linked to the nucleic acid via a carbon atom

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CPC
C12N2310/352

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2310/00Structure or type of the nucleic acid

Current Industry

C12N2310/352linked to the nucleic acid via a carbon atom

Industries

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Patents Grantslast 30 patents

Information Patent Grant
17ß-hydroxysteroid dehydrogenase type 13 (HSD17B13) iRNA compositio...
- Patent number 12,359,201
- Issue date Jul 15, 2025
- REGENERON PHARMACEUTICALS, INC.
- Gregory Hinkle
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for reducing ATXN3 expression
- Patent number 12,350,285
- Issue date Jul 8, 2025
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified nucleic acids, hybrid guide RNAS, and uses thereof
- Patent number 12,338,433
- Issue date Jun 24, 2025
- OHIO STATE INNOVATION FOUNDATION
- Yizhou Dong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of gene transcription using antisense oligonucleotides t...
- Patent number 12,319,916
- Issue date Jun 3, 2025
- CAMP4 THERAPEUTICS CORPORATION
- Alfica Sehgal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating apolipoprotein (a) expression
- Patent number 12,291,709
- Issue date May 6, 2025
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Antisense oligonucleotide targeting ATN1 mRNA or pre-mRNA
- Patent number 12,291,710
- Issue date May 6, 2025
- Nippon Shinyaku Co., Ltd.
- Takao Kawano
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compounds and methods for reducing LRRK2 expression
- Patent number 12,241,067
- Issue date Mar 4, 2025
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapeutic oligonucleotides
- Patent number 12,234,455
- Issue date Feb 25, 2025
- IFOM Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d′Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating neuronal excitability and m...
- Patent number 12,163,130
- Issue date Dec 10, 2024
- Icahn School of Medicine at Mount Sinai
- Anne Schaefer
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Bi specific aptamer
- Patent number 12,138,279
- Issue date Nov 12, 2024
- City of Hope
- John J. Rossi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Base editing of ANGPTL3 and methods of using same for treatment of...
- Patent number 12,115,230
- Issue date Oct 15, 2024
- Verve Therapeutics, Inc.
- Alexandra Chadwick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
GLP-1 receptor ligand moiety conjugated oligonucleotides and uses t...
- Patent number 12,115,225
- Issue date Oct 15, 2024
- Astrazeneca AB
- Brett P. Monia
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeted inhibition using engineered oligonucleotides
- Patent number 12,104,157
- Issue date Oct 1, 2024
- MIRECULE, INC.
- Robert Place
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Insulin receptor aptamer and pharmaceutical composition for treatin...
- Patent number 12,060,560
- Issue date Aug 13, 2024
- APTAMER SCIENCES INC.
- Youndong Kim
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for targeting RNA polymerases and non-codi...
- Patent number 12,043,839
- Issue date Jul 23, 2024
- The Regents of the University of California
- Steve E. Jacobsen
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Base editing of PCSK9 and methods of using same for treatment of di...
- Patent number 12,029,795
- Issue date Jul 9, 2024
- Verve Therapeutics, Inc.
- Alexandra Chadwick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Single-stranded RNA-editing oligonucleotides
- Patent number 12,018,257
- Issue date Jun 25, 2024
- ProQR Therapeutics II B.V.
- Janne Juha Turunen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
RNA interference mediated inhibition of prolyl hydroxylase domain 2...
- Patent number 11,952,573
- Issue date Apr 9, 2024
- SIRNA Therapeutics, Inc.
- Brandon Ason
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Reducing intron retention
- Patent number 11,891,605
- Issue date Feb 6, 2024
- University of Southampton
- Igor Vorechovsky
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Complement component C5 iRNA compositions and methods of use thereof
- Patent number 11,873,491
- Issue date Jan 16, 2024
- Alnylam Pharmaceuticals, Inc.
- Kevin Fitzgerald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and methods for reducing LRRK2 expression
- Patent number 11,873,495
- Issue date Jan 16, 2024
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Glucokinase (GCK) iRNA compositions and methods of use thereof
- Patent number 11,859,185
- Issue date Jan 2, 2024
- Alnylam Pharmaceuticals, Inc.
- Kevin Fitzgerald
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Antisense oligonucleotide compositions
- Patent number 11,859,180
- Issue date Jan 2, 2024
- Ionis Pharmaceuticals, Inc.
- Andrew Dibble
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for modulating apolipoprotein (a) expression
- Patent number 11,851,655
- Issue date Dec 26, 2023
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified nucleic acids, hybrid guide RNAs, and uses thereof
- Patent number 11,845,929
- Issue date Dec 19, 2023
- OHIO STATE INNOVATION FOUNDATION
- Yizhou Dong
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Allele selective inhibition of mutant C9orf72 foci expression by du...
- Patent number 11,840,690
- Issue date Dec 12, 2023
- The Board of Regents of the University of Texas System
- David Corey
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of prekallikrein (PKK) expression
- Patent number 11,840,686
- Issue date Dec 12, 2023
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Compositions and methods for treating transthyretin (TTR) mediated...
- Patent number 11,806,360
- Issue date Nov 7, 2023
- Alnylam Pharmaceuticals, Inc.
- Jared Gollob
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeted inhibition using engineered oligonucleotides
- Patent number 11,795,459
- Issue date Oct 24, 2023
- MIRECULE, INC.
