Vectors comprising a coding region that has been codon optimised for expression in a respective host

Industry

CPC
C12N2800/22

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Parent Industries

CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2800/00Nucleic acids vectors

Current Industry

C12N2800/22Vectors comprising a coding region that has been codon optimised for expression in a respective host

Industries

Patents Grantslast 30 patents

Information Patent Grant
Treatment for restoring ureagenesis in carbamoyl phosphate syntheta...
- Patent number 12,281,323
- Issue date Apr 22, 2025
- The Regents of the University of California
- Gerald Lipshutz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized factor IX gene
- Patent number 12,275,970
- Issue date Apr 15, 2025
- Bioverativ Therapeutics Inc.
- Siyuan Tan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized FIG4 genes and expression cassettes and their use
- Patent number 12,270,057
- Issue date Apr 8, 2025
- The University of North Carolina at Chapel Hill
- Steven James Gray
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Composition for treating or preventing colorectal disease containin...
- Patent number 12,269,850
- Issue date Apr 8, 2025
- Cell Biotech Co., Ltd.
- Myung Jun Chung
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
CRISPR systems with engineered dual guide nucleic acids
- Patent number 12,270,044
- Issue date Apr 8, 2025
- Celyntra Therapeutics SA
- Ryan T. Gill
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized mini-dystrophin genes and expression cassettes and their use
- Patent number 12,257,321
- Issue date Mar 25, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Optimised coding sequence and promoter
- Patent number 12,257,319
- Issue date Mar 25, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Delivery, Engineering and optimization of systems, methods and comp...
- Patent number 12,252,707
- Issue date Mar 18, 2025
- The Broad Institute, Inc.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for therapeutic administration of messenger ribonucleic aci...
- Patent number 12,246,030
- Issue date Mar 11, 2025
- ModernaTX, Inc.
- Stephen Hoge
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus factor VIII vectors
- Patent number 12,239,692
- Issue date Mar 4, 2025
- Biomarin Pharmaceutical Inc.
- Peter Cameron Colosi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
GLP-1 and use thereof in compositions for treating metabolic diseases
- Patent number 12,221,615
- Issue date Feb 11, 2025
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA-targeting system
- Patent number 12,215,326
- Issue date Feb 4, 2025
- The Broad Institute, Inc.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus (AAV) delivery of anti-FAM19A5 antibodies
- Patent number 12,215,338
- Issue date Feb 4, 2025
- Neuracle Science Co., Ltd.
- Jong-Mook Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Balanced indels
- Patent number 12,215,363
- Issue date Feb 4, 2025
- Keygene N.V.
- Paul Bundock
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV-IDUA vector for treatment of MPS I-associated blindness
- Patent number 12,201,697
- Issue date Jan 21, 2025
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-guided nucleases
- Patent number 12,195,749
- Issue date Jan 14, 2025
- Inscripta, Inc.
- Andrew Garst
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant RSV with silent mutations, vaccines, and methods relate...
- Patent number 12,186,386
- Issue date Jan 7, 2025
- Emory University and Children's Healthcare of Atlanta, Inc.
- Martin L. Moore
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified plant endosperm specific promoter and use thereof
- Patent number 12,188,030
- Issue date Jan 7, 2025
- WUHAN HEALTHGEN BIOTECHNOLOGY CORP.
- Daichang Yang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid-guided nucleases
- Patent number 12,180,502
- Issue date Dec 31, 2024
- Inscripta, Inc.
- Andrew Garst
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Engineered CRISPR-Cas9 nucleases with altered PAM specificity
- Patent number 12,180,520
- Issue date Dec 31, 2024
