L-Iduronidase (3.2.1.76)

Industry

CPC
C12Y302/01076

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Parent Industries

CCHEMISTRY METALLURGY C12Biochemistry C12YENZYMES C12Y302/00Hydrolases acting on glycosyl compounds

Current Industry

C12Y302/01076L-Iduronidase (3.2.1.76)

Industries

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Patents Grantslast 30 patents

Information Patent Grant
AAV-IDUA vector for treatment of MPS I-associated blindness
- Patent number 12,201,697
- Issue date Jan 21, 2025
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for the treatment of steatosis-associated...
- Patent number 12,171,731
- Issue date Dec 24, 2024
- Duke University
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods to treat mucopolysaccharidosis type II or deficiency in idu...
- Patent number 12,121,567
- Issue date Oct 22, 2024
- Regents of The University of Minnesota
- R. Scott McIvor
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cleavable lipids
- Patent number 12,102,720
- Issue date Oct 1, 2024
- Translate Bio, Inc.
- Braydon Charles Guild
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods and compositions for the treatment of cytoplasmic glycogen...
- Patent number 12,036,190
- Issue date Jul 16, 2024
- Duke University
- Priya Kishnani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for the treatment of lysosomal storage dis...
- Patent number 11,898,158
- Issue date Feb 13, 2024
- Sangamo Therapeutics, Inc.
- Edward J. Rebar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV9-mediated gene therapy for treating mucopolysaccharidosis type I
- Patent number 11,890,329
- Issue date Feb 6, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for the treatment of mucopolysaccharidosis type I
- Patent number 11,857,641
- Issue date Jan 2, 2024
- Sangamo Therapeutics, Inc.
- Dale Ando
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for the treatment of steatosis-associated...
- Patent number 11,690,812
- Issue date Jul 4, 2023
- Duke University
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for increasing alpha-L-iduronidase activit...
- Patent number 11,512,145
- Issue date Nov 29, 2022
- ARMAGEN, INC.
- William M. Pardridge
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Engineered target specific nucleases
- Patent number 11,401,512
- Issue date Aug 2, 2022
- Sangamo Therapeutics, Inc.
- Russell DeKelver
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Plant lectins as carriers of associated drug substances into animal...
- Patent number 11,377,649
- Issue date Jul 5, 2022
- BIOSTRATEGIES LC
- David N. Radin
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Anti-human transferrin receptor antibody permeating blood-brain bar...
- Patent number 11,248,045
- Issue date Feb 15, 2022
- JCR Pharmaceuticals Co., Ltd.
- Hiroyuki Sonoda
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cleavable lipids
- Patent number 11,234,936
- Issue date Feb 1, 2022
- Translate Bio, Inc.
- Braydon Charles Guild
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
AAV-IDUA vector for treatment of MPS I-associated blindness
- Patent number 11,116,850
- Issue date Sep 14, 2021
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Delivering enzyme using an injectable hydrogel depot
- Patent number 11,034,950
- Issue date Jun 15, 2021
- Saint Louis University
- Adriana M. Montaño
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for treating mucopolysaccharidosis type I
- Patent number 10,973,929
- Issue date Apr 13, 2021
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Structure, manufacturing and uses of human-derived cell-permeable p...
- Patent number 10,947,539
- Issue date Mar 16, 2021
- Portage Pharmaceuticals Ltd.
- Bruce H. Littman
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods and compositions for the treatment of steatosis-associated...
- Patent number 10,940,125
- Issue date Mar 9, 2021
- Duke University
- Dwight D. Koeberl
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Oligosaccharides comprising an aminooxy group and conjugates thereof
- Patent number 10,907,142
- Issue date Feb 2, 2021
- Genzyme Corporation
