having a combination of backbone and sugar modifications

Industry

CPC
C12N2310/346

This industry / category may be too specific. Please go to a parent level for more data

Parent Industries

CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

Current Industry

C12N2310/346having a combination of backbone and sugar modifications

Industries

Please log in for detailed analytics

Patents Grantslast 30 patents

Information Patent Grant
RNAi agents and compositions for inhibiting expression of apolipopr...
- Patent number 12,365,899
- Issue date Jul 22, 2025
- Arrowhead Pharmaceuticals, Inc.
- Zhen Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for reducing ATXN3 expression
- Patent number 12,350,285
- Issue date Jul 8, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antiviral agents
- Patent number RE50474
- Issue date Jul 1, 2025
- Meharry Medical College
- Donald J. Alcendor
Information Patent Grant
Nanoparticle formulations for delivery of nucleic acid complexes
- Patent number 12,318,489
- Issue date Jun 3, 2025
- Translate Bio MA, Inc.
- Fatih Ozsolak
- B82 - NANO-TECHNOLOGY
Information Patent Grant
Oligonucleotides targeting frataxin and related methods
- Patent number 12,312,585
- Issue date May 27, 2025
- UNIVERSITY OF MASSACHUSETTS
- Feng Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
BBB-crossing lipid ligand of hetero nucleic acid
- Patent number 12,305,169
- Issue date May 20, 2025
- National University Corporation Tokyo Medical and Dental University
- Takanori Yokota
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...
- Patent number 12,303,525
- Issue date May 20, 2025
- Hoffman-La Roche Inc.
- Susanne Kammler
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Oligonucleotides for the treatment of nucleotide repeat expansion d...
- Patent number 12,297,432
- Issue date May 13, 2025
- Takeda Pharmaceuticals U.S.A., Inc.
- Nessan Anthony Bermingham
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of huntingtin expression
- Patent number 12,297,431
- Issue date May 13, 2025
- Ionis Pharmaceuticals, Inc.
- Gene Hung
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating apolipoprotein (a) expression
- Patent number 12,291,709
- Issue date May 6, 2025
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Modified RNAi agents
- Patent number 12,290,573
- Issue date May 6, 2025
- Alnylam Pharmaceuticals, Inc.
- Kallanthottathil G. Rajeev
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligomers and oligomer conjugates
- Patent number 12,281,307
- Issue date Apr 22, 2025
- HOFFMANN-LA ROCHE INC.
- Hassan Javanbakht
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid, composition and conjugate containing same, preparatio...
- Patent number 12,274,752
- Issue date Apr 15, 2025
- Suzhou Ribo Life Science Co., Ltd.
- Hongyan Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides for inducing paternal UBE3A expression
- Patent number 12,259,380
- Issue date Mar 25, 2025
- HOFFMANN-LA ROCHE INC.
- Veronica Costa
- G01 - MEASURING TESTING
Information Patent Grant
FN3 domain-siRNA conjugates and uses thereof
- Patent number 12,239,710
- Issue date Mar 4, 2025
- ARO BIOTHERAPEUTICS COMPANY
- Swapnil Kulkarni
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
REVERSIR™ compounds
- Patent number 12,241,064
- Issue date Mar 4, 2025
- Alnylam Pharmaceuticals, Inc.
- Vasant Jadhav
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for reducing LRRK2 expression
- Patent number 12,241,067
- Issue date Mar 4, 2025
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of diacyglycerol acyltransferase 2 (DGAT2)
- Patent number 12,215,321
- Issue date Feb 4, 2025
- Ionis Pharmaceuticals, Inc.
- Eric E. Swayze
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Angelman syndrome antisense treatment
- Patent number 12,180,480
- Issue date Dec 31, 2024
- The Texas A&M University System
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Fully stabilized asymmetric siRNA
- Patent number 12,173,286
- Issue date Dec 24, 2024
- UNIVERSITY OF MASSACHUSETTS
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified guide RNAs
- Patent number 12,173,284
- Issue date Dec 24, 2024
- Intellia Therapeutics, Inc.
- Amy Madison Rhoden Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified double-stranded RNA agents
- Patent number 12,168,767
- Issue date Dec 17, 2024
- Alnylam Pharmaceuticals, Inc.
- Martin Maier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides to restore dysferlin protein expression...
- Patent number 12,163,129
- Issue date Dec 10, 2024
- University of Massachusetts
- Robert H. Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating neuronal excitability and m...
- Patent number 12,163,130
- Issue date Dec 10, 2024
- Icahn School of Medicine at Mount Sinai
- Anne Schaefer
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Selective antisense compounds and uses thereof
- Patent number 12,152,244
- Issue date Nov 26, 2024
- Ionis Pharmaceuticals, Inc.
- Michael Oestergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compositions for treating pain via multiple targets
- Patent number 12,152,243
- Issue date Nov 26, 2024
- QUELLTX, INC.
- Graham T. Dempsey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides for the treatment of Leber congenital am...
- Patent number 12,139,711
- Issue date Nov 12, 2024
- STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM
- Robert Wilhelmus Johanna Collin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for targeting pain directed at metabolic pathways
- Patent number 12,128,062
- Issue date Oct 29, 2024