- The General Hospital Corporation
- J. Keith Joung
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Codon-optimized reduced-size ATP7A CDNA and uses for treatment of c...
- Patent number 12,173,306
- Issue date Dec 24, 2024
- The United States of America, as represented by the Secretary, Dept. of Healt...
- Stephen G. Kaler
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for ciliopathies
- Patent number 12,171,794
- Issue date Dec 24, 2024
- UCL BUSINESS LTD
- Philip Beales
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for controlling gene editing
- Patent number 12,173,290
- Issue date Dec 24, 2024
- CRISPR THERAPEUTICS AG
- Ryo Takeuchi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating or preventing pyruvate kinase deficiency
- Patent number 12,163,151
- Issue date Dec 10, 2024
- CENTRO DE INVESTIGACIONES ENERGETICAS, MEDIOAMBIENTALES Y TECNOLOGICAS O.A, M.P.
- Jose C. Segovia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for treatment of ocular disorders and blin...
- Patent number 12,097,267
- Issue date Sep 24, 2024
- The Trustees of the University of Pennsylvania
- Jeannette Bennicelli
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Codon-optimized acid alpha-glucosidase expression cassettes and met...
- Patent number 12,084,693
- Issue date Sep 10, 2024
- SPARK THERAPEUTICS, INC.
- Xavier Anguela
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transgene cassettes, AAV vectors and AAV viral vectors for the expr...
- Patent number 12,077,772
- Issue date Sep 3, 2024
- The Board of Regents of the University of Texas System
- Steven J. Gray
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods and materials for producing recombinant viruses in eukaryot...
- Patent number 12,077,748
- Issue date Sep 3, 2024
- The Research Institute at Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Fusion protein between short form rod-derived cone viability factor...
- Patent number 12,076,367
- Issue date Sep 3, 2024
- Pharma Cinq, LLC
- Tianci Luo
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Viral synthetic nucleic acid sequences and use thereof
- Patent number 12,065,651
- Issue date Aug 20, 2024
- SYNVACCINE LTD.
- Tamir Tuller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
CODON-OPTIMIZED SMAD7 GENE THERAPY TO TREAT AND PREVENT MUSCLE WAST...
- Publication number 20250135037
- Publication date May 1, 2025
- AAVogen Inc.
- Buel D. Rodgers
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Novel Epstein Barr Virus Immunotherapies
- Publication number 20250127884
- Publication date Apr 24, 2025
- The Wistar Institute of Anatomy and Biology
- David Weiner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CODON-OPTIMIZED REDUCED-SIZE ATP7A CDNA AND USES FOR TREATMENT OF C...
- Publication number 20250129382
- Publication date Apr 24, 2025
- The United States of America, as Represented by the Secretary, Dept. of Healt...
- Stephen G. Kaler
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF IMPROVING PROTEIN EXPRESSION
- Publication number 20250115660
- Publication date Apr 10, 2025
- AstraZeneca AB
- Sarah DUNN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR GENETIC HEARING LOSS
- Publication number 20250114480
- Publication date Apr 10, 2025
- BridgeBio Gene Therapy Research, Inc.
- Clayton BEARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FUSION PROTEINS, COMPOSITIONS COMPRISING THE SAME, AND METHODS OF U...
- Publication number 20250109389
- Publication date Apr 3, 2025
- PAIRWISE PLANTS SERVICES, INC.
- Nathaniel Allen Wesley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MATERIALS AND METHODS FOR CONTROLLING GENE EDITING
- Publication number 20250101439
- Publication date Mar 27, 2025
- CRISPR Therapeutics AG
- Ryo TAKEUCHI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...
- Publication number 20250101396
- Publication date Mar 27, 2025
- Spark Therapeutics, Inc.
- Xavier Anguela
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NUCLEIC ACID-GUIDED NUCLEASES
- Publication number 20250075232
- Publication date Mar 6, 2025
- Inscripta, Inc.
- Andrew Garst
