Gapmers

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Patents Applicationslast 30 patents

  • Information Patent Application

    OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

    • Publication number 20240150756
    • Publication date May 9, 2024
    • WAVE LIFE SCIENCES LTD.
    • Maria David Frank-Kamenetsky
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Selective Antisense Compounds and Uses Thereof

    • Publication number 20240141343
    • Publication date May 2, 2024
    • Ionis Pharmaceuticals, Inc.
    • Punit P. Seth
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODULATION OF GYS1 EXPRESSION

    • Publication number 20240141355
    • Publication date May 2, 2024
    • Ionis Pharmaceuticals, Inc.
    • Tamar R. Grossman
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ANTISENSE OLIGONUCLEOTIDES FOR USE IN THE TREATMENT OF CORNEAL DYST...

    • Publication number 20240141340
    • Publication date May 2, 2024
    • ProQR Therapeutics II B.V.
    • Elisabeth Laurentina Wilhelmina Maria VAN MIERLO
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODULATION OF TRANSTHYRETIN EXPRESSION

    • Publication number 20240132885
    • Publication date Apr 25, 2024
    • Ionis Pharmaceuticals, Inc.
    • Brett P. Monia
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODIFIED HETERO NUCLEIC ACIDS

    • Publication number 20240117346
    • Publication date Apr 11, 2024
    • NATIONAL UNIVERSITY CORPORATION TOKYO MEDICAL AND DENTAL UNIVERSITY
    • Takanori Yokota
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODULATION OF AAV-BASED GENE EXPRESSION

    • Publication number 20240100132
    • Publication date Mar 28, 2024
    • Prevail Therapeutics, Inc.
    • Benjamin Shykind
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOUNDS AND METHODS FOR MODULATING SCN2A

    • Publication number 20240102012
    • Publication date Mar 28, 2024
    • Ionis Pharmaceuticals, Inc.
    • Paymaan Jafar-Nejad
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (P...

    • Publication number 20240102020
    • Publication date Mar 28, 2024
    • Alnylam Pharmaceuticals, Inc.
    • Gregory Hinkle
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ANTISENSE OLIGONUCLEOTIDES INCREASING FOXG1 EXPRESSION

    • Publication number 20240093192
    • Publication date Mar 21, 2024
    • EliGab Tx LLC
    • Scott REICH
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJ...

    • Publication number 20240093201
    • Publication date Mar 21, 2024
    • Ionis Pharmaceuticals, Inc.
    • Thazha P. Prakash
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION

    • Publication number 20240085402
    • Publication date Mar 14, 2024
    • HOFFMANN-LA ROCHE INC.
    • Veronica COSTA
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ANTISENSE OLIGOMERS TARGETING PCSK9

    • Publication number 20240084307
    • Publication date Mar 14, 2024
    • Roche Innovation Center Copenhagen A/S
    • Nanna Albaek
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION

    • Publication number 20240082291
    • Publication date Mar 14, 2024
    • Ionis Pharmaceuticals, Inc.
    • Susan M. Freier
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOUNDS AND METHODS FOR MODULATING ATXN1

    • Publication number 20240067962
    • Publication date Feb 29, 2024
    • Ionis Pharmaceuticals, Inc.
    • Susan M. Freier
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ORAL DELIVERY OF ANTISENSE CONJUGATES TARGETING PCSK9

    • Publication number 20240067965
    • Publication date Feb 29, 2024
    • CiVi Biopharma, Inc.
    • Henrik OERUM
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    POLY-MORPHOLINO OLIGONUCLEOTIDE GAPMERS

    • Publication number 20240060068
    • Publication date Feb 22, 2024
    • Eisai R&D Management Co., Ltd.
    • Francis G. Fang
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ANTISENSE COMPOUNDS

    • Publication number 20240058370
    • Publication date Feb 22, 2024
    • Ionis Pharmaceuticals, Inc.
    • Eric E. Swayze
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OLIGONUCLEOTIDE AND USE THEREOF AGAINST HEPATITIS B VIRUS AND HEPAT...

    • Publication number 20240052350
    • Publication date Feb 15, 2024
    • ZHEJIANG PALO ALTO PHARMACEUTICALS, INC.
    • Zhijian XI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOUNDS AND METHODS FOR MODULATING SCN2A

    • Publication number 20240026353
    • Publication date Jan 25, 2024
    • Ionis Pharmaceuticals, Inc.
    • Paymaan Jafar-Nejad
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION

    • Publication number 20240026360
    • Publication date Jan 25, 2024
    • HOFFMANN-LA ROCHE INC.
    • Peter HAGEDORN
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION

    • Publication number 20240026364
    • Publication date Jan 25, 2024
    • Ionis Pharmaceuticals, Inc.
    • Shuling Guo
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    NUCLEIC ACID DUPLEXES

    • Publication number 20240002853
    • Publication date Jan 4, 2024
    • ALPHA ANOMERIC SAS
    • Wolfgang RENNER
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    OLIGONUCLEOTIDES CONTAINING 2'-DEOXY-2'FLUORO-BETA-D-ARABINOSE NUCL...

    • Publication number 20240000824
    • Publication date Jan 4, 2024
    • CITY OF HOPE
    • John J. Rossi
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    COMPOUNDS FOR MODULATING CHMP7

    • Publication number 20240002852
    • Publication date Jan 4, 2024
    • Ionis Pharmaceuticals, Inc.
    • Huynh-Hoa Bui
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF

    • Publication number 20240002851
    • Publication date Jan 4, 2024
    • Ionis Pharmaceuticals, Inc.
    • Brooke A. Anderson
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    UMLILO ANTISENSE TRANSCRIPTION INHIBITORS

    • Publication number 20230416734
    • Publication date Dec 28, 2023
    • LEMBA BV
    • Gabriel Virgil TURCU
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODIFIED GAPMER OLIGOMERS AND METHODS OF USE THEREOF

    • Publication number 20230383296
    • Publication date Nov 30, 2023
    • ALIGOS THERAPEUTICS, INC.
    • Leonid Beigelman
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    TARGETING XIST AND RNA METHYLATION FOR X REACTIVATION THERAPY

    • Publication number 20230383292
    • Publication date Nov 30, 2023
    • The General Hospital Corporation
    • Jeannie T. Lee
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    Compositions and Methods Targeting circ2082 for the Treatment of Ca...

    • Publication number 20230374508
    • Publication date Nov 23, 2023
    • The Brigham & Women's Hospital, Inc.
    • Jakub Godlewski
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...