relating to complementing cells and packaging systems for producing virus or viral particles

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C12N2750/14152

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2750/00ssDNA Viruses

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C12N2750/14152relating to complementing cells and packaging systems for producing virus or viral particles

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Patents Grantslast 30 patents

Information Patent Grant
Nucleic acid constructs for VA RNA transcription
- Patent number 12,312,606
- Issue date May 27, 2025
- HOFFMANN-LA ROCHE INC.
- Ulrich Goepfert
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dual helper plasmid
- Patent number 12,305,188
- Issue date May 20, 2025
- NEURACLE GENETICS INC.
- Joo Seok Han
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cell hybrids as virus packaging cells for high efficiency productio...
- Patent number 12,252,713
- Issue date Mar 18, 2025
- Cho Plus, Inc.
- Lawrence Forman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Mammalian cells and methods for engineering the same
- Patent number 12,241,062
- Issue date Mar 4, 2025
- 64-X, Inc.
- Alexis Rovner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adenoassociated virus vectors for the treatment of mucopolysacchari...
- Patent number 12,146,169
- Issue date Nov 19, 2024
- ESTEVE PHARMACEUTICALS, S.A.
- Maria Fátima Bosch Tubert
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Life-cycle-defective adenovirus helper viruses, their production an...
- Patent number 12,123,027
- Issue date Oct 22, 2024
- Ascend Advanced Therapies Limited
- Markus Hörer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Codon-optimized acid alpha-glucosidase expression cassettes and met...
- Patent number 12,084,693
- Issue date Sep 10, 2024
- SPARK THERAPEUTICS, INC.
- Xavier Anguela
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Suspension system for adeno associated virus production
- Patent number 12,077,784
- Issue date Sep 3, 2024
- Life Technologies Corporation
- Xin Yu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus compositions for PAH gene transfer and metho...
- Patent number 12,064,486
- Issue date Aug 20, 2024
- HOMOLOGY MEDICINES, INC.
- Albert Barnes Seymour
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Inducible AAV REP genes
- Patent number 12,060,569
- Issue date Aug 13, 2024
- Cevec Pharmaceuticals, GmbH
- Kerstin Hein
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Stable cell lines for inducible production of rAAV virions
- Patent number 12,054,738
- Issue date Aug 6, 2024
- Shape Therapeutics Inc.
- Kenneth Prentice
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Hybrid recombinant adeno-associated virus serotype between AAV9 and...
- Patent number 12,037,362
- Issue date Jul 16, 2024
- Genethon
- Isabelle Richard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Delivery and use of the CRISPR-CAS systems, vectors and composition...
- Patent number 12,018,275
- Issue date Jun 25, 2024
- The Broad Institute, Inc.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Engineered producer cell lines and methods of making and using the...
- Patent number 12,018,288
- Issue date Jun 25, 2024
- Ultragenyx Pharmaceutical Inc.
- Aubrey R. Tiernan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for analysis of viral capsid protein composition
- Patent number 11,981,913
- Issue date May 14, 2024
- REGENERON PHARMACEUTICALS, INC.
- Shunhai Wang
- G01 - MEASURING TESTING
Information Patent Grant
Adeno-associated virus vector variants for high efficiency genome e...
- Patent number 11,965,174
- Issue date Apr 23, 2024
- City of Hope
- Saswati Chatterjee
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods and compositions for modifying assembly-activating protein...
- Patent number 11,958,884
- Issue date Apr 16, 2024
- Massachusetts Eye and Ear Infirmary
- Luk H. Vandenberghe
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Adeno-associated virus compositions for PAH gene transfer and metho...
- Patent number 11,951,183
- Issue date Apr 9, 2024
- HOMOLOGY MEDICINES, INC.
- Albert Barnes Seymour
