Special targeting system for viral vectors

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  • Information Patent Application

    CAPSID VARIANTS AND METHODS OF USING THE SAME

    • Publication number 20250066428
    • Publication date Feb 27, 2025
    • DYNO THERAPEUTICS, INC.
    • Ina Chen
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODIFIED VIRAL PARTICLES FOR GENE THERAPY

    • Publication number 20250057976
    • Publication date Feb 20, 2025
    • European Molecular Biology Laboratory
    • Paul Alexander HEPPENSTALL
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ADENO-ASSOCIATED VIRAL VECTORS AND USES THEREOF

    • Publication number 20250057986
    • Publication date Feb 20, 2025
    • THE BROAD INSTITUTE, INC.
    • Benjamin E. Deverman
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    IN VIVO REPROGRAMMING OF PHOTORECEPTOR CELLS

    • Publication number 20250049956
    • Publication date Feb 13, 2025
    • CENTRE FOR EYE RESEARCH AUSTRALIA LTD
    • Ching Bong WONG
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    FACTOR H VARIANTS FOR TREATMENT OF DISEASE

    • Publication number 20250051408
    • Publication date Feb 13, 2025
    • The Trustees of the University of Pennsylvania
    • Wenchao Song
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ADENO-ASSOCIATED VIRUS WITH ENGINEERED CAPSID

    • Publication number 20250051799
    • Publication date Feb 13, 2025
    • Tenaya Therapeutics, Inc.
    • Christopher A. REID
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ENGINEERED MUSCLE TARGETING COMPOSITIONS

    • Publication number 20250051800
    • Publication date Feb 13, 2025
    • THE BROAD INSTITUTE, INC.
    • Pardis SABETI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ENGINEERED MUSCLE TARGETING COMPOSITIONS

    • Publication number 20250043309
    • Publication date Feb 6, 2025
    • THE BROAD INSTITUTE, INC.
    • Pardis SABETI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    GENE THERAPY FOR HEARING LOSS

    • Publication number 20250041451
    • Publication date Feb 6, 2025
    • Perceive Biotherapeutics, Inc.
    • Derek Welsbie
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES TH...

    • Publication number 20250025574
    • Publication date Jan 23, 2025
    • Regenxbio Inc.
    • Randolph Qian
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV CAPSID VARIANTS AND USES THEREOF

    • Publication number 20250011372
    • Publication date Jan 9, 2025
    • VOYAGER THRAPEUTICS, INC.
    • Mathieu Emmanuel Nonnenmacher
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    KCNV2 Variants and Their Use

    • Publication number 20250011386
    • Publication date Jan 9, 2025
    • Artema Therapeutics, Inc.
    • Shamil Sultanov
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    METHODS FOR EVALUATING TREATMENTS FOR BESTROPHINOPATHIES

    • Publication number 20250009905
    • Publication date Jan 9, 2025
    • The Trustees of the University of Pennsylvania
    • Karina E. Guziewicz
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODULATORS OF ADENO-ASSOCIATED VIRUS TRANSDUCTION AND USES THEREOF

    • Publication number 20250001013
    • Publication date Jan 2, 2025
    • Novartis AG
    • Eloise Hudry
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT ADENO-ASSOCIATED VIRUSES FOR TARGETED DELIVERY

    • Publication number 20250001006
    • Publication date Jan 2, 2025
    • Regenxbio Inc.
    • Olivier Danos
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ADENO-ASSOCIATED VIRUS COMPOSITIONS HAVING PREFERRED HEART AND SKEL...

    • Publication number 20250001007
    • Publication date Jan 2, 2025
    • California Institute of Technology
    • Viviana Gradinaru
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    ENGINEERED CENTRAL NERVOUS SYSTEM COMPOSITIONS

    • Publication number 20250002541
    • Publication date Jan 2, 2025
    • THE BROAD INSTITUTE, INC.
    • Pardis Sabeti
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    VIRAL ADAPTORS AND USES THEREOF

    • Publication number 20250002938
    • Publication date Jan 2, 2025
    • The Francis Crick Institute Limited
    • Samuel Gordon Rodriques
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    CAPSID VARIANTS AND METHODS OF USING THE SAME

    • Publication number 20240425551
    • Publication date Dec 26, 2024
    • DYNO THERAPEUTICS, INC.
    • Ina Chen
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    CAPSID VARIANTS AND METHODS OF USING THE SAME

    • Publication number 20240425552
    • Publication date Dec 26, 2024
    • DYNO THERAPEUTICS, INC.
    • Ina Chen
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    CAPSID VARIANTS AND METHODS OF USING THE SAME

    • Publication number 20240417430
    • Publication date Dec 19, 2024
    • DYNO THERAPEUTICS, INC.
    • Ina Chen
    • A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
  • Information Patent Application

    TREATMENT OF HEREDITARY ANGIOEDEMA WITH AAV GENE THERAPY VECTORS AN...

    • Publication number 20240408240
    • Publication date Dec 12, 2024
    • BioMarin Pharmaceutical Inc.
    • Peter COLOSI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEP...

    • Publication number 20240398992
    • Publication date Dec 5, 2024
    • Skyline Therapeutics Limited
    • Yanqun SHU
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV8 CAPSID VARIANTS WITH ENHANCED LIVER TARGETING

    • Publication number 20240390517
    • Publication date Nov 28, 2024
    • Takeda Pharmaceutical Company Limited
    • Janina HAAR
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    TARGETING MOIETIES PROMOTING TRANSDUCTION OF CENTRAL NERVOUS SYSTEM...

    • Publication number 20240384299
    • Publication date Nov 21, 2024
    • THE BROAD INSTITUTE, INC.
    • Benjamin Deverman
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV Vectors Targeted to Oligodendrocytes

    • Publication number 20240374662
    • Publication date Nov 14, 2024
    • The University of North Carolina at Chapel Hill
    • Thomas McCown
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    AAV CAPSID COMPOSITIONS AND METHODS FOR DELIVERY

    • Publication number 20240376495
    • Publication date Nov 14, 2024
    • BioMarin Pharmaceutical Inc.
    • Peter COLOSI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUR...

    • Publication number 20240376164
    • Publication date Nov 14, 2024
    • Wuhan Neurophth Biotechnology Limited Company
    • Bin LI
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    Adeno-associated virus vectors modified to bind High-Density Lipopr...

    • Publication number 20240374755
    • Publication date Nov 14, 2024
    • uniQure biopharma B.V.
    • Sander Jan Hendrik Van Deventer
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
  • Information Patent Application

    MODIFIED AAV CAPSIDS AND VECTORS

    • Publication number 20240352077
    • Publication date Oct 24, 2024
    • Children's Medical Research Institute
    • Marti Cabanes Creus
    • C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...