- Yunxiang Zhu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for treating MPSI
- Patent number 10,792,343
- Issue date Oct 6, 2020
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Use of P97 as an enzyme delivery system for the delivery of therape...
- Patent number 10,716,862
- Issue date Jul 21, 2020
- BiOasis Advanced Technologies Inc.
- Christopher M. Starr
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cleavable lipids
- Patent number 10,702,478
- Issue date Jul 7, 2020
- Translate Bio, Inc.
- Braydon Charles Guild
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Method of treating mucopolysaccharidosis type I or II
- Patent number 10,648,001
- Issue date May 12, 2020
- Sangamo Therapeutics, Inc.
- Edward J. Rebar
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Engineered enzyme for enzyme replacement therapy
- Patent number 10,604,747
- Issue date Mar 31, 2020
- Academia Sinica
- Steve Roffler
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Treatment of lysosomal storage diseases
- Patent number 10,576,168
- Issue date Mar 3, 2020
- UCL BUSINESS LTD
- Bobby Gaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Intranasal administration of guanidinylated aminoglycosides
- Patent number 10,543,283
- Issue date Jan 28, 2020
- The Regents of the University of California
- Jeffrey D. Esko
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for increasing N-acetylglucosaminidase (NA...
- Patent number 10,538,589
- Issue date Jan 21, 2020
- ARMAGEN INC.
- William M. Pardridge
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Cleavable lipids
- Patent number 10,507,183
- Issue date Dec 17, 2019
- Translate Bio, Inc.
- Braydon Charles Guild
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Treatment of alpha-L-iduronidase (IDUA) related diseases by inhibit...
- Patent number 10,435,690
- Issue date Oct 8, 2019
- CuRNA, Inc.
- Joseph Collard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
CD40L ANTAGONIST AND USES THEREOF
- Publication number 20250019408
- Publication date Jan 16, 2025
- Viela Bio, Inc.
- Jorn DRAPPA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Lyophilized Pharmaceutical Compositions Comprising a Lipid Nanopart...
- Publication number 20240408020
- Publication date Dec 12, 2024
- Translate Bio, Inc.
- Braydon Charles Guild
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR INCREASING N-ACETYLGLUCOSAMINIDASE ACT...
- Publication number 20240409650
- Publication date Dec 12, 2024
- ArmaGen, Inc.
- William M. Pardridge
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Methods and Compositions for the Treatment of Cytoplasmic Glycogen...
- Publication number 20240398729
- Publication date Dec 5, 2024
- DUKE UNIVERSITY
- Priya Kishnani
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCL...
- Publication number 20240316217
- Publication date Sep 26, 2024
- Regents of the University of Minnesota
- R. Scott McIvor
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AAV9-MEDIATED GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I
- Publication number 20240307511
- Publication date Sep 19, 2024
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Pharmaceutical Composition for Treatment of Mucopolysaccharidosis T...
- Publication number 20240269244
- Publication date Aug 15, 2024
- JCR PHARMACEUTICALS CO., LTD
- Hideto MORIMOTO
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Method for Producing Antibody-Lysosomal Enzyme Fusion Protein
- Publication number 20240158436
- Publication date May 16, 2024
- JCR PHARMACEUTICALS CO., LTD
- Shinji Kakimoto
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF MUCOPOLYSACCHARIDOSIS I WITH FULLY-HUMAN GLYCOSYLATED...
- Publication number 20240050537
- Publication date Feb 15, 2024
- Regenxbio Inc.
- Stephen Yoo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I
- Publication number 20240024510
- Publication date Jan 25, 2024
- The Trustees of The University of Pennsylania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR THE IMPROVED RECOVERY OF SECRETED COMPOUNDS IN A HAIRY...
- Publication number 20240026370
- Publication date Jan 25, 2024
- SAMABRIVA
