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Patents Grantslast 30 patents

Information Patent Grant
Modulators of APOL1 expression
- Patent number 12,168,766
- Issue date Dec 17, 2024
- Astrazeneca AB
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified double-stranded RNA agents
- Patent number 12,168,767
- Issue date Dec 17, 2024
- Alnylam Pharmaceuticals, Inc.
- Martin Maier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Systems and methods for sample analysis
- Patent number 12,169,198
- Issue date Dec 17, 2024
- 10X GENOMICS, INC.
- Andrew D. Price
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for the delivery of nucleic acids
- Patent number 12,161,659
- Issue date Dec 10, 2024
- Case Western Reserve University
- Zheng-Rong Lu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Matrix bound nanovesicles and their use
- Patent number 12,161,778
- Issue date Dec 10, 2024
- University of Pittsburgh of the Commonwealth System of Higher Education
- Stephen Francis Badylak
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of engineering transferrin receptor binding polypeptides
- Patent number 12,162,948
- Issue date Dec 10, 2024
- Denali Therapeutics Inc.
- Xiaocheng Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Facile assembly of soft nanoarchitectures and co-loading of hydroph...
- Patent number 12,162,997
- Issue date Dec 10, 2024
- Northwestern University
- Evan A. Scott
- B01 - PHYSICAL OR CHEMICAL PROCESSES OR APPARATUS IN GENERAL
Information Patent Grant
Engineered class 2 type V CRISPR systems
- Patent number 12,163,125
- Issue date Dec 10, 2024
- Scribe Therapeutics Inc.
- Gayathri Vijayakumar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Ferrochelatase inhibitors and methods of use
- Patent number 12,161,642
- Issue date Dec 10, 2024
- Indiana University Research and Technology Corporation
- Timothy W. Corson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method to synthesize a biodegradable dextran for agent delivery
- Patent number 12,161,727
- Issue date Dec 10, 2024
- The Johns Hopkins University
- Zaver M. Bhujwalla
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and uses for treatment thereof
- Patent number 12,163,128
- Issue date Dec 10, 2024
- Board of Supervisors of Louisiana State University and Agricultural and Mecha...
- Edward L. Grabczyk
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides to restore dysferlin protein expression...
- Patent number 12,163,129
- Issue date Dec 10, 2024
- University of Massachusetts
- Robert H. Brown
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Bioactive renal cells
- Patent number 12,157,887
- Issue date Dec 3, 2024
- ProKidney
- Timothy A. Bertram
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Method for delivering RNA to neurons to treat herpes infections
- Patent number 12,156,919
- Issue date Dec 3, 2024
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods to detect motor neuron disease comprising micro-RNAs
- Patent number 12,157,889
- Issue date Dec 3, 2024
- Washington University
- Timothy M. Miller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA editing via recruitment of spliceosome components
- Patent number 12,152,239
- Issue date Nov 26, 2024
- Tacit Therapeutics, Inc.
- David A. Nelles
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
T cells with improved functionality
- Patent number 12,152,251
- Issue date Nov 26, 2024
- Kite Pharma, Inc.
- Saikat Banerjee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Selective antisense compounds and uses thereof
- Patent number 12,152,244
- Issue date Nov 26, 2024
- Ionis Pharmaceuticals, Inc.
- Michael Oestergaard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR therapy
- Patent number 12,152,242
- Issue date Nov 26, 2024
- The Curators of the University of Missouri
- Dongsheng Duan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic compositions for treating pain via multiple targets
- Patent number 12,152,243
- Issue date Nov 26, 2024
- QUELLTX, INC.
- Graham T. Dempsey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Target-specific extracellular vesicles
- Patent number 12,146,238
- Issue date Nov 19, 2024
- EVERCYTE GMBH
- Gordana Wozniak-Knopp
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
T-lymphocyte binding aptamers
- Patent number 12,146,140
- Issue date Nov 19, 2024
- Aummune Ltd.
- Guy Neev
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Direct and selective inhibition of MDM4 for treatment of cancer
- Patent number 12,139,712
- Issue date Nov 12, 2024
- VIB VZW
- Jean-Christophe Marine
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotides for the treatment of Leber congenital am...
- Patent number 12,139,711
- Issue date Nov 12, 2024
- STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM
- Robert Wilhelmus Johanna Collin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods for upregulating immune responses using combinations of ant...
- Patent number 12,139,535
- Issue date Nov 12, 2024
- Dana-Farber Cancer Institute, Inc.
- Gordon J. Freeman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligomers and methods of using the same for treating dise...
- Patent number 12,139,709
- Issue date Nov 12, 2024
- Sarepta Therapeutics, Inc.
- Frederick Joseph Schnell
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for organ specific delivery of nucleic acids
- Patent number 12,133,924
- Issue date Nov 5, 2024
- The Board of Regents of the University of Texas System
- Qiang Cheng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for treatment of hemoglobinopathies
- Patent number 12,134,767
- Issue date Nov 5, 2024
- Vertex Pharmaceuticals Incorporated
- Matthew Hebden Porteus
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
MicroRNA-198 as a tumor suppressor in ovarian cancer
- Patent number 12,134,769
- Issue date Nov 5, 2024
- Baylor College of Medicine