- University of Maryland, Baltimore
- Ohannes Kevork Melemedjian
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Selective reduction of allelic variants
- Patent number 12,110,491
- Issue date Oct 8, 2024
- Ionis Pharmaceuticals, Inc.
- C. Frank Bennett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
Selective Reduction of Allelic Variants
- Publication number 20250223589
- Publication date Jul 10, 2025
- Ionis Pharmaceuticals, Inc.
- C. Frank Bennett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED RNAi AGENTS
- Publication number 20250213720
- Publication date Jul 3, 2025
- Kallanthottathil G. RAJEEV
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF DESIGNING CONDITIONAL-ACTIVATABLE SMALL INTERFERING RNA...
- Publication number 20250191692
- Publication date Jun 12, 2025
- Switch Therapeutics Inc.
- Si-ping Han
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF...
- Publication number 20250188456
- Publication date Jun 12, 2025
- Alnylam Pharmaceuticals, Inc.
- Gregory Hinkle
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FULLY STABILIZED ASYMMETRIC SIRNA
- Publication number 20250188458
- Publication date Jun 12, 2025
- University of Massachusetts
- Anastasia Khvorova
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TARGETED COMPOSITIONS
- Publication number 20250179496
- Publication date Jun 5, 2025
- ARBUTUS BIOPHARMA CORPORATION
- James HEYES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS
- Publication number 20250163419
- Publication date May 22, 2025
- QUELLTX, INC.
- Graham T. Dempsey
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MODULATION OF ALPHA SYNUCLEIN EXPRESSION
- Publication number 20250136982
- Publication date May 1, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
- Publication number 20250116656
- Publication date Apr 10, 2025
- HOFFMANN-LA ROCHE INC.
- Veronica COSTA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS
- Publication number 20250109164
- Publication date Apr 3, 2025
- Ionis Pharmaceuticals, Inc.
- Stanley T. Crooke
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANC...
- Publication number 20250101422
- Publication date Mar 27, 2025
- Larry J. Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TARGETED COMPOSITIONS
- Publication number 20250099594
- Publication date Mar 27, 2025
- ARBUTUS BIOPHARMA CORPORATION
- James HEYES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GUIDE RNA WITH CHEMICAL MODIFICATIONS
- Publication number 20250092389
- Publication date Mar 20, 2025
- Agilent Technologies, Inc.
- Daniel E. Ryan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PIKFYVE ANTISENSE OLIGONUCLEOTIDES
- Publication number 20250092404
- Publication date Mar 20, 2025
- AcuraStem Incorporated
- Wen-Hsuan CHANG
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...
- Publication number 20250075215
- Publication date Mar 6, 2025
- Icahn School of Medicine at Mount Sinai
- Anne SCHAEFER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDAS...
- Publication number 20250064936
- Publication date Feb 27, 2025
- Alnylam Pharmaceuticals, Inc.
- William Querbes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORS OF APOL1 EXPRESSION
- Publication number 20250066785
- Publication date Feb 27, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANGELMAN SYNDROME ANTISENSE TREATMENT
- Publication number 20250066786
- Publication date Feb 27, 2025
- THE TEXAS A&M UNIVERSITY SYSTEM
- Scott Victor Dindot
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
- Publication number 20250066775
- Publication date Feb 27, 2025
- WAVE LIFE SCIENCES LTD.
- Chandra Vargeese
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Modified Guide RNAs
- Publication number 20250059532
- Publication date Feb 20, 2025
- INTELLIA THERAPEUTICS, INC.
- Amy Madison Rhoden Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDIT...
- Publication number 20250059534
- Publication date Feb 20, 2025
- Eberhard-Karls-Universitat Tubingen
- Thorsten STAFFORST
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Oligonucleotide for Targeting Progranulin
- Publication number 20250051772
- Publication date Feb 13, 2025
- HOFFMANN-LA ROCHE INC.
- Ravi Jagasia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP)...
- Publication number 20250034570
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Kevin Fitzgerald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED DOUBLE-STRANDED RNA AGENTS
- Publication number 20250034572
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Martin MAIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Com...
- Publication number 20250034577
- Publication date Jan 30, 2025
- Arrowhead Pharmaceuticals, Inc.
- Anthony Nicholas
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION
- Publication number 20250027081
- Publication date Jan 23, 2025
- Ionis Pharmaceuticals, Inc.
- Gene Hung
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...
- Publication number 20250011784
- Publication date Jan 9, 2025
- VICO Therapeutics B.V.
- Peter Christian DE VISSER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED DOUBLE-STRANDED RNA AGENTS
- Publication number 20240409942
- Publication date Dec 12, 2024
- Alnylam Pharmaceuticals, Inc.
- Martin MAIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...
- Publication number 20240401038
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Chemically Modified Guide RNAs for CRISPR/CAS-Mediated Gene Correction
- Publication number 20240401034
- Publication date Dec 5, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Matthew H. Porteus
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

