Use of virus, viral particle or viral elements as a vector

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C12N2750/14141

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2750/00ssDNA Viruses

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C12N2750/14141Use of virus, viral particle or viral elements as a vector

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Patents Grantslast 30 patents

Information Patent Grant
Relative potency assay for viral vector encoding isomerohydrolases
- Patent number 12,359,239
- Issue date Jul 15, 2025
- SPARK THERAPEUTICS, INC.
- Linda Couto
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of predicting ancestral virus sequences and uses thereof
- Patent number 12,359,174
- Issue date Jul 15, 2025
- The Schepens Eye Research Institute, Inc.
- Luk H. Vandenberghe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV capsid variants and uses thereof
- Patent number 12,296,025
- Issue date May 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Pharmaceutical composition comprising AIMP2-DX2 for preventing or t...
- Patent number 12,233,134
- Issue date Feb 25, 2025
- GENEROATH CO., LTD
- Jin Woo Choi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus (AAV) delivery of anti-FAM19A5 antibodies
- Patent number 12,215,338
- Issue date Feb 4, 2025
- Neuracle Science Co., Ltd.
- Jong-Mook Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV-IDUA vector for treatment of MPS I-associated blindness
- Patent number 12,201,697
- Issue date Jan 21, 2025
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Composition for regulating production of interfering ribonucleic acid
- Patent number 12,195,747
- Issue date Jan 14, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated viral vector for gene delivery
- Patent number 12,188,039
- Issue date Jan 7, 2025
- The Board of Regents of the University of Texas System
- Qinglan Ling
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Reducing abnormal accumulation of TDP-43 in motor neurons in amyotr...
- Patent number 12,161,728
- Issue date Dec 10, 2024
- Macquarie University
- Stephanie Rayner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR therapy
- Patent number 12,152,242
- Issue date Nov 26, 2024
- The Curators of the University of Missouri
- Dongsheng Duan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of predicting ancestral virus sequences and uses thereof
- Patent number 12,134,786
- Issue date Nov 5, 2024
- Schepens Eye Research Institute, Inc.
- Luk H. Vandenberghe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of brain cancers using central nervous system mediated ge...
- Patent number 12,122,844
- Issue date Oct 22, 2024
- Cornell University
- Ronald G. Crystal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Butyrylcholinesterases having an enhanced ability to hydrolyze acyl...
- Patent number 12,116,602
- Issue date Oct 15, 2024
- Mayo Foundation for Medical Education and Research
- Liyi Geng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy
- Patent number 12,059,478
- Issue date Aug 13, 2024
- Ospedale San Raffaele S.r.l.
- Anna Christina Kajaste-Rudnitski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for dual glycan binding AAV vectors
- Patent number 12,049,478
- Issue date Jul 30, 2024
- The University of North Carolina at Chapel Hill
- Aravind Asokan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oxidation-resistant AAT gene therapy
- Patent number 12,031,144
- Issue date Jul 9, 2024
- Cornell University
- Ronald G. Crystal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of brain cancers using central nervous system mediated ge...
- Patent number 12,024,568
- Issue date Jul 2, 2024
- Cornell University
- Ronald G. Crystal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of muscular dystrophies
- Patent number 12,012,439
- Issue date Jun 18, 2024
- Royal Holloway and Bedford New College
- John George Dickson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Bicistronic AAV vector for RNA interference in ALS
- Patent number 11,872,290
- Issue date Jan 16, 2024
- Ecole Polytechnique Federale de Lausanne (EPFL)
- Julianne Aebischer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for regulating production of a precursor p...
- Patent number 11,873,505
- Issue date Jan 16, 2024
- Wyvern Pharmaceuticals Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cas-ready mouse embryonic stem cells and mice and uses thereof
- Patent number 11,866,794
- Issue date Jan 9, 2024
- REGENERON PHARMACEUTICALS, INC.
- Guochun Gong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transgenic RPE cells overexpressing OTX2 for the treatment of retin...
- Patent number 11,865,189
- Issue date Jan 9, 2024
- SORBONNE UNIVERSITE
- Thierry Leveillard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Genetic modification of the AAV capsid resulting in altered tropism...
- Patent number 11,821,009
- Issue date Nov 21, 2023
- Cornell University
- Ronald G. Crystal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Liver targeting adeno-associated viral vectors
- Patent number 11,821,008
- Issue date Nov 21, 2023
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated variants, formulations and methods for pulmonary d...
- Patent number 11,807,868
- Issue date Nov 7, 2023
- 4D MOLECULAR THERAPEUTICS INC.
- Melissa Kotterman
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
CRISPR/Cas 9-mediated integration of polynucleotides by sequential...
- Patent number 11,773,409
- Issue date Oct 3, 2023
- The Board of Trustees of the Leland Stanford Junior University
- Rasmus O. Bak
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV treatment of Huntington's disease
- Patent number 11,773,392
- Issue date Oct 3, 2023
- University of Massachusetts
- Christian Mueller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Delivery of card protein as therapy for ocular inflammation
- Patent number 11,739,130
- Issue date Aug 29, 2023
- University of Florida Research Foundation, Incorporated
- Cristhian J. Ildefonso
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated virus vector delivery of micro-dystrophin to treat...
- Patent number 11,723,986
- Issue date Aug 15, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Treatment of muscular dystrophies
- Patent number 11,725,032
- Issue date Aug 15, 2023
- Royal Holloway and Bedford New College
- George Dickson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20250228967
- Publication date Jul 17, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Targeted CRISPR Delivery Platforms
- Publication number 20250223611
- Publication date Jul 10, 2025
- University of Massachusetts
- Erik J. Sontheimer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Targeted CRISPR Delivery Platforms
- Publication number 20250197889
- Publication date Jun 19, 2025
- University of Massachusetts
- Erik J. Sontheimer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250171804
- Publication date May 29, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163464
- Publication date May 22, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...
- Publication number 20250161490
- Publication date May 22, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163466
- Publication date May 22, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163467
- Publication date May 22, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163460
- Publication date May 22, 2025
- Wyvem Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163461
- Publication date May 22, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163463
- Publication date May 22, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163462
- Publication date May 22, 2025
- Wyvem Pharmaceuticals Inc.
- Bradley G. THOMPSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
- Publication number 20250163465
- Publication date May 22, 2025
- Wyvern Pharmaceuticals, Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE...
- Publication number 20250154486
- Publication date May 15, 2025
- PRECISION BIOSCIENCES, INC.
- Derek JANTZ
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS
- Publication number 20250145670
- Publication date May 8, 2025
- The University of North Carolina at Chapel Hill
- Aravind ASOKAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTERS, EXPRESSION CASSETTES, VECTORS, KITS, AND METHODS FOR THE...
- Publication number 20250121092
- Publication date Apr 17, 2025
- Beacon Therapeutics Limited
- Guo-jie Ye
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NEUROPEPTIDE-EXPRESSING VECTORS AND METHODS FOR THE TREATMENT OF EP...
- Publication number 20250034592
- Publication date Jan 30, 2025
- CHARITE-UNIVERSITATSMEDIZIN BERLIN
- Regine HEILBRONN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20240374756
- Publication date Nov 14, 2024
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS
- Publication number 20240327468
- Publication date Oct 3, 2024
- The University of North Carolina at Chapel Hill
- Aravind ASOKAN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ADENO-ASSOCIATED VIRUS (AAV) SYSTEMS FOR TREATMENT OF PROGRANULIN A...
- Publication number 20240318199
- Publication date Sep 26, 2024
- Beacon Therapeutics Limited
- Juan Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TARGETING OF C9orf72
- Publication number 20240309344
- Publication date Sep 19, 2024
- Scribe Therapeutics Inc.
- Benjamin OAKES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SELF-POLARIZING IMMUNE CELLS
- Publication number 20240299543
- Publication date Sep 12, 2024
- Carisma Therapeutics Inc.
- Michael Klichinsky
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE...
- Publication number 20240271111
- Publication date Aug 15, 2024
- PRECISION BIOSCIENCES, INC.
- Derek JANTZ
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DELIVERY OF CARD PROTEIN AS THERAPY FOR OCCULAR INFLAMMATION
- Publication number 20240254178
- Publication date Aug 1, 2024
- University of Florida Research Foundation, Incorporated
- Cristhian J. Ildefonso
- C07 - ORGANIC CHEMISTRY
Information Patent Application
CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS...
- Publication number 20240229068
- Publication date Jul 11, 2024
- NXGEN VECTOR SOLUTIONS, LLC
- Joseph E. Rabinowitz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT...
- Publication number 20240229031
- Publication date Jul 11, 2024
- Rutgers, The State University of New Jersey
- M. Maral Mouradian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS...
- Publication number 20240132912
- Publication date Apr 25, 2024
- NXGEN VECTOR SOLUTIONS, LLC
- Joseph E. Rabinowitz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT...
- Publication number 20240132891
- Publication date Apr 25, 2024
- Rutgers, The State University of New Jersey
- M. Maral Mouradian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CAS-READY MOUSE EMBRYONIC STEM CELLS AND MICE AND USES THEREOF
- Publication number 20240093316
- Publication date Mar 21, 2024
- Regeneron Pharmaceuticals, Inc.
- Guochun Gong
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV TREATMENT OF HUNTINGTON’S DISEASE
- Publication number 20240084303
- Publication date Mar 14, 2024
- University of Massachusetts
- Christian Mueller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Use of virus, viral particle or viral elements as a vector

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Relative potency assay for viral vector encoding isomerohydrolases

Methods of predicting ancestral virus sequences and uses thereof

AAV capsid variants and uses thereof

Pharmaceutical composition comprising AIMP2-DX2 for preventing or t...

Adeno-associated virus (AAV) delivery of anti-FAM19A5 antibodies

AAV-IDUA vector for treatment of MPS I-associated blindness

Composition for regulating production of interfering ribonucleic acid

Recombinant adeno-associated viral vector for gene delivery

Reducing abnormal accumulation of TDP-43 in motor neurons in amyotr...

CRISPR therapy

Methods of predicting ancestral virus sequences and uses thereof

Treatment of brain cancers using central nervous system mediated ge...

Butyrylcholinesterases having an enhanced ability to hydrolyze acyl...

Gene therapy

Methods and compositions for dual glycan binding AAV vectors

Oxidation-resistant AAT gene therapy

Treatment of brain cancers using central nervous system mediated ge...

Treatment of muscular dystrophies

Bicistronic AAV vector for RNA interference in ALS

Compositions and methods for regulating production of a precursor p...

Cas-ready mouse embryonic stem cells and mice and uses thereof

Transgenic RPE cells overexpressing OTX2 for the treatment of retin...

Genetic modification of the AAV capsid resulting in altered tropism...

Liver targeting adeno-associated viral vectors

Adeno-associated variants, formulations and methods for pulmonary d...

CRISPR/Cas 9-mediated integration of polynucleotides by sequential...

AAV treatment of Huntington's disease

Delivery of card protein as therapy for ocular inflammation

Adeno-associated virus vector delivery of micro-dystrophin to treat...

Treatment of muscular dystrophies

Patents Applicationslast 30 patents

AAV CAPSID VARIANTS AND USES THEREOF

Targeted CRISPR Delivery Platforms

Targeted CRISPR Delivery Platforms

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID

ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE...

METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS

PROMOTERS, EXPRESSION CASSETTES, VECTORS, KITS, AND METHODS FOR THE...

NEUROPEPTIDE-EXPRESSING VECTORS AND METHODS FOR THE TREATMENT OF EP...

AAV CAPSID VARIANTS AND USES THEREOF

METHODS AND COMPOSITIONS FOR DUAL GLYCAN BINDING AAV VECTORS

ADENO-ASSOCIATED VIRUS (AAV) SYSTEMS FOR TREATMENT OF PROGRANULIN A...

COMPOSITIONS AND METHODS FOR THE TARGETING OF C9orf72

SELF-POLARIZING IMMUNE CELLS

ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE...

DELIVERY OF CARD PROTEIN AS THERAPY FOR OCCULAR INFLAMMATION

CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS...

MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT...

CONSTRUCTS AND METHODS FOR DELIVERYING MOLECULES VIA VIRAL VECTORS...

MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT...

CAS-READY MOUSE EMBRYONIC STEM CELLS AND MICE AND USES THEREOF

AAV TREATMENT OF HUNTINGTON’S DISEASE