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characterised by an aspect of the delivery route
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A61K48/0075
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HUMAN NECESSITIES
A61
Medical science
A61K
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
A61K48/00
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy
Current Industry
A61K48/0075
characterised by an aspect of the delivery route
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Patents Grants
last 30 patents
Information
Patent Grant
Gene therapy for neurometabolic disorders
Patent number
11,957,765
Issue date
Apr 16, 2024
Genzyme Corporation
Marco A. Passini
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Lipid nanoparticle compositions and methods for MRNA delivery
Patent number
11,951,180
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Lipid nanoparticle compositions and methods for mRNA delivery
Patent number
11,951,181
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Lipid nanoparticle compositions and methods for MRNA delivery
Patent number
11,951,179
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Biologically active compounds
Patent number
11,944,688
Issue date
Apr 2, 2024
SUTURA THERAPEUTICS LTD
Keith Foster
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Polynucleotides encoding phenylalanine hydroxylase for the treatmen...
Patent number
11,939,601
Issue date
Mar 26, 2024
ModernaTX, Inc.
Raj Rajendran
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Therapeutical tools and methods for treating blindness by targeting...
Patent number
11,931,427
Issue date
Mar 19, 2024
FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
Josephine Juettner
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Methods and materials for NT-3 gene therapy
Patent number
11,926,653
Issue date
Mar 12, 2024
Research Institute at Nationwide Children's Hospital
Zarife Sahenk
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Gene therapy for neurodegenerative disorders
Patent number
11,911,440
Issue date
Feb 27, 2024
Genzyme Corporation
Marco A. Passini
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Hydrodynamic methods for delivering fluids to kidney tissues and re...
Patent number
11,911,487
Issue date
Feb 27, 2024
Indiana University Research and Technology Corporation
Robert Bacallao
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Expression cassette with a SynP160 promoter
Patent number
11,883,507
Issue date
Jan 30, 2024
FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
Dominik Hartl
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Gene therapy for AADC deficiency
Patent number
11,865,188
Issue date
Jan 9, 2024
NATIONAL TAIWAN UNIVERSITY
Mark Pykett
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Recombinant adeno-associated vectors for targeted treatment
Patent number
11,833,226
Issue date
Dec 5, 2023
City of Hope
Saswati Chatterjee
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Gene therapy for ocular disorders
Patent number
11,827,898
Issue date
Nov 28, 2023
The Trustees of the University of Pennsylvania
Jean Bennett
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Gene therapy for the regeneration of chondrocytes or cartilage type...
Patent number
11,819,555
Issue date
Nov 21, 2023
Figene, LLC
Pete O'Heeron
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Selective gene therapy expression system
Patent number
11,819,478
Issue date
Nov 21, 2023
Genethon
Ana Maria Buj Bello
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Recombinant expression vector and lipid membrane structure having s...
Patent number
11,814,640
Issue date
Nov 14, 2023
LUCA Science Inc.
Hideyoshi Harashima
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Gene therapies for lysosomal disorders
Patent number
11,807,849
Issue date
Nov 7, 2023
Prevail Therapeutics, Inc.
Asa Abeliovich
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Methods and compositions for treating cone-rod retinal dystrophy
Patent number
11,806,408
Issue date
Nov 7, 2023
University of Florida Research Foundation, Incorporated
Shannon E. Boye
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Codon optimized GLA genes and uses thereof
Patent number
11,802,278
Issue date
Oct 31, 2023
David H. Kirn
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
RNA containing modified nucleosides and methods of use thereof
Patent number
11,801,314
Issue date
Oct 31, 2023
The Trustees of the University of Pennsylvania
Katalin Kariko
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Methods for selective kinase inhibition by endogenously produced an...
Patent number
11,793,889
Issue date
Oct 24, 2023
KINASE PHARMA INC.
Bradley G Thompson
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
ELOVL2 constructs for human gene therapy
Patent number
11,793,890
Issue date
Oct 24, 2023
Visgenx, Inc.
Christopher Chavez
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Compositions and methods for treating non-age-associated hearing im...
Patent number
11,781,145
Issue date
Oct 10, 2023
Akouos, Inc.
Emmanuel John Simons
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Using DREADD for neuronal modulation in treating neuronal diseases
Patent number
11,771,778
Issue date
Oct 3, 2023
Fadi Assaf
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Treatments for retinal disease
Patent number
11,766,487
Issue date
Sep 26, 2023
4D MOLECULAR THERAPEUTICS INC.
David H. Kirn
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Adeno-associated virus variant capsids and use for inhibiting angio...
Patent number
11,766,489
Issue date
Sep 26, 2023
4D Molecular Therapeutics, Inc.
David H. Kirn
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
Patent number
11,759,506
Issue date
Sep 19, 2023
VOYAGER THERAPEUTICS, INC.
Maria Scheel
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
AAV-mediated delivery of ATP1A3 genes to central nervous system
Patent number
11,738,093
Issue date
Aug 29, 2023
Hope for Annabel
Simon Frost
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
RNA preparations comprising purified modified RNA for reprogramming...
Patent number
11,739,300
Issue date
Aug 29, 2023
Katalin Kariko
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Patents Applications
last 30 patents
Information
Patent Application
COMPOSITIONS AND METHODS FOR TREATMENT OF NIEMANN PICK TYPE A DISEASE
Publication number
20240115733
Publication date
Apr 11, 2024
The Trustees of the University of Pennsylvania
James M. WILSON
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR DOPAMINE TRANSPORTER DEFICIENCY SYNDROME
Publication number
20240115737
Publication date
Apr 11, 2024
UCL Business LTD
Joanna NG
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS AND COMPOSITIONS FOR TREATMENT OF CYSTIC FIBROSIS
Publication number
20240115738
Publication date
Apr 11, 2024
Spirovant Sciences, Inc.
