being an intron or intervening sequence for splicing and/or stability of RNA

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CPC
C12N2830/42

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

Current Industry

C12N2830/42being an intron or intervening sequence for splicing and/or stability of RNA

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Patents Grantslast 30 patents

Information Patent Grant
Compositions and methods for enhanced gene expression in cone cells
- Patent number 12,275,959
- Issue date Apr 15, 2025
- Adverum Biotechnologies, Inc.
- Thomas W. Chalberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Eukaryotic cells comprising adenovirus-associated virus polynucleot...
- Patent number 12,234,472
- Issue date Feb 25, 2025
- REGENERON PHARMACEUTICALS, INC.
- Michael Goren
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Coronavirus vaccine compositions and methods
- Patent number 12,220,455
- Issue date Feb 11, 2025
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for gene editing by targeting transferrin
- Patent number 12,215,320
- Issue date Feb 4, 2025
- CRISPR Therapeutics AG
- Alan Richard Brooks
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression cassette for production of high-expression and high-func...
- Patent number 12,188,036
- Issue date Jan 7, 2025
- Celltrion Inc.
- Man Su Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Intron fragments
- Patent number 12,173,304
- Issue date Dec 24, 2024
- NEURACLE GENETICS INC.
- Hoon Young Kong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Hepatocyte based insulin gene therapy for diabetes
- Patent number 12,163,147
- Issue date Dec 10, 2024
- Wisconsin Alumni Research Foundation
- Tausif Alam
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and materials for GALGT2 gene therapy
- Patent number 12,121,595
- Issue date Oct 22, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
DNA vectors, transposons and transposases for eukaryotic genome mod...
- Patent number 12,122,995
- Issue date Oct 22, 2024
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
DNA vectors, transposons and transposases for eukaryotic genome mod...
- Patent number 12,054,702
- Issue date Aug 6, 2024
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Synthetic genetic elements for biomanufacture
- Patent number 12,049,638
- Issue date Jul 30, 2024
- Janssen Biotech, Inc.
- William Lloyd Perry
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
- Patent number 11,975,056
- Issue date May 7, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Bicistronic AAV vector for RNA interference in ALS
- Patent number 11,872,290
- Issue date Jan 16, 2024
- Ecole Polytechnique Federale de Lausanne (EPFL)
- Julianne Aebischer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Replicative minicircle vectors with improved expression
- Patent number 11,851,665
- Issue date Dec 26, 2023
- ALDEVRON, LLC
- James A. Williams
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression
- Patent number 11,773,406
- Issue date Oct 3, 2023
- Adverum Biotechnologies, Inc.
- Annahita Keravala
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for inducing immune responses
- Patent number 11,759,515
- Issue date Sep 19, 2023
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Coronavirus vaccine compositions and methods
- Patent number 11,744,887
- Issue date Sep 5, 2023
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Vectors
- Patent number 11,725,216
- Issue date Aug 15, 2023
- National University of Singapore
- Volker Patzel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Regulation of gene expression through aptamer-modulated polyadenyla...
- Patent number 11,697,815
- Issue date Jul 11, 2023
- MEIRAGTX UK II LIMITED
- Michael J. Volles
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lentiviral vector expressing membrane-anchored or secreted antibody
- Patent number 11,623,950
- Issue date Apr 11, 2023
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- Floriane Fusil
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
RP2 and RPGR vectors for treating X-linked retinitis pigmentosa
- Patent number 11,617,801
- Issue date Apr 4, 2023
- The United States of America,as represented by the Secretary, Department of H...
- Zhijian Wu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for selecting polypeptide producing cells
- Patent number 11,591,383
- Issue date Feb 28, 2023
- HOFFMANN-LA ROCHE INC.
- Erhard Kopetzki
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified mGluR6 promoter and methods of use
- Patent number 11,583,595
- Issue date Feb 21, 2023
- Wayne State University
- Zhuo-Hua Pan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid molecules comprising a variant inc coding strand
- Patent number 11,549,116
- Issue date Jan 10, 2023
- CJ Cheiljedang Corporation
- Ji Sun Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for treating citrullenemia
- Patent number 11,535,866
- Issue date Dec 27, 2022
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Liver-specific constructs factor VIII expression cassettes and meth...
- Patent number 11,452,782
- Issue date Sep 27, 2022
- Sangamo Therapeutics, Inc.
- Brigit E. Riley
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Vectors for liver-directed gene therapy of hemophilia and methods a...
- Patent number 11,419,950
- Issue date Aug 23, 2022
- Vrije Universiteit Brussel
- Thierry Vandendriessche
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Integration of nucleic acid constructs into eukaryotic cells with a...
- Patent number 11,401,521
- Issue date Aug 2, 2022
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression
- Patent number 11,352,644
- Issue date Jun 7, 2022
- Adverum Biotechnologies, Inc.
- Annahita Keravala
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
SCHWANN CELL-SPECIFIC PROMOTER
- Publication number 20250115906
- Publication date Apr 10, 2025
- Toolgen Incorporated
