viral genome or elements thereof as genetic vector

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C12N2750/14143

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2750/00ssDNA Viruses

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C12N2750/14143viral genome or elements thereof as genetic vector

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Patents Grantslast 30 patents

Information Patent Grant
Variant RNAi against alpha-synuclein
- Patent number 12,365,895
- Issue date Jul 22, 2025
- Genzyme Corporation
- Bradford Elmer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid molecules and uses thereof for non-viral gene therapy
- Patent number 12,364,774
- Issue date Jul 22, 2025
- Bioverativ Therapeutics Inc.
- Tongyao Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Anti-VEGF antibody constructs
- Patent number 12,365,726
- Issue date Jul 22, 2025
- Akouos, Inc.
- Emmanuel John Simons
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for improving production of car T cells
- Patent number 12,365,733
- Issue date Jul 22, 2025
- Cellectis
- Alex Boyne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for making epigenetic modifications
- Patent number 12,365,884
- Issue date Jul 22, 2025
- Whitehead Institute for Biomedical Research
- Edwin Neumann
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Scalable clarification process for recombinant AAV production
- Patent number 12,365,865
- Issue date Jul 22, 2025
- REGENXBIO Inc.
- Claire G. Zhang
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Grant
Conserved region T cell vaccines for coronavirus and methods of use
- Patent number 12,364,750
- Issue date Jul 22, 2025
- Triad National Security, LLC
- Bette T. M. Korber
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized CYP4V2 gene and application thereof
- Patent number 12,357,706
- Issue date Jul 15, 2025
- SUZHOU NGGT BIOTECHNOLOGY CO., LTD.
- Qing Cao
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Intrathecal delivery of recombinant adeno-associated virus encoding...
- Patent number 12,357,663
- Issue date Jul 15, 2025
- Nationwide Children's Hospital, Inc.
- Brian K. Kaspar
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Capsid-modified rAAV vector compositions and methods therefor
- Patent number 12,358,954
- Issue date Jul 15, 2025
- University of Florida Research Foundation, Incorporated
- Arun Srivastava
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for expressing otoferlin
- Patent number 12,359,221
- Issue date Jul 15, 2025
- The Regents of the University of California
- Sanford L. Boye
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating laminopathies
- Patent number 12,357,707
- Issue date Jul 15, 2025
- Encoded Therapeutics, Inc.
- Sirika Wood
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Methods of predicting ancestral virus sequences and uses thereof
- Patent number 12,359,174
- Issue date Jul 15, 2025
- The Schepens Eye Research Institute, Inc.
- Luk H. Vandenberghe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CNS gene delivery using peripheral administration of AAV vectors
- Patent number 12,351,816
- Issue date Jul 8, 2025
- Genethon
- Martine Barkats
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Delivery of large payloads
- Patent number 12,350,368
- Issue date Jul 8, 2025
- The Broad Institute, Inc.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated virus particle purification with multi...
- Patent number 12,351,832
- Issue date Jul 8, 2025
- Institut National de la Sante et de la Recherche Medicale (INSERM)
- Nicole Brument
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Grant
Gene therapy for neurodegenerative disorders
- Patent number 12,350,311
- Issue date Jul 8, 2025
- Genzyme Corporation
- Marco A. Passini
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Composition for regulating production of proteins
- Patent number 12,351,835
- Issue date Jul 8, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Viral vector production
- Patent number 12,344,857
- Issue date Jul 1, 2025
- UNIVERSITY OF MASSACHUSETTS
- Jun Xie
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV-mediated subcellular targeting of heterologous rhodopsins in re...
- Patent number 12,343,408
- Issue date Jul 1, 2025
- Wayne State University
- Zhuo-Hua Pan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treating and preventing macular degene...
- Patent number 12,344,842
- Issue date Jul 1, 2025
- Genzyme Corporation
- Samuel Wadsworth
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Preparation method and system for recombinant adeno-associated viru...
- Patent number 12,344,856
- Issue date Jul 1, 2025
- Genevoyager (Wuhan) Co., Ltd.
- Ting Mei
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Non-viral DNA vectors and uses thereof for expressing FVIII therape...
- Patent number 12,338,275
- Issue date Jun 24, 2025
- Generation Bio Co.
- Douglas Anthony Kerr
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Treatment and prevention of ocular neurodegenerative disorder
- Patent number 12,336,986
- Issue date Jun 24, 2025
- The Jackson Laboratory
- Simon W. M. John
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
OPA1 antisense oligomers for treatment of conditions and diseases
- Patent number 12,338,437
- Issue date Jun 24, 2025
- Stoke Therapeutics, Inc.
- Isabel Aznarez
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Enhanced modified viral capsid proteins
- Patent number 12,338,449
- Issue date Jun 24, 2025
- Research Institute at Nationwide Children's Hospital
- Scott Allen Loiler
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Dystrophin R16/R17 syntrophin PDZ fusion proteins
- Patent number 12,337,040
- Issue date Jun 24, 2025
- The Curators of the University of Missouri
- Dongsheng Duan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions useful in treatment of metachromatic leukodystrophy
- Patent number 12,338,451
- Issue date Jun 24, 2025
- James M. Wilson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions for regulating production of an antibody like protein...
- Patent number 12,338,452
- Issue date Jun 24, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Viral vectors exhibiting improved gene delivery properties
- Patent number 12,338,267
- Issue date Jun 24, 2025
- President and Fellows of Harvard College
- George M. Church
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250235550
- Publication date Jul 24, 2025
- Allen Institute
- Tanya Daigle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
- Publication number 20250235554
- Publication date Jul 24, 2025
- Novartis AG
- Keith MANSFIELD
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS FOR INTRATUMORAL DELIVERY OF CRISPR/CAS SYSTEMS
- Publication number 20250235555
- Publication date Jul 24, 2025
- Christiana Care Gene Editing Institute, Inc.
- Eric B. Kmiec
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Tissue Engineered Spinal Tracts For Functional Regeneration After S...
- Publication number 20250235585
- Publication date Jul 24, 2025
- The Trustees of the University of Pennsylvania
- Daniel Kacy Cullen
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
LARGE SERINE RECOMBINASES, SYSTEMS AND USES THEREOF
- Publication number 20250236852
- Publication date Jul 24, 2025
- Beam Therapeutics Inc.
- Zharko DANILOSKI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EX...
- Publication number 20250236886
- Publication date Jul 24, 2025
- Allen Institute
- Lucas T. Graybuck
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERING AND OPTIMIZATION OF IMPROVED SYSTEMS, METHODS AND ENZYM...
- Publication number 20250236856
- Publication date Jul 24, 2025
- THE BROAD INSTITUTE, INC.
- Feng Zhang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT PARVOVIRAL VECTORS AND METHOD OF MAKING AND USE THEREOF
- Publication number 20250236888
- Publication date Jul 24, 2025
- Nikegen LIMITED
- Weidong XIAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTORS AND METHODS FOR THE TREATMENT OF NEURODEGENERATION, DELAYIN...
- Publication number 20250235513
- Publication date Jul 24, 2025
- The General Hospital Corporation
- Cinzia VICIDOMINI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY FOR AUTOSOMAL DOMINANT DISEASES
- Publication number 20250235556
- Publication date Jul 24, 2025
- THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK
- Wen-Hsuan WU
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
DEGRON FUSION CONSTRUCTS
- Publication number 20250235558
- Publication date Jul 24, 2025
- VectorY B.V.
- Barbara Sanders
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHOD FOR TARGETED GENE INSERTION INTO IMMUNE CELLS
- Publication number 20250235477
- Publication date Jul 24, 2025
- Miltenyi Biotec B.V. & Co. KG
- Dominik LOCK
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SAFETY SWITCHES TO CONTROL IN VITRO AND IN VIVO PROLIFERATION OF CE...
- Publication number 20250230470
- Publication date Jul 17, 2025
- Sana Biotechnology, Inc.
- Eleonore THAM
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODIFIED BATCH AAV PRODUCTION SYSTEMS AND METHODS
- Publication number 20250230418
- Publication date Jul 17, 2025
- ULTRAGENYX PHARMACEUTICAL INC.
- Cameron Tage Fulco
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSID VARIANTS AND USES THEREOF
- Publication number 20250228967
- Publication date Jul 17, 2025
- VOYAGER THERAPEUTICS, INC.
- Mathieu Emmanuel Nonnenmacher
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHOD OF PRODUCTION AND USE OF PREPARATION COMPRISING CODON-OPTIMI...
- Publication number 20250228972
- Publication date Jul 17, 2025
- CHILDREN'S HOSPITAL OF ZHEJIANG UNIVERSITY SCHOOL OF MEDICINE
- YONGMIN TANG
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY
- Publication number 20250228973
- Publication date Jul 17, 2025
- PRECISION BIOSCIENCES, INC.
- James Jefferson Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
BASE EDITING METHODS AND COMPOSITIONS FOR TREATING TRIPLET REPEAT D...
- Publication number 20250228981
- Publication date Jul 17, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR THE TREATMENT OF COGNITIVE DISORDERS
- Publication number 20250228970
- Publication date Jul 17, 2025
- The Regents of the University of California
- Mark Tuszynski
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...
- Publication number 20250230467
- Publication date Jul 17, 2025
- The Johns Hopkins University
- Ingie Hong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR EFFICIENT AND STABLE GENETIC MODIFICAT...
- Publication number 20250228940
- Publication date Jul 17, 2025
- Yale University
- Sidi Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INTEGRATIVE PLASMID
- Publication number 20250230448
- Publication date Jul 17, 2025
- Synplogen Co., Ltd
- Shunsuke SAITO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE EDITING TO IMPROVE JOINT FUNCTION
- Publication number 20250228969
- Publication date Jul 17, 2025
- Orthobio Therapeutics, Inc.
- Peter J. Millet
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS...
- Publication number 20250228976
- Publication date Jul 17, 2025
- THE BROAD INSTITUTE, INC.
- Benjamin Deverman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR THE MAKING AND USING OF GUIDE NUCLEIC...
- Publication number 20250230432
- Publication date Jul 17, 2025
- JumpCode Genomics, Inc.
- Stephane B. GOURGUECHON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DYNAMIN-1 VARI...
- Publication number 20250230443
- Publication date Jul 17, 2025
- Research Institute at Nationwide Children's Hospital
- Scott Quenton Harper
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treating Striatonigral Degeneration
- Publication number 20250228977
- Publication date Jul 17, 2025
- Texas Scottish Rite Hospital for Children
- Jonathan J. Rios
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TA...
- Publication number 20250228885
- Publication date Jul 17, 2025
- The Board of Regents of the University of Texas System
- Hao Zhu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Novel systems for nucleic acid regulation
- Publication number 20250230437
- Publication date Jul 17, 2025
- uniQure biopharma B.V.
- Irena Bockaj
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION
- Publication number 20250222139
- Publication date Jul 10, 2025
- Shape Therapeutics Inc.
- Jacob Michael TOME
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

viral genome or elements thereof as genetic vector

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Variant RNAi against alpha-synuclein

Nucleic acid molecules and uses thereof for non-viral gene therapy

Anti-VEGF antibody constructs

Method for improving production of car T cells

Compositions and methods for making epigenetic modifications

Scalable clarification process for recombinant AAV production

Conserved region T cell vaccines for coronavirus and methods of use

Optimized CYP4V2 gene and application thereof

Intrathecal delivery of recombinant adeno-associated virus encoding...

Capsid-modified rAAV vector compositions and methods therefor

Compositions and methods for expressing otoferlin

Compositions and methods for treating laminopathies

Methods of predicting ancestral virus sequences and uses thereof

CNS gene delivery using peripheral administration of AAV vectors

Delivery of large payloads

Recombinant adeno-associated virus particle purification with multi...

Gene therapy for neurodegenerative disorders

Composition for regulating production of proteins

Viral vector production

AAV-mediated subcellular targeting of heterologous rhodopsins in re...

Compositions and methods for treating and preventing macular degene...

Preparation method and system for recombinant adeno-associated viru...

Non-viral DNA vectors and uses thereof for expressing FVIII therape...

Treatment and prevention of ocular neurodegenerative disorder

OPA1 antisense oligomers for treatment of conditions and diseases

Enhanced modified viral capsid proteins

Dystrophin R16/R17 syntrophin PDZ fusion proteins

Compositions useful in treatment of metachromatic leukodystrophy

Compositions for regulating production of an antibody like protein...

Viral vectors exhibiting improved gene delivery properties

Patents Applicationslast 30 patents

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY

METHODS FOR INTRATUMORAL DELIVERY OF CRISPR/CAS SYSTEMS

Tissue Engineered Spinal Tracts For Functional Regeneration After S...

LARGE SERINE RECOMBINASES, SYSTEMS AND USES THEREOF

ARTIFICIAL EXPRESSION CONSTRUCTS FOR SELECTIVELY MODULATING GENE EX...

ENGINEERING AND OPTIMIZATION OF IMPROVED SYSTEMS, METHODS AND ENZYM...

RECOMBINANT PARVOVIRAL VECTORS AND METHOD OF MAKING AND USE THEREOF

VECTORS AND METHODS FOR THE TREATMENT OF NEURODEGENERATION, DELAYIN...

GENE THERAPY FOR AUTOSOMAL DOMINANT DISEASES

DEGRON FUSION CONSTRUCTS

METHOD FOR TARGETED GENE INSERTION INTO IMMUNE CELLS

SAFETY SWITCHES TO CONTROL IN VITRO AND IN VIVO PROLIFERATION OF CE...

MODIFIED BATCH AAV PRODUCTION SYSTEMS AND METHODS

AAV CAPSID VARIANTS AND USES THEREOF

METHOD OF PRODUCTION AND USE OF PREPARATION COMPRISING CODON-OPTIMI...

GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY

BASE EDITING METHODS AND COMPOSITIONS FOR TREATING TRIPLET REPEAT D...

GENE THERAPY FOR THE TREATMENT OF COGNITIVE DISORDERS

METHODS AND MATERIALS FOR TREATING SYNGAP1-ASSOCIATED NEURODEVELOPM...

COMPOSITIONS AND METHODS FOR EFFICIENT AND STABLE GENETIC MODIFICAT...

INTEGRATIVE PLASMID

GENE EDITING TO IMPROVE JOINT FUNCTION

AAV CAPSIDS THAT ENABLE CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS...

METHODS AND COMPOSITIONS FOR THE MAKING AND USING OF GUIDE NUCLEIC...

PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DYNAMIN-1 VARI...

Compositions and Methods for Treating Striatonigral Degeneration

COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TA...

Novel systems for nucleic acid regulation

PROMOTER SWITCHES FOR TISSUE-SPECIFIC EXPRESSION