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV-based conditional expression system
- Patent number 11,926,841
- Issue date Mar 12, 2024
- Ulrich Koszinowski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cell culture methods involving HDAC inhibitors or rep proteins
- Patent number 11,898,170
- Issue date Feb 13, 2024
- Ultragenyx Pharmaceutical Inc.
- Aubrey R. Tiernan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
High titer recombinant AAV vector production in adherent and suspen...
- Patent number 11,834,683
- Issue date Dec 5, 2023
- Huiren Zhao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Liver targeting adeno-associated viral vectors
- Patent number 11,821,008
- Issue date Nov 21, 2023
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cancer treatment
- Patent number 11,820,792
- Issue date Nov 21, 2023
- Imperial College Innovations Limited
- Amin Hajitou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Use of tonicifying agents to enhance recombinant adeno-associated v...
- Patent number 11,795,473
- Issue date Oct 24, 2023
- Ultragenyx Pharmaceutical Inc.
- Ying Jing
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Mammalian cells for producing adeno-associated viruses
- Patent number 11,781,116
- Issue date Oct 10, 2023
- Lonza Ltd
- Marc Feary
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Viral vector production
- Patent number 11,767,539
- Issue date Sep 26, 2023
- University of Massachusetts
- Jun Xie
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adenoviral vector expressing Zika antigen with improved...
- Patent number 11,713,469
- Issue date Aug 1, 2023
- Janssen Vaccines & Prevention B.V.
- Taco Gilles Uil
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Column-based fully scalable rAAV manufacturing process
- Patent number 11,702,639
- Issue date Jul 18, 2023
- SPARK THERAPEUTICS, INC.
- Guang Qu
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Grant
Vector for the production of AAV particles
- Patent number 11,697,824
- Issue date Jul 11, 2023
- Oxford Genetics Limited
- Ryan Cawood
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Inducible AAV Rep genes
- Patent number 11,685,932
- Issue date Jun 27, 2023
- Cevec Pharmaceuticals, GmbH
- Kerstin Hein
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR
- Publication number 20250171801
- Publication date May 29, 2025
- The Trustees of the University of Pennsylvania
- Luk VANDENBERGHE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INTEGRATIVE PLASMID
- Publication number 20250163438
- Publication date May 22, 2025
- Synplogen Co., Ltd.
- Shunsuke SAITO
- C07 - ORGANIC CHEMISTRY
Information Patent Application
AGENT FOR ENHANCING PRODUCTION OF VIRAL VECTOR AND METHOD FOR PRODU...
- Publication number 20250163456
- Publication date May 22, 2025
- NIPPON MEDICAL SCHOOL FOUNDATION
- Yoshitaka MIYAGAWA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPROVED CELL LINES AND METHODS FOR THE PRODUCTION OF ADENO-ASSOCIA...
- Publication number 20250163459
- Publication date May 22, 2025
- CEVEC Pharmaceuticals GmbH
- Michelle Hussong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR VARIANTS FOR HIGH EFFICIENCY GENOME E...
- Publication number 20250154534
- Publication date May 15, 2025
- CITY OF HOPE
- Saswati CHATTERJEE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSIDS FOR IMPROVED HEART TRANSDUCTION AND DETARGETING OF LIVER
- Publication number 20250144243
- Publication date May 8, 2025
- The Trustees of the University of Pennsylvania
- Jacob Hoffman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Stable Cell Lines for Inducible Production of rAAV Virions
- Publication number 20250146020
- Publication date May 8, 2025
- Shape Therapeutics Inc.
- Kenneth Prentice
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT OF ACQUIRED FOCAL EPILEPSY
- Publication number 20250144244
- Publication date May 8, 2025
- UCL Business LTD
- Matthew Charles WALKER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY
- Publication number 20250122530
- Publication date Apr 17, 2025
- BioMarin Pharmaceutical Inc.
- Peter COLOSI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Stable Cell Lines for Inducible Production of rAAV Virions
- Publication number 20250109410
- Publication date Apr 3, 2025
- Shape Therapeutics Inc.
- Kenneth Prentice
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED VECTOR, CONSTRUCTION METHOD, AND APPLICATION OF MODIFIED A...
- Publication number 20250108127
- Publication date Apr 3, 2025
- SHANGHAI OPHTHAL-BRIGHT BIOMEDICINE TECHNOLOGY
- Shiqing ZHANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DELIVERY AND USE OF THE CRISPR-CAS SYSTEMS, VECTORS AND COMPOSITION...
- Publication number 20250101468
- Publication date Mar 27, 2025
- THE BROAD INSTITUTE, INC.
- Feng ZHANG
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...
- Publication number 20250101396
- Publication date Mar 27, 2025
- Spark Therapeutics, Inc.
- Xavier Anguela
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
EXPRESSION CASSETTES FOR TREATING EPILEPSY AND NEUROPATHIC PAIN
- Publication number 20250090689
- Publication date Mar 20, 2025
- TRAMES BIO, INC.
- Annahita Keravala
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
LARGE SCALE ADENO-ASSOCIATED VIRUS PRODUCTION SYSTEMS
- Publication number 20250084383
- Publication date Mar 13, 2025
- BioMarin Pharmaceutical Inc.
- Tomas CINEK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT
- Publication number 20250082779
- Publication date Mar 13, 2025
- Capsida, Inc.
- Nicholas C. Flytzanis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF MUCOPOLYSACCHARI...
- Publication number 20250075194
- Publication date Mar 6, 2025
- ESTEVE PHARMACEUTICALS, S.A.
- Maria-Fàtima BOSCH-TUBERT
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
BACULOVIRUS VECTOR AND USE THEREOF IN PREPARATION OF RECOMBINANT AD...
- Publication number 20250066814
- Publication date Feb 27, 2025
- GENEVOYAGER (WUHAN) CO., LTD.
- He XIAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV) GENOME AND SINGLE-POLARIT...
- Publication number 20250059562
- Publication date Feb 20, 2025
- SUZHOU GENEHEALTH BIOTECHNOLOGY, CO., LTD.
- Jiahong SHAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IN VIVO REPROGRAMMING OF PHOTORECEPTOR CELLS
- Publication number 20250049956
- Publication date Feb 13, 2025
- CENTRE FOR EYE RESEARCH AUSTRALIA LTD
- Ching Bong WONG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
- Publication number 20250041445
- Publication date Feb 6, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND SYSTEMS FOR TRANSFECTING HOST CELLS
- Publication number 20250034590
- Publication date Jan 30, 2025
- Biogen MA Inc.
- Jenny Wang-Yuanzhen Shupe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES TH...
- Publication number 20250025574
- Publication date Jan 23, 2025
- Regenxbio Inc.
- Randolph Qian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO...
- Publication number 20250019668
- Publication date Jan 16, 2025
- ULTRAGENYX PHARMACEUTICAL INC.
- Nicholas Richards
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRODUCTION OF RECOMBINANT AAV VECTORS FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250018059
- Publication date Jan 16, 2025
- Sarepta Therapeutics, Inc.
- Maroof ALAM
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL LINES WITH IMPROVED AAV PRODUCTION CAPACITY
- Publication number 20250019669
- Publication date Jan 16, 2025
- The Children's Hospital of Philadelphia
- Beverly L. DAVIDSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VIRAL VECTOR PRODUCTION
- Publication number 20250011809
- Publication date Jan 9, 2025
- CELL THERAPY CATAPULT LIMITED
- Jonathan APPLEBY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Inducible AAV REP genes
- Publication number 20250011813
- Publication date Jan 9, 2025
- Cevec Pharmaceuticals, GmbH
- Kerstin Hein
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
STABLE PRODUCTION SYSTEMS FOR AAV VECTOR PRODUCTION
- Publication number 20250011811
- Publication date Jan 9, 2025
- Asimov Inc.
- Christopher S. Stach
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATORS OF ADENO-ASSOCIATED VIRUS TRANSDUCTION AND USES THEREOF
- Publication number 20250001013
- Publication date Jan 2, 2025
- Novartis AG
- Eloise Hudry
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