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HVT AIV VECTORS AND USES THEREOF
- Publication number 20250064917
- Publication date Feb 27, 2025
- Teshome Mebatsion
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID-GUIDED NUCLEASES
- Publication number 20250066818
- Publication date Feb 27, 2025
- Inscripta, Inc.
- Andrew Garst
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR CILIOPATHIES
- Publication number 20250057899
- Publication date Feb 20, 2025
- UCL Business LTD
- Philip Beales
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED ONCOLYTIC HERPESVIRUSES
- Publication number 20250049867
- Publication date Feb 13, 2025
- VIROGIN BIOTECH CANADA LTD
- Michael FLOYD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING BAG-3 RELATED CARDIOMYOPATHY...
- Publication number 20250041453
- Publication date Feb 6, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL CRISPR-ASSOCIATED (CAS) PROTEIN
- Publication number 20250043257
- Publication date Feb 6, 2025
- Locanabio, Inc.
- Matthew Merrill Carter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING MYBPC3 RELATED HYPERTROPHIC C...
- Publication number 20250041452
- Publication date Feb 6, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR IMPROVING THE EFFICACY OF CAS9-BASED K...
- Publication number 20250034562
- Publication date Jan 30, 2025
- AstraZeneca AB
- MARCELLO MARESCA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES TH...
- Publication number 20250025574
- Publication date Jan 23, 2025
- Regenxbio Inc.
- Randolph Qian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTI-CANCER PEPTIDE
- Publication number 20250011469
- Publication date Jan 9, 2025
- Minerva Biotechnologies Corporation
- Cynthia BAMDAD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CPF1 PROTEIN AND ITS USE IN GENE EDITING
- Publication number 20250002882
- Publication date Jan 2, 2025
- ZHEJIANG LAB
- JIN TANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GA...
- Publication number 20240424141
- Publication date Dec 26, 2024
- CANbridge Pharmaceuticals, Inc.
- Yunxiang Zhu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
AADC POLYNUCLEOTIDES FOR THE TREATMENT OF PARKINSON'S DISEASE
- Publication number 20240415943
- Publication date Dec 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV-MEDIATED THERAPIES FOR VISION LOSS ASSOCIATED WITH FRIEDREICH’S...
- Publication number 20240415983
- Publication date Dec 19, 2024
- University of Florida Research Foundation, Incorporated
- Sanford L. Boye
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLY-TAILED AND POLY-CAPPED MRNA AND USES THEREOF
- Publication number 20240392311
- Publication date Nov 28, 2024
- THE BROAD INSTITUTE, INC.
- Xiao WANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSGENE CASSETTES, AAV VECTORS AND AAV VIRAL VECTORS FOR THE EXPR...
- Publication number 20240376498
- Publication date Nov 14, 2024
- The Board of Regents of the University of Texas System
- Steven J. GRAY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUR...
- Publication number 20240376164
- Publication date Nov 14, 2024
- Wuhan Neurophth Biotechnology Limited Company
- Bin LI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FUSION PROTEIN BETWEEN SHORT FORM ROD-DERIVED CONE VIABILITY FACTOR...
- Publication number 20240374683
- Publication date Nov 14, 2024
- PHARMA CINQ, LLC
- Tianci LUO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR PRODUCING RECOMBINANT VIRUSES IN EUKARYOT...
- Publication number 20240368528
- Publication date Nov 7, 2024
- The Research Institute at Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANIMAL FREE- ALPHA-LACTALBUMIN AND BETA-LACTOGLOBULIN FUSION MILK P...
- Publication number 20240352091
- Publication date Oct 24, 2024
- HENI INNOVATION PRIVATE LIMITED
- PARINI KAPADIA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VACCINE COMPOSITIONS AND METHODS FOR ENHANCED ANTIGEN-SPECIFIC VACC...
- Publication number 20240350606
- Publication date Oct 24, 2024
- DUKE UNIVERSITY
- YOU-WEN HE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Vectors comprising a coding region that has been codon optimised for expression in a respective host

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Treatment for restoring ureagenesis in carbamoyl phosphate syntheta...

Optimized factor IX gene

Optimized FIG4 genes and expression cassettes and their use

Composition for treating or preventing colorectal disease containin...

CRISPR systems with engineered dual guide nucleic acids

Optimized mini-dystrophin genes and expression cassettes and their use

Optimised coding sequence and promoter

Delivery, Engineering and optimization of systems, methods and comp...

Methods for therapeutic administration of messenger ribonucleic aci...

Adeno-associated virus factor VIII vectors

GLP-1 and use thereof in compositions for treating metabolic diseases

RNA-targeting system

Adeno-associated virus (AAV) delivery of anti-FAM19A5 antibodies

Balanced indels

AAV-IDUA vector for treatment of MPS I-associated blindness

Nucleic acid-guided nucleases

Recombinant RSV with silent mutations, vaccines, and methods relate...

Modified plant endosperm specific promoter and use thereof

Nucleic acid-guided nucleases

Engineered CRISPR-Cas9 nucleases with altered PAM specificity

Codon-optimized reduced-size ATP7A CDNA and uses for treatment of c...

Gene therapy for ciliopathies

Materials and methods for controlling gene editing

Methods of treating or preventing pyruvate kinase deficiency

Methods and compositions for treatment of ocular disorders and blin...

Codon-optimized acid alpha-glucosidase expression cassettes and met...

Transgene cassettes, AAV vectors and AAV viral vectors for the expr...

Methods and materials for producing recombinant viruses in eukaryot...

Fusion protein between short form rod-derived cone viability factor...

Viral synthetic nucleic acid sequences and use thereof

Patents Applicationslast 30 patents

CODON-OPTIMIZED SMAD7 GENE THERAPY TO TREAT AND PREVENT MUSCLE WAST...

Novel Epstein Barr Virus Immunotherapies

CODON-OPTIMIZED REDUCED-SIZE ATP7A CDNA AND USES FOR TREATMENT OF C...

METHODS OF IMPROVING PROTEIN EXPRESSION

GENE THERAPY FOR GENETIC HEARING LOSS

FUSION PROTEINS, COMPOSITIONS COMPRISING THE SAME, AND METHODS OF U...

MATERIALS AND METHODS FOR CONTROLLING GENE EDITING

CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...

NUCLEIC ACID-GUIDED NUCLEASES

HVT AIV VECTORS AND USES THEREOF

NUCLEIC ACID-GUIDED NUCLEASES

GENE THERAPY FOR CILIOPATHIES

ENGINEERED ONCOLYTIC HERPESVIRUSES

METHODS AND COMPOSITIONS FOR TREATING BAG-3 RELATED CARDIOMYOPATHY...

NOVEL CRISPR-ASSOCIATED (CAS) PROTEIN

METHODS AND COMPOSITIONS FOR TREATING MYBPC3 RELATED HYPERTROPHIC C...

COMPOSITIONS AND METHODS FOR IMPROVING THE EFFICACY OF CAS9-BASED K...

ENGINEERED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USES TH...

ANTI-CANCER PEPTIDE

CPF1 PROTEIN AND ITS USE IN GENE EDITING

AAV PARTICLES COMPRISING A LIVER-TROPIC CAPSID PROTEIN AND ALPHA-GA...

AADC POLYNUCLEOTIDES FOR THE TREATMENT OF PARKINSON'S DISEASE

AAV-MEDIATED THERAPIES FOR VISION LOSS ASSOCIATED WITH FRIEDREICH’S...

POLY-TAILED AND POLY-CAPPED MRNA AND USES THEREOF

TRANSGENE CASSETTES, AAV VECTORS AND AAV VIRAL VECTORS FOR THE EXPR...

COMPOSITIONS AND METHODS FOR TREATING LEBER'S HEREDITARY OPTIC NEUR...

FUSION PROTEIN BETWEEN SHORT FORM ROD-DERIVED CONE VIABILITY FACTOR...

METHODS AND MATERIALS FOR PRODUCING RECOMBINANT VIRUSES IN EUKARYOT...

ANIMAL FREE- ALPHA-LACTALBUMIN AND BETA-LACTOGLOBULIN FUSION MILK P...

VACCINE COMPOSITIONS AND METHODS FOR ENHANCED ANTIGEN-SPECIFIC VACC...