characterised by an aspect of the delivery route

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A61K48/0075

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

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A61K48/0075characterised by an aspect of the delivery route

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Patents Grantslast 30 patents

Information Patent Grant
Compositions and methods of treating ocular diseases
- Patent number 12,310,997
- Issue date May 27, 2025
- The Regents of the University of California
- David V. Schaffer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for modifying mucous membranes
- Patent number 12,303,607
- Issue date May 20, 2025
- Nicholas L. Abbott
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
AAV capsid variants and uses thereof
- Patent number 12,296,025
- Issue date May 13, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene editing to improve joint function
- Patent number 12,290,572
- Issue date May 6, 2025
- ORTHOBIO THERAPEUTICS, INC.
- Peter J. Millett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Riboswitch modulated gene therapy for retinal diseases
- Patent number 12,286,631
- Issue date Apr 29, 2025
- The Medical College of Wisconsin, Inc.
- Daniel M. Lipinski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lipid nanoparticle formulations for delivery of MRNA
- Patent number 12,280,117
- Issue date Apr 22, 2025
- Translate Bio, Inc.
- Frank DeRosa
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Recombinant adeno-associated viruses encoding serpin peptides and u...
- Patent number 12,274,757
- Issue date Apr 15, 2025
- University of Florida Research Foundation, Incorporated
- Alexandra Rose Lucas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Composition and methods for treatment of ornithine transcarbamylase...
- Patent number 12,268,754
- Issue date Apr 8, 2025
- Translate Bio, Inc.
- Kim Askew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for limb-girdle muscular dystrophy type 2C
- Patent number 12,263,230
- Issue date Apr 1, 2025
- Research Institute at Nationwide Children's Hospital
- Louise R. Rodino-Klapac
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus virions for treatment of epilepsy
- Patent number 12,263,231
- Issue date Apr 1, 2025
- Jichi Medical University
- Shin-ichi Muramatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating non-age-associated hearing im...
- Patent number 12,264,317
- Issue date Apr 1, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Adeno-associated virus vector delivery of a fragment of micro-dystr...
- Patent number 12,257,317
- Issue date Mar 25, 2025
- Newcastle University
- Hanns Lochmuller
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Polynucleotide compositions, related formulations, and methods of u...
- Patent number 12,257,318
- Issue date Mar 25, 2025
- ReCode Therapeutics, Inc.
- Mirko Hennig
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for NMNAT1-associated retinal degeneration
- Patent number 12,257,320
- Issue date Mar 25, 2025
- Massachusetts Eye and Ear Infirmary
- Eric A. Pierce
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for transient gene therapy with enhanced s...
- Patent number 12,258,560
- Issue date Mar 25, 2025
- Dana-Farber Cancer Institute, Inc.
- Michael Goldberg
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Closed-ended linear duplex DNA for non-viral gene transfer
- Patent number 12,252,703
- Issue date Mar 18, 2025
- UNIVERSITY OF MASSACHUSETTS
- Robert M. Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV vectors for retinal and CNS gene therapy
- Patent number 12,241,078
- Issue date Mar 4, 2025
- Genzyme Corporation
- Abraham Scaria
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and uses thereof
- Patent number 12,234,290
- Issue date Feb 25, 2025
- AVIDITY BIOSCIENCES, INC.
- Andrew John Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for eosinophilic disorders
- Patent number 12,226,492
- Issue date Feb 18, 2025
- Cornell University
- Ronald G. Crystal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Sulfamidase (SGSH) variants, vectors, compositions and methods and...
- Patent number 12,221,635
- Issue date Feb 11, 2025
- The Childeren's Hospital of Philadelphia
- Beverly L. Davidson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic applications of CPF1-based genome editing
- Patent number 12,214,056
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Intrathecal delivery of recombinant adeno-associated virus 9
- Patent number 12,208,144
- Issue date Jan 28, 2025
- Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for treatment of hereditary haemochromatosis
- Patent number 12,186,406
- Issue date Jan 7, 2025
- CRISPR THERAPEUTICS AG
- Roman Lvovitch Bogorad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Isoform Nell-1 peptide
- Patent number 12,186,367
- Issue date Jan 7, 2025
- The Regents of the University of California
- Kang Ting
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for recessive dystrophic epidermolysis bullosa using g...
- Patent number 12,173,314
- Issue date Dec 24, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Zurab Siprashvili
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Collagen-mimetic peptide mediated delivery of nucleic acid carriers...
- Patent number 12,171,809
- Issue date Dec 24, 2024
- University of Delaware
- Kristi Kiick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression vector for cholesterol 24-hydrolase in therapy of polygl...
- Patent number 12,138,298
- Issue date Nov 12, 2024
- BRAINVECTIS
- Sandro Alves
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for treating or alleviating a bone-loss related disease or...
- Patent number 12,133,896
- Issue date Nov 5, 2024
- Kaohsiung Medical University
- Chau-Zen Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunostimulating vector system
- Patent number 12,133,898
- Issue date Nov 5, 2024
- Provecs Medical GmbH
- Frank Schnieders
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy delivery of Parkin mutants having increased activity t...