- Qizhi Yao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Structural domains of antisense RNA molecules up-regulating transla...
- Patent number 12,134,768
- Issue date Nov 5, 2024
- Fondazione Istituto Italiano di Tecnologia
- Stefano Gustincich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
- Publication number 20240415868
- Publication date Dec 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
- Publication number 20240417706
- Publication date Dec 19, 2024
- EDITAS MEDICINE, INC.
- Jennifer Leah GORI
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN
- Publication number 20240415857
- Publication date Dec 19, 2024
- Sarepta Therapeutics, Inc.
- Dan V. Mourich
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR SKIPPING EXON 45 IN DUCHENNE MUSCULAR...
- Publication number 20240417429
- Publication date Dec 19, 2024
- Entrada Therapeutics, Inc.
- Xiang Li
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
- Publication number 20240417721
- Publication date Dec 19, 2024
- ProQR Therapeutics II B.V.
- Janne Juha TURUNEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR IMMUNOONCOLOGY
- Publication number 20240417722
- Publication date Dec 19, 2024
- Novartis AG
- Ming-Wei CHEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION
- Publication number 20240417723
- Publication date Dec 19, 2024
- University of Massachusetts
- Anastasia Khvorova
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS AND COMPOSITIONS FOR GENOME EDITING
- Publication number 20240409961
- Publication date Dec 12, 2024
- Salk Institute for Biological Studies
- Juan Carlos IZPISUA BELMONTE
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
METHODS OF CELL CULTURE FOR ADOPTIVE CELL THERAPY
- Publication number 20240408200
- Publication date Dec 12, 2024
- WILSON WOLF MANUFACTURING
- Juan F. Vera
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSO...
- Publication number 20240409936
- Publication date Dec 12, 2024
- Ovid Therapeutics Inc.
- Noelle Germain
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID DETECTION KIT AND DETECTION METHOD BASED ON THE PHOTO-...
- Publication number 20240409986
- Publication date Dec 12, 2024
- South China Normal University
- Xiaoming ZHOU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSTHYRETIN (TTR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
- Publication number 20240409929
- Publication date Dec 12, 2024
- Alnylam Pharmaceuticals, Inc.
- Mark K. Schlegel
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF CENTRAL NERVOUS SY...
- Publication number 20240409938
- Publication date Dec 12, 2024
- Vanderbilt University
- Craig L. Duvall
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
BIOACTIVE RENAL CELLS
- Publication number 20240409941
- Publication date Dec 12, 2024
- ProKidney
- Timothy A. Bertram
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL RNA TRANSCRIPT
- Publication number 20240409928
- Publication date Dec 12, 2024
- PTC THERAPEUTICS, INC.
- Anuradha BHATTACHARYYA
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA-GUIDED TRANS-SPLICING OF RNA
- Publication number 20240409920
- Publication date Dec 12, 2024
- THE BROAD INSTITUTE, INC.
- Feng Zhang
- C07 - ORGANIC CHEMISTRY
Information Patent Application
CORRECTION OF SPLICING MUTATIONS CAUSING PRIMARY CILIARY DYSKINESIA...
- Publication number 20240409932
- Publication date Dec 12, 2024
- The University of North Carolina at Chapel Hill
- Silvia Kreda
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TR...
- Publication number 20240409933
- Publication date Dec 12, 2024
- Switch Therapeutics Inc.
- Si-ping Han
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
Atg8ylation coordinates stress granule formation and mTOR inactivat...
- Publication number 20240409935
- Publication date Dec 12, 2024
- UNM Rainforest Innovations
- Vojo P. Deretic
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
MODIFIED DOUBLE-STRANDED RNA AGENTS
- Publication number 20240409942
- Publication date Dec 12, 2024
- Alnylam Pharmaceuticals, Inc.
- Martin MAIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PRODUCTS AND METHODS FOR MYELIN PROTEIN ZERO SILENCING AND TREATING...
- Publication number 20240401046
- Publication date Dec 5, 2024
- Research Institute at Nationwide Children's Hospital
- Scott Quenton Harper
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MICRORNA-541-3P AS A THERAPEUTIC AGENT AS WELL AS ZNF101 AND CASZ1...
- Publication number 20240401048
- Publication date Dec 5, 2024
- NEW YORK UNIVERSITY
- Abulaish Ansari
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE
- Publication number 20240401060
- Publication date Dec 5, 2024
- Alnylam Pharmaceuticals, Inc.
- Dinah Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...
- Publication number 20240401038
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTIBODY-MEDIATED DELIVERY OF CAS9 TO MAMMALIAN CELLS
- Publication number 20240400684
- Publication date Dec 5, 2024
- THE REGENTS OF THE UNIVESITY OF CALIFORNIA
- Jacob Corn
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
- Publication number 20240401036
- Publication date Dec 5, 2024
- UCL Business LTD
- Pietro Fratta
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
- Publication number 20240401037
- Publication date Dec 5, 2024
- Universite de Mons
- Alexandra Belayew
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR IMPROVING RELAXATION OF STRIATED MYOCYTES
- Publication number 20240401041
- Publication date Dec 5, 2024
- INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE
- Jean-Sébastien HULOT
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi induced C9ORF72 suppression for the treatment of ALS/FTD
- Publication number 20240398988
- Publication date Dec 5, 2024
- uniQure IP B.V.
- Raygene Michaël MARTIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CATIONIC POLYMERS
- Publication number 20240398720
- Publication date Dec 5, 2024
- Translate Bio, Inc.
- Frank DeRosa
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Applications Uses

Industry

Parent Industries

Current Industry

Sub Industries

Patents Grantslast 30 patents

Modulators of APOL1 expression

Modified double-stranded RNA agents

Systems and methods for sample analysis

Compositions and methods for the delivery of nucleic acids

Matrix bound nanovesicles and their use

Methods of engineering transferrin receptor binding polypeptides

Facile assembly of soft nanoarchitectures and co-loading of hydroph...

Engineered class 2 type V CRISPR systems

Ferrochelatase inhibitors and methods of use

Method to synthesize a biodegradable dextran for agent delivery

Compositions and uses for treatment thereof

Antisense oligonucleotides to restore dysferlin protein expression...

Bioactive renal cells

Method for delivering RNA to neurons to treat herpes infections

Methods to detect motor neuron disease comprising micro-RNAs

RNA editing via recruitment of spliceosome components

T cells with improved functionality

Selective antisense compounds and uses thereof

CRISPR therapy

Therapeutic compositions for treating pain via multiple targets

Target-specific extracellular vesicles

T-lymphocyte binding aptamers

Direct and selective inhibition of MDM4 for treatment of cancer

Antisense oligonucleotides for the treatment of Leber congenital am...

Methods for upregulating immune responses using combinations of ant...

Antisense oligomers and methods of using the same for treating dise...

Compositions and methods for organ specific delivery of nucleic acids

Materials and methods for treatment of hemoglobinopathies

MicroRNA-198 as a tumor suppressor in ovarian cancer

Structural domains of antisense RNA molecules up-regulating transla...

Patents Applicationslast 30 patents

COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE

SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

ANTISENSE-INDUCED EXON EXCLUSION IN TYPE VII COLLAGEN

COMPOSITIONS AND METHODS FOR SKIPPING EXON 45 IN DUCHENNE MUSCULAR...

SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES

COMPOSITIONS AND METHODS FOR IMMUNOONCOLOGY

OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION

METHODS AND COMPOSITIONS FOR GENOME EDITING

METHODS OF CELL CULTURE FOR ADOPTIVE CELL THERAPY

RNAi TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSO...

NUCLEIC ACID DETECTION KIT AND DETECTION METHOD BASED ON THE PHOTO-...

TRANSTHYRETIN (TTR) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF CENTRAL NERVOUS SY...

BIOACTIVE RENAL CELLS

NOVEL RNA TRANSCRIPT

RNA-GUIDED TRANS-SPLICING OF RNA

CORRECTION OF SPLICING MUTATIONS CAUSING PRIMARY CILIARY DYSKINESIA...

CONDITION-ACTIVATABLE NUCLEIC ACID CONSTRUCTS AND THEIR USES FOR TR...

Atg8ylation coordinates stress granule formation and mTOR inactivat...

MODIFIED DOUBLE-STRANDED RNA AGENTS

PRODUCTS AND METHODS FOR MYELIN PROTEIN ZERO SILENCING AND TREATING...

MICRORNA-541-3P AS A THERAPEUTIC AGENT AS WELL AS ZNF101 AND CASZ1...

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF MUTANT EGFR GENE

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...

ANTIBODY-MEDIATED DELIVERY OF CAS9 TO MAMMALIAN CELLS

THERAPEUTICS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS

AGENTS USEFUL IN TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

METHODS FOR IMPROVING RELAXATION OF STRIATED MYOCYTES

RNAi induced C9ORF72 suppression for the treatment of ALS/FTD

CATIONIC POLYMERS