viral genome or elements thereof as genetic vector

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CPC
C12N2750/14143

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2750/00ssDNA Viruses

Current Industry

C12N2750/14143viral genome or elements thereof as genetic vector

Industries

Patents Grantslast 30 patents

Information Patent Grant
Compositions and methods for internalizing enzymes
- Patent number 12,215,138
- Issue date Feb 4, 2025
- REGENERON PHARMACEUTICALS, INC.
- Andrew Baik
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic applications of CPF1-based genome editing
- Patent number 12,214,056
- Issue date Feb 4, 2025
- Duke University
- Charles A. Gersbach
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Pharmaceutical composition for prevention or treatment of heart fai...
- Patent number 12,215,362
- Issue date Feb 4, 2025
- BETHPHAGEN INC.
- Tae Hwan Kwak
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for gene editing by targeting transferrin
- Patent number 12,215,320
- Issue date Feb 4, 2025
- CRISPR Therapeutics AG
- Alan Richard Brooks
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for making epigenetic modifications
- Patent number 12,215,361
- Issue date Feb 4, 2025
- Whitehead Institute for Biomedical Research
- Edwin Neumann
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Systems and methods for treating hyper-igm syndrome
- Patent number 12,214,055
- Issue date Feb 4, 2025
- Cecillia Cotta-Ramusino
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Modified adeno-associated virus 5 capsids and uses thereof
- Patent number 12,209,251
- Issue date Jan 28, 2025
- The University of North Carolina at Chapel Hill
- Xiao Xiao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Effective delivery of large genes by dual AAV vectors
- Patent number RE50283
- Issue date Jan 28, 2025
- FONDAZIONE TELETHON ETS
- Alberto Auricchio
Information Patent Grant
Intrathecal delivery of recombinant adeno-associated virus 9
- Patent number 12,208,144
- Issue date Jan 28, 2025
- Nationwide Children's Hospital
- Brian K. Kaspar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Factor IX encoding nucleotides
- Patent number 12,209,262
- Issue date Jan 28, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Viral gene therapy as treatment for cholesterol storage disease or...
- Patent number 12,201,658
- Issue date Jan 21, 2025
- The United States of America, as represented by the Secretary, Department of...
- Charles P. Venditti
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for retinitis pigmentosa
- Patent number 12,201,698
- Issue date Jan 21, 2025
- Genzyme Corporation
- Catherine O'Riordan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus compositions for restoring PAH gene function...
- Patent number 12,203,094
- Issue date Jan 21, 2025
- HOMOLOGY MEDICINES, INC.
- Albert Barnes Seymour
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treatment of dominant retinitis pigmen...
- Patent number 12,203,074
- Issue date Jan 21, 2025
- University of Florida Research Foundation, Incorporated
- Alfred S. Lewin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV-IDUA vector for treatment of MPS I-associated blindness
- Patent number 12,201,697
- Issue date Jan 21, 2025
- The University of North Carolina at Chapel Hill
- Matthew Louis Hirsch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapeutics for treating bone disorders
- Patent number 12,194,108
- Issue date Jan 14, 2025
- UNIVERSITY OF MASSACHUSETTS
- Jae-Hyuck Shim
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for modulating transduction efficiency of...
- Patent number 12,195,745
- Issue date Jan 14, 2025
- Massachusetts Eye and Ear Infirmary
- Luk H. Vandenberghe
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated virus gene therapy for 21-hydroxylase deficiency
- Patent number 12,195,767
- Issue date Jan 14, 2025
- Adrenas Therapeutics, Inc.
- Pierre Bougneres
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Synthetic combinatorial AAV3 capsid library
- Patent number 12,188,037
- Issue date Jan 7, 2025
- University of Florida Research Foundation, Incorporated
- Sergei Zolotukhin
- C40 - COMBINATORIAL CHEMISTRY
Information Patent Grant
Codon optimized otoferlin AAV dual vector gene therapy
- Patent number 12,188,041
- Issue date Jan 7, 2025
- University of Florida Research Foundation, Incorporated
- Frank M. Dyka
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy strategy to restore electrical and cardiac function, a...
- Patent number 12,186,369
- Issue date Jan 7, 2025
- The Regents of the University of California
- Farah Sheikh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for enhancing gene expression using AAV vector
- Patent number 12,188,040
- Issue date Jan 7, 2025
- GENE THERAPY RESEARCH INSTITUTION CO., LTD.
- Shin-ichi Muramatsu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric capsids
- Patent number 12,180,500
- Issue date Dec 31, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Systemic gene replacement therapy for treatment of X-linked myotubu...
- Patent number 12,178,856
- Issue date Dec 31, 2024
- Wake Forest University Health Sciences Genethon
- Martin K. Childers
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Factor H variants for treatment of disease
- Patent number 12,180,254
- Issue date Dec 31, 2024
- The Trustees of the University of Pennsylvania
- Wenchao Song
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for rapid generation of single and multipl...
- Patent number 12,180,510
- Issue date Dec 31, 2024
- RXCELL INC.
- Xianmin Zeng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Automated production of viral vectors
- Patent number 12,180,511
- Issue date Dec 31, 2024
- Lonza Walkersville, Inc.
- Matthew Hewitt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions relating to the treatment of tumors
- Patent number 12,178,845
- Issue date Dec 31, 2024
- The General Hospital Corporation
- Gary J. Brenner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for impeding transcription of expanded mic...
- Patent number 12,180,499
- Issue date Dec 31, 2024
- University of Florida Research Foundation, Inc.
- Eric Tzy-Shi Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CDKN2A companion diagnostic for bladder cancer interferon therapy
- Patent number 12,178,865
- Issue date Dec 31, 2024
- Trizell Limited
- Colin P. Dinney
- G01 - MEASURING TESTING

Patents Applicationslast 30 patents

Information Patent Application
ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF
- Publication number 20250041450
- Publication date Feb 6, 2025
- Insmed Incorporated
- Brian KASPAR
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING BAG-3 RELATED CARDIOMYOPATHY...
- Publication number 20250041453
- Publication date Feb 6, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUTANT MYOCILIN DISEASE MODEL AND USES THEREOF
- Publication number 20250040522
- Publication date Feb 6, 2025
- Regeneron Pharmaceuticals, Inc.
- Gaurang Patel
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTI-TFR:GAA AND ANTI-CD63:GAA INSERTION FOR TREATMENT OF POMPE DIS...
- Publication number 20250041455
- Publication date Feb 6, 2025
- Regeneron Pharmaceuticals, Inc.
- Andrew Baik
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED MUSCLE TARGETING COMPOSITIONS
- Publication number 20250043309
- Publication date Feb 6, 2025
- THE BROAD INSTITUTE, INC.
- Pardis SABETI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Gene Therapy of Fibroblast Growth Factor 23 Related Hypophosphatemi...
- Publication number 20250041448
- Publication date Feb 6, 2025
- GENETHON
- Giuseppe RONZITTI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR HEARING LOSS
- Publication number 20250041451
- Publication date Feb 6, 2025
- Perceive Biotherapeutics, Inc.
- Derek Welsbie
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT AAV VECTORS FOR TREATING NEURODEGENERATIVE DISORDERS
- Publication number 20250041456
- Publication date Feb 6, 2025
- SHANGHAI VITALGEN BIOPHARMA CO., LTD.
- Yezheng TAO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RESCUING VOLTAGE-GATED SODIUM CHANNEL FUNCTION IN INHIBITORY NEURONS
- Publication number 20250041384
- Publication date Feb 6, 2025
- Allen Institute
- John K. Mich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
- Publication number 20250041445
- Publication date Feb 6, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Use of Long Non-Coding RNA (lncRNA) in Preparation of Drug for Cont...
- Publication number 20250041444
- Publication date Feb 6, 2025
- Yanbian University
- Lan Hong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF PROTEOPATHIES
- Publication number 20250042958
- Publication date Feb 6, 2025
- SOLA BIOSCIENCES LLC
- Akinori Hishiya
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING MYBPC3 RELATED HYPERTROPHIC C...
- Publication number 20250041452
- Publication date Feb 6, 2025
- University of Florida Research Foundation, Incorporated
- Barry John Byrne
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...
- Publication number 20250041454
- Publication date Feb 6, 2025
- Allen Institute
- Edward Sebastian Lein
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENHANCERS FOR DIRECTED EXPRESSION OF GENES IN NEURONAL CELL POPULAT...
- Publication number 20250032646
- Publication date Jan 30, 2025
- THE BROAD INSTITUTE, INC.
- Jordane Dimidschstein
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
OPTOGENETIC VISUAL RESTORATION USING LIGHT-SENSITIVE GQ-COUPLED NEU...
- Publication number 20250032577
- Publication date Jan 30, 2025
- GENANS BIOTECHNOLOGY CO., LTD
- Tao Yu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
HIGH EFFICIENCY LIBRARY-IDENTIFIED AAV VECTORS
- Publication number 20250034555
- Publication date Jan 30, 2025
- University of Massachusetts
- Miguel Sena Esteves
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS
- Publication number 20250034556
- Publication date Jan 30, 2025
- THE BROAD INSTITUTE, INC.
- Binhui Zhao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND SYSTEMS FOR TRANSFECTING HOST CELLS
- Publication number 20250034590
- Publication date Jan 30, 2025
- Biogen MA Inc.
- Jenny Wang-Yuanzhen Shupe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions And Methods For Treating Mucopolysaccharidosis IIIA
- Publication number 20250034533
- Publication date Jan 30, 2025
- Amicus Therapeutics, Inc.
- Leida Rassouli-Taylor
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLYNUCLEOTIDES ENCODING ENGINEERED MEGANUCLEASES HAVING SPECIFICIT...
- Publication number 20250034536
- Publication date Jan 30, 2025
- PRECISION BIOSCIENCES, INC.
- Gary Owens
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF NONALCOHOLIC STEATOHE...
- Publication number 20250032645
- Publication date Jan 30, 2025
- THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK
- Ira TABAS
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CRISPR-MEDIATED TRANSGENE INSERTION IN NEONATAL CELLS
- Publication number 20250032642
- Publication date Jan 30, 2025
- Regeneron Pharmaceuticals, Inc.
- Andrew Baik
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SYNTHETIC RECEPTORS
- Publication number 20250032643
- Publication date Jan 30, 2025
- UCL Business LTD
- Dimitri KULLMANN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MIR155 AS THE INTEGRATION SITE TO OVERCOME ACUTE GRAFT VERSUS HOST...
- Publication number 20250032545
- Publication date Jan 30, 2025
- Ohio State Innovation Foundation
- Parvathi Ranganathan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING HYPOPHOSPHATASIA
- Publication number 20250034534
- Publication date Jan 30, 2025
- SANFORD BURNHAM PREBYS MEDICAL DISCOVERY INSTITUTE
- Koichi MIYAKE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODOLOGY TO CHARACTERIZE EMPTY-FULL RATIO IN CRUDE AAV SAMPLES
- Publication number 20250035532
- Publication date Jan 30, 2025
- Regeneron Pharmaceuticals, Inc.
- Deepanshu Choudhary
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Application
METHODS FOR DETECTING AAV
- Publication number 20250027951
- Publication date Jan 23, 2025
- Genzyme Corporation
- Xiaoying JIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Cell-Specific Expression of Target Genes
- Publication number 20250025575
- Publication date Jan 23, 2025
- The Trustees of Princeton University
- Carola Maturana
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND MATERIALS FOR GALGT2 GENE THERAPY
- Publication number 20250025578
- Publication date Jan 23, 2025
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

viral genome or elements thereof as genetic vector

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Compositions and methods for internalizing enzymes

Therapeutic applications of CPF1-based genome editing

Pharmaceutical composition for prevention or treatment of heart fai...

Compositions and methods for gene editing by targeting transferrin

Compositions and methods for making epigenetic modifications

Systems and methods for treating hyper-igm syndrome

Modified adeno-associated virus 5 capsids and uses thereof

Effective delivery of large genes by dual AAV vectors

Intrathecal delivery of recombinant adeno-associated virus 9

Factor IX encoding nucleotides

Viral gene therapy as treatment for cholesterol storage disease or...

Gene therapy for retinitis pigmentosa

Adeno-associated virus compositions for restoring PAH gene function...

Compositions and methods for treatment of dominant retinitis pigmen...

AAV-IDUA vector for treatment of MPS I-associated blindness

Gene therapeutics for treating bone disorders

Compositions and methods for modulating transduction efficiency of...

Adeno-associated virus gene therapy for 21-hydroxylase deficiency

Synthetic combinatorial AAV3 capsid library

Codon optimized otoferlin AAV dual vector gene therapy

Gene therapy strategy to restore electrical and cardiac function, a...

Method for enhancing gene expression using AAV vector

Chimeric capsids

Systemic gene replacement therapy for treatment of X-linked myotubu...

Factor H variants for treatment of disease

Methods and compositions for rapid generation of single and multipl...

Automated production of viral vectors

Methods and compositions relating to the treatment of tumors

Compositions and methods for impeding transcription of expanded mic...

CDKN2A companion diagnostic for bladder cancer interferon therapy

Patents Applicationslast 30 patents

ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF

METHODS AND COMPOSITIONS FOR TREATING BAG-3 RELATED CARDIOMYOPATHY...

MUTANT MYOCILIN DISEASE MODEL AND USES THEREOF

ANTI-TFR:GAA AND ANTI-CD63:GAA INSERTION FOR TREATMENT OF POMPE DIS...

ENGINEERED MUSCLE TARGETING COMPOSITIONS

Gene Therapy of Fibroblast Growth Factor 23 Related Hypophosphatemi...

GENE THERAPY FOR HEARING LOSS

RECOMBINANT AAV VECTORS FOR TREATING NEURODEGENERATIVE DISORDERS

RESCUING VOLTAGE-GATED SODIUM CHANNEL FUNCTION IN INHIBITORY NEURONS

GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

Use of Long Non-Coding RNA (lncRNA) in Preparation of Drug for Cont...

COMPOSITIONS AND METHODS FOR THE TREATMENT OF PROTEOPATHIES

METHODS AND COMPOSITIONS FOR TREATING MYBPC3 RELATED HYPERTROPHIC C...

ARTIFICIAL EXPRESSION CONSTRUCTS FOR MODULATING GENE EXPRESSION IN...

ENHANCERS FOR DIRECTED EXPRESSION OF GENES IN NEURONAL CELL POPULAT...

OPTOGENETIC VISUAL RESTORATION USING LIGHT-SENSITIVE GQ-COUPLED NEU...

HIGH EFFICIENCY LIBRARY-IDENTIFIED AAV VECTORS

COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS

METHODS AND SYSTEMS FOR TRANSFECTING HOST CELLS

Compositions And Methods For Treating Mucopolysaccharidosis IIIA

POLYNUCLEOTIDES ENCODING ENGINEERED MEGANUCLEASES HAVING SPECIFICIT...

COMPOSITIONS AND METHODS FOR THE TREATMENT OF NONALCOHOLIC STEATOHE...

CRISPR-MEDIATED TRANSGENE INSERTION IN NEONATAL CELLS

SYNTHETIC RECEPTORS

MIR155 AS THE INTEGRATION SITE TO OVERCOME ACUTE GRAFT VERSUS HOST...

METHODS AND COMPOSITIONS FOR TREATING HYPOPHOSPHATASIA

METHODOLOGY TO CHARACTERIZE EMPTY-FULL RATIO IN CRUDE AAV SAMPLES

METHODS FOR DETECTING AAV

Compositions and Methods for Cell-Specific Expression of Target Genes

METHODS AND MATERIALS FOR GALGT2 GENE THERAPY