Adeno-associated virus

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CPC
C12N15/8645

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N15/00Mutation or genetic engineering DNA or RNA concerning genetic engineering, vectors

Current Industry

C12N15/8645Adeno-associated virus

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Scalable purification method for AAV1
- Patent number 12,163,160
- Issue date Dec 10, 2024
- The Trustees of the University of Pennsylvania
- Martin Lock
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Grant
Methods and materials for GALGT2 gene therapy
- Patent number 12,121,595
- Issue date Oct 22, 2024
- Research Institute at Nationwide Children's Hospital
- Paul Taylor Martin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Butyrylcholinesterases having an enhanced ability to hydrolyze acyl...
- Patent number 12,116,602
- Issue date Oct 15, 2024
- Mayo Foundation for Medical Education and Research
- Liyi Geng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant virus products and methods for inducing DUX4 exon skipping
- Patent number 12,084,658
- Issue date Sep 10, 2024
- Research Institute at Nationwide Children's Hospital
- Scott Quenton Harper
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AAV vectors targeted to oligodendrocytes
- Patent number 12,076,351
- Issue date Sep 3, 2024
- The University of North Carolina at Chapel Hill
- Thomas McCown
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Stable cell lines for inducible production of rAAV virions
- Patent number 12,054,738
- Issue date Aug 6, 2024
- Shape Therapeutics Inc.
- Kenneth Prentice
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Frataxin expression constructs
- Patent number 11,998,618
- Issue date Jun 4, 2024
- PRECIGEN, INC.
- Stephen Schauer
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapies for lysosomal disorders
- Patent number 11,993,790
- Issue date May 28, 2024
- Prevail Therapeutics, Inc.
- Asa Abeliovich
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Muscle-specific nucleic acid regulatory elements and methods and us...
- Patent number 11,975,078
- Issue date May 7, 2024
- Universiteit Gent
- Thierry Vandendriessche
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for neurometabolic disorders
- Patent number 11,957,765
- Issue date Apr 16, 2024
- Genzyme Corporation
- Marco A. Passini
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Restrictive inverted terminal repeats for viral vectors
- Patent number 11,939,597
- Issue date Mar 26, 2024
- The University of North Carolina at Chapel Hill
- Curtis Hewitt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression cassette with a SynP160 promoter
- Patent number 11,883,507
- Issue date Jan 30, 2024
- FRIEDRICH MIESCHER INSTITUTE FOR BIOMEDICAL RESEARCH
- Dominik Hartl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated viruses for delivering gene editing mo...
- Patent number 11,882,815
- Issue date Jan 30, 2024
- University of Massachusetts
- Jaime Antonio Rivera-Perez
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Scalable manufacturing platform for viral vector purification and v...
- Patent number 11,878,056
- Issue date Jan 23, 2024
- The Children's Hospital of Philadelphia
- John Fraser Wright
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapy for AADC deficiency
- Patent number 11,865,188
- Issue date Jan 9, 2024
- NATIONAL TAIWAN UNIVERSITY
- Mark Pykett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transgenic RPE cells overexpressing OTX2 for the treatment of retin...
- Patent number 11,865,189
- Issue date Jan 9, 2024
- SORBONNE UNIVERSITE
- Thierry Leveillard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Programmable assembly of virus composites for receptor-targeted gen...
- Patent number 11,851,671
- Issue date Dec 26, 2023
- Regents of The University of Minnesota
- Daniel Schmidt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus variant capsids and methods of use thereof
- Patent number 11,840,704
- Issue date Dec 12, 2023
- 4D MOLECULAR THERAPEUTICS INC.
- David H. Kirn
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Gene therapy for treating peroxisomal disorders
- Patent number 11,793,887
- Issue date Oct 24, 2023
- The Trustees of the University of Pennsylvania