- Robert Place
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Defined multi-conjugates oligonucleotides
- Patent number 11,767,531
- Issue date Sep 26, 2023
- MPEG LA, LLC
- Philipp Hadwiger
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF...
- Publication number 20250188456
- Publication date Jun 12, 2025
- Alnylam Pharmaceuticals, Inc.
- Gregory Hinkle
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
BASE EDITING OF ANGPTL3 AND METHODS OF USING SAME FOR TREATMENT OF...
- Publication number 20250152746
- Publication date May 15, 2025
- Verve Therapeutics, Inc.
- Alexandra Chadwick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Antisense Nucleic Acids
- Publication number 20250145997
- Publication date May 8, 2025
- Nippon Shinyaku co., Ltd.
- Tatsushi Wakayama
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...
- Publication number 20250075215
- Publication date Mar 6, 2025
- Icahn School of Medicine at Mount Sinai
- Anne SCHAEFER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA INTERFERENCE MEDIATED INHIBITION OF PROLYL HYDROXYLASE DOMAIN 2...
- Publication number 20250066791
- Publication date Feb 27, 2025
- SIRNA THERAPEUTICS, INC.
- Brandon Ason
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPEUTIC OLIGONUCLEOTIDES
- Publication number 20250066784
- Publication date Feb 27, 2025
- IFOM - Fondazione Istituto FIRC di Oncologia Molecolare
- Fabrizio d'Adda di Fagagna
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE NUCLEIC ACIDS
- Publication number 20250042933
- Publication date Feb 6, 2025
- NIPPON SHINYAKU CO., LTD
- Naoki Watanabe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
- Publication number 20250034566
- Publication date Jan 30, 2025
- Alnylam Pharmaceuticals, Inc.
- Brian Bettencourt
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE...
- Publication number 20250017953
- Publication date Jan 16, 2025
- Alnylam Pharmaceuticals, Inc.
- David Erbe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...
- Publication number 20250011784
- Publication date Jan 9, 2025
- VICO Therapeutics B.V.
- Peter Christian DE VISSER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES
- Publication number 20240417721
- Publication date Dec 19, 2024
- ProQR Therapeutics II B.V.
- Janne Juha TURUNEN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...
- Publication number 20240401038
- Publication date Dec 5, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
BASE EDITING OF PCSK9 AND METHODS OF USING SAME FOR TREATMENT OF DI...
- Publication number 20240390523
- Publication date Nov 28, 2024
- Verve Therapeutics, Inc.
- Alexandra Chadwick
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES
- Publication number 20240368596
- Publication date Nov 7, 2024
- BioMarin Pharmaceutical Inc.
- Thomas Aaron Hartl
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Compounds and Methods for Reducing LRRK2 Expression
- Publication number 20240360453
- Publication date Oct 31, 2024
- Ionis Pharmaceuticals, Inc.
- Tracy A. Cole
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CA...
- Publication number 20240352462
- Publication date Oct 24, 2024
- Dana-Farber Cancer Institute, Inc.
- Nikhil C. Munshi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN (a) EXPRESSION
- Publication number 20240352455
- Publication date Oct 24, 2024
- Ionis Pharmaceuticals, Inc.
- Thazha P. Prakash
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS
- Publication number 20240344072
- Publication date Oct 17, 2024
- UCL Business LTD
- Haiyan Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATION OF GENE TRANSCRIPTION USING ANTISENSE OLIGONUCLEOTIDES T...
- Publication number 20240336924
- Publication date Oct 10, 2024
- CAMP4 THERAPEUTICS CORPORATION
- Alfica Sehgal
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF
- Publication number 20240327839
- Publication date Oct 3, 2024
- Eli Lilly and Company
- Patrick Joseph ANTONELLIS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ALLELE-SELECTIVE COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN EX...
- Publication number 20240325425
- Publication date Oct 3, 2024
- Ionis Pharmaceuticals, Inc.
- Michael OESTERGAARD
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
CRISPR-BASED COMPOSITIONS AND METHODS OF USE
- Publication number 20240318171
- Publication date Sep 26, 2024
- Integrated DNA Technologies, Inc.
- Michael Allen Collingwood
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA
- Publication number 20240318181
- Publication date Sep 26, 2024
- NIPPON SHINYAKU CO., LTD.
- Takao KAWANO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MODULATION OF PREKALLIKREIN (PKK) EXPRESSION
- Publication number 20240318183
- Publication date Sep 26, 2024
- Ionis Pharmaceuticals, Inc.
- Susan M. Freier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
- Publication number 20240309387
- Publication date Sep 19, 2024
- Alnylam Pharmaceuticals, Inc.
- James Butler
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
REDUCING INTRON RETENTION
- Publication number 20240309377
- Publication date Sep 19, 2024
- UNIVERSITY OF SOUTHAMPTON
- Igor Vorechovsky
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
STABILIZATION OF OLIGONUCLEOTIDE AND OLIGONUCLEOTIDE-PROTEIN COMPLE...
- Publication number 20240309372
- Publication date Sep 19, 2024
- University of Massachusetts
- Ken Yamada
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
iRNA Compositions and Methods for Silencing Filamin A (FLNA)
- Publication number 20240301418
- Publication date Sep 12, 2024
- Alnylam Pharmaceuticals, Inc.
- KIRK BROWN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTRO...
- Publication number 20240301428
- Publication date Sep 12, 2024
- The University of Chicago
- Elizabeth McNally
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION
- Publication number 20240301422
- Publication date Sep 12, 2024
- Biogen MA Inc.
- Holly Kordasiewicz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

