Special therapeutic applications

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C12N2320/30

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2320/00Applications Uses

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C12N2320/30Special therapeutic applications

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Patents Grantslast 30 patents

Information Patent Grant
Thrombin binding circular aptamer and use thereof
- Patent number 12,365,904
- Issue date Jul 22, 2025
- HEFEI UNIVERSITY OF TECHNOLOGY
- Lei Zheng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Structurally designed shRNAs
- Patent number 12,351,802
- Issue date Jul 8, 2025
- Cold Spring Harbor Laboratory
- Gregory J. Hannon
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Process for preparing rhenium chelated MAG3 oligonucleotides
- Patent number 12,344,625
- Issue date Jul 1, 2025
- ROCHE INNOVATION CENTER COPENHAGEN A/S
- Dennis Jul Hansen
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions of asymmetric interfering RNA and uses thereof
- Patent number 12,344,840
- Issue date Jul 1, 2025
- 1GLOBE HEALTH INSTITUTE LLC
- Chiang Jia Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dual-acting siRNA based modulation of C9orf72
- Patent number 12,344,839
- Issue date Jul 1, 2025
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selectively altering microbiota for immune modulation
- Patent number 12,318,445
- Issue date Jun 3, 2025
- SNIPR TECHNOLOGIES LIMITED
- Jasper Clube
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides targeting frataxin and related methods
- Patent number 12,312,585
- Issue date May 27, 2025
- UNIVERSITY OF MASSACHUSETTS
- Feng Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for monitoring, diagnosis, prognosis, dete...
- Patent number 12,303,494
- Issue date May 20, 2025
- GLAX Health LLC
- Shivani Shrivastava
- G01 - MEASURING TESTING
Information Patent Grant
Compositions and methods for treating cancer
- Patent number 12,305,171
- Issue date May 20, 2025
- bioAffinity Technologies, Inc.
- David J. Elzi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
DNA compositions and related methods
- Patent number 12,303,526
- Issue date May 20, 2025
- FLAGSHIP PIONEERING INNOVATIONS VII, LLC
- Alexandra Rachael Sneider
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Dual-acting siRNA based modulation of C9orf72
- Patent number 12,297,429
- Issue date May 13, 2025
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligomers and oligomer conjugates
- Patent number 12,281,307
- Issue date Apr 22, 2025
- HOFFMANN-LA ROCHE INC.
- Hassan Javanbakht
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Inhibition of protein kinases to treat Friedreich ataxia
- Patent number 12,281,308
- Issue date Apr 22, 2025
- UNIVERSITY OF MASSACHUSETTS
- Michael R. Green
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides for PRNP modulation
- Patent number 12,258,566
- Issue date Mar 25, 2025
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lipid nanoparticle formulations
- Patent number 12,251,470
- Issue date Mar 18, 2025
- ARBUTUS BIOPHARMA CORPORATION
- James Heyes
- B82 - NANO-TECHNOLOGY
Information Patent Grant
Methods of treating decreased bone mineral density with cluster of...
- Patent number 12,234,460
- Issue date Feb 25, 2025
- REGENERON PHARMACEUTICALS, INC.
- Jonas Bovijn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for inhibiting expression of transthyretin
- Patent number 12,227,744
- Issue date Feb 18, 2025
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNAi agents for inhibiting expression of HIF-2 alpha (EPAS1), compo...
- Patent number 12,221,610
- Issue date Feb 11, 2025
- Arrowhead Pharmaceuticals, Inc.
- Zhen Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Aptamer for specifically recognizing soluble ST2 protein and applic...
- Patent number 12,188,022
- Issue date Jan 7, 2025
- BEIJING INST OF HEART LUNG & BLOOD VESSEL DISEASES
- Jie Du
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chiral design
- Patent number 12,180,472
- Issue date Dec 31, 2024
- WAVE LIFE SCIENCES LTD.
- Meena Meena
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Angelman syndrome antisense treatment
- Patent number 12,180,480
- Issue date Dec 31, 2024
- The Texas A&M University System
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotide-ligand conjugates and process for their preparation
- Patent number 12,173,288
- Issue date Dec 24, 2024
- Alnylam Pharmaceuticals, Inc.
- Muthiah Manoharan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Bioactive renal cells
- Patent number 12,157,887
- Issue date Dec 3, 2024
- ProKidney
- Timothy A. Bertram
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods to detect motor neuron disease comprising micro-RNAs
- Patent number 12,157,889
- Issue date Dec 3, 2024
- Washington University
- Timothy M. Miller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
T cells with improved functionality
- Patent number 12,152,251
- Issue date Nov 26, 2024
- Kite Pharma, Inc.
- Saikat Banerjee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
T-lymphocyte binding aptamers
- Patent number 12,146,140
- Issue date Nov 19, 2024
- Aummune Ltd.
- Guy Neev
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
MicroRNA-198 as a tumor suppressor in ovarian cancer
- Patent number 12,134,769
- Issue date Nov 5, 2024
- Baylor College of Medicine
- Qizhi Yao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA construct and methods of use thereof for enhancing the therapeu...
- Patent number 12,128,061
- Issue date Oct 29, 2024
- VYCELLIX, INC.
- Evren Alici
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods of treating liver diseases with phosphodiesterase 3B (PDE3B...