Mark SMITH
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
TREATMENT OF MUCOPOLYSACCHARIDOSIS II WITH RECOMBINANT HUMAN IDURON...
Publication number
20240117328
Publication date
Apr 11, 2024
Regenxbio Inc.
Stephen Joseph PAKOLA
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
INJECTION OF SINGLE-STRANDED OR SELF-COMPLEMENTARY ADENO-ASSOCIATED...
Publication number
20240108761
Publication date
Apr 4, 2024
Emory University
Anthony Donsante
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
NUCLEIC ACID TRANSPORTERS IN NANOCHAIN FORM, PREPARATION METHOD THE...
Publication number
20240108759
Publication date
Apr 4, 2024
ELBIO INC
Jong Hoon CHUNG
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
Self-complementary AAV vectors carrying dominant negative RhoA and...
Publication number
20240100193
Publication date
Mar 28, 2024
IVIEW Therapeutics, Inc.
Terete Borras
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
ADENO-ASSOCIATED VIRAL VECTOR VARIANTS
Publication number
20240100194
Publication date
Mar 28, 2024
The Children's Hospital of Philadelphia
Beverly DAVIDSON
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR AADC DEFICIENCY
Publication number
20240100186
Publication date
Mar 28, 2024
National Taiwan University
Mark Pykett
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR NEURONAL CEROID LIPOFUSCINOSES
Publication number
20240091380
Publication date
Mar 21, 2024
Regenxbio Inc.
Marie-Laure Nevoret
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
Systemic Delivery of Polypeptides
Publication number
20240091384
Publication date
Mar 21, 2024
President and Fellows of Harvard College
Denitsa M. Milanova
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
EXPRESSION OF THE HUMAN LEKTI GENE FROM THE CHROMOSOME OF STAPHYLOC...
Publication number
20240092869
Publication date
Mar 21, 2024
Azitra Inc
Trudy H. Grossman
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
METHODS AND COMPOSITIONS FOR MODIFYING MUCOUS MEMBRANES
Publication number
20240082170
Publication date
Mar 14, 2024
Nicholas L. Abbott
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
METHOD OF GENE DELIVERY TO RETINAL ASTROCYTES
Publication number
20240075167
Publication date
Mar 7, 2024
The Board of Trustees of the Leland Stanford Junior University
Jeffrey L. Goldberg
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
ELECTROTRANSFER METHODS FOR TREATING TUMORS
Publication number
20240075145
Publication date
Mar 7, 2024
University of South Florida
Loree C. HELLER
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
METHODS AND DEVICES FOR DELIVERING AGENTS TO THE RESPIRATORY SYSTEM
Publication number
20240074775
Publication date
Mar 7, 2024
WOMEN'S AND CHILDREN'S LOCAL HEALTH NETWORK INC.
Martin DONNELLEY
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
GENE THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA USING G...
Publication number
20240067926
Publication date
Feb 29, 2024
The Board of Trustees of the Leland Stanford Junior University
Zurab Siprashvili
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS OF TREATING EYE DISEASES
Publication number
20240066151
Publication date
Feb 29, 2024
Visgenx, Inc.
Christopher Chavez
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS WITH IMPROVED RETINAL TRANSD...
Publication number
20240066145
Publication date
Feb 29, 2024
4D MOLECULAR THERAPEUTICS INC.
David H. KIRN
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
Adeno-Associated Virus Factor VIII Vectors, Associated Viral Partic...
Publication number
20240058423
Publication date
Feb 22, 2024
BioMarin Pharmaceutical Inc.
Stuart Bunting
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
TREATMENT OF NEUROLOGICAL DISEASES
Publication number
20240050589
Publication date
Feb 15, 2024
Haibo ZHOU
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
METHODS OF TREATING AGE-RELATED MACULAR DISEASES USING AIMP2-DX2 AN...
Publication number
20240050527
Publication date
Feb 15, 2024
Generoath Co., Ltd
Jin Woo CHOI
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
Gene Therapy For Neurodegenerative Disorders
Publication number
20240033323
Publication date
Feb 1, 2024
Genzyme Corporation
Marco A. PASSINI
C07 - ORGANIC CHEMISTRY
Information
Patent Application
TREATMENT OF DANON DISEASE
Publication number
20240033325
Publication date
Feb 1, 2024
Spacecraft Seven, LLC
Jose M. TREVEJO
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
COMPOSITIONS USEFUL FOR TREATING SPINAL AND BULBAR MUSCULAR ATROPHY...
Publication number
20240033375
Publication date
Feb 1, 2024
The Trustees of the University of Pennsylvania
Eileen Workman
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
METHODS AND COMPOSITIONS FOR CONSISTENT INTRACORONARY ADMINISTRATIO...
Publication number
20240024635
Publication date
Jan 25, 2024
Sardocor Corp.
Brian Jaski
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I
Publication number
20240024510
Publication date
Jan 25, 2024
The Trustees of The University of Pennsylania
Christian Hinderer
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
MRNA THERAPEUTIC COMPOSITIONS AND USE TO TREAT DISEASES AND DISORDERS
Publication number
20240024516
Publication date
Jan 25, 2024
Translate Bio, Inc.
Michael Heartlein
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR TREATING CEREBROSPINAL FLUID DISORDERS
Publication number
20240024509
Publication date
Jan 25, 2024
The Children's Medical Center Corporation
Maria K. LEHTINEN
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-SYNUCLEIN AGGREGATION
Publication number
20240025953
Publication date
Jan 25, 2024
Seelos Therapeutics, Inc.
Raj Mehra
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...