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ENGINEERED MUSCLE TARGETING COMPOSITIONS
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THE BROAD INSTITUTE, INC.
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METHODS FOR DETECTING AAV
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Genzyme Corporation
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SELF-INACTIVATING VECTORS FOR GENE EDITING
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Scribe Therapeutics Inc.
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TREATMENT OF COMPLEMENT-MEDIATED DISORDERS
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CAMBRIDGE ENTERPRISE LIMITED
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Peter Lachmann
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METHOD FOR PRODUCING VIRUS PARTICLES
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THE UNIVERSITY OF TOKYO
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Takashi OKADA
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METHODS FOR DETECTING AAV
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Genzyme Corporation
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Xiaoying JIN
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G01 - MEASURING TESTING
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AAV CAPSID DESIGNS
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University of Massachusetts
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Guangping Gao
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ENGINEERED AAV VECTORS
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Ludwig-Maximilians-Universitat Munchen
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Stylianos MICHALAKIS
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ADENO-ASSOCIATED VIRUS VECTORS
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The Children's Medical Center Corporation
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Zhigang HE
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MATERIALS AND METHODS FOR VIRAL PURIFICATION
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JANSSEN BIOTECH, INC.
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Brian E. Tomkowicz
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CHARACTERIZATION OF GENE THERAPY VECTORS
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Puridify Limited
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Matthew Miell
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NOVEL AAV VARIANT
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WUXI APPTEC (SHANGHAI) CO., LTD.
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Qunsheng JI
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VIRAL CAPSID POLYPEPTIDES
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President and Fellows of Harvard College
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Eric KELSIC
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FACTOR VIII POLYPEPTIDE
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FREELINE THERAPEUTICS LIMITED
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Azadeh KIA
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