- Florian CARDON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IN UTERO AND POSTNATAL GENE EDITING AND THERAPY FOR TREATMENT OF MO...
- Publication number 20230340486
- Publication date Oct 26, 2023
- The Children's Hospital of Philadelphia
- William H. Peranteau
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR THE TREATMENT OF NEUROLOGIC DISEASE
- Publication number 20230330195
- Publication date Oct 19, 2023
- Sangamo Therapeutics, Inc.
- Russell DeKelver
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPLANTABLE CELL CHAMBER DEVICE AND USES THEREOF
- Publication number 20230310712
- Publication date Oct 5, 2023
- Takeda Pharmaceutical Company Limited
- Vincent Ling
- C07 - ORGANIC CHEMISTRY
Information Patent Application
Methods and Compositions for the Treatment of Steatosis-Associated...
- Publication number 20230285328
- Publication date Sep 14, 2023
- DUKE UNIVERSITY
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Methods and Compositions for the Treatment of Steatosis-Associated...
- Publication number 20230285329
- Publication date Sep 14, 2023
- DUKE UNIVERSITY
- Dwight D. Koeberl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MATERIALS AND METHODS FOR MITIGATING IMMUNE-SENSITIZATION
- Publication number 20230285553
- Publication date Sep 14, 2023
- Biostrategies LC
- DAVID N. RADIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR INCREASING ALPHA-L-IDURONIDASE ACTIVIT...
- Publication number 20230279156
- Publication date Sep 7, 2023
- Armagen, Inc.
- William M. Pardridge
- C07 - ORGANIC CHEMISTRY
Information Patent Application
TARGETING THE HUMAN CCR5 LOCUS AS A SAFE HARBOR FOR THE EXPRESSION...
- Publication number 20230265440
- Publication date Aug 24, 2023
- The Board of Trustees of the Leland Stanford Junior University
- Natalia Gomez-Ospina
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS FOR THERAPEUTIC DELIVERY TO CENTRAL NERVOUS...
- Publication number 20230226225
- Publication date Jul 20, 2023
- Regents of the University of Minnesota
- R. Scott McIvor
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMBINATION THERAPY FOR TREATING MPS1
- Publication number 20230140216
- Publication date May 4, 2023
- GAIN THERAPEUTICS SA
- Ana Maria GARCÍA COLLAZO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED TARGET SPECIFIC NUCLEASES
- Publication number 20230067653
- Publication date Mar 2, 2023
- Sangamo Therapeutics, Inc.
- Russell DeKelver
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION
- Publication number 20220389457
- Publication date Dec 8, 2022
- The Trustees of the University of Pennsylvania
- James M. Wilson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS, TYPE I
- Publication number 20220339296
- Publication date Oct 27, 2022
- BLUEBIRD BIO, INC.
- Kendrick A. GOSS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INTRANASAL ADMINISTRATION OF ADENO-ASSOCIATED VIRUS TO TREAT CENTRA...
- Publication number 20220211875
- Publication date Jul 7, 2022
- Regents of the University of Minnesota
- R. Scott McIvor
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
OLIGOSACCHARIDES COMPRISING AN AMINOOXY GROUP AND CONJUGATES THEREOF
- Publication number 20220204963
- Publication date Jun 30, 2022
- Genzyme Corporation
- Yunxiang Zhu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
B CELLS FOR IN VIVO DELIVERY OF THERAPEUTIC AGENTS AND DOSAGES THEREOF
- Publication number 20220193129
- Publication date Jun 23, 2022
- IMMUSOFT CORPORATION
- Matthew Rein Scholz
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHOD FOR IMPROVING NEUROLOGICAL FUNCTION IN MPSI AND MPSII AND OT...
- Publication number 20220096659
- Publication date Mar 31, 2022
- Regents of the University of Minnesota
- Kanut Laoharawee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Anti-Human Transferrin Receptor Antibody Permeating Blood-Brain Bar...
- Publication number 20220064288
- Publication date Mar 3, 2022
- JCR PHARMACEUTICALS CO., LTD
- Hiroyuki Sonoda
- C07 - ORGANIC CHEMISTRY
Information Patent Application
AAV-IDUA VECTOR FOR TREATMENT OF MPS I-ASSOCIATED BLINDNESS
- Publication number 20220047721
- Publication date Feb 17, 2022
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