relating to complementing cells and packaging systems for producing virus or viral particles

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Nucleic acid constructs for VA RNA transcription

Dual helper plasmid

Cell hybrids as virus packaging cells for high efficiency productio...

Mammalian cells and methods for engineering the same

Adenoassociated virus vectors for the treatment of mucopolysacchari...

Life-cycle-defective adenovirus helper viruses, their production an...

Codon-optimized acid alpha-glucosidase expression cassettes and met...

Suspension system for adeno associated virus production

Adeno-associated virus compositions for PAH gene transfer and metho...

Inducible AAV REP genes

Stable cell lines for inducible production of rAAV virions

Hybrid recombinant adeno-associated virus serotype between AAV9 and...

Delivery and use of the CRISPR-CAS systems, vectors and composition...

Engineered producer cell lines and methods of making and using the...

Methods for analysis of viral capsid protein composition

Adeno-associated virus vector variants for high efficiency genome e...

Methods and compositions for modifying assembly-activating protein...

Adeno-associated virus compositions for PAH gene transfer and metho...

AAV-based conditional expression system

Cell culture methods involving HDAC inhibitors or rep proteins

High titer recombinant AAV vector production in adherent and suspen...

Liver targeting adeno-associated viral vectors

Cancer treatment

Use of tonicifying agents to enhance recombinant adeno-associated v...

Mammalian cells for producing adeno-associated viruses

Viral vector production

Recombinant adenoviral vector expressing Zika antigen with improved...

Column-based fully scalable rAAV manufacturing process

Vector for the production of AAV particles

Inducible AAV Rep genes

Patents Applicationslast 30 patents

METHOD OF INCREASING THE FUNCTION OF AN AAV VECTOR

INTEGRATIVE PLASMID

AGENT FOR ENHANCING PRODUCTION OF VIRAL VECTOR AND METHOD FOR PRODU...

IMPROVED CELL LINES AND METHODS FOR THE PRODUCTION OF ADENO-ASSOCIA...

ADENO-ASSOCIATED VIRUS VECTOR VARIANTS FOR HIGH EFFICIENCY GENOME E...

AAV CAPSIDS FOR IMPROVED HEART TRANSDUCTION AND DETARGETING OF LIVER

Stable Cell Lines for Inducible Production of rAAV Virions

TREATMENT OF ACQUIRED FOCAL EPILEPSY

AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY

Stable Cell Lines for Inducible Production of rAAV Virions

MODIFIED VECTOR, CONSTRUCTION METHOD, AND APPLICATION OF MODIFIED A...

DELIVERY AND USE OF THE CRISPR-CAS SYSTEMS, VECTORS AND COMPOSITION...

CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...

EXPRESSION CASSETTES FOR TREATING EPILEPSY AND NEUROPATHIC PAIN

LARGE SCALE ADENO-ASSOCIATED VIRUS PRODUCTION SYSTEMS

ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING INCREASED BRAIN ENRICHMENT

ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF MUCOPOLYSACCHARI...

BACULOVIRUS VECTOR AND USE THEREOF IN PREPARATION OF RECOMBINANT AD...

RECOMBINANT ADENO-ASSOCIATED VIRUS (RAAV) GENOME AND SINGLE-POLARIT...

IN VIVO REPROGRAMMING OF PHOTORECEPTOR CELLS

GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

METHODS AND SYSTEMS FOR TRANSFECTING HOST CELLS

ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES TH...

ENGINEERED CELL LINES FOR INCREASED PRODUCTION OF RECOMBINANT ADENO...

PRODUCTION OF RECOMBINANT AAV VECTORS FOR TREATING MUSCULAR DYSTROPHY

CELL LINES WITH IMPROVED AAV PRODUCTION CAPACITY

VIRAL VECTOR PRODUCTION

Inducible AAV REP genes

STABLE PRODUCTION SYSTEMS FOR AAV VECTOR PRODUCTION

MODULATORS OF ADENO-ASSOCIATED VIRUS TRANSDUCTION AND USES THEREOF