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OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
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Publication number 20240150756
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Publication date May 9, 2024
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WAVE LIFE SCIENCES LTD.
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Maria David Frank-Kamenetsky
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MODULATION OF GYS1 EXPRESSION
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Publication number 20240141355
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Publication date May 2, 2024
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Ionis Pharmaceuticals, Inc.
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Tamar R. Grossman
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MODULATION OF TRANSTHYRETIN EXPRESSION
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Publication number 20240132885
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Publication date Apr 25, 2024
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Ionis Pharmaceuticals, Inc.
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Brett P. Monia
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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MODIFIED HETERO NUCLEIC ACIDS
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Publication number 20240117346
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Publication date Apr 11, 2024
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NATIONAL UNIVERSITY CORPORATION TOKYO MEDICAL AND DENTAL UNIVERSITY
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Takanori Yokota
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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MODULATION OF AAV-BASED GENE EXPRESSION
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Publication number 20240100132
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Publication date Mar 28, 2024
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Prevail Therapeutics, Inc.
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Benjamin Shykind
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOUNDS AND METHODS FOR MODULATING SCN2A
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Publication number 20240102012
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Publication date Mar 28, 2024
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Ionis Pharmaceuticals, Inc.
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Paymaan Jafar-Nejad
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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ANTISENSE OLIGOMERS TARGETING PCSK9
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Publication number 20240084307
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Publication date Mar 14, 2024
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Roche Innovation Center Copenhagen A/S
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Nanna Albaek
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOUNDS AND METHODS FOR MODULATING ATXN1
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Publication number 20240067962
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Publication date Feb 29, 2024
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Ionis Pharmaceuticals, Inc.
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Susan M. Freier
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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POLY-MORPHOLINO OLIGONUCLEOTIDE GAPMERS
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Publication number 20240060068
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Publication date Feb 22, 2024
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Eisai R&D Management Co., Ltd.
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Francis G. Fang
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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ANTISENSE COMPOUNDS
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Publication number 20240058370
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Publication date Feb 22, 2024
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Ionis Pharmaceuticals, Inc.
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Eric E. Swayze
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOUNDS AND METHODS FOR MODULATING SCN2A
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Publication number 20240026353
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Publication date Jan 25, 2024
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Ionis Pharmaceuticals, Inc.
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Paymaan Jafar-Nejad
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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NUCLEIC ACID DUPLEXES
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Publication number 20240002853
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Publication date Jan 4, 2024
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ALPHA ANOMERIC SAS
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Wolfgang RENNER
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOUNDS FOR MODULATING CHMP7
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Publication number 20240002852
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Publication date Jan 4, 2024
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Ionis Pharmaceuticals, Inc.
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Huynh-Hoa Bui
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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UMLILO ANTISENSE TRANSCRIPTION INHIBITORS
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Publication number 20230416734
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Publication date Dec 28, 2023
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LEMBA BV
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Gabriel Virgil TURCU
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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