being an intron or intervening sequence for splicing and/or stability of RNA

Industry

CPC
C12N2830/42

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Parent Industries

CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

Current Industry

C12N2830/42being an intron or intervening sequence for splicing and/or stability of RNA

Industries

Patents Grantslast 30 patents

Information Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
- Patent number 11,975,056
- Issue date May 7, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Bicistronic AAV vector for RNA interference in ALS
- Patent number 11,872,290
- Issue date Jan 16, 2024
- Ecole Polytechnique Federale de Lausanne (EPFL)
- Julianne Aebischer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Replicative minicircle vectors with improved expression
- Patent number 11,851,665
- Issue date Dec 26, 2023
- ALDEVRON, LLC
- James A. Williams
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression
- Patent number 11,773,406
- Issue date Oct 3, 2023
- Adverum Biotechnologies, Inc.
- Annahita Keravala
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for inducing immune responses
- Patent number 11,759,515
- Issue date Sep 19, 2023
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Coronavirus vaccine compositions and methods
- Patent number 11,744,887
- Issue date Sep 5, 2023
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Vectors
- Patent number 11,725,216
- Issue date Aug 15, 2023
- National University of Singapore
- Volker Patzel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Regulation of gene expression through aptamer-modulated polyadenyla...
- Patent number 11,697,815
- Issue date Jul 11, 2023
- MEIRAGTX UK II LIMITED
- Michael J. Volles
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lentiviral vector expressing membrane-anchored or secreted antibody
- Patent number 11,623,950
- Issue date Apr 11, 2023
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- Floriane Fusil
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
RP2 and RPGR vectors for treating X-linked retinitis pigmentosa
- Patent number 11,617,801
- Issue date Apr 4, 2023
- The United States of America,as represented by the Secretary, Department of H...
- Zhijian Wu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for selecting polypeptide producing cells
- Patent number 11,591,383
- Issue date Feb 28, 2023
- HOFFMANN-LA ROCHE INC.
- Erhard Kopetzki
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified mGluR6 promoter and methods of use
- Patent number 11,583,595
- Issue date Feb 21, 2023
- Wayne State University
- Zhuo-Hua Pan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid molecules comprising a variant inc coding strand
- Patent number 11,549,116
- Issue date Jan 10, 2023
- CJ Cheiljedang Corporation
- Ji Sun Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for treating citrullenemia
- Patent number 11,535,866
- Issue date Dec 27, 2022
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Liver-specific constructs factor VIII expression cassettes and meth...
- Patent number 11,452,782
- Issue date Sep 27, 2022
- Sangamo Therapeutics, Inc.
- Brigit E. Riley
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Vectors for liver-directed gene therapy of hemophilia and methods a...
- Patent number 11,419,950
- Issue date Aug 23, 2022
- Vrije Universiteit Brussel
- Thierry Vandendriessche
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Integration of nucleic acid constructs into eukaryotic cells with a...
- Patent number 11,401,521
- Issue date Aug 2, 2022
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression
- Patent number 11,352,644
- Issue date Jun 7, 2022
- Adverum Biotechnologies, Inc.
- Annahita Keravala
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric gene constructs for generation of fluorescent transgenic o...
- Patent number 11,259,509
- Issue date Mar 1, 2022
- National University of Singapore
- Zhiyuan Gong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for enhanced gene expression in cone cells
- Patent number 11,248,214
- Issue date Feb 15, 2022
- Adverum Biotechnologies, Inc.
- Thomas W. Chalberg
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid molecules containing spacers and methods of use thereof
- Patent number 11,230,720
- Issue date Jan 25, 2022
- Audentes Therapeutics, Inc.
- John T. Gray
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Reagents and methods for modulating cone photoreceptor activity
- Patent number 11,160,488
- Issue date Nov 2, 2021
- Universty of Washington
- Jay Neitz
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Replicative minicircle vectors with improved expression
- Patent number 11,098,313
- Issue date Aug 24, 2021
- Nature Technology Corporation
- James A. Williams
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Factor VIII mutation repair and tolerance induction
- Patent number 11,083,801
- Issue date Aug 10, 2021
- Haplomics, Inc.
- Vincent Laterza
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vectors for treatment of glycogen storage di...
- Patent number 11,060,110
- Issue date Jul 13, 2021
- The United States of America, as represented by the Secretary, Department of...
- Janice J. Chou
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Integration of nucleic acid constructs into eukaryotic cells with a...
- Patent number 11,060,098
- Issue date Jul 13, 2021
- DNA TWOPOINTO INC.
- Jeremy Minshull
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
- Patent number 11,027,000
- Issue date Jun 8, 2021
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Hybrid promoter and uses thereof
- Patent number 11,028,410
- Issue date Jun 8, 2021
- JUST-EVOTEC BIOLOGICS, INC.
- Jeffrey T. McGrew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized liver-specific expression systems for FVIII and FIX
- Patent number 11,007,280
- Issue date May 18, 2021
- Vrije Universiteit Brussel
- Marinee Chuah
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods of modifying genes in eukaryotic cells
- Patent number 10,988,776
- Issue date Apr 27, 2021
- REGENERON PHARMACEUTICALS, INC.
- Aris N. Economides
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMPACT PROMOTERS FOR GENE EXPRESSION
- Publication number 20240173436
- Publication date May 30, 2024
- HUNTERIAN MEDICINE LLC
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS
- Publication number 20240175046
- Publication date May 30, 2024
- National University of Singapore
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPACT PROMOTERS FOR GENE EDITING
- Publication number 20240175006
- Publication date May 30, 2024
- HUNTERIAN MEDICINE LLC
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS...
- Publication number 20240139344
- Publication date May 2, 2024
- Akouos, Inc.
- Emmanuel John Simons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR USING ALTERNATIVE SPLICING TO CONTROL...
- Publication number 20240108756
- Publication date Apr 4, 2024
- The Johns Hopkins University
- Jonathan P. Ling
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ABCA4 TRANS-SPLICING MOLECULES
- Publication number 20240091381
- Publication date Mar 21, 2024
- Ascidian Therapeutics, Inc.
- Rebekka Krumbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ABCA4 TRANS-SPLICING MOLECULES
- Publication number 20240042057
- Publication date Feb 8, 2024
- Ascidian Therapeutics, Inc.
- Rebekka Krumbach
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY
- Publication number 20240042060
- Publication date Feb 8, 2024
- Tenaya Therapeutics, Inc.
- Huanyu ZHOU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXPRESSION AND SECRETION SYSTEM
- Publication number 20240043831
- Publication date Feb 8, 2024
- Genentech, Inc.
- Devin Tesar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF HYPERBILIRUBINEMIA
- Publication number 20230414724
- Publication date Dec 28, 2023
- Genethon
- FEDERICO MINGOZZI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SCREENING SYSTEM FOR MYCOBACTERIUM TUBERCULOSIS INTEIN SPLICING INH...
- Publication number 20230392179
- Publication date Dec 7, 2023
- SOOCHOW UNIVERSITY
- Xingmei QI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CIRCULAR RNA VACCINES AND METHODS OF USE THEREOF
- Publication number 20230346921
- Publication date Nov 2, 2023
- Peking University
- Wensheng WEI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TRANSGENE EXPRESSION SYSTEM
- Publication number 20230323391
- Publication date Oct 12, 2023
- THE UNIVERSITY COURT OF THE UNIVERSITY OF EDINBURGH
- Stuart Robert COBB
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED MGLUR6 PROMOTER AND METHODS OF USE
- Publication number 20230310657
- Publication date Oct 5, 2023
- Wayne State University
- Zhuo-Hua Pan
- C07 - ORGANIC CHEMISTRY
Information Patent Application
METHODS TO GENETICALLY MODIFY CELLS FOR DELIVERY OF THERAPEUTIC PRO...
- Publication number 20230279440
- Publication date Sep 7, 2023
- CELLECTIS S.A.
- Alexandre JUILLERAT
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR ENHANCED GENE EXPRESSION
- Publication number 20230257777
- Publication date Aug 17, 2023
- Adverum Biotechnologies, Inc.
- Annahita Keravala
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR REDUCING REVERSE PACKAGING OF CAP AND...
- Publication number 20230235353
- Publication date Jul 27, 2023
- ULTRAGENYX PHARMACEUTICAL INC.
- Brady Camplin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EUKARYOTIC CELLS COMPRISING ADENOVIRUS-ASSOCIATED VIRUS POLYNUCLEOT...
- Publication number 20230193312
- Publication date Jun 22, 2023
- Regeneron Pharmaceuticals, Inc.
- Michael Goren
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SELF-LIMITING VIRAL VECTORS ENCODING NUCLEASES
- Publication number 20230183664
- Publication date Jun 15, 2023
- PRECISION BIOSCIENCES, INC.
- Hui Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED VECTORS FOR PRODUCTION OF RETROVIRUS
- Publication number 20230151388
- Publication date May 18, 2023
- GlaxoSmithKline Intellectual Property Development Limited
- Nathan SWEENEY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS FOR THE TREATMENT OF ACID CERAMIDASE DEFICIENCY
- Publication number 20230151390
- Publication date May 18, 2023
- Genethon
- ANA BUJ BELLO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY
- Publication number 20230133924
- Publication date May 4, 2023
- Tenaya Therapeutics, Inc.
- Huanyu ZHOU
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Information Patent Application
LIVER-SPECIFIC CONSTRUCTS, FACTOR VIII EXPRESSION CASSETTES AND MET...
- Publication number 20230119850
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- Sangamo Therapeutics, Inc.
- Brigit E. Riley
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- DNA TWOPOINTO INC.
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CLOSED-END DNA PRODUCTION WITH INVERTED TERMINAL REPEAT SEQUENCES
- Publication number 20230091932
- Publication date Mar 23, 2023
- Bioverativ Therapeutics Inc.
- Ajay Maghodia
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COMPOSITIONS AND METHODS FOR CIRCULAR RNA EXPRESSION
- Publication number 20230072954
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- DUKE UNIVERSITY
- Aravind Asokan
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Treatment of Ocular Diseases with Fully-Human Post-Translationally...
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- Regenxbio Inc.
- Curran Matthew SIMPSON
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ADENO-ASSOCIATED VIRUS VECTORS BASED GENE THERAPY FOR HEREDITARY AN...
- Publication number 20230043051
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- Shire Human Genetic Therapies, Inc
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THERAPEUTIC ADENO-ASSOCIATED VIRUS COMPRISING LIVER-SPECIFIC PROMOT...
- Publication number 20230038520
- Publication date Feb 9, 2023
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Michael ROBERTS
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GENE THERAPY VECTORS
- Publication number 20220411821
- Publication date Dec 29, 2022
- University of Florida Research Foundation, Incorporated
- Eric Tzy-Shi Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

being an intron or intervening sequence for splicing and/or stability of RNA

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

AADC polynucleotides for the treatment of Parkinson's disease

Bicistronic AAV vector for RNA interference in ALS

Replicative minicircle vectors with improved expression

Compositions and methods for enhanced gene expression

Compositions and methods for inducing immune responses

Coronavirus vaccine compositions and methods

Vectors

Regulation of gene expression through aptamer-modulated polyadenyla...

Lentiviral vector expressing membrane-anchored or secreted antibody

RP2 and RPGR vectors for treating X-linked retinitis pigmentosa

Method for selecting polypeptide producing cells

Modified mGluR6 promoter and methods of use

Nucleic acid molecules comprising a variant inc coding strand

Gene therapy for treating citrullenemia

Liver-specific constructs factor VIII expression cassettes and meth...

Vectors for liver-directed gene therapy of hemophilia and methods a...

Integration of nucleic acid constructs into eukaryotic cells with a...

Compositions and methods for enhanced gene expression

Chimeric gene constructs for generation of fluorescent transgenic o...

Compositions and methods for enhanced gene expression in cone cells

Nucleic acid molecules containing spacers and methods of use thereof

Reagents and methods for modulating cone photoreceptor activity

Replicative minicircle vectors with improved expression

Factor VIII mutation repair and tolerance induction

Adeno-associated virus vectors for treatment of glycogen storage di...

Integration of nucleic acid constructs into eukaryotic cells with a...

AADC polynucleotides for the treatment of Parkinson's disease

Hybrid promoter and uses thereof

Optimized liver-specific expression systems for FVIII and FIX

Methods of modifying genes in eukaryotic cells

Patents Applicationslast 30 patents

COMPACT PROMOTERS FOR GENE EXPRESSION

VECTORS

COMPACT PROMOTERS FOR GENE EDITING

COMPOSITIONS AND METHODS FOR TREATING CLRN1-ASSOCIATED HEARING LOSS...

COMPOSITIONS AND METHODS FOR USING ALTERNATIVE SPLICING TO CONTROL...

ABCA4 TRANS-SPLICING MOLECULES

ABCA4 TRANS-SPLICING MOLECULES

OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

EXPRESSION AND SECRETION SYSTEM

TREATMENT OF HYPERBILIRUBINEMIA

SCREENING SYSTEM FOR MYCOBACTERIUM TUBERCULOSIS INTEIN SPLICING INH...

CIRCULAR RNA VACCINES AND METHODS OF USE THEREOF

TRANSGENE EXPRESSION SYSTEM

MODIFIED MGLUR6 PROMOTER AND METHODS OF USE

METHODS TO GENETICALLY MODIFY CELLS FOR DELIVERY OF THERAPEUTIC PRO...

COMPOSITIONS AND METHODS FOR ENHANCED GENE EXPRESSION

COMPOSITIONS AND METHODS FOR REDUCING REVERSE PACKAGING OF CAP AND...

EUKARYOTIC CELLS COMPRISING ADENOVIRUS-ASSOCIATED VIRUS POLYNUCLEOT...

SELF-LIMITING VIRAL VECTORS ENCODING NUCLEASES

MODIFIED VECTORS FOR PRODUCTION OF RETROVIRUS

VECTORS FOR THE TREATMENT OF ACID CERAMIDASE DEFICIENCY

OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

LIVER-SPECIFIC CONSTRUCTS, FACTOR VIII EXPRESSION CASSETTES AND MET...

INTEGRATION OF NUCLEIC ACID CONSTRUCTS INTO EUKARYOTIC CELLS WITH A...

CLOSED-END DNA PRODUCTION WITH INVERTED TERMINAL REPEAT SEQUENCES

COMPOSITIONS AND METHODS FOR CIRCULAR RNA EXPRESSION

Treatment of Ocular Diseases with Fully-Human Post-Translationally...

ADENO-ASSOCIATED VIRUS VECTORS BASED GENE THERAPY FOR HEREDITARY AN...

THERAPEUTIC ADENO-ASSOCIATED VIRUS COMPRISING LIVER-SPECIFIC PROMOT...

GENE THERAPY VECTORS