- Nancy Braverman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
- Patent number 11,759,506
- Issue date Sep 19, 2023
- VOYAGER THERAPEUTICS, INC.
- Maria Scheel
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy vectors for treating heart disease
- Patent number 11,759,531
- Issue date Sep 19, 2023
- Tenaya Therapeutics, Inc.
- Laura Lombardi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Recombinant adeno-associated virus vectors with CD14 promoter and u...
- Patent number 11,761,020
- Issue date Sep 19, 2023
- Aavocyte, Inc.
- Aiquan Chang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus (AAV) producer cell line and related methods
- Patent number 11,739,347
- Issue date Aug 29, 2023
- LONZA WALKERVILLE, INC.
- Bingnan Gu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Scalable purification method for AAV9
- Patent number 11,732,245
- Issue date Aug 22, 2023
- The Trustees of the University of Pennsylvania
- Martin Lock
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vector delivery of micro-dystrophin to treat...
- Patent number 11,723,986
- Issue date Aug 15, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Scalable purification method for AAV8
- Patent number 11,718,835
- Issue date Aug 8, 2023
- Ths Trustees of the University of Pennsylvania
- Martin Lock
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Scalable purification method for AAVRH10
- Patent number 11,713,449
- Issue date Aug 1, 2023
- Ths Trustees of the University of Pennsylvania
- Martin Lock
- G01 - MEASURING TESTING
Information Patent Grant
Scalable purification method for AAV1
- Patent number 11,713,450
- Issue date Aug 1, 2023
- Ths Trustees of the University of Pennsylvania
- Martin Lock
- G01 - MEASURING TESTING
Information Patent Grant
Rational polyploid adeno-associated virus vectors for the treatment...
- Patent number 11,702,676
- Issue date Jul 18, 2023
- The University of North Carolina at Chapel Hill
- Chengwen Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapies for lysosomal disorders
- Patent number 11,661,585
- Issue date May 30, 2023
- Prevail Therapeutics, Inc.
- Asa Abeliovich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMPOSITIONS USEFUL IN TREATMENT OF CDKL5 DEFICIENCY DISORDER (CDD)
- Publication number 20240425882
- Publication date Dec 26, 2024
- The Trustees of the University of Pennsylvania
- James M. Wilson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
DIFFERENTIAL PROLIFERATION OF HUMAN HEMATOPOIETIC STEM AND PROGENIT...
- Publication number 20240409958
- Publication date Dec 12, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Matthew H. Porteus
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Treatment of Dry Age-Related Macular Degeneration
- Publication number 20240401082
- Publication date Dec 5, 2024
- Genzyme Corporation
- Matthew Adamowicz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HOST CELL LINES AND METHODS FOR IDENTIFYING AND USING SUCH HOST CEL...
- Publication number 20240392318
- Publication date Nov 28, 2024
- SANOFI
- Barak Balva
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR TREATING A PREMATURE TERMINATION CODON...
- Publication number 20240384300
- Publication date Nov 21, 2024
- Tevard Biosciences, Inc.
- Peter M. Eimon
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV Vectors Targeted to Oligodendrocytes
- Publication number 20240374662
- Publication date Nov 14, 2024
- The University of North Carolina at Chapel Hill
- Thomas McCown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE PRODUCTION OF LIBRARIES
- Publication number 20240352485
- Publication date Oct 24, 2024
- Flagship Pioneering Innovations VII, LLC
- Patrick Leo JONES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTOGENETIC VISUAL RESTORATION USING CHRIMSON
- Publication number 20240165198
- Publication date May 23, 2024
- Gensight Biologics SA
- Didier PRUNEAU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEASE-MEDIATED GENOME EDITING OF PRIMARY CELLS AND RELATED KITS
- Publication number 20240124895
- Publication date Apr 18, 2024
- The Board of Trustees of the Leland Stanford Junior University
- Daniel P. Dever
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions and Methods for Treating Hereditary Angioedema
- Publication number 20240110201
- Publication date Apr 4, 2024
- Spark Therapeutics, Inc.
