SITU CIRCULARIZED RNAS

    • Publication number 20250163454
    • Publication date May 22, 2025
    • The Regents of the University of California
    • Prashant Mali
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    INTRON FRAGMENTS

    • Publication number 20250163455
    • Publication date May 22, 2025
    • NEURACLE GENETICS INC.
    • Hoon Young KONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS OF TREATING NEURODEGENERATIVE DISORDERS

    • Publication number 20250152744
    • Publication date May 15, 2025
    • Genzyme Corporation
    • Shyam RAMACHANDRAN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    BASE EDITING AND CRISPR/CAS9 GENE EDITING STRATEGIES TO CORRECT CD3...

    • Publication number 20250144147
    • Publication date May 8, 2025
    • The Regents of the University of California
    • Donald B. KOHN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS FOR USE OF VIRAL VECTOR CONSTRUCTS FOR THE TREATMENT OF FAB...

    • Publication number 20250144240
    • Publication date May 8, 2025
    • Sangamo Therapeutics, Inc.
    • Cristobal PASSALACQUA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT...

    • Publication number 20250136651
    • Publication date May 1, 2025
    • THE UNIVERSITY COURT OF THE UNIVERSITY OF EDINBURGH
    • Stuart Robert Cobb
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF

    • Publication number 20250135040
    • Publication date May 1, 2025
    • Spacecraft Seven, LLC
    • Christopher Dean HERZOG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT VIRUS EXPRESSING TPK AND USE THEREOF IN TREATMENT OF AL...

    • Publication number 20250121095
    • Publication date Apr 17, 2025
    • SHANGHAI RAISING PHARMACEUTICAL CO., LTD.
    • Jingjing WANG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    LENTIVIRAL GENE THERAPY RESCUES FUNCTION IN A MOUSE MODEL OF USHER 1B

    • Publication number 20250121093
    • Publication date Apr 17, 2025
    • University of Kansas
    • Hinrich STAECKER
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Gene Therapy Methods for Age-Related Diseases and Conditions

    • Publication number 20250122267
    • Publication date Apr 17, 2025
    • President and Fellows of Harvard College
    • Noah Davidsohn
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    SCHWANN CELL-SPECIFIC PROMOTER

    • Publication number 20250115906
    • Publication date Apr 10, 2025
    • Toolgen Incorporated
    • Dong Woo SONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    LENTIVIRAL VECTOR FOR OVEREXPRESSING EGF, RECOMBINANT STEM CELL, AN...

    • Publication number 20250114481
    • Publication date Apr 10, 2025
    • Centre for Regenerative Medicine and Health, Hong Kong Institute of Science &...
    • Dajiang QIN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENE THERAPY FOR GENETIC HEARING LOSS

    • Publication number 20250114480
    • Publication date Apr 10, 2025
    • BridgeBio Gene Therapy Research, Inc.
    • Clayton BEARD
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OPTIMIZED AAV-BASED VACCINE

    • Publication number 20250101458
    • Publication date Mar 27, 2025
    • Massachusetts Eye and Ear Infirmary
    • Luc H. Vandenberghe
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    COMPOSITIONS FOR TREATING CANCER

    • Publication number 20250099615
    • Publication date Mar 27, 2025
    • Kelonia Therapeutics, Inc.
    • Kevin M. Friedman
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT LENTIVIRAL VECTOR FOR STEM CELL-BASED GENE THERAPY OF S...

    • Publication number 20250084437
    • Publication date Mar 13, 2025
    • Institut National de la Sante et de la Recherche Medicale (INSERM)
    • Annarita MICCIO
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    WPRE MUTANT CONSTRUCTS, COMPOSITIONS, AND METHODS THEREOF

    • Publication number 20250075230
    • Publication date Mar 6, 2025
    • Immatics US, Inc.
    • Melinda MATA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    THERAPY

    • Publication number 20250064975
    • Publication date Feb 27, 2025
    • The University of Bristol
    • Moin Ahson Saleem-Uddin
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV GENE THERAPY FOR THE KIDNEY

    • Publication number 20250064984
    • Publication date Feb 27, 2025
    • The University of Bristol
    • Moin Ahson Saleem-Uddin
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...