L-Iduronidase (3.2.1.76)

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

AAV-IDUA vector for treatment of MPS I-associated blindness

Methods and compositions for the treatment of steatosis-associated...

Methods to treat mucopolysaccharidosis type II or deficiency in idu...

Cleavable lipids

Methods and compositions for the treatment of cytoplasmic glycogen...

Methods and compositions for the treatment of lysosomal storage dis...

AAV9-mediated gene therapy for treating mucopolysaccharidosis type I

Method for the treatment of mucopolysaccharidosis type I

Methods and compositions for the treatment of steatosis-associated...

Methods and compositions for increasing alpha-L-iduronidase activit...

Engineered target specific nucleases

Plant lectins as carriers of associated drug substances into animal...

Anti-human transferrin receptor antibody permeating blood-brain bar...

Cleavable lipids

AAV-IDUA vector for treatment of MPS I-associated blindness

Delivering enzyme using an injectable hydrogel depot

Gene therapy for treating mucopolysaccharidosis type I

Structure, manufacturing and uses of human-derived cell-permeable p...

Methods and compositions for the treatment of steatosis-associated...

Oligosaccharides comprising an aminooxy group and conjugates thereof

Compositions and methods for treating MPSI

Use of P97 as an enzyme delivery system for the delivery of therape...

Cleavable lipids

Method of treating mucopolysaccharidosis type I or II

Engineered enzyme for enzyme replacement therapy

Treatment of lysosomal storage diseases

Intranasal administration of guanidinylated aminoglycosides

Methods and compositions for increasing N-acetylglucosaminidase (NA...

Cleavable lipids

Treatment of alpha-L-iduronidase (IDUA) related diseases by inhibit...

Patents Applicationslast 30 patents

CD40L ANTAGONIST AND USES THEREOF

Lyophilized Pharmaceutical Compositions Comprising a Lipid Nanopart...

METHODS AND COMPOSITIONS FOR INCREASING N-ACETYLGLUCOSAMINIDASE ACT...

Methods and Compositions for the Treatment of Cytoplasmic Glycogen...

METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCL...

AAV9-MEDIATED GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I

Pharmaceutical Composition for Treatment of Mucopolysaccharidosis T...

Method for Producing Antibody-Lysosomal Enzyme Fusion Protein

TREATMENT OF MUCOPOLYSACCHARIDOSIS I WITH FULLY-HUMAN GLYCOSYLATED...

GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I

METHODS FOR THE IMPROVED RECOVERY OF SECRETED COMPOUNDS IN A HAIRY...

IN UTERO AND POSTNATAL GENE EDITING AND THERAPY FOR TREATMENT OF MO...

METHODS AND COMPOSITIONS FOR THE TREATMENT OF NEUROLOGIC DISEASE

IMPLANTABLE CELL CHAMBER DEVICE AND USES THEREOF

Methods and Compositions for the Treatment of Steatosis-Associated...

Methods and Compositions for the Treatment of Steatosis-Associated...

MATERIALS AND METHODS FOR MITIGATING IMMUNE-SENSITIZATION

METHODS AND COMPOSITIONS FOR INCREASING ALPHA-L-IDURONIDASE ACTIVIT...

TARGETING THE HUMAN CCR5 LOCUS AS A SAFE HARBOR FOR THE EXPRESSION...

ADENO-ASSOCIATED VIRUS FOR THERAPEUTIC DELIVERY TO CENTRAL NERVOUS...

COMBINATION THERAPY FOR TREATING MPS1

ENGINEERED TARGET SPECIFIC NUCLEASES

COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION

GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS, TYPE I

INTRANASAL ADMINISTRATION OF ADENO-ASSOCIATED VIRUS TO TREAT CENTRA...

OLIGOSACCHARIDES COMPRISING AN AMINOOXY GROUP AND CONJUGATES THEREOF

B CELLS FOR IN VIVO DELIVERY OF THERAPEUTIC AGENTS AND DOSAGES THEREOF

METHOD FOR IMPROVING NEUROLOGICAL FUNCTION IN MPSI AND MPSII AND OT...

Anti-Human Transferrin Receptor Antibody Permeating Blood-Brain Bar...

AAV-IDUA VECTOR FOR TREATMENT OF MPS I-ASSOCIATED BLINDNESS