- Christopher Riling
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR AADC DEFICIENCY
- Publication number 20240100186
- Publication date Mar 28, 2024
- National Taiwan University
- Mark Pykett
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS WITH CD14 PROMOTER AND U...
- Publication number 20240076693
- Publication date Mar 7, 2024
- Aavocyte, Inc.
- Aiquan CHANG
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I
- Publication number 20240024510
- Publication date Jan 25, 2024
- The Trustees of The University of Pennsylania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS (AAV) PRODUCER CELL LINE AND RELATED METHODS
- Publication number 20240018545
- Publication date Jan 18, 2024
- Lonza Walkersville, Inc.
- Bingnan GU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
FRATAXIN EXPRESSION CONSTRUCTS
- Publication number 20240000973
- Publication date Jan 4, 2024
- PRECIGEN, INC.
- Stephen SCHAUER
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SCALABLE PURIFICATION METHOD FOR AAV9
- Publication number 20230416695
- Publication date Dec 28, 2023
- The Trustees of the University of Pennsylvania
- Martin Lock
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Application
RATIONAL POLYPLOID ADENO-ASSOCIATED VIRUS VECTORS FOR THE TREATMENT...
- Publication number 20230392167
- Publication date Dec 7, 2023
- The University of North Carolina at Chapel Hill
- Chengwen Li
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY VECTORS FOR TREATING HEART DISEASE
- Publication number 20230372541
- Publication date Nov 23, 2023
- Tenaya Therapeutics, Inc.
- Laura LOMBARDI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR AMYOTROPHIC LATERAL SCLEROSIS AND OTHER SPINAL COR...
- Publication number 20230364200
- Publication date Nov 16, 2023
- Genzyme Corporation
- James Dodge
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF
- Publication number 20230332179
- Publication date Oct 19, 2023
- University of Massachusetts
- Guangping Gao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SCALABLE PURIFICATION METHOD FOR AAV1
- Publication number 20230323312
- Publication date Oct 12, 2023
- The Trustees of the University of Pennsylvania
- Martin Lock
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HIGH EFFICIENCY PURIFICATION OF DIVERGENT AAV SEROTYPES USING AAVX...
- Publication number 20230303983
- Publication date Sep 28, 2023
- President and Fellows of Harvard College
- Michael Florea
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS AND METHODS OF USE THEREOF
- Publication number 20230279435
- Publication date Sep 7, 2023
- 4D MOLECULAR THERAPEUTICS INC.
- David H. KIRN
- C07 - ORGANIC CHEMISTRY
Information Patent Application
TAU MODULATORS AND METHODS AND COMPOSITIONS FOR DELIVERY THEREOF
- Publication number 20230270774
- Publication date Aug 31, 2023
- Sangamo Therapeutics, Inc.
- Annemarie Ledeboer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compositions Useful in Treatment of Spinal Muscular Atrophy
- Publication number 20230265459
- Publication date Aug 24, 2023
- The Trustees of the University of Pennsylvania
- James M. Wilson
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TISSUE SELECTIVE TRANSGENE EXPRESSION
- Publication number 20230203531
- Publication date Jun 29, 2023
- Encoded Therapeutics, Inc.
- Stephanie TAGLIATELA
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR THE PURIFICATION OF ADENO-ASSOCIATED V...
- Publication number 20230183659
- Publication date Jun 15, 2023
- HOMOLOGY MEDICINES, INC.
- Michael MERCALDI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...
- Publication number 20230173101
- Publication date Jun 8, 2023
- Research Institute at Nationwide Children's Hospital
- Louise Rodino-Klapac
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RESTRICTIVE INVERTED TERMINAL REPEATS FOR VIRAL VECTORS
- Publication number 20230167418
- Publication date Jun 1, 2023
- The University of North Carolina at Chapel Hill
- Curtis Hewitt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTORS ENCODING MODIFIED G6PC AND USES THEREOF
- Publication number 20230144834
- Publication date May 11, 2023
- The USA, as represented by the Secretary, Department of Health and Human Serv...
- Janice J. Chou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Adeno-associated virus

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Scalable purification method for AAV1

Methods and materials for GALGT2 gene therapy

Butyrylcholinesterases having an enhanced ability to hydrolyze acyl...

Recombinant virus products and methods for inducing DUX4 exon skipping

AAV vectors targeted to oligodendrocytes

Stable cell lines for inducible production of rAAV virions

Frataxin expression constructs

Gene therapies for lysosomal disorders

Muscle-specific nucleic acid regulatory elements and methods and us...

Gene therapy for neurometabolic disorders

Restrictive inverted terminal repeats for viral vectors

Expression cassette with a SynP160 promoter

Recombinant adeno-associated viruses for delivering gene editing mo...

Scalable manufacturing platform for viral vector purification and v...

Gene therapy for AADC deficiency

Transgenic RPE cells overexpressing OTX2 for the treatment of retin...

Programmable assembly of virus composites for receptor-targeted gen...

Adeno-associated virus variant capsids and methods of use thereof

Gene therapy for treating peroxisomal disorders

AADC polynucleotides for the treatment of Parkinson's disease

Gene therapy vectors for treating heart disease

Recombinant adeno-associated virus vectors with CD14 promoter and u...

Adeno-associated virus (AAV) producer cell line and related methods

Scalable purification method for AAV9

Adeno-associated virus vector delivery of micro-dystrophin to treat...

Scalable purification method for AAV8

Scalable purification method for AAVRH10

Scalable purification method for AAV1

Rational polyploid adeno-associated virus vectors for the treatment...

Gene therapies for lysosomal disorders

Patents Applicationslast 30 patents

COMPOSITIONS USEFUL IN TREATMENT OF CDKL5 DEFICIENCY DISORDER (CDD)

DIFFERENTIAL PROLIFERATION OF HUMAN HEMATOPOIETIC STEM AND PROGENIT...

Treatment of Dry Age-Related Macular Degeneration

HOST CELL LINES AND METHODS FOR IDENTIFYING AND USING SUCH HOST CEL...

METHODS AND COMPOSITIONS FOR TREATING A PREMATURE TERMINATION CODON...

AAV Vectors Targeted to Oligodendrocytes

COMPOSITIONS AND METHODS FOR THE PRODUCTION OF LIBRARIES

OPTOGENETIC VISUAL RESTORATION USING CHRIMSON

NUCLEASE-MEDIATED GENOME EDITING OF PRIMARY CELLS AND RELATED KITS

Compositions and Methods for Treating Hereditary Angioedema

GENE THERAPY FOR AADC DEFICIENCY

RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS WITH CD14 PROMOTER AND U...

GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I

ADENO-ASSOCIATED VIRUS (AAV) PRODUCER CELL LINE AND RELATED METHODS

FRATAXIN EXPRESSION CONSTRUCTS

SCALABLE PURIFICATION METHOD FOR AAV9

RATIONAL POLYPLOID ADENO-ASSOCIATED VIRUS VECTORS FOR THE TREATMENT...

GENE THERAPY VECTORS FOR TREATING HEART DISEASE

GENE THERAPY FOR AMYOTROPHIC LATERAL SCLEROSIS AND OTHER SPINAL COR...

CNS TARGETING AAV VECTORS AND METHODS OF USE THEREOF

SCALABLE PURIFICATION METHOD FOR AAV1

HIGH EFFICIENCY PURIFICATION OF DIVERGENT AAV SEROTYPES USING AAVX...

ADENO-ASSOCIATED VIRUS VARIANT CAPSIDS AND METHODS OF USE THEREOF

TAU MODULATORS AND METHODS AND COMPOSITIONS FOR DELIVERY THEREOF

Compositions Useful in Treatment of Spinal Muscular Atrophy

TISSUE SELECTIVE TRANSGENE EXPRESSION

METHODS AND COMPOSITIONS FOR THE PURIFICATION OF ADENO-ASSOCIATED V...

ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT...

RESTRICTIVE INVERTED TERMINAL REPEATS FOR VIRAL VECTORS

ADENO-ASSOCIATED VIRUS VECTORS ENCODING MODIFIED G6PC AND USES THEREOF