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CPC
C12N2310/341

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

Current Industry

C12N2310/341Gapmers

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Compounds and methods for reducing ATXN3 expression
- Patent number 12,350,285
- Issue date Jul 8, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric double-stranded nucleic acid
- Patent number 12,344,841
- Issue date Jul 1, 2025
- National University Corporation Tokyo Medical and Dental University
- Takanori Yokota
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of gene transcription using antisense oligonucleotides t...
- Patent number 12,319,916
- Issue date Jun 3, 2025
- CAMP4 THERAPEUTICS CORPORATION
- Alfica Sehgal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
BBB-crossing lipid ligand of hetero nucleic acid
- Patent number 12,305,169
- Issue date May 20, 2025
- National University Corporation Tokyo Medical and Dental University
- Takanori Yokota
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...
- Patent number 12,303,525
- Issue date May 20, 2025
- Hoffman-La Roche Inc.
- Susanne Kammler
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Modulation of huntingtin expression
- Patent number 12,297,431
- Issue date May 13, 2025
- Ionis Pharmaceuticals, Inc.
- Gene Hung
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating apolipoprotein (a) expression
- Patent number 12,291,709
- Issue date May 6, 2025
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Oral delivery of antisense conjugates targeting PCSK9
- Patent number 12,291,708
- Issue date May 6, 2025
- CiVi Biopharma, Inc.
- Henrik Oerum
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Antisense oligonucleotide targeting ATN1 mRNA or pre-mRNA
- Patent number 12,291,710
- Issue date May 6, 2025
- Nippon Shinyaku Co., Ltd.
- Takao Kawano
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compounds and methods for reducing prion expression
- Patent number 12,281,305
- Issue date Apr 22, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of improving anemias by combining agents
- Patent number 12,263,205
- Issue date Apr 1, 2025
- The Children's Hospital of Philadelphia
- Stefano Rivella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides for inducing paternal UBE3A expression
- Patent number 12,259,380
- Issue date Mar 25, 2025
- HOFFMANN-LA ROCHE INC.
- Veronica Costa
- G01 - MEASURING TESTING
Information Patent Grant
Compounds and methods for reducing LRRK2 expression
- Patent number 12,241,067
- Issue date Mar 4, 2025
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides targeting alpha-synuclein and uses thereof
- Patent number 12,241,065
- Issue date Mar 4, 2025
- Bristol-Myers Squibb Company
- Richard E. Olson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic oligonucleotides
- Patent number 12,234,455
- Issue date Feb 25, 2025
- IFOM Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d′Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating cancer and/or enhancing sensitivity to cancer t...
- Patent number 12,234,459
- Issue date Feb 25, 2025
- Mark David Vincent
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating SCN2A
- Patent number 12,227,746
- Issue date Feb 18, 2025
- Ionis Pharmaceuticals, Inc.
- Paymaan Jafar-nejad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of diacyglycerol acyltransferase 2 (DGAT2)
- Patent number 12,215,321
- Issue date Feb 4, 2025
- Ionis Pharmaceuticals, Inc.
- Eric E. Swayze
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating ATXN1
- Patent number 12,180,479
- Issue date Dec 31, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Angelman syndrome antisense treatment
- Patent number 12,180,480
- Issue date Dec 31, 2024
- The Texas A&M University System
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...
- Patent number 12,163,132
- Issue date Dec 10, 2024
- Children's National Medical Center
- Yi-Wen Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating neuronal excitability and m...
- Patent number 12,163,130
- Issue date Dec 10, 2024
- Icahn School of Medicine at Mount Sinai
- Anne Schaefer
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Oligonucleotides for modulating Tau expression
- Patent number 12,163,131
- Issue date Dec 10, 2024
- HOFFMANN-LA ROCHE INC.
- Peter Hagedorn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulating the cellular stress response
- Patent number 12,157,888
- Issue date Dec 3, 2024
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of MALAT1 expression
- Patent number 12,157,890
- Issue date Dec 3, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective antisense compounds and uses thereof
- Patent number 12,152,244
- Issue date Nov 26, 2024
- Ionis Pharmaceuticals, Inc.
- Michael Oestergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeting human satellite II (HSATII)
- Patent number 12,152,241
- Issue date Nov 26, 2024
- The General Hospital Corporation
- David T. Ting
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compositions for treating pain via multiple targets
- Patent number 12,152,243
- Issue date Nov 26, 2024
- QUELLTX, INC.
- Graham T. Dempsey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating UBE3A-ATS
- Patent number 12,129,466
- Issue date Oct 29, 2024
- Ionis Pharmaceuticals, Inc.
- Paymaan Jafar-nejad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
Selective Reduction of Allelic Variants
- Publication number 20250223589
- Publication date Jul 10, 2025
- Ionis Pharmaceuticals, Inc.
- C. Frank Bennett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE NUCLEIC ACID CAPABLE OF INHIBITING BIOSYNTHESIS OF CHONDR...
- Publication number 20250223596
- Publication date Jul 10, 2025
- Aichi Medical University
- Kosei TAKEUCHI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYF2 ANTISENSE OLIGONUCLEOTIDES
- Publication number 20250223591
- Publication date Jul 10, 2025
- AcuraStem Incorported
- Emily Elizabeth LEE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS...
- Publication number 20250207128
- Publication date Jun 26, 2025
- Alnylam Pharmaceuticals, Inc.
- Gregory Hinkle
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS...
- Publication number 20250197856
- Publication date Jun 19, 2025
- Takeda Pharmaceuticals U.S.A. Inc.
- Irina ANTONIJEVIC
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF
- Publication number 20250188463
- Publication date Jun 12, 2025
- Bristol-Myers Squibb Company
- Richard E. OLSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HETERONUCLEIC ACID INCLUDING 2'-MODIFIED NUCLEOSIDE
- Publication number 20250179486
- Publication date Jun 5, 2025
- NATIONAL UNIVERSITY CORPORATION TOKYO MEDICAL AND DENTAL UNIVERSITY
- Takanori Yokota
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER T...
- Publication number 20250179501
- Publication date Jun 5, 2025
- Mark David Vincent
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS
- Publication number 20250163419
- Publication date May 22, 2025
- QUELLTX, INC.
- Graham T. Dempsey
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Composition and Methods for Modulating Nuclear Enriched Abundant Tr...
- Publication number 20250136983
- Publication date May 1, 2025
- MUSC Foundation for Research Development
- Hongkuan Fan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATION OF ALPHA SYNUCLEIN EXPRESSION
- Publication number 20250136982
- Publication date May 1, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORS OF MALAT1 EXPRESSION
- Publication number 20250136986
- Publication date May 1, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD FOR REDUCING HEPATIC TRIGLYCERIDES
- Publication number 20250129370
- Publication date Apr 24, 2025
- ADAERATA, LIMITED PARTNERSHIP
- Nabil G. SEIDAH
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
- Publication number 20250122505
- Publication date Apr 17, 2025
- Alnyiam Pharmaceuticals, Inc.
- Brian Bettencourt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMBINATIONS WITH MODULATORS OF PNPLA3 EXPRESSION
- Publication number 20250122504
- Publication date Apr 17, 2025
- AstraZeneca AB
- Daniel LINDÉN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS FOR INHIBITING AMANZI
- Publication number 20250115909
- Publication date Apr 10, 2025
- LEMBA BV
- Ezio Fok
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
- Publication number 20250116656
- Publication date Apr 10, 2025
- HOFFMANN-LA ROCHE INC.
- Veronica COSTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS FOR INHIBITION OF IL-1BETA EXPRESSION
- Publication number 20250115914
- Publication date Apr 10, 2025
- LEMBA BV
- Makiri Kawasaki
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATING THE CELLULAR STRESS RESPONSE
- Publication number 20250115910
- Publication date Apr 10, 2025
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6
- Publication number 20250115904
- Publication date Apr 10, 2025
- LONZA SALES AG
- Dalia BURZYN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTIONS
- Publication number 20250092401
- Publication date Mar 20, 2025
- GlaxoSmithKline Intellectual Property Development Limited
- Jared Loren DELAHAYE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PIKFYVE ANTISENSE OLIGONUCLEOTIDES
- Publication number 20250092404
- Publication date Mar 20, 2025
- AcuraStem Incorporated
- Wen-Hsuan CHANG
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Modified Oligonucleotides and Methods of Use
- Publication number 20250092400
- Publication date Mar 20, 2025
- Janssen Pharmaceutica N.V.
- Sergei GRYAZNOV
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS OF TREATMENT OF SCN2A-RELATED DISORDERS
- Publication number 20250092405
- Publication date Mar 20, 2025
- PRAXIS PRECISION MEDICINES, INC.
- William Motel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...
- Publication number 20250075215
- Publication date Mar 6, 2025
- Icahn School of Medicine at Mount Sinai
- Anne SCHAEFER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ACVR1R206H ALLELE-SPECIFIC THERAPY AND USES THEREOF FOR TREATMENT O...
- Publication number 20250066795
- Publication date Feb 27, 2025
- Oligomicstx Inc.
- Toshifumi YOKOTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC OLIGONUCLEOTIDES
- Publication number 20250066784
- Publication date Feb 27, 2025
- IFOM - Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d'Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORS OF APOL1 EXPRESSION
- Publication number 20250066785
- Publication date Feb 27, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANGELMAN SYNDROME ANTISENSE TREATMENT
- Publication number 20250066786
- Publication date Feb 27, 2025
- THE TEXAS A&M UNIVERSITY SYSTEM
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
- Publication number 20250066775
- Publication date Feb 27, 2025
- WAVE LIFE SCIENCES LTD.
- Chandra Vargeese
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compounds and methods for reducing ATXN3 expression