- Dong Woo SONG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENERATION OF LARGE PROTEINS BY CO-DELIVERY OF MULTIPLE VECTORS
- Publication number 20250099616
- Publication date Mar 27, 2025
- University of Washington
- Jeffrey S. CHAMBERLAIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Expression Cassette for Production of High-Expression and High-Func...
- Publication number 20250084433
- Publication date Mar 13, 2025
- CELLTRION INC.
- Man Su Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AADC/GDNF POLYNUCLEOTIDE, AND USE THEREOF IN TREATING PARKINSON'S D...
- Publication number 20250051750
- Publication date Feb 13, 2025
- SHANGHAI REGENELEAD THERAPIES CO., LTD.
- Jun Jiang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY
- Publication number 20250049959
- Publication date Feb 13, 2025
- Tenaya Therapeutics, Inc.
- Huanyu ZHOU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DNA VECTORS, TRANSPOSONS AND TRANSPOSASES FOR EUKARYOTIC GENOME MOD...
- Publication number 20250043235
- Publication date Feb 6, 2025
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Lentiviral Vectors
- Publication number 20250034589
- Publication date Jan 30, 2025
- OXFORD BIOMEDICA (UK) LIMITED
- Daniel Farley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR GALGT2 GENE THERAPY
- Publication number 20250025578
- Publication date Jan 23, 2025
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Vectors for Increasing NPRL2 Expression in Cancer Cells and Methods...
- Publication number 20250002546
- Publication date Jan 2, 2025
- Genprex, Inc.
- Michael Redman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AADC POLYNUCLEOTIDES FOR THE TREATMENT OF PARKINSON'S DISEASE
- Publication number 20240415943
- Publication date Dec 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS USEFUL FOR TREATMENT OF CHARCOT-MARIE-TOOTH DISEASE
- Publication number 20240401078
- Publication date Dec 5, 2024
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CIRCULAR RNA AND PREPARATION METHOD THEREOF
- Publication number 20240392304
- Publication date Nov 28, 2024
- Center for Excellence in Molecular Cell Science, Chinese Academy of Sciences
- Siqi LI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUR...
- Publication number 20240376164
- Publication date Nov 14, 2024
- Wuhan Neurophth Biotechnology Limited Company
- Bin LI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED ITR SEQUENCES AND METHODS OF USE
- Publication number 20240350671
- Publication date Oct 24, 2024
- Bioverativ Therapeutics Inc.
- Ajay Maghodia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE PRODUCTION OF LIBRARIES
- Publication number 20240352485
- Publication date Oct 24, 2024
- Flagship Pioneering Innovations VII, LLC
- Patrick Leo JONES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYNTHETIC GENETIC ELEMENTS FOR BIOMANUFACTURE
- Publication number 20240327869
- Publication date Oct 3, 2024
- JANSSEN BIOTECH, INC.
- William Lloyd Perry
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treating Fabry Disease
- Publication number 20240301380
- Publication date Sep 12, 2024
- Spark Therapeutics, Inc.
- Sean Armour
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR THE TREATMENT OF HYPER-IgE SYNDROME (HIES) BY TARG...
- Publication number 20240299453
- Publication date Sep 12, 2024
- CELLECTIS S.A.
- Toni Cathomen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXPRESSION CASSETTE INCLUDING INTRON FOR HIGH EXPRESSION OF PROTEIN...
- Publication number 20240287541
- Publication date Aug 29, 2024
- CELLTRION INC.
- Man Su KIM
- C07 - ORGANIC CHEMISTRY
Information Patent Application
CONSTRUCTS AND METHODS FOR PREPARING CIRCULAR RNAS AND USE THEREOF
- Publication number 20240279676
- Publication date Aug 22, 2024
- Shanghai Circode Biomed Co., Ltd.
- Yun YANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR LESCH-NYHAN DISORDERS AND...
- Publication number 20240269328
- Publication date Aug 15, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV FOR THE GENE THERAPY OF WET-AMD
- Publication number 20240252686
- Publication date Aug 1, 2024
- Skyline Therapeutics Limited
- Jinzhao HOU
- C07 - ORGANIC CHEMISTRY
Information Patent Application
EXPRESSION CASSETTE FOR EXPRESSING GENE COMPRISING OVERLAPPING OPEN...
- Publication number 20240247282
- Publication date Jul 25, 2024
- GENEVOYAGER (WUHAN) CO., LTD.
- He XIAO
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Information Patent Application
REPLICATIVE MINICIRCLE VECTORS WITH IMPROVED EXPRESSION
- Publication number 20240218382
- Publication date Jul 4, 2024
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- James A. Williams
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ALPHAVIRUS VECTORS CONTAINING UNIVERSAL CLONING ADAPTORS
- Publication number 20240218395
- Publication date Jul 4, 2024
- Replicate Bioscience, Inc.
- Nathaniel Stephen WANG
- C07 - ORGANIC CHEMISTRY
Information Patent Application
REGULATION OF GENE EXPRESSION THROUGH APTAMER-MODULATED POLYADENYLA...
- Publication number 20240191239
- Publication date Jun 13, 2024
- MEIRAGTX UK II LIMITED
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Information Patent Application
COMPACT PROMOTERS FOR GENE EXPRESSION
- Publication number 20240173436
- Publication date May 30, 2024
- HUNTERIAN MEDICINE LLC
- Vinod Jaskula-Ranga
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS
- Publication number 20240175046
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- National University of Singapore
- Volker PATZEL
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Information Patent Application
COMPACT PROMOTERS FOR GENE EDITING
- Publication number 20240175006
- Publication date May 30, 2024
- HUNTERIAN MEDICINE LLC
- Vinod Jaskula-Ranga
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS...
- Publication number 20240139344
- Publication date May 2, 2024
- Akouos, Inc.
- Emmanuel John Simons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

being an intron or intervening sequence for splicing and/or stability of RNA

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compositions and methods for enhanced gene expression in cone cells

Eukaryotic cells comprising adenovirus-associated virus polynucleot...

Coronavirus vaccine compositions and methods

Compositions and methods for gene editing by targeting transferrin

Expression cassette for production of high-expression and high-func...

Intron fragments

Hepatocyte based insulin gene therapy for diabetes

Optimized expression cassettes for gene therapy

Methods and materials for GALGT2 gene therapy

DNA vectors, transposons and transposases for eukaryotic genome mod...

DNA vectors, transposons and transposases for eukaryotic genome mod...

Synthetic genetic elements for biomanufacture

AADC polynucleotides for the treatment of Parkinson's disease

Bicistronic AAV vector for RNA interference in ALS

Replicative minicircle vectors with improved expression

Compositions and methods for enhanced gene expression

Compositions and methods for inducing immune responses

Coronavirus vaccine compositions and methods

Vectors

Regulation of gene expression through aptamer-modulated polyadenyla...

Lentiviral vector expressing membrane-anchored or secreted antibody

RP2 and RPGR vectors for treating X-linked retinitis pigmentosa

Method for selecting polypeptide producing cells

Modified mGluR6 promoter and methods of use

Nucleic acid molecules comprising a variant inc coding strand

Gene therapy for treating citrullenemia

Liver-specific constructs factor VIII expression cassettes and meth...

Vectors for liver-directed gene therapy of hemophilia and methods a...

Integration of nucleic acid constructs into eukaryotic cells with a...

Compositions and methods for enhanced gene expression

Patents Applicationslast 30 patents

SCHWANN CELL-SPECIFIC PROMOTER

GENERATION OF LARGE PROTEINS BY CO-DELIVERY OF MULTIPLE VECTORS

Expression Cassette for Production of High-Expression and High-Func...

AADC/GDNF POLYNUCLEOTIDE, AND USE THEREOF IN TREATING PARKINSON'S D...

OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

DNA VECTORS, TRANSPOSONS AND TRANSPOSASES FOR EUKARYOTIC GENOME MOD...

Lentiviral Vectors

METHODS AND MATERIALS FOR GALGT2 GENE THERAPY

Vectors for Increasing NPRL2 Expression in Cancer Cells and Methods...

AADC POLYNUCLEOTIDES FOR THE TREATMENT OF PARKINSON'S DISEASE

COMPOSITIONS USEFUL FOR TREATMENT OF CHARCOT-MARIE-TOOTH DISEASE

CIRCULAR RNA AND PREPARATION METHOD THEREOF

COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUR...

ENGINEERED ITR SEQUENCES AND METHODS OF USE

COMPOSITIONS AND METHODS FOR THE PRODUCTION OF LIBRARIES

SYNTHETIC GENETIC ELEMENTS FOR BIOMANUFACTURE

Compositions and Methods for Treating Fabry Disease

GENE THERAPY FOR THE TREATMENT OF HYPER-IgE SYNDROME (HIES) BY TARG...

EXPRESSION CASSETTE INCLUDING INTRON FOR HIGH EXPRESSION OF PROTEIN...

CONSTRUCTS AND METHODS FOR PREPARING CIRCULAR RNAS AND USE THEREOF

RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR LESCH-NYHAN DISORDERS AND...

AAV FOR THE GENE THERAPY OF WET-AMD

EXPRESSION CASSETTE FOR EXPRESSING GENE COMPRISING OVERLAPPING OPEN...

REPLICATIVE MINICIRCLE VECTORS WITH IMPROVED EXPRESSION

ALPHAVIRUS VECTORS CONTAINING UNIVERSAL CLONING ADAPTORS

REGULATION OF GENE EXPRESSION THROUGH APTAMER-MODULATED POLYADENYLA...

COMPACT PROMOTERS FOR GENE EXPRESSION

VECTORS

COMPACT PROMOTERS FOR GENE EDITING

COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS...