Non-coding nucleic acids modulating the expression of genes, e.g.antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids

Industry

CPC
C12N15/113

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N15/00Mutation or genetic engineering DNA or RNA concerning genetic engineering, vectors

Current Industry

C12N15/113Non-coding nucleic acids modulating the expression of genes, e.g.antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids

Industries

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Patents Grantslast 30 patents

Information Patent Grant
Hexokinase 2-specific inhibitors for use in acute central nervous s...
- Patent number 12,319,750
- Issue date Jun 3, 2025
- GUANGZHOU CELLPROTEK PHARMACEUTICAL CO., LTD
- Guangmei Yan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
MicroRNA expression promoting agent and food or beverage for promot...
- Patent number 12,319,912
- Issue date Jun 3, 2025
- KEWPIE CORPORATION
- Kurataka Otsuka
- A23 - FOODS OR FOODSTUFFS THEIR TREATMENT, NOT COVERED BY OTHER CLASSES
Information Patent Grant
Methods and compositions for modulating gene expression using oligo...
- Patent number 12,319,914
- Issue date Jun 3, 2025
- Larry J. Smith
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulation of gene transcription using antisense oligonucleotides t...
- Patent number 12,319,916
- Issue date Jun 3, 2025
- CAMP4 THERAPEUTICS CORPORATION
- Alfica Sehgal
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Incorporation of unnatural nucleotides and methods thereof
- Patent number 12,319,944
- Issue date Jun 3, 2025
- The Scripps Research Institute
- Jerod Ptacin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Rotavirus vaccines
- Patent number 12,318,444
- Issue date Jun 3, 2025
- Cure Vac SE
- Susanne Rauch
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
P-ethoxy nucleic acids for STAT3 inhibition
- Patent number 12,319,911
- Issue date Jun 3, 2025
- BIO-PATH HOLDINGS, INC.
- Ana Tari Ashizawa
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
5-halouracil-modified microRNAs and their use in the treatment of c...
- Patent number 12,319,913
- Issue date Jun 3, 2025
- The Research Foundation for the State University of New York
- Jingfang Ju
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Cytotoxic fluoropyrimidine polymers and methods of use thereof
- Patent number 12,319,915
- Issue date Jun 3, 2025
- Wake Forest University Health Sciences
- William H. Gmeiner
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Complexes comprising an anti-transferrin receptor antibody linked t...
- Patent number 12,319,743
- Issue date Jun 3, 2025
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods of treating ocular diseases
- Patent number 12,310,997
- Issue date May 27, 2025
- The Regents of the University of California
- David V. Schaffer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
SOD1 dual expression vectors and uses thereof
- Patent number 12,312,587
- Issue date May 27, 2025
- UNIVERSITY OF MASSACHUSETTS
- Christian Mueller
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Anti-PVRIG antibodies and methods of use
- Patent number 12,312,404
- Issue date May 27, 2025
- COMPUGEN LTD
- Mark White
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Targeted intracellular delivery of large nucleic acids
- Patent number 12,312,386
- Issue date May 27, 2025
- Hoffmann-La Roche Inc.
- Ulrich Brinkmann
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for nanoparticle lyophile forms
- Patent number 12,311,055
- Issue date May 27, 2025
- Nitto Denko Corporation
- Roger Adami
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
MicroRNA-based logic gates and uses thereof
- Patent number 12,312,583
- Issue date May 27, 2025
- Massachusetts Institute of Technology
- Ron Weiss
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
cGMP exosome loaded therapeutics for treating sickle cell disease
- Patent number 12,312,584
- Issue date May 27, 2025
- EXOSOME THERAPEUTICS, INC.
- Gerardo Rodriguez-Araujo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Oligonucleotides targeting frataxin and related methods
- Patent number 12,312,585
- Issue date May 27, 2025
- UNIVERSITY OF MASSACHUSETTS
- Feng Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Treatment of MST1 related diseases and disorders
- Patent number 12,312,586
- Issue date May 27, 2025
- EMPIRICO INC.
- Omri Gottesman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
BBB-crossing lipid ligand of hetero nucleic acid
- Patent number 12,305,169
- Issue date May 20, 2025
- National University Corporation Tokyo Medical and Dental University
- Takanori Yokota
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for monitoring, diagnosis, prognosis, dete...
- Patent number 12,303,494
- Issue date May 20, 2025
- GLAX Health LLC
- Shivani Shrivastava
- G01 - MEASURING TESTING
Information Patent Grant
Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...
- Patent number 12,303,525
- Issue date May 20, 2025
- Hoffman-La Roche Inc.
- Susanne Kammler
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
RNAi insecticide materials and methods
- Patent number 12,302,904
- Issue date May 20, 2025
- Indiana University Research and Technology Corporation
- Molly Duman Scheel
- A01 - AGRICULTURE FORESTRY ANIMAL HUSBANDRY HUNTING TRAPPING FISHING
Information Patent Grant
Compositions and methods for treating cancer
- Patent number 12,305,171
- Issue date May 20, 2025
- bioAffinity Technologies, Inc.
- David J. Elzi
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Composition for regulating production of interfering ribonucleic acid
- Patent number 12,305,170
- Issue date May 20, 2025
- Wyvern Pharmaceuticals Inc.
- Bradley G. Thompson
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Tetragalnac and peptide containing conjugates and methods for deliv...
- Patent number 12,304,925
- Issue date May 20, 2025
- SIRNA Therapeutics, Inc.
- David Tellers
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Lipid nanoparticle compositions and uses thereof
- Patent number 12,303,569
- Issue date May 20, 2025
- Cytodigm, Inc.
- Bin Wu
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
High performance multi-input microRNA sensors and uses thereof
- Patent number 12,297,506
- Issue date May 13, 2025
- Massachusetts Institute of Technology
- Ron Weiss
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nanomaterials comprising triols