Chimeric double-stranded nucleic acid

Modulation of gene transcription using antisense oligonucleotides t...

BBB-crossing lipid ligand of hetero nucleic acid

Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...

Modulation of huntingtin expression

Compositions and methods for modulating apolipoprotein (a) expression

Oral delivery of antisense conjugates targeting PCSK9

Antisense oligonucleotide targeting ATN1 mRNA or pre-mRNA

Compounds and methods for reducing prion expression

Methods of improving anemias by combining agents

Oligonucleotides for inducing paternal UBE3A expression

Compounds and methods for reducing LRRK2 expression

Antisense oligonucleotides targeting alpha-synuclein and uses thereof

Therapeutic oligonucleotides

Methods of treating cancer and/or enhancing sensitivity to cancer t...

Compounds and methods for modulating SCN2A

Modulators of diacyglycerol acyltransferase 2 (DGAT2)

Compounds and methods for modulating ATXN1

Angelman syndrome antisense treatment

Modulators of APOL1 expression

Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...

Compositions and methods for modulating neuronal excitability and m...

Oligonucleotides for modulating Tau expression

Modulating the cellular stress response

Modulators of MALAT1 expression

Selective antisense compounds and uses thereof

Targeting human satellite II (HSATII)

Therapeutic compositions for treating pain via multiple targets

Compounds and methods for modulating UBE3A-ATS

Patents Applicationslast 30 patents

Selective Reduction of Allelic Variants

ANTISENSE NUCLEIC ACID CAPABLE OF INHIBITING BIOSYNTHESIS OF CHONDR...

SYF2 ANTISENSE OLIGONUCLEOTIDES

POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS...

METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS...

ANTISENSE OLIGONUCLEOTIDES TARGETING ALPHA-SYNUCLEIN AND USES THEREOF

HETERONUCLEIC ACID INCLUDING 2'-MODIFIED NUCLEOSIDE

METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER T...

THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS

Composition and Methods for Modulating Nuclear Enriched Abundant Tr...

MODULATION OF ALPHA SYNUCLEIN EXPRESSION

MODULATORS OF MALAT1 EXPRESSION

METHOD FOR REDUCING HEPATIC TRIGLYCERIDES

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

COMBINATIONS WITH MODULATORS OF PNPLA3 EXPRESSION

COMPOUNDS FOR INHIBITING AMANZI

OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION

COMPOUNDS FOR INHIBITION OF IL-1BETA EXPRESSION

MODULATING THE CELLULAR STRESS RESPONSE

EXTRACELLULAR VESICLE-ASO CONSTRUCTS TARGETING STAT6

COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTIONS

PIKFYVE ANTISENSE OLIGONUCLEOTIDES

Modified Oligonucleotides and Methods of Use

METHODS OF TREATMENT OF SCN2A-RELATED DISORDERS

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...

ACVR1R206H ALLELE-SPECIFIC THERAPY AND USES THEREOF FOR TREATMENT O...

THERAPEUTIC OLIGONUCLEOTIDES

MODULATORS OF APOL1 EXPRESSION

ANGELMAN SYNDROME ANTISENSE TREATMENT

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF