Gapmers

Industry

CPC
C12N2310/341

This industry / category may be too specific. Please go to a parent level for more data

Parent Industries

CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

Current Industry

C12N2310/341Gapmers

Industries

Please log in for detailed analytics

Patents Grantslast 30 patents

Information Patent Grant
Oligonucleotides for inducing paternal UBE3A expression
- Patent number 12,259,380
- Issue date Mar 25, 2025
- HOFFMANN-LA ROCHE INC.
- Veronica Costa
- G01 - MEASURING TESTING
Information Patent Grant
Compounds and methods for reducing LRRK2 expression
- Patent number 12,241,067
- Issue date Mar 4, 2025
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides targeting alpha-synuclein and uses thereof
- Patent number 12,241,065
- Issue date Mar 4, 2025
- Bristol-Myers Squibb Company
- Richard E. Olson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic oligonucleotides
- Patent number 12,234,455
- Issue date Feb 25, 2025
- IFOM Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d′Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating cancer and/or enhancing sensitivity to cancer t...
- Patent number 12,234,459
- Issue date Feb 25, 2025
- Mark David Vincent
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating SCN2A
- Patent number 12,227,746
- Issue date Feb 18, 2025
- Ionis Pharmaceuticals, Inc.
- Paymaan Jafar-nejad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of diacyglycerol acyltransferase 2 (DGAT2)
- Patent number 12,215,321
- Issue date Feb 4, 2025
- Ionis Pharmaceuticals, Inc.
- Eric E. Swayze
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating ATXN1
- Patent number 12,180,479
- Issue date Dec 31, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Angelman syndrome antisense treatment
- Patent number 12,180,480
- Issue date Dec 31, 2024
- The Texas A&M University System
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...
- Patent number 12,163,132
- Issue date Dec 10, 2024
- Children's National Medical Center
- Yi-Wen Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating neuronal excitability and m...
- Patent number 12,163,130
- Issue date Dec 10, 2024
- Icahn School of Medicine at Mount Sinai
- Anne Schaefer
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Oligonucleotides for modulating Tau expression
- Patent number 12,163,131
- Issue date Dec 10, 2024
- HOFFMANN-LA ROCHE INC.
- Peter Hagedorn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulating the cellular stress response
- Patent number 12,157,888
- Issue date Dec 3, 2024
- The General Hospital Corporation
- Jeannie T. Lee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of MALAT1 expression
- Patent number 12,157,890
- Issue date Dec 3, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective antisense compounds and uses thereof
- Patent number 12,152,244
- Issue date Nov 26, 2024
- Ionis Pharmaceuticals, Inc.
- Michael Oestergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeting human satellite II (HSATII)
- Patent number 12,152,241
- Issue date Nov 26, 2024
- The General Hospital Corporation
- David T. Ting
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compositions for treating pain via multiple targets
- Patent number 12,152,243
- Issue date Nov 26, 2024
- QUELLTX, INC.
- Graham T. Dempsey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for modulating UBE3A-ATS
- Patent number 12,129,466
- Issue date Oct 29, 2024
- Ionis Pharmaceuticals, Inc.
- Paymaan Jafar-nejad
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides for modulating SCN9A expression
- Patent number 12,116,576
- Issue date Oct 15, 2024
- HOFFMANN-LA ROCHE INC.
- Lykke Pedersen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective reduction of allelic variants
- Patent number 12,110,491
- Issue date Oct 8, 2024
- Ionis Pharmaceuticals, Inc.
- C. Frank Bennett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
PIKFYVE antisense oligonucleotides
- Patent number 12,104,159
- Issue date Oct 1, 2024
- ACURASTEM INCORPORATED
- Wen-Hsuan Chang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions for modulating tau expression
- Patent number 12,091,662
- Issue date Sep 17, 2024
- Biogen MA Inc.
- Holly Kordasiewicz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified oligonucleotides and methods of use
- Patent number 12,077,757
- Issue date Sep 3, 2024
- JANSSEN PHARMACEUTICA NV
- Sergei Gryaznov
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Targeting enhancer RNAs for the treatment of primary brain tumors
- Patent number 12,060,557
- Issue date Aug 13, 2024
- Brown University
- Nikolaos Tapinos
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of alpha synuclein expression
- Patent number 12,043,831
- Issue date Jul 23, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for reducing pathogenic isoforms
- Patent number 12,043,832
- Issue date Jul 23, 2024
- Washington University
- Andrew Findlay
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compounds and methods for modulating factor XII
- Patent number 12,018,261
- Issue date Jun 25, 2024
- Ionis Pharmaceuticals, Inc.
- Huynh-Hoa Bui
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Enhancing plasmin activity to prevent soft tissue calcification
- Patent number 12,011,455
- Issue date Jun 18, 2024
- Vanderbilt University
- Jonathan Schoenecker
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for inhibiting PMP22 expression
- Patent number 11,959,080
- Issue date Apr 16, 2024
- Ionis Pharmaceuticals, Inc.
- Gene Hung
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTIONS
- Publication number 20250092401
- Publication date Mar 20, 2025
- GlaxoSmithKline Intellectual Property Development Limited
- Jared Loren DELAHAYE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
PIKFYVE ANTISENSE OLIGONUCLEOTIDES
- Publication number 20250092404
- Publication date Mar 20, 2025
- AcuraStem Incorporated
- Wen-Hsuan CHANG
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Modified Oligonucleotides and Methods of Use
- Publication number 20250092400
- Publication date Mar 20, 2025
- Janssen Pharmaceutica N.V.
- Sergei GRYAZNOV
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS OF TREATMENT OF SCN2A-RELATED DISORDERS
- Publication number 20250092405
- Publication date Mar 20, 2025
- PRAXIS PRECISION MEDICINES, INC.
- William Motel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...
- Publication number 20250075215
- Publication date Mar 6, 2025
- Icahn School of Medicine at Mount Sinai
- Anne SCHAEFER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ACVR1R206H ALLELE-SPECIFIC THERAPY AND USES THEREOF FOR TREATMENT O...
- Publication number 20250066795
- Publication date Feb 27, 2025
- Oligomicstx Inc.
- Toshifumi YOKOTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC OLIGONUCLEOTIDES
- Publication number 20250066784
- Publication date Feb 27, 2025
- IFOM - Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d'Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORS OF APOL1 EXPRESSION
- Publication number 20250066785
- Publication date Feb 27, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANGELMAN SYNDROME ANTISENSE TREATMENT
- Publication number 20250066786
- Publication date Feb 27, 2025
- THE TEXAS A&M UNIVERSITY SYSTEM
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
- Publication number 20250066775
- Publication date Feb 27, 2025
- WAVE LIFE SCIENCES LTD.
- Chandra Vargeese
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INHIBIN SUBUNIT BETA E (INHBE) MODULATOR COMPOSITIONS AND METHODS O...
- Publication number 20250051779
- Publication date Feb 13, 2025
- Alnylam Pharmaceuticals, Inc.
- Aimee M. Deaton
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA
- Publication number 20250051769
- Publication date Feb 13, 2025
- Nippon Shinyaku Co., Ltd.
- Takao KAWANO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS A...
- Publication number 20250051776
- Publication date Feb 13, 2025
- HAYA Therapeutics SA
- Samir OUNZAIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
- Publication number 20250051777
- Publication date Feb 13, 2025
- HOFFMANN-LA ROCHE INC.
- Peter HAGEDORN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF SILENCING EXPRESSION OF GENES AND USES THEREOF
- Publication number 20250034574
- Publication date Jan 30, 2025
- UNIVERSITY OF MIAMI
- Ramin SHIEKHATTAR
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION
- Publication number 20250027081
- Publication date Jan 23, 2025
- Ionis Pharmaceuticals, Inc.
- Gene Hung
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Oligonucleotides for Modulating Synaptogyrin-3 Expression
- Publication number 20250011793
- Publication date Jan 9, 2025
- VIB VZW
- Patrik Verstreken
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR TARGETING COMPLEMENT C5
- Publication number 20240417725
- Publication date Dec 19, 2024
- Vanqua Bio, Inc.
- Kevin Hunt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSO...
- Publication number 20240409936
- Publication date Dec 12, 2024
- Ovid Therapeutics Inc.
- Noelle Germain
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S...
- Publication number 20240409945
- Publication date Dec 12, 2024
- Ovid Therapeutics Inc.
- Noelle Germain
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PREVENTIVE OR THERAPEUTIC AGENT FOR BENIGN ADULT FAMILIAL MYOCLONIC...
- Publication number 20240409926
- Publication date Dec 12, 2024
- RIKEN
- Haruhisa INOUE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...
- Publication number 20240401038
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING PKK EXPRESSION
- Publication number 20240401054
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compounds and Methods for Reducing ATXN2 Expression
- Publication number 20240401039
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Oligonucleotides
- Publication number 20240384268
- Publication date Nov 21, 2024
- Hudson Institute of Medical Research
- Michael Paul Marie Gantier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Selective Antisense Compounds and Uses Thereof
- Publication number 20240368592
- Publication date Nov 7, 2024
- Ionis Pharmaceuticals, Inc.
- Punit P. Seth
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GAPMER OLIGONUCLEOTIDES COMPRISING A PHOSPHORODITHIOATE INTERNUCLEO...
- Publication number 20240368593
- Publication date Nov 7, 2024
- Roche Innovation Center Copenhagen A/S
- Konrad Bleicher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES COMPRISING SEGMENTED GAP STRUCTURES
- Publication number 20240368602
- Publication date Nov 7, 2024
- AUSPERBIO THERAPEUTICS INC.
- Guofeng CHENG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDE THERAPY FOR H3.3 K27M DIFFUSE MIDLINE GLI...
- Publication number 20240360450
- Publication date Oct 31, 2024
- COLD SPRING HARBOR HARBOR LABORATORY
- Adrian Krainer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compounds and Methods for Reducing LRRK2 Expression
- Publication number 20240360453
- Publication date Oct 31, 2024
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Oligonucleotides for inducing paternal UBE3A expression

Compounds and methods for reducing LRRK2 expression

Antisense oligonucleotides targeting alpha-synuclein and uses thereof

Therapeutic oligonucleotides

Methods of treating cancer and/or enhancing sensitivity to cancer t...

Compounds and methods for modulating SCN2A

Modulators of diacyglycerol acyltransferase 2 (DGAT2)

Compounds and methods for modulating ATXN1

Angelman syndrome antisense treatment

Modulators of APOL1 expression

Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating...

Compositions and methods for modulating neuronal excitability and m...

Oligonucleotides for modulating Tau expression

Modulating the cellular stress response

Modulators of MALAT1 expression

Selective antisense compounds and uses thereof

Targeting human satellite II (HSATII)

Therapeutic compositions for treating pain via multiple targets

Compounds and methods for modulating UBE3A-ATS

Oligonucleotides for modulating SCN9A expression

Selective reduction of allelic variants

PIKFYVE antisense oligonucleotides

Compositions for modulating tau expression

Modified oligonucleotides and methods of use

Targeting enhancer RNAs for the treatment of primary brain tumors

Modulation of alpha synuclein expression

Methods and compositions for reducing pathogenic isoforms

Compounds and methods for modulating factor XII

Enhancing plasmin activity to prevent soft tissue calcification

Methods and compositions for inhibiting PMP22 expression

Patents Applicationslast 30 patents

COMBINATION THERAPY FOR TREATING HEPATITIS B VIRUS INFECTIONS

PIKFYVE ANTISENSE OLIGONUCLEOTIDES

Modified Oligonucleotides and Methods of Use

METHODS OF TREATMENT OF SCN2A-RELATED DISORDERS

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...

ACVR1R206H ALLELE-SPECIFIC THERAPY AND USES THEREOF FOR TREATMENT O...

THERAPEUTIC OLIGONUCLEOTIDES

MODULATORS OF APOL1 EXPRESSION

ANGELMAN SYNDROME ANTISENSE TREATMENT

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

INHIBIN SUBUNIT BETA E (INHBE) MODULATOR COMPOSITIONS AND METHODS O...

ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA

COMPOSITIONS AND METHODS OF MODULATING LONG NONCODING TRANSCRIPTS A...

OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION

METHODS OF SILENCING EXPRESSION OF GENES AND USES THEREOF

METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION

Oligonucleotides for Modulating Synaptogyrin-3 Expression

OLIGONUCLEOTIDES FOR TARGETING COMPLEMENT C5

RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSO...

RNAi TARGETING PPP2R5D MISSENSE MUTATIONS FOR TREATMENT OF JORDAN’S...

PREVENTIVE OR THERAPEUTIC AGENT FOR BENIGN ADULT FAMILIAL MYOCLONIC...

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...

COMPOSITIONS AND METHODS FOR MODULATING PKK EXPRESSION

Compounds and Methods for Reducing ATXN2 Expression

Oligonucleotides

Selective Antisense Compounds and Uses Thereof

GAPMER OLIGONUCLEOTIDES COMPRISING A PHOSPHORODITHIOATE INTERNUCLEO...

OLIGONUCLEOTIDES COMPRISING SEGMENTED GAP STRUCTURES

ANTISENSE OLIGONUCLEOTIDE THERAPY FOR H3.3 K27M DIFFUSE MIDLINE GLI...

Compounds and Methods for Reducing LRRK2 Expression