Dinah Wen-Yee Sah

Person

Boston, MA, US

People

Patents Grantslast 30 patents

Information Patent Grant
Compositions and methods for delivery of AAV
- Patent number 12,305,189
- Issue date May 20, 2025
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Tau binding compounds
- Patent number 12,291,565
- Issue date May 6, 2025
- VOYAGER THERAPEUTICS, INC.
- Wencheng Liu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Frataxin expression constructs having engineered promoters and meth...
- Patent number 12,281,321
- Issue date Apr 22, 2025
- VOYAGER THERAPEUTICS, INC.
- Holger Patzke
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for inhibiting expression of transthyretin
- Patent number 12,227,744
- Issue date Feb 18, 2025
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Rescue of central and peripheral neurological phenotype of friedrei...
- Patent number 12,146,150
- Issue date Nov 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating amyotrophic lateral sclerosis...
- Patent number 12,123,002
- Issue date Oct 22, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of amyotrophic lateral sclerosis (ALS)
- Patent number 12,116,589
- Issue date Oct 15, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulatory polynucleotides
- Patent number 12,084,659
- Issue date Sep 10, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating Huntington's disease
- Patent number 11,951,121
- Issue date Apr 9, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of amyotrophic lateral sclerosis (ALS)
- Patent number 11,931,375
- Issue date Mar 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods of treating Huntington's disease
- Patent number 11,752,181
- Issue date Sep 12, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating amyotrophic lateral sclerosis...
- Patent number 11,603,542
- Issue date Mar 14, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating amyotrophic lateral sclerosis...
- Patent number 11,542,506
- Issue date Jan 3, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for delivery of AAV
- Patent number 11,512,327
- Issue date Nov 29, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of amyotrophic lateral sclerosis (ALS)
- Patent number 11,434,502
- Issue date Sep 6, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Modulatory polynucleotides
- Patent number 11,193,129
- Issue date Dec 7, 2021
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Assays for the detection of AAV neutralizing antibodies
- Patent number 10,983,110
- Issue date Apr 20, 2021
- VOYAGER THERAPEUTICS, INC.
- Tatiana I. Novobrantseva
- G01 - MEASURING TESTING
Information Patent Grant
Compositions and methods of treating amyotrophic lateral sclerosis...
- Patent number 10,920,227
- Issue date Feb 16, 2021
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating amyotrophic lateral sclerosis...
- Patent number 10,597,660
- Issue date Mar 24, 2020
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulatory polynucleotides
- Patent number 10,584,337
- Issue date Mar 10, 2020
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatments for neurological disorders
- Patent number 10,328,125
- Issue date Jun 25, 2019
- GLORIANA THERAPEUTICS, INC.
- Anthony Rossomando
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting expression of transthyretin
- Patent number 10,240,152
- Issue date Mar 26, 2019
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting expression of mutant EGFR gene
- Patent number 9,957,507
- Issue date May 1, 2018
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Selective inhibition of polyglutamine protein expression
- Patent number 9,574,191
- Issue date Feb 21, 2017
- The Board of Regents of the University of Texas System
- David R. Corey
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Lipid formulated compositions and methods for inhibiting expression...
- Patent number 9,339,513
- Issue date May 17, 2016
- Alnylam Pharmaceuticals, Inc.
- Jared Gollob
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting expression of transthyretin
- Patent number 9,234,196
- Issue date Jan 12, 2016
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for inhibiting expression of mutant EGFR gene
- Patent number 9,212,364
- Issue date Dec 15, 2015
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting expression of an RNA from w...
- Patent number 9,200,282
- Issue date Dec 1, 2015
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lipid formulated compositions and methods for inhibiting expression...
- Patent number 9,101,643
- Issue date Aug 11, 2015
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for inhibiting expression of GSK-3 genes
- Patent number 9,029,525
- Issue date May 12, 2015
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...
- Publication number 20250146000
- Publication date May 8, 2025
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
- Publication number 20250084435
- Publication date Mar 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
- Publication number 20240415868
- Publication date Dec 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
- Publication number 20240401060
- Publication date Dec 5, 2024
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TAU BINDING COMPOUNDS
- Publication number 20240391988
- Publication date Nov 28, 2024
- VOYAGER THERAPEUTICS, INC.
- Wencheng Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
- Publication number 20240325427
- Publication date Oct 3, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CENTRAL NERVOUS SYSTEM TARGETING POLYNUCLEOTIDES
- Publication number 20240285667
- Publication date Aug 29, 2024
- VOYAGER THERAPEUTICS, INC.
- Gregory Robert Stewart
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
- Publication number 20240226203
- Publication date Jul 11, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
- Publication number 20240131093
- Publication date Apr 25, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
- Publication number 20230399642
- Publication date Dec 14, 2023
- VOYAGER THERAPEUTICS, INC.
- Jinzhao Hou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
- Publication number 20230340473
- Publication date Oct 26, 2023
- Alnylam Pharmaceuticals, Inc.
- Yukio Ando
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...
- Publication number 20230332156
- Publication date Oct 19, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
- Publication number 20230323388
- Publication date Oct 12, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
- Publication number 20230304032
- Publication date Sep 28, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee SAH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...
- Publication number 20230295663
- Publication date Sep 21, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee SAH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
- Publication number 20230257740
- Publication date Aug 17, 2023
- Alnylam Pharmaceuticals, Inc.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORIZED ANTIBODIES (vAb) AND USES THEREOF
- Publication number 20230075314
- Publication date Mar 9, 2023
- VOYAGER THERAPEUTICS, INC.
- Jinzhao Hou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
- Publication number 20230053332
- Publication date Feb 23, 2023
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RESCUE OF CENTRAL AND PERIPHERAL NEUROLOGICAL PHENOTYPE OF FRIEDREI...
- Publication number 20230044444
- Publication date Feb 9, 2023
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF TAUOPATHY
- Publication number 20220339270
- Publication date Oct 27, 2022
- VOYAGER THERAPEUTICS, INC.
- Wencheng Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORY POLYNUCLEOTIDES
- Publication number 20220333131
- Publication date Oct 20, 2022
- VOYAGER THERAPEUTICS, INC.
- Jinzhao Hou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ASSAYS AND METHODS FOR DETERMINING ACTIVITY OF A THERAPEUTIC AGENT...
- Publication number 20220307083
- Publication date Sep 29, 2022
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VARIANTS WITH ENHANCED TROPISM
- Publication number 20220281922
- Publication date Sep 8, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee SAH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
- Publication number 20220275367
- Publication date Sep 1, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
- Publication number 20220211744
- Publication date Jul 7, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS AND DISORDERS ASSOCIATED...
- Publication number 20220168450
- Publication date Jun 2, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee SAH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORY POLYNUCLEOTIDES
- Publication number 20220162609
- Publication date May 26, 2022
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FRATAXIN EXPRESSION CONSTRUCTS HAVING ENGINEERED PROMOTERS AND METH...
- Publication number 20210395776
- Publication date Dec 23, 2021
- VOYAGER THERAPEUTICS, INC.
- Holger PATZKE
- C07 - ORGANIC CHEMISTRY
Information Patent Application
COMPOSITIONS AND METHODS FOR DELIVERY OF AAV
- Publication number 20210371470
- Publication date Dec 2, 2021
- VOYAGER THERAPEUTICS, INC.
- Giridhar Murlidharan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS AND METHODS FOR PRODUCING GENE THERAPY FORMULATIONS
- Publication number 20210355454
- Publication date Nov 18, 2021
- VOYAGER THERAPEUTICS, INC.
- Jacob J. Cardinal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Dinah Wen-Yee Sah

Person

Patents Grantslast 30 patents

Compositions and methods for delivery of AAV

Tau binding compounds

Frataxin expression constructs having engineered promoters and meth...

Compositions and methods for inhibiting expression of transthyretin

Rescue of central and peripheral neurological phenotype of friedrei...

Compositions and methods of treating amyotrophic lateral sclerosis...

Treatment of amyotrophic lateral sclerosis (ALS)

Modulatory polynucleotides

Compositions and methods for treating Huntington's disease

Treatment of amyotrophic lateral sclerosis (ALS)

Compositions and methods of treating Huntington's disease

Compositions and methods of treating amyotrophic lateral sclerosis...

Compositions and methods of treating amyotrophic lateral sclerosis...

Compositions and methods for delivery of AAV

Treatment of amyotrophic lateral sclerosis (ALS)

Modulatory polynucleotides

Assays for the detection of AAV neutralizing antibodies

Compositions and methods of treating amyotrophic lateral sclerosis...

Compositions and methods of treating amyotrophic lateral sclerosis...

Modulatory polynucleotides

Treatments for neurological disorders

Compositions and methods for inhibiting expression of transthyretin

Compositions and methods for inhibiting expression of mutant EGFR gene

Selective inhibition of polyglutamine protein expression

Lipid formulated compositions and methods for inhibiting expression...

Compositions and methods for inhibiting expression of transthyretin

Compositions and methods for inhibiting expression of mutant EGFR gene

Compositions and methods for inhibiting expression of an RNA from w...

Lipid formulated compositions and methods for inhibiting expression...

Compositions and methods for inhibiting expression of GSK-3 genes

Patents Applicationslast 30 patents

COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

TAU BINDING COMPOUNDS

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

CENTRAL NERVOUS SYSTEM TARGETING POLYNUCLEOTIDES

COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE

COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE

COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

COMPOSITIONS AND METHODS FOR DELIVERY OF AAV

COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS...

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN

VECTORIZED ANTIBODIES (vAb) AND USES THEREOF

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

RESCUE OF CENTRAL AND PERIPHERAL NEUROLOGICAL PHENOTYPE OF FRIEDREI...

COMPOSITIONS AND METHODS FOR THE TREATMENT OF TAUOPATHY

MODULATORY POLYNUCLEOTIDES

ASSAYS AND METHODS FOR DETERMINING ACTIVITY OF A THERAPEUTIC AGENT...

AAV VARIANTS WITH ENHANCED TROPISM

COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS AND DISORDERS ASSOCIATED...

MODULATORY POLYNUCLEOTIDES

FRATAXIN EXPRESSION CONSTRUCTS HAVING ENGINEERED PROMOTERS AND METH...

COMPOSITIONS AND METHODS FOR DELIVERY OF AAV

SYSTEMS AND METHODS FOR PRODUCING GENE THERAPY FORMULATIONS