characterised by an aspect of the delivery route

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A61K48/0075

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AHUMAN NECESSITIES A61Medical science A61KPREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

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A61K48/0075characterised by an aspect of the delivery route

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Patents Grantslast 30 patents

Information Patent Grant
Adeno-associated virus vector delivery of a fragment of micro-dystr...
- Patent number 12,257,317
- Issue date Mar 25, 2025
- Newcastle University
- Hanns Lochmuller
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Polynucleotide compositions, related formulations, and methods of u...
- Patent number 12,257,318
- Issue date Mar 25, 2025
- ReCode Therapeutics, Inc.
- Mirko Hennig
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for NMNAT1-associated retinal degeneration
- Patent number 12,257,320
- Issue date Mar 25, 2025
- Massachusetts Eye and Ear Infirmary
- Eric A. Pierce
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for transient gene therapy with enhanced s...
- Patent number 12,258,560
- Issue date Mar 25, 2025
- Dana-Farber Cancer Institute, Inc.
- Michael Goldberg
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Closed-ended linear duplex DNA for non-viral gene transfer
- Patent number 12,252,703
- Issue date Mar 18, 2025
- UNIVERSITY OF MASSACHUSETTS
- Robert M. Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV vectors for retinal and CNS gene therapy
- Patent number 12,241,078
- Issue date Mar 4, 2025
- Genzyme Corporation
- Abraham Scaria
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-polypeptide compositions and uses thereof
- Patent number 12,234,290
- Issue date Feb 25, 2025
- AVIDITY BIOSCIENCES, INC.
- Andrew John Geall
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for eosinophilic disorders
- Patent number 12,226,492
- Issue date Feb 18, 2025
- Cornell University
- Ronald G. Crystal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Sulfamidase (SGSH) variants, vectors, compositions and methods and...
- Patent number 12,221,635
- Issue date Feb 11, 2025
- The Childeren's Hospital of Philadelphia
- Beverly L. Davidson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic applications of CPF1-based genome editing
- Patent number 12,214,056
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Intrathecal delivery of recombinant adeno-associated virus 9
- Patent number 12,208,144
- Issue date Jan 28, 2025
- Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for treatment of hereditary haemochromatosis
- Patent number 12,186,406
- Issue date Jan 7, 2025
- CRISPR THERAPEUTICS AG
- Roman Lvovitch Bogorad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Isoform Nell-1 peptide
- Patent number 12,186,367
- Issue date Jan 7, 2025
- The Regents of the University of California
- Kang Ting
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for recessive dystrophic epidermolysis bullosa using g...
- Patent number 12,173,314
- Issue date Dec 24, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Zurab Siprashvili
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Collagen-mimetic peptide mediated delivery of nucleic acid carriers...
- Patent number 12,171,809
- Issue date Dec 24, 2024
- University of Delaware
- Kristi Kiick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression vector for cholesterol 24-hydrolase in therapy of polygl...
- Patent number 12,138,298
- Issue date Nov 12, 2024
- BRAINVECTIS
- Sandro Alves
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for treating or alleviating a bone-loss related disease or...
- Patent number 12,133,896
- Issue date Nov 5, 2024
- Kaohsiung Medical University
- Chau-Zen Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunostimulating vector system
- Patent number 12,133,898
- Issue date Nov 5, 2024
- Provecs Medical GmbH
- Frank Schnieders
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy delivery of Parkin mutants having increased activity t...
- Patent number 12,133,897
- Issue date Nov 5, 2024
- NysnoBio GT Neurology, LLC
- Jennifer Johnston
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Lipid nanoparticle compositions and methods for mRNA delivery
- Patent number 12,121,592
- Issue date Oct 22, 2024
- Translate Bio, Inc.
- Frank DeRosa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and materials for GALGT2 gene therapy
- Patent number 12,121,595
- Issue date Oct 22, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for nucleic acid and protein payload delivery
- Patent number 12,123,012
- Issue date Oct 22, 2024
- LIGANDAL, INC.
- Andre Ronald Watson
- B82 - NANO-TECHNOLOGY
Information Patent Grant
Gene therapy for recessive dystrophic epidermolysis bullosa using g...
- Patent number 12,110,504
- Issue date Oct 8, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Zurab Siprashvili
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Satiation peptide administration
- Patent number 12,109,251
- Issue date Oct 8, 2024
- University of Florida Research Foundation, Incorporated
- Sergei Zolotukhin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for expressing proteins in axons
- Patent number 12,103,952
- Issue date Oct 1, 2024
- Cornell University
- Samie R. Jaffrey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for efficient delivery of therapeutic molecules in vitro an...
- Patent number 12,102,691
- Issue date Oct 1, 2024
- Massachusetts Eye and Ear Infirmary
- Zheng-Yi Chen
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods and compositions for treatment of ocular disorders and blin...
- Patent number 12,097,267
- Issue date Sep 24, 2024
- The Trustees of the University of Pennsylvania
- Jeannette Bennicelli
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
System and method for controlling oxygen delivery to implanted cells
- Patent number 12,090,300
- Issue date Sep 17, 2024
- Giner, Inc.
- Simon G. Stone
- C25 - ELECTROLYTIC OR ELECTROPHORETIC PROCESSES APPARATUS THEREFOR
Information Patent Grant
Rabies vaccine
- Patent number 12,083,190
- Issue date Sep 10, 2024
- CureVac SE
- Margit Schnee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
System for gas treatment of a cell implant
- Patent number 12,070,383
- Issue date Aug 27, 2024
- Giner, Inc.
- Linda Tempelman
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
METHODS AND COMPOSITIONS FOR THE TREATMENT OF RARE DISEASES
- Publication number 20250099624
- Publication date Mar 27, 2025
- Sangamo Therapeutics, Inc.
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SATIATION PEPTIDE ADMINISTRATION
- Publication number 20250099546
- Publication date Mar 27, 2025
- University of Florida Research Foundation, Incorporated
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TARGETED DELIVERY OF MODIFIED RNA
- Publication number 20250099367
- Publication date Mar 27, 2025
- The Chinese University of Hong Kong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED AAV CAPSID PROTEIN AND USE THEREOF
- Publication number 20250101386
- Publication date Mar 27, 2025
- CHENGDU ORIGEN BIOTECHNOLOGY CO., LTD.
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LYMPHANGIOGENESIS-PROMOTING AGENTS
- Publication number 20250090634
- Publication date Mar 20, 2025
- AnGes, Inc.
- RYUICHI MORISHITA
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
EXPRESSION VECTOR FOR CHOLESTEROL 24-HYDROLASE IN THERAPY OF POLYGL...
- Publication number 20250090641
- Publication date Mar 20, 2025
- BRAINVECTIS
- Sandro ALVES
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
POLYNUCLEOTIDES ENCODING GLUCOSE-6-PHOSPHATASE FOR THE TREATMENT OF...
- Publication number 20250090684
- Publication date Mar 20, 2025
- ModernaTX, Inc.
- Husain Attarwala
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS OF EX VIVO DOSING AND ADMINISTRATION OF LIPID PARTICLES OR...
- Publication number 20250082777
- Publication date Mar 13, 2025
- Sana Biotechnology, Inc.
- Aaron Edward FOSTER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTORS
- Publication number 20250084436
- Publication date Mar 13, 2025
- University of Pittsburgh of the Commonwealth System of Higher Education
- Leah Caroline THOMAS BYRNE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF ONCOLOGY-RELATED PRO...
- Publication number 20250074962
- Publication date Mar 6, 2025
- ModernaTX, Inc.
- Antonin DE FOUGEROLLES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPROVED COMPOSITIONS FOR DELIVERY OF MRNA
- Publication number 20250073351
- Publication date Mar 6, 2025
- Translate Bio, Inc.
- Shrirang KARVE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING G...
- Publication number 20250075178
- Publication date Mar 6, 2025
- The Board of Trustees of the Leland Stanford Junior University
- Zurab Siprashvili
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FACTOR VIII (FVIII) GENE THERAPY METHODS
- Publication number 20250073353
- Publication date Mar 6, 2025
- Spark Therapeutics, Inc.
- Xavier ANGUELA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY METHODS FOR TREATMENT OF DIABETES
- Publication number 20250064978
- Publication date Feb 27, 2025
- Jaguar Gene Therapy, LLC
- Michael Hughes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Nucleic Acid-Based Compositions and Methods for Treating Small Vess...
- Publication number 20250064977
- Publication date Feb 27, 2025
- The Schepens Eye Research Institute, Inc.
- Joseph F. Arboleda-Velasquez
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF
- Publication number 20250064981
- Publication date Feb 27, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GLUCAGON PROMOTER FOR DIABETES GENE THERAPY
- Publication number 20250066444
- Publication date Feb 27, 2025
- University of Pittsburgh of the Commonwealth System of Higher Education
- George Gittes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treatment of Ocular Disease Associated...
- Publication number 20250057987
- Publication date Feb 20, 2025
- 4D MOLECULAR THERAPEUTICS INC.
- Christian BURNS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY DELIVERY OF PARKIN MUTANTS HAVING INCREASED ACTIVITY T...
- Publication number 20250049958
- Publication date Feb 13, 2025
- NysnoBio GT Neurology, LLC
- Jennifer JOHNSTON
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF
- Publication number 20250041450
- Publication date Feb 6, 2025
- Insmed Incorporated
- Brian KASPAR
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
USE OF ADENO-ASSOCIATED VIRAL VECTORS TO CORRECT GENE DEFECTS/ EXPR...
- Publication number 20250041457
- Publication date Feb 6, 2025
- Akouos, Inc.
- Emmanuel John Simons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
- Publication number 20250041445
- Publication date Feb 6, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYNTHETIC RECEPTORS
- Publication number 20250032643
- Publication date Jan 30, 2025
- UCL Business LTD
- Dimitri KULLMANN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Compositions and Methods for Cell-Specific Expression of Target Genes
- Publication number 20250025575
- Publication date Jan 23, 2025
- The Trustees of Princeton University
- Carola Maturana
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR GALGT2 GENE THERAPY
- Publication number 20250025578
- Publication date Jan 23, 2025
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treatment of Diseases Associated with...
- Publication number 20250025580
- Publication date Jan 23, 2025
- INTELLIA THERAPEUTICS, INC.
- Sean Michael Burns
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FUNCTIONAL AAV CAPSIDS FOR INTRAVITREAL ADMINISTRATION
- Publication number 20250026795
- Publication date Jan 23, 2025
- Shape Therapeutics Inc.
- Thomas PACKARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD FOR DECREASING DEGENERATION OF RETINAL GANGLION CELLS
- Publication number 20250018058
- Publication date Jan 16, 2025
- Icahn School of Medicine at Mount Sinai
- Bo CHEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF BIOLOGICS AND PROTEI...
- Publication number 20250018062
- Publication date Jan 16, 2025
- Moderna TX, Inc.
- Antonin DE FOUGEROLLES
- Y02 - TECHNOLOGIES OR APPLICATIONS FOR MITIGATION OR ADAPTATION AGAINST CLIMA...
Information Patent Application
POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...
- Publication number 20250019409
- Publication date Jan 16, 2025
- ReCode Therapeutics, Inc.
- Mirko Hennig
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

characterised by an aspect of the delivery route

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Adeno-associated virus vector delivery of a fragment of micro-dystr...

Polynucleotide compositions, related formulations, and methods of u...

Gene therapy for NMNAT1-associated retinal degeneration

Compositions and methods for transient gene therapy with enhanced s...

Closed-ended linear duplex DNA for non-viral gene transfer

AAV vectors for retinal and CNS gene therapy

Nucleic acid-polypeptide compositions and uses thereof

Gene therapy for eosinophilic disorders

Sulfamidase (SGSH) variants, vectors, compositions and methods and...

Therapeutic applications of CPF1-based genome editing

Intrathecal delivery of recombinant adeno-associated virus 9

Materials and methods for treatment of hereditary haemochromatosis

Isoform Nell-1 peptide

Gene therapy for recessive dystrophic epidermolysis bullosa using g...

Collagen-mimetic peptide mediated delivery of nucleic acid carriers...

Expression vector for cholesterol 24-hydrolase in therapy of polygl...

Methods for treating or alleviating a bone-loss related disease or...

Immunostimulating vector system

Gene therapy delivery of Parkin mutants having increased activity t...

Lipid nanoparticle compositions and methods for mRNA delivery

Methods and materials for GALGT2 gene therapy

Methods and compositions for nucleic acid and protein payload delivery

Gene therapy for recessive dystrophic epidermolysis bullosa using g...

Satiation peptide administration

Methods for expressing proteins in axons

Methods for efficient delivery of therapeutic molecules in vitro an...

Methods and compositions for treatment of ocular disorders and blin...

System and method for controlling oxygen delivery to implanted cells

Rabies vaccine

System for gas treatment of a cell implant

Patents Applicationslast 30 patents

METHODS AND COMPOSITIONS FOR THE TREATMENT OF RARE DISEASES

SATIATION PEPTIDE ADMINISTRATION

TARGETED DELIVERY OF MODIFIED RNA

MODIFIED AAV CAPSID PROTEIN AND USE THEREOF

LYMPHANGIOGENESIS-PROMOTING AGENTS

EXPRESSION VECTOR FOR CHOLESTEROL 24-HYDROLASE IN THERAPY OF POLYGL...

POLYNUCLEOTIDES ENCODING GLUCOSE-6-PHOSPHATASE FOR THE TREATMENT OF...

METHODS OF EX VIVO DOSING AND ADMINISTRATION OF LIPID PARTICLES OR...

ADENO-ASSOCIATED VIRUS VECTORS

MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF ONCOLOGY-RELATED PRO...

IMPROVED COMPOSITIONS FOR DELIVERY OF MRNA

GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING G...

FACTOR VIII (FVIII) GENE THERAPY METHODS

GENE THERAPY METHODS FOR TREATMENT OF DIABETES

Nucleic Acid-Based Compositions and Methods for Treating Small Vess...

AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF

GLUCAGON PROMOTER FOR DIABETES GENE THERAPY

Compositions and Methods for Treatment of Ocular Disease Associated...

GENE THERAPY DELIVERY OF PARKIN MUTANTS HAVING INCREASED ACTIVITY T...

ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF

USE OF ADENO-ASSOCIATED VIRAL VECTORS TO CORRECT GENE DEFECTS/ EXPR...

GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

SYNTHETIC RECEPTORS

Compositions and Methods for Cell-Specific Expression of Target Genes

METHODS AND MATERIALS FOR GALGT2 GENE THERAPY

Compositions and Methods for Treatment of Diseases Associated with...

FUNCTIONAL AAV CAPSIDS FOR INTRAVITREAL ADMINISTRATION

METHOD FOR DECREASING DEGENERATION OF RETINAL GANGLION CELLS

MODIFIED POLYNUCLEOTIDES FOR THE PRODUCTION OF BIOLOGICS AND PROTEI...

POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...