- Patent number 12,123,001
- Issue date Oct 22, 2024
- REGENERON PHARMACEUTICALS, INC.
- Niek Verweij
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of amyotrophic lateral sclerosis (ALS)
- Patent number 12,116,589
- Issue date Oct 15, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
Methods Of Treating Decreased Bone Mineral Density With Cluster Of...
- Publication number 20250236873
- Publication date Jul 24, 2025
- Regeneron Pharmaceuticals, Inc.
- Jonas Bovijn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250236869
- Publication date Jul 24, 2025
- Sarepta Therapeutics, Inc.
- Richard K. BESTWICK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES
- Publication number 20250213724
- Publication date Jul 3, 2025
- CureVac SE
- Mariola FOTIN-MLECZEK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Use of Telomerase Inhibitors for the Treatment of Myeloproliferativ...
- Publication number 20250207136
- Publication date Jun 26, 2025
- Geron Corporation
- Monic J. Stuart
- B82 - NANO-TECHNOLOGY
Information Patent Application
METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS...
- Publication number 20250197856
- Publication date Jun 19, 2025
- Takeda Pharmaceuticals U.S.A. Inc.
- Irina ANTONIJEVIC
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B...
- Publication number 20250188473
- Publication date Jun 12, 2025
- Regeneron Pharmaceuticals, Inc.
- Niek Verweij
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TRE...
- Publication number 20250179495
- Publication date Jun 5, 2025
- The University of Chicago
- Elizabeth McNally
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Promotion of Cardiomyocyte Proliferation and Regenerative Treatment...
- Publication number 20250163420
- Publication date May 22, 2025
- University of Cincinnati
- Yigang Wang
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS O...
- Publication number 20250163414
- Publication date May 22, 2025
- THE UNIVERSITY OF WESTERN AUSTRALIA
- Stephen Donald Wilton
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT FOR NUCLEOTIDE REPEAT EXPANSION DISEASE
- Publication number 20250154480
- Publication date May 15, 2025
- The Johns Hopkins University
- Jiou Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD
- Publication number 20250154507
- Publication date May 15, 2025
- Sarepta Therapeutics, Inc.
- Peter SAZANI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250145991
- Publication date May 8, 2025
- Sarepta Therapeutics, Inc.
- Richard K. BESTWICK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
T CELLS WITH IMPROVED FUNCTIONALITY
- Publication number 20250145952
- Publication date May 8, 2025
- Kite Pharma, Inc.
- Saikat Banerjee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOP...
- Publication number 20250136980
- Publication date May 1, 2025
- Royal College of Surgeons in Ireland
- David HENSHALL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS
- Publication number 20250115912
- Publication date Apr 10, 2025
- FUNDACIÓ INSTITUT DE RECERCA BIOMÈDICA (IRB BARCELONA)
- Roger GOMIS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Interferon Production Using Short RNA Duplexes
- Publication number 20250101434
- Publication date Mar 27, 2025
- Yale University
- Anna Marie Pyle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER
- Publication number 20250092402
- Publication date Mar 20, 2025
- Baylor College of Medicine
- Qizhi Yao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF...
- Publication number 20250082735
- Publication date Mar 13, 2025
- PRECISION BIOSCIENCES, INC.
- James Jefferson Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
- Publication number 20250084435
- Publication date Mar 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION
- Publication number 20250075208
- Publication date Mar 6, 2025
- Alnylam Pharmaceuticals, Inc.
- Muthiah MANOHARAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FO...
- Publication number 20250075211
- Publication date Mar 6, 2025
- Alnylam Pharmaceuticals, Inc.
- Tracy Zimmermann
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEI...
- Publication number 20250066792
- Publication date Feb 27, 2025
- Ionis Pharmaceuticals, Inc.
- Eric E. Swayze
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANGELMAN SYNDROME ANTISENSE TREATMENT
- Publication number 20250066786
- Publication date Feb 27, 2025
- THE TEXAS A&M UNIVERSITY SYSTEM
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
- Publication number 20250043286
- Publication date Feb 6, 2025
- The General Hospital Corporation
- Gary Ruvkun
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR SNCA MODULATION
- Publication number 20250043284
- Publication date Feb 6, 2025
- University of Massachusetts
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
- Publication number 20250034566
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Brian Bettencourt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND M...
- Publication number 20250019763
- Publication date Jan 16, 2025
- Zhenglun Zhu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Purification and Purity Assessment of RNA Molecules Synthesized wit...
- Publication number 20250019719
- Publication date Jan 16, 2025
- The Trustees of the University of Pennsylvania
- Drew Weissman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...
- Publication number 20250011784
- Publication date Jan 9, 2025
- VICO Therapeutics B.V.
- Peter Christian DE VISSER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESIST...
- Publication number 20250003969
- Publication date Jan 2, 2025
- NATIONAL JEWISH HEALTH
- Donald Y.M. LEUNG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Special therapeutic applications

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Thrombin binding circular aptamer and use thereof

Structurally designed shRNAs

Process for preparing rhenium chelated MAG3 oligonucleotides

Compositions of asymmetric interfering RNA and uses thereof

Dual-acting siRNA based modulation of C9orf72

Selectively altering microbiota for immune modulation

Oligonucleotides targeting frataxin and related methods

Compositions and methods for monitoring, diagnosis, prognosis, dete...

Compositions and methods for treating cancer

DNA compositions and related methods

Dual-acting siRNA based modulation of C9orf72

Oligomers and oligomer conjugates

Inhibition of protein kinases to treat Friedreich ataxia

Oligonucleotides for PRNP modulation

Lipid nanoparticle formulations

Methods of treating decreased bone mineral density with cluster of...

Compositions and methods for inhibiting expression of transthyretin

RNAi agents for inhibiting expression of HIF-2 alpha (EPAS1), compo...

Aptamer for specifically recognizing soluble ST2 protein and applic...

Chiral design

Angelman syndrome antisense treatment

Oligonucleotide-ligand conjugates and process for their preparation

Bioactive renal cells

Methods to detect motor neuron disease comprising micro-RNAs

T cells with improved functionality

T-lymphocyte binding aptamers

MicroRNA-198 as a tumor suppressor in ovarian cancer

RNA construct and methods of use thereof for enhancing the therapeu...

Methods of treating liver diseases with phosphodiesterase 3B (PDE3B...

Treatment of amyotrophic lateral sclerosis (ALS)

Patents Applicationslast 30 patents

Methods Of Treating Decreased Bone Mineral Density With Cluster Of...

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

RNA CONTAINING COMPOSITION FOR TREATMENT OF TUMOR DISEASES

Use of Telomerase Inhibitors for the Treatment of Myeloproliferativ...

METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS...

Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B...

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TRE...

Promotion of Cardiomyocyte Proliferation and Regenerative Treatment...

ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS O...

TREATMENT FOR NUCLEOTIDE REPEAT EXPANSION DISEASE

MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

T CELLS WITH IMPROVED FUNCTIONALITY

MODULATION OF MICRORNA-335-5P FOR THE TREATMENT OF SODIUM CHANNELOP...

METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS

Interferon Production Using Short RNA Duplexes

MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER

PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF...

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

OLIGONUCLEOTIDE-LIGAND CONJUGATES AND PROCESS FOR THEIR PREPARATION

TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FO...

COMPOUNDS AND METHODS FOR MODULATION OF DYSTROPHIA MYOTONICA-PROTEI...

ANGELMAN SYNDROME ANTISENSE TREATMENT

METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE

OLIGONUCLEOTIDES FOR SNCA MODULATION

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

HOMEOBOX TRANSCRIPTION FACTOR VENTX REGULATES DIFFERENTIATION AND M...

Purification and Purity Assessment of RNA Molecules Synthesized wit...

RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...

METHODS TO IDENTIFY AND TREAT SUBJECTS HAVING CORTICOSTEROID-RESIST...