having a combination of backbone and sugar modifications

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

RNAi agents and compositions for inhibiting expression of apolipopr...

Compounds and methods for reducing ATXN3 expression

Antiviral agents

Nanoparticle formulations for delivery of nucleic acid complexes

Oligonucleotides targeting frataxin and related methods

BBB-crossing lipid ligand of hetero nucleic acid

Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...

Oligonucleotides for the treatment of nucleotide repeat expansion d...

Modulation of huntingtin expression

Compositions and methods for modulating apolipoprotein (a) expression

Modified RNAi agents

Oligomers and oligomer conjugates

Nucleic acid, composition and conjugate containing same, preparatio...

Oligonucleotides for inducing paternal UBE3A expression

FN3 domain-siRNA conjugates and uses thereof

REVERSIR™ compounds

Compounds and methods for reducing LRRK2 expression

Modulators of diacyglycerol acyltransferase 2 (DGAT2)

Angelman syndrome antisense treatment

Fully stabilized asymmetric siRNA

Modified guide RNAs

Modulators of APOL1 expression

Modified double-stranded RNA agents

Antisense oligonucleotides to restore dysferlin protein expression...

Compositions and methods for modulating neuronal excitability and m...

Selective antisense compounds and uses thereof

Therapeutic compositions for treating pain via multiple targets

Antisense oligonucleotides for the treatment of Leber congenital am...

Methods for targeting pain directed at metabolic pathways

Selective reduction of allelic variants

Patents Applicationslast 30 patents

Selective Reduction of Allelic Variants

MODIFIED RNAi AGENTS

METHODS OF DESIGNING CONDITIONAL-ACTIVATABLE SMALL INTERFERING RNA...

HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF...

FULLY STABILIZED ASYMMETRIC SIRNA

TARGETED COMPOSITIONS

THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS

MODULATION OF ALPHA SYNUCLEIN EXPRESSION

OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION

COMPOUNDS AND METHODS FOR THE MODULATION OF PROTEINS

METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANC...

TARGETED COMPOSITIONS

GUIDE RNA WITH CHEMICAL MODIFICATIONS

PIKFYVE ANTISENSE OLIGONUCLEOTIDES

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...

COMPOSITIONS AND METHODS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDAS...

MODULATORS OF APOL1 EXPRESSION

ANGELMAN SYNDROME ANTISENSE TREATMENT

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

Modified Guide RNAs

ANTISENSE OLIGONUCLEOTIDES (ASO) FOR EFFICIENT AND PRECISE RNA EDIT...

Antisense Oligonucleotide for Targeting Progranulin

STEROL REGULATORY ELEMENT BINDING PROTEIN (SREBP) CHAPERONE (SCAP)...

MODIFIED DOUBLE-STRANDED RNA AGENTS

RNAi Agents for Inhibiting Expression of PNPLA3, Pharmaceutical Com...

METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION

RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...

MODIFIED DOUBLE-STRANDED RNA AGENTS

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...

Chemically Modified Guide RNAs for CRISPR/CAS-Mediated Gene Correction