- Patent number 12,296,053
- Issue date May 13, 2025
- Beam Therapeutics Inc.
- Cory Dane Sago
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Sequence specific antimicrobials
- Patent number 12,295,993
- Issue date May 13, 2025
- The Rockefeller University
- David Bikard
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIO...
- Publication number 20250177377
- Publication date Jun 5, 2025
- University of Florida Research Foundation, Incorporated
- Kirill MARTEMYANOV
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
HETERONUCLEIC ACID INCLUDING 2'-MODIFIED NUCLEOSIDE
- Publication number 20250179486
- Publication date Jun 5, 2025
- NATIONAL UNIVERSITY CORPORATION TOKYO MEDICAL AND DENTAL UNIVERSITY
- Takanori Yokota
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMBINATION THERAPY FOR TREATMENT OF DISEASE
- Publication number 20250179169
- Publication date Jun 5, 2025
- MEREO BIOPHARMA 5, INC.
- Christopher Lamond MURRIEL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREA...
- Publication number 20250179485
- Publication date Jun 5, 2025
- AptamiR Therapeutics, Inc.
- Marc Thibonnier
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER T...
- Publication number 20250179501
- Publication date Jun 5, 2025
- Mark David Vincent
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TARGETING NEUROPILIN 2 (NRP2) IN LETHAL PROSTATE CANCER
- Publication number 20250179502
- Publication date Jun 5, 2025
- University of Massachusetts
- Arthur M. MERCURIO
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF USING OLIGOMERIC COMPOUNDS TO TREAT SCN2A-RELATED DISORDERS
- Publication number 20250179503
- Publication date Jun 5, 2025
- PRAXIS PRECISION MEDICINES, INC.
- Michael S. Oldham
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND...
- Publication number 20250179529
- Publication date Jun 5, 2025
- Life Edit Therapeutics, Inc.
- Tyson D. Bowen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DIRECT REPLACEMENT GENOME EDITING
- Publication number 20250179468
- Publication date Jun 5, 2025
- Transit Therapeutics, Inc.
- Schaked Omer HALPERIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...
- Publication number 20250177549
- Publication date Jun 5, 2025
- Dyne Therapeutics, Inc.
- Romesh R. Subramanian
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
INHIBITION OF DNA POLYMERASES BY URACIL-DNA GLYCOSYLASE-CLEAVABLE O...
- Publication number 20250179444
- Publication date Jun 5, 2025
- Cepheid
- Igor V. Kutyavin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENETICALLY ENGINEERED T CELLS WITH REGNASE-1 AND/OR TGFBRII DISRUP...
- Publication number 20250179146
- Publication date Jun 5, 2025
- CRISPR Therapeutics AG
- Mary-Lee Dequeant
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
- Publication number 20250179488
- Publication date Jun 5, 2025
- EDITAS MEDICINE, INC.
- Jennifer Leah GORI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS OF TREATING GLAUCOMA
- Publication number 20250179490
- Publication date Jun 5, 2025
- PYC Therapeutics Limited
- Janya Grainok
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOUNDS AND METHODS FOR MODULATING SMN2
- Publication number 20250179493
- Publication date Jun 5, 2025
- Ionis Pharmaceuticals, Inc.
- Frank Rigo
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TARGETED COMPOSITIONS
- Publication number 20250179496
- Publication date Jun 5, 2025
- ARBUTUS BIOPHARMA CORPORATION
- James HEYES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE
- Publication number 20250177543
- Publication date Jun 5, 2025
- Oxford University Innovation Limited
- Matthew WOOD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND CONTROL COMPOSITIONS FOR SEQUENCING
- Publication number 20250179479
- Publication date Jun 5, 2025
- Battelle Memorial Institute
- Rachel R. SPURBECK
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
- Publication number 20250179487
- Publication date Jun 5, 2025
- Sarepta Therapeutics, Inc.
- Frederick Joseph SCHNELL
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ATXN2 RNA INTERFERENCE AGENTS
- Publication number 20250179491
- Publication date Jun 5, 2025
- Eli Lilly and Company
- Andrew Peter McCARTHY
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RIBOZYME-ENHANCED RNA TRANS-SPLICING
- Publication number 20250179494
- Publication date Jun 5, 2025
- Massachusetts Institute of Institute of Technology
- Omar Abudayyeh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
USE OF DINUCLEOTIDE REPEAT RNAS TO TREAT CANCER
- Publication number 20250179497
- Publication date Jun 5, 2025
- Northwestern University
- Marcus Ernst Peter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
PHARMACEUTICAL COMPOSITION COMPRISING SETMAR INHIBITOR FOR PREVENTI...
- Publication number 20250179500
- Publication date Jun 5, 2025
- Korea Advanced Institute of Science and Technology
- Kwang Hyun Cho
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT AAV VECTORS AND USES THEREOF
- Publication number 20250179520
- Publication date Jun 5, 2025
- University of Massachusetts
- Guangping Gao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC
- Publication number 20250177478
- Publication date Jun 5, 2025
- University of Florida Research Foundation, Incorporated
- Kirill Martemyanov
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO
- Publication number 20250179150
- Publication date Jun 5, 2025
- American Gene Technologies International Inc.
- Charles David Pauza
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IL-6 INHIBITOR AS TREATMENT FOR NEPHROPATHY
- Publication number 20250179167
- Publication date Jun 5, 2025
- Yale University
- Julie GOODWIN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED REPEAT-ASSOC...
- Publication number 20250177431
- Publication date Jun 5, 2025
- University of Massachusetts
- Joel D. Richter
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SYSTEMS
- Publication number 20250179489
- Publication date Jun 5, 2025
- NEW YORK STEM CELL FOUNDATION, INC.
- Malin Parmar
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS OF MODIFIED TREMS AND USES THEREOF
- Publication number 20250179492
- Publication date Jun 5, 2025
- Flagship Pioneering Innovations VI, LLC.
- Theonie Anastassiadis
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Non-coding nucleic acids modulating the expression of genes, e.g.antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Hexokinase 2-specific inhibitors for use in acute central nervous s...

MicroRNA expression promoting agent and food or beverage for promot...

Methods and compositions for modulating gene expression using oligo...

Modulation of gene transcription using antisense oligonucleotides t...

Incorporation of unnatural nucleotides and methods thereof

Rotavirus vaccines

P-ethoxy nucleic acids for STAT3 inhibition

5-halouracil-modified microRNAs and their use in the treatment of c...

Cytotoxic fluoropyrimidine polymers and methods of use thereof

Complexes comprising an anti-transferrin receptor antibody linked t...

Compositions and methods of treating ocular diseases

SOD1 dual expression vectors and uses thereof

Anti-PVRIG antibodies and methods of use

Targeted intracellular delivery of large nucleic acids

Compositions and methods for nanoparticle lyophile forms

MicroRNA-based logic gates and uses thereof

cGMP exosome loaded therapeutics for treating sickle cell disease

Oligonucleotides targeting frataxin and related methods

Treatment of MST1 related diseases and disorders

BBB-crossing lipid ligand of hetero nucleic acid

Compositions and methods for monitoring, diagnosis, prognosis, dete...

Nucleic acid molecule for reduction of PAPD5 and PAPD7 mRNA for tre...

RNAi insecticide materials and methods

Compositions and methods for treating cancer

Composition for regulating production of interfering ribonucleic acid

Tetragalnac and peptide containing conjugates and methods for deliv...

Lipid nanoparticle compositions and uses thereof

High performance multi-input microRNA sensors and uses thereof

Nanomaterials comprising triols

Sequence specific antimicrobials

Patents Applicationslast 30 patents

TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIO...

HETERONUCLEIC ACID INCLUDING 2'-MODIFIED NUCLEOSIDE

COMBINATION THERAPY FOR TREATMENT OF DISEASE

ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREA...

METHODS OF TREATING CANCER AND/OR ENHANCING SENSITIVITY TO CANCER T...

TARGETING NEUROPILIN 2 (NRP2) IN LETHAL PROSTATE CANCER

METHODS OF USING OLIGOMERIC COMPOUNDS TO TREAT SCN2A-RELATED DISORDERS

RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND...

DIRECT REPLACEMENT GENOME EDITING

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHIN...

INHIBITION OF DNA POLYMERASES BY URACIL-DNA GLYCOSYLASE-CLEAVABLE O...

GENETICALLY ENGINEERED T CELLS WITH REGNASE-1 AND/OR TGFBRII DISRUP...

SYSTEMS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

METHODS OF TREATING GLAUCOMA

COMPOUNDS AND METHODS FOR MODULATING SMN2

TARGETED COMPOSITIONS

CELL-PENETRATING PEPTIDE CONJUGATES AND METHODS OF THEIR USE

METHODS AND CONTROL COMPOSITIONS FOR SEQUENCING

EXON SKIPPING OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY

ATXN2 RNA INTERFERENCE AGENTS

RIBOZYME-ENHANCED RNA TRANS-SPLICING

USE OF DINUCLEOTIDE REPEAT RNAS TO TREAT CANCER

PHARMACEUTICAL COMPOSITION COMPRISING SETMAR INHIBITOR FOR PREVENTI...

RECOMBINANT AAV VECTORS AND USES THEREOF

G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC

NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO

IL-6 INHIBITOR AS TREATMENT FOR NEPHROPATHY

COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED REPEAT-ASSOC...

SYSTEMS

COMPOSITIONS OF MODIFIED TREMS AND USES THEREOF