linked to the nucleic acid via a carbon atom

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

17ß-hydroxysteroid dehydrogenase type 13 (HSD17B13) iRNA compositio...

Compounds and methods for reducing ATXN3 expression

Modified nucleic acids, hybrid guide RNAS, and uses thereof

Modulation of gene transcription using antisense oligonucleotides t...

Compositions and methods for modulating apolipoprotein (a) expression

Antisense oligonucleotide targeting ATN1 mRNA or pre-mRNA

Compounds and methods for reducing LRRK2 expression

Therapeutic oligonucleotides

Compositions and methods for modulating neuronal excitability and m...

Bi specific aptamer

Base editing of ANGPTL3 and methods of using same for treatment of...

GLP-1 receptor ligand moiety conjugated oligonucleotides and uses t...

Targeted inhibition using engineered oligonucleotides

Insulin receptor aptamer and pharmaceutical composition for treatin...

Methods and compositions for targeting RNA polymerases and non-codi...

Base editing of PCSK9 and methods of using same for treatment of di...

Single-stranded RNA-editing oligonucleotides

RNA interference mediated inhibition of prolyl hydroxylase domain 2...

Reducing intron retention

Complement component C5 iRNA compositions and methods of use thereof

Compounds and methods for reducing LRRK2 expression

Glucokinase (GCK) iRNA compositions and methods of use thereof

Antisense oligonucleotide compositions

Compositions and methods for modulating apolipoprotein (a) expression

Modified nucleic acids, hybrid guide RNAs, and uses thereof

Allele selective inhibition of mutant C9orf72 foci expression by du...

Modulation of prekallikrein (PKK) expression

Compositions and methods for treating transthyretin (TTR) mediated...

Targeted inhibition using engineered oligonucleotides

Defined multi-conjugates oligonucleotides

Patents Applicationslast 30 patents

HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF...

BASE EDITING OF ANGPTL3 AND METHODS OF USING SAME FOR TREATMENT OF...

Antisense Nucleic Acids

COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND M...

RNA INTERFERENCE MEDIATED INHIBITION OF PROLYL HYDROXYLASE DOMAIN 2...

THERAPEUTIC OLIGONUCLEOTIDES

ANTISENSE NUCLEIC ACIDS

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

LACTATE DEHYDROGENASE A (LDHA) iRNA COMPOSITIONS AND METHODS OF USE...

RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR T...

SINGLE-STRANDED RNA-EDITING OLIGONUCLEOTIDES

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN C-III EXPRES...

BASE EDITING OF PCSK9 AND METHODS OF USING SAME FOR TREATMENT OF DI...

DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES

Compounds and Methods for Reducing LRRK2 Expression

ANTISENSE INHIBITORS OF MIR17HG PRE-RNA AS THERAPEUTIC AGENTS IN CA...

COMPOSITIONS AND METHODS FOR MODULATING APOLIPOPROTEIN (a) EXPRESSION

TREATMENT FOR TYROSINE DEGRADATION-ASSOCIATED DISORDERS

MODULATION OF GENE TRANSCRIPTION USING ANTISENSE OLIGONUCLEOTIDES T...

NOVEL THERAPEUTIC DELIVERY MOIETIES AND USES THEREOF

ALLELE-SELECTIVE COMPOUNDS AND METHODS FOR MODULATING HUNTINGTIN EX...

CRISPR-BASED COMPOSITIONS AND METHODS OF USE

ANTISENSE OLIGONUCLEOTIDE TARGETING ATN1 MRNA OR PRE-MRNA

MODULATION OF PREKALLIKREIN (PKK) EXPRESSION

TMPRSS6 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

REDUCING INTRON RETENTION

STABILIZATION OF OLIGONUCLEOTIDE AND OLIGONUCLEOTIDE-PROTEIN COMPLE...

iRNA Compositions and Methods for Silencing Filamin A (FLNA)

COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTRO...

COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION