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ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID
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Publication number 20240084327
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Publication date Mar 14, 2024
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Tenaya Therapeutics, Inc.
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Christopher A. REID
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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AAV TREATMENT OF HUNTINGTON’S DISEASE
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Publication number 20240084303
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Publication date Mar 14, 2024
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University of Massachusetts
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Christian Mueller
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS IIIB
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Publication number 20240009327
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Publication date Jan 11, 2024
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The Trustees of the University of Pennsylvania
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James M. Wilson
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
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Publication number 20230304032
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Publication date Sep 28, 2023
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VOYAGER THERAPEUTICS, INC.
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Dinah Wen-Yee SAH
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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GENE THERAPIES FOR LYSOSOMAL DISORDERS
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Publication number 20230287358
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Publication date Sep 14, 2023
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Prevail Therapeutics, Inc.
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Asa ABELIOVICH
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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TREATMENT OF GLYCOGEN STORAGE DISEASE III
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Publication number 20230190965
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Publication date Jun 22, 2023
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Genethon
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FEDERICO MINGOZZI
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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Gene Therapy For Neurodegenerative Disorders
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Publication number 20230135379
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Publication date May 4, 2023
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Genzyme Corporation
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Marco A. PASSINI
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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Gene Therapy For Neurodegenerative Disorders
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Publication number 20230084580
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Publication date Mar 16, 2023
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Genzyme Corporation
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Marco A. PASSINI
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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