characterised by an aspect of the delivery route

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A61K48/0075

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

Current Industry

A61K48/0075characterised by an aspect of the delivery route

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Method of using NAP-2 and TGF-α to improve cardiac function
- Patent number 12,357,676
- Issue date Jul 15, 2025
- Mayo Foundation for Medical Education and Research
- Atta Behfar
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
CNS gene delivery using peripheral administration of AAV vectors
- Patent number 12,351,816
- Issue date Jul 8, 2025
- Genethon
- Martine Barkats
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and uses thereof
- Patent number 12,351,637
- Issue date Jul 8, 2025
- AVIDITY BIOSCIENCES, INC.
- Andrew John Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for neurodegenerative disorders
- Patent number 12,350,311
- Issue date Jul 8, 2025
- Genzyme Corporation
- Marco A. Passini
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment and prevention of ocular neurodegenerative disorder
- Patent number 12,336,986
- Issue date Jun 24, 2025
- The Jackson Laboratory
- Simon W. M. John
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Non-viral DNA vectors and uses thereof for expressing FVIII therape...
- Patent number 12,338,275
- Issue date Jun 24, 2025
- Generation Bio Co.
- Douglas Anthony Kerr
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods of treating ocular diseases
- Patent number 12,310,997
- Issue date May 27, 2025
- The Regents of the University of California
- David V. Schaffer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for modifying mucous membranes
- Patent number 12,303,607
- Issue date May 20, 2025
- Nicholas L. Abbott
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
AAV capsid variants and uses thereof
- Patent number 12,296,025
- Issue date May 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene editing to improve joint function
- Patent number 12,290,572
- Issue date May 6, 2025
- ORTHOBIO THERAPEUTICS, INC.
- Peter J. Millett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Riboswitch modulated gene therapy for retinal diseases
- Patent number 12,286,631
- Issue date Apr 29, 2025
- The Medical College of Wisconsin, Inc.
- Daniel M. Lipinski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lipid nanoparticle formulations for delivery of MRNA
- Patent number 12,280,117
- Issue date Apr 22, 2025
- Translate Bio, Inc.
- Frank DeRosa
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Recombinant adeno-associated viruses encoding serpin peptides and u...
- Patent number 12,274,757
- Issue date Apr 15, 2025
- University of Florida Research Foundation, Incorporated
- Alexandra Rose Lucas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Composition and methods for treatment of ornithine transcarbamylase...
- Patent number 12,268,754
- Issue date Apr 8, 2025
- Translate Bio, Inc.
- Kim Askew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating non-age-associated hearing im...
- Patent number 12,264,317
- Issue date Apr 1, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Gene therapy for limb-girdle muscular dystrophy type 2C
- Patent number 12,263,230
- Issue date Apr 1, 2025
- Research Institute at Nationwide Children's Hospital
- Louise R. Rodino-Klapac
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus virions for treatment of epilepsy
- Patent number 12,263,231
- Issue date Apr 1, 2025
- Jichi Medical University
- Shin-ichi Muramatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vector delivery of a fragment of micro-dystr...
- Patent number 12,257,317
- Issue date Mar 25, 2025
- Newcastle University
- Hanns Lochmuller
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Polynucleotide compositions, related formulations, and methods of u...
- Patent number 12,257,318
- Issue date Mar 25, 2025
- ReCode Therapeutics, Inc.
- Mirko Hennig
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for NMNAT1-associated retinal degeneration
- Patent number 12,257,320
- Issue date Mar 25, 2025
- Massachusetts Eye and Ear Infirmary
- Eric A. Pierce
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for transient gene therapy with enhanced s...
- Patent number 12,258,560
- Issue date Mar 25, 2025
- Dana-Farber Cancer Institute, Inc.
- Michael Goldberg
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Closed-ended linear duplex DNA for non-viral gene transfer
- Patent number 12,252,703
- Issue date Mar 18, 2025
- UNIVERSITY OF MASSACHUSETTS
- Robert M. Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV vectors for retinal and CNS gene therapy
- Patent number 12,241,078
- Issue date Mar 4, 2025
- Genzyme Corporation
- Abraham Scaria
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and uses thereof
- Patent number 12,234,290
- Issue date Feb 25, 2025
- AVIDITY BIOSCIENCES, INC.
- Andrew John Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for eosinophilic disorders
- Patent number 12,226,492
- Issue date Feb 18, 2025
- Cornell University
- Ronald G. Crystal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Sulfamidase (SGSH) variants, vectors, compositions and methods and...
- Patent number 12,221,635
- Issue date Feb 11, 2025
- The Childeren's Hospital of Philadelphia
- Beverly L. Davidson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic applications of CPF1-based genome editing
- Patent number 12,214,056
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Intrathecal delivery of recombinant adeno-associated virus 9
- Patent number 12,208,144
- Issue date Jan 28, 2025
- Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for treatment of hereditary haemochromatosis
- Patent number 12,186,406
- Issue date Jan 7, 2025
- CRISPR THERAPEUTICS AG
- Roman Lvovitch Bogorad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Isoform Nell-1 peptide
- Patent number 12,186,367
- Issue date Jan 7, 2025