- Patent number 12,133,897
- Issue date Nov 5, 2024
- NysnoBio GT Neurology, LLC
- Jennifer Johnston
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING ALPHA-SYNUCLEIN EXPRESSION
- Publication number 20250177568
- Publication date Jun 5, 2025
- The Board of Trustees of the Leland Stanford Junior University
- C. Alejandra Morato Torres
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RETROVIRAL VECTORS
- Publication number 20250177574
- Publication date Jun 5, 2025
- IP2IPO INNOVATIONS LIMITED
- Deborah R. Gill
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...
- Publication number 20250179450
- Publication date Jun 5, 2025
- The Board of Regents of the University of Texas System
- Yu ZHANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Adeno-Associated Viral (AAV)-Mediated Sphingosine-1-Phosphate Lyase...
- Publication number 20250177563
- Publication date Jun 5, 2025
- The Regents of the University of California
- Julie D. Saba
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS USEFUL IN TREATMENT OF METACHROMATIC LEUKODYSTROPHY
- Publication number 20250177495
- Publication date Jun 5, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Materials & Methods for Treatment of Macular Degeneration
- Publication number 20250177573
- Publication date Jun 5, 2025
- The University of Bristol
- Ying Kai Chan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLYOMAVIRAL GENE DELIVERY VECTOR PARTICLE COMPRISING A NUCLEIC ACI...
- Publication number 20250170272
- Publication date May 29, 2025
- AMARNA HOLDING B.V.
- Ferdy Rudolph Van Diemen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE DELIVERY VECTOR FOR DELIVERING HUMAN VEGF RECEPTOR FUSION PROT...
- Publication number 20250170276
- Publication date May 29, 2025
- Shanghai Correge Pharmaceutical Technology Co., Ltd.
- Lihui CHEN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VECTORS FOR DELIVERY OF GLP-1 RECEPTOR AGONIST FUSIONS
- Publication number 20250171515
- Publication date May 29, 2025
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
- Publication number 20250171544
- Publication date May 29, 2025
- Avidity Biosciences, Inc.
- Andrew John GEALL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250163458
- Publication date May 22, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...
- Publication number 20250161490
- Publication date May 22, 2025
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED TREATMENT OF...
- Publication number 20250161493
- Publication date May 22, 2025
- The Trustees of the University of Pennsylvania
- Lili Wang
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE EDITING TO IMPROVE JOINT FUNCTION
- Publication number 20250161487
- Publication date May 22, 2025
- Orthobio Therapeutics, Inc.
- Peter J. Millet
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CHIMERIC NEUROTROPIC AAV CAPSIDS
- Publication number 20250161486
- Publication date May 22, 2025
- The University of North Carolina at Chapel Hill
- Bin Xiao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR DECREASING PATHOLOGIC ALPHA-SYNUCLEIN USING AGENTS THAT...
- Publication number 20250161413
- Publication date May 22, 2025
- Dana-Farber Cancer Institute, Inc.
- Bruce M. Spiegelman
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20250161485
- Publication date May 22, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITION AND METHODS FOR TREATMENT OF ORNITHINE TRANSCARBAMYLASE...
- Publication number 20250152739
- Publication date May 15, 2025
- Translate Bio, Inc.
- Kim Askew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING GAUCHER DISEASE AND GBA-PARKINSON’S DISEASE
- Publication number 20250152747
- Publication date May 15, 2025
- Genzyme Corporation
- Swathi AYLOO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LIPID NANOPARTICLES COMPRISING VENEZUELAN EQUINE ENCEPHALITIS (VEE)...
- Publication number 20250152737
- Publication date May 15, 2025
- STRAND THERAPEUTICS INC.
- Ryan SOWELL
- B82 - NANO-TECHNOLOGY
Information Patent Application
HYDRODYNAMIC GENE DELIVERY
- Publication number 20250152748
- Publication date May 15, 2025
- Johns Hopkins University
- Robert L. Kruse
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Lipid Nanoparticle Compositions and Methods for mRNA Delivery
- Publication number 20250152735
- Publication date May 15, 2025
- Translate Bio, Inc.
- Frank DeRosa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING NEURODEGENERATIVE DISORDERS
- Publication number 20250152744
- Publication date May 15, 2025
- Genzyme Corporation
- Shyam RAMACHANDRAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FORMULATIONS TO ENHANCE THE DELIVERY OF GENE THERAPY VECTORS
- Publication number 20250144247
- Publication date May 8, 2025
- University of Iowa Research Foundation
- Ashley Cooney
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF ACQUIRED FOCAL EPILEPSY
- Publication number 20250144244
- Publication date May 8, 2025
- UCL Business LTD
- Matthew Charles WALKER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VEST...
- Publication number 20250136673
- Publication date May 1, 2025
- Akouos, Inc.
- Emmanuel John Simons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INJECTION OF SINGLE-STRANDED OR SELF-COMPLEMENTARY ADENO-ASSOCIATED...
- Publication number 20250135041
- Publication date May 1, 2025
- Emory University
- Anthony Donsante
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF
- Publication number 20250135040
- Publication date May 1, 2025
- Spacecraft Seven, LLC
- Christopher Dean HERZOG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING OCULAR NEOVASCULAR DISEASES USING AAV2 VARIANTS...
- Publication number 20250137011
- Publication date May 1, 2025
- Adverum Biotechnologies, Inc.
- Kelly Hanna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL IMMUNOSTIMULATING VECTOR SYSTEM
- Publication number 20250127931
- Publication date Apr 24, 2025
- Provecs Medical GmbH
- Frank Schnieders
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the delivery route

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compositions and methods of treating ocular diseases

Methods and compositions for modifying mucous membranes

AAV capsid variants and uses thereof

Gene editing to improve joint function

Riboswitch modulated gene therapy for retinal diseases

Lipid nanoparticle formulations for delivery of MRNA

Recombinant adeno-associated viruses encoding serpin peptides and u...

Composition and methods for treatment of ornithine transcarbamylase...

Gene therapy for limb-girdle muscular dystrophy type 2C

Adeno-associated virus virions for treatment of epilepsy

Compositions and methods for treating non-age-associated hearing im...

Adeno-associated virus vector delivery of a fragment of micro-dystr...

Polynucleotide compositions, related formulations, and methods of u...

Gene therapy for NMNAT1-associated retinal degeneration

Compositions and methods for transient gene therapy with enhanced s...

Closed-ended linear duplex DNA for non-viral gene transfer

AAV vectors for retinal and CNS gene therapy

Nucleic acid-polypeptide compositions and uses thereof

Gene therapy for eosinophilic disorders

Sulfamidase (SGSH) variants, vectors, compositions and methods and...

Therapeutic applications of CPF1-based genome editing

Intrathecal delivery of recombinant adeno-associated virus 9

Materials and methods for treatment of hereditary haemochromatosis

Isoform Nell-1 peptide

Gene therapy for recessive dystrophic epidermolysis bullosa using g...

Collagen-mimetic peptide mediated delivery of nucleic acid carriers...

Expression vector for cholesterol 24-hydrolase in therapy of polygl...

Methods for treating or alleviating a bone-loss related disease or...

Immunostimulating vector system

Gene therapy delivery of Parkin mutants having increased activity t...

Patents Applicationslast 30 patents

COMPOSITIONS AND METHODS FOR MODULATING ALPHA-SYNUCLEIN EXPRESSION

RETROVIRAL VECTORS

CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHEN...

Adeno-Associated Viral (AAV)-Mediated Sphingosine-1-Phosphate Lyase...

COMPOSITIONS USEFUL IN TREATMENT OF METACHROMATIC LEUKODYSTROPHY

Materials & Methods for Treatment of Macular Degeneration

POLYOMAVIRAL GENE DELIVERY VECTOR PARTICLE COMPRISING A NUCLEIC ACI...

GENE DELIVERY VECTOR FOR DELIVERING HUMAN VEGF RECEPTOR FUSION PROT...

AAV VECTORS FOR DELIVERY OF GLP-1 RECEPTOR AGONIST FUSIONS

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...

COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED TREATMENT OF...

GENE EDITING TO IMPROVE JOINT FUNCTION

CHIMERIC NEUROTROPIC AAV CAPSIDS

METHODS FOR DECREASING PATHOLOGIC ALPHA-SYNUCLEIN USING AGENTS THAT...

AAV CAPSID VARIANTS AND USES THEREOF

COMPOSITION AND METHODS FOR TREATMENT OF ORNITHINE TRANSCARBAMYLASE...

METHODS OF TREATING GAUCHER DISEASE AND GBA-PARKINSON’S DISEASE

LIPID NANOPARTICLES COMPRISING VENEZUELAN EQUINE ENCEPHALITIS (VEE)...

HYDRODYNAMIC GENE DELIVERY

Lipid Nanoparticle Compositions and Methods for mRNA Delivery

METHODS OF TREATING NEURODEGENERATIVE DISORDERS

FORMULATIONS TO ENHANCE THE DELIVERY OF GENE THERAPY VECTORS

TREATMENT OF ACQUIRED FOCAL EPILEPSY

ANTI-VEGF ANTIBODY CONSTRUCTS AND RELATED METHODS FOR TREATING VEST...

INJECTION OF SINGLE-STRANDED OR SELF-COMPLEMENTARY ADENO-ASSOCIATED...

ADENO-ASSOCIATED VIRAL VECTOR FOR GLUT1 EXPRESSION AND USES THEREOF

METHODS OF TREATING OCULAR NEOVASCULAR DISEASES USING AAV2 VARIANTS...

NOVEL IMMUNOSTIMULATING VECTOR SYSTEM