- The Regents of the University of California
- Kang Ting
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250235550
- Publication date Jul 24, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND PHARMACEUTICAL COMPOSITIONS FOR MODULATING TEAR FILM CO...
- Publication number 20250235492
- Publication date Jul 24, 2025
- INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE
- Frédéric MICHON
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
- Publication number 20250235554
- Publication date Jul 24, 2025
- Novartis AG
- Keith MANSFIELD
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MATERIALS AND METHODS FOR TREATMENT OF HEREDITARY HAEMOCHROMATOSIS
- Publication number 20250235561
- Publication date Jul 24, 2025
- CRISPR Therapeutics AG
- Roman Lvovitch Bogorad
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TREATING ORTHOPEDIC INJURY WITH A VECTOR DRIVING EXPRESSION OF ACID...
- Publication number 20250228908
- Publication date Jul 17, 2025
- Icahn School of Medicine at Mount Sinai
- Efrat ELIYAHU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20250228967
- Publication date Jul 17, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
BASE EDITING METHODS AND COMPOSITIONS FOR TREATING TRIPLET REPEAT D...
- Publication number 20250228981
- Publication date Jul 17, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR THE TREATMENT OF COGNITIVE DISORDERS
- Publication number 20250228970
- Publication date Jul 17, 2025
- The Regents of the University of California
- Mark Tuszynski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE EDITING TO IMPROVE JOINT FUNCTION
- Publication number 20250228969
- Publication date Jul 17, 2025
- Orthobio Therapeutics, Inc.
- Peter J. Millet
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treating Striatonigral Degeneration
- Publication number 20250228977
- Publication date Jul 17, 2025
- Texas Scottish Rite Hospital for Children
- Jonathan J. Rios
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VECTOR ENCODING ANTI-VEGF-A AND ANG-2 BISPECIFIC ANTIBODY
- Publication number 20250223345
- Publication date Jul 10, 2025
- STARRYGENE THERAPEUTICS CO., LTD.
- Yuan CAI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLYCOGEN STORAGE DISO...
- Publication number 20250222134
- Publication date Jul 10, 2025
- University of Connecticut
- Youngmok Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RET...
- Publication number 20250222135
- Publication date Jul 10, 2025
- University of Pittsburgh of the Commonwealth System of Higher Education
- Leah Caroline THOMAS BYRNE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR THE TREATMENT OF PARKINSON'S DISEASE
- Publication number 20250222072
- Publication date Jul 10, 2025
- ASKLEPIOS BIOPHARMACEUTICAL, INC.
- Krystof S. BANKIEWICZ
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL ANELLOVIRIDAE FAMILY VECTOR COMPOSITIONS AND METHODS
- Publication number 20250213725
- Publication date Jul 3, 2025
- FLAGSHIP PIONEERING INNOVATIONS V, INC.
- Lianna Swanson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL...
- Publication number 20250213722
- Publication date Jul 3, 2025
- UNIVERSITY OF PITTSBURGH - OF THE COMMONWEALTH SYSTEM OF HIGHER EDUCATION
- Leah Caroline THOMAS BYRNE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ULTRASOUND-MEDIATED GENE THERAPY FOR DEEP VEIN THROMBOSIS AND POST-...
- Publication number 20250213695
- Publication date Jul 3, 2025
- Cedars-Sinai Medical Center
- Dan Gazit
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT REGIMENS FOR THERAPEUTIC EFFECTOR COMPONENTS THAT ACT VIA...
- Publication number 20250205361
- Publication date Jun 26, 2025
- Sapreme Technologies B.V.
- Miriam Verena Bujny
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Intrathecal Delivery of Recombinant Adeno-Associated Virus 9
- Publication number 20250205368
- Publication date Jun 26, 2025
- NATIONWIDE CHILDREN'S HOSPITAL
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF
- Publication number 20250205366
- Publication date Jun 26, 2025
- Huidagene Therapeutics (Singapore) Pte. Ltd.
- Xing Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION
- Publication number 20250205363
- Publication date Jun 26, 2025
- Shape Therapeutics Inc.
- Thomas PACKARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...
- Publication number 20250205365
- Publication date Jun 26, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DRUG AND METHOD FOR FORMING GABAERGIC NEURONS
- Publication number 20250205364
- Publication date Jun 26, 2025
- JINAN UNIVERSITY
- Gong CHEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CONSTRUCTS, VIRAL VECTORS AND PHARMACEUTICAL COMPOSITIONS COMPRISIN...
- Publication number 20250207133
- Publication date Jun 26, 2025
- Trustees of Tufts College
- Jinkun Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING TMEM43 RELATED CARDIOMYOPATHY...
- Publication number 20250195695
- Publication date Jun 19, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND SYSTEMS FOR IMPROVED DELIVERY VIA ULTRASOUND
- Publication number 20250195923
- Publication date Jun 19, 2025
- SonoThera, Inc.
- Steven B. FEINSTEIN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RETINAL PROTECTIVE FACTOR 2 (RPF2) PROTEIN DELIVERED BY ADENO-ASSOC...
- Publication number 20250195696
- Publication date Jun 19, 2025
- University of Florida Research Foundation, Incorporated
- John Ash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING OSMIDROSIS
- Publication number 20250188461
- Publication date Jun 12, 2025
- Roger L. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VIRAL VECTORS ENCODING GLP-2 RECEPTOR AGONIST FUSIONS AND USES THER...
- Publication number 20250186613
- Publication date Jun 12, 2025
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
USING DREADD FOR NEURONAL MODULATION IN TREATING NEURONAL DISEASES
- Publication number 20250186610
- Publication date Jun 12, 2025
- Fadi ASSAF
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the delivery route

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Method of using NAP-2 and TGF-α to improve cardiac function

CNS gene delivery using peripheral administration of AAV vectors

Nucleic acid-polypeptide compositions and uses thereof

Gene therapy for neurodegenerative disorders

Treatment and prevention of ocular neurodegenerative disorder

Non-viral DNA vectors and uses thereof for expressing FVIII therape...

Compositions and methods of treating ocular diseases

Methods and compositions for modifying mucous membranes

AAV capsid variants and uses thereof

Gene editing to improve joint function

Riboswitch modulated gene therapy for retinal diseases

Lipid nanoparticle formulations for delivery of MRNA

Recombinant adeno-associated viruses encoding serpin peptides and u...

Composition and methods for treatment of ornithine transcarbamylase...

Compositions and methods for treating non-age-associated hearing im...

Gene therapy for limb-girdle muscular dystrophy type 2C

Adeno-associated virus virions for treatment of epilepsy

Adeno-associated virus vector delivery of a fragment of micro-dystr...

Polynucleotide compositions, related formulations, and methods of u...

Gene therapy for NMNAT1-associated retinal degeneration

Compositions and methods for transient gene therapy with enhanced s...

Closed-ended linear duplex DNA for non-viral gene transfer

AAV vectors for retinal and CNS gene therapy

Nucleic acid-polypeptide compositions and uses thereof

Gene therapy for eosinophilic disorders

Sulfamidase (SGSH) variants, vectors, compositions and methods and...

Therapeutic applications of CPF1-based genome editing

Intrathecal delivery of recombinant adeno-associated virus 9

Materials and methods for treatment of hereditary haemochromatosis

Isoform Nell-1 peptide

Patents Applicationslast 30 patents

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

METHODS AND PHARMACEUTICAL COMPOSITIONS FOR MODULATING TEAR FILM CO...

METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY

MATERIALS AND METHODS FOR TREATMENT OF HEREDITARY HAEMOCHROMATOSIS

TREATING ORTHOPEDIC INJURY WITH A VECTOR DRIVING EXPRESSION OF ACID...

AAV CAPSID VARIANTS AND USES THEREOF

BASE EDITING METHODS AND COMPOSITIONS FOR TREATING TRIPLET REPEAT D...

GENE THERAPY FOR THE TREATMENT OF COGNITIVE DISORDERS

GENE EDITING TO IMPROVE JOINT FUNCTION

Compositions and Methods for Treating Striatonigral Degeneration

AAV VECTOR ENCODING ANTI-VEGF-A AND ANG-2 BISPECIFIC ANTIBODY

COMPOSITIONS AND METHODS FOR THE TREATMENT OF GLYCOGEN STORAGE DISO...

ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RET...

METHODS AND COMPOSITIONS FOR THE TREATMENT OF PARKINSON'S DISEASE

NOVEL ANELLOVIRIDAE FAMILY VECTOR COMPOSITIONS AND METHODS

ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL...

ULTRASOUND-MEDIATED GENE THERAPY FOR DEEP VEIN THROMBOSIS AND POST-...

TREATMENT REGIMENS FOR THERAPEUTIC EFFECTOR COMPONENTS THAT ACT VIA...

Intrathecal Delivery of Recombinant Adeno-Associated Virus 9

GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF

FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION

METHODS AND COMPOSITIONS FOR TREATING RBM20 RELATED CARDIOMYOPATHY...

DRUG AND METHOD FOR FORMING GABAERGIC NEURONS

CONSTRUCTS, VIRAL VECTORS AND PHARMACEUTICAL COMPOSITIONS COMPRISIN...

METHODS AND COMPOSITIONS FOR TREATING TMEM43 RELATED CARDIOMYOPATHY...

METHODS AND SYSTEMS FOR IMPROVED DELIVERY VIA ULTRASOUND

RETINAL PROTECTIVE FACTOR 2 (RPF2) PROTEIN DELIVERED BY ADENO-ASSOC...

METHODS OF TREATING OSMIDROSIS

VIRAL VECTORS ENCODING GLP-2 RECEPTOR AGONIST FUSIONS AND USES THER...

USING DREADD FOR NEURONAL MODULATION IN TREATING NEURONAL DISEASES