regulating RNA stability, not being an intron

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CCHEMISTRY METALLURGY C12Biochemistry C12NMICRO-ORGANISMS OR ENZYMES COMPOSITIONS THEREOF PROPAGATING, PRESERVING OR MAINTAINING MICRO-ORGANISMS MUTATION OR GENETIC ENGINEERING CULTURE MEDIA C12N2830/00Vector systems having a special element relevant for transcription

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C12N2830/50regulating RNA stability, not being an intron

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Patents Grantslast 30 patents

Information Patent Grant
Method to prevent the myelin abnormalites associated with arginase...
- Patent number 12,234,474
- Issue date Feb 25, 2025
- The Regents of the University of California
- Gerald Lipshutz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Eukaryotic cells comprising adenovirus-associated virus polynucleot...
- Patent number 12,234,472
- Issue date Feb 25, 2025
- REGENERON PHARMACEUTICALS, INC.
- Michael Goren
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adenoviral expression vector and methods and cell lines for production
- Patent number 12,227,754
- Issue date Feb 18, 2025
- Lung Biotechnology PBC
- Colin Exline
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods of treating non-syndromic sensorineural hearing loss
- Patent number 12,226,493
- Issue date Feb 18, 2025
- Akouos, Inc.
- Emmanuel John Simons
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Coronavirus vaccine compositions and methods
- Patent number 12,220,455
- Issue date Feb 11, 2025
- Arcturus Therapeutics, Inc.
- Sean Michael Sullivan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Systems and methods for treating hyper-igm syndrome
- Patent number 12,214,055
- Issue date Feb 4, 2025
- Cecillia Cotta-Ramusino
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Compositions and methods for gene editing by targeting transferrin
- Patent number 12,215,320
- Issue date Feb 4, 2025
- CRISPR Therapeutics AG
- Alan Richard Brooks
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Factor IX encoding nucleotides
- Patent number 12,209,262
- Issue date Jan 28, 2025
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Engineered post-poly A signal RNA and uses thereof
- Patent number 12,203,069
- Issue date Jan 21, 2025
- Massachusetts Institute of Technology
- Ron Weiss
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Nucleic acid comprising or coding for a histone stem-loop and a pol...
- Patent number 12,201,680
- Issue date Jan 21, 2025
- CureVac SE
- Andreas Thess
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Lassa virus vaccine
- Patent number 12,161,711
- Issue date Dec 10, 2024
- CureVac SE
- Edith Jasny
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR therapy
- Patent number 12,152,242
- Issue date Nov 26, 2024
- The Curators of the University of Missouri
- Dongsheng Duan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Therapy
- Patent number 12,121,593
- Issue date Oct 22, 2024
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Self-replicating RNA and uses thereof
- Patent number 12,115,217
- Issue date Oct 15, 2024
- TRUSTEES OF BOSTON UNIVERSITY
- Joshua Edward McGee
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Adeno-associated virus vectors for treatment of Rett syndrome
- Patent number 12,104,163
- Issue date Oct 1, 2024
- Sarepta Therapeutics, Inc.
- Colin O'Banion
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modified adenoviruses
- Patent number 12,098,383
- Issue date Sep 24, 2024
- GRITSTONE BIO, INC.
- Karin Jooss
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
Codon-optimized acid alpha-glucosidase expression cassettes and met...
- Patent number 12,084,693
- Issue date Sep 10, 2024
- SPARK THERAPEUTICS, INC.
- Xavier Anguela
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Transgene cassettes, AAV vectors and AAV viral vectors for the expr...
- Patent number 12,077,772
- Issue date Sep 3, 2024
- The Board of Regents of the University of Texas System
- Steven J. Gray
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated virus compositions for restoring PAH gene function...
- Patent number 12,076,420
- Issue date Sep 3, 2024
- HOMOLOGY MEDICINES, INC.
- Jason Boke Wright
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Stabilization of poly(A) sequence encoding DNA sequences
- Patent number 12,054,723
- Issue date Aug 6, 2024
- BIONTECH SE
- Florian Eberle
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Synthetic genetic elements for biomanufacture
- Patent number 12,049,638
- Issue date Jul 30, 2024
- Janssen Biotech, Inc.
- William Lloyd Perry
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
BCMA chimeric antigen receptors
- Patent number 12,006,369
- Issue date Jun 11, 2024
- 2seventy bio, Inc.
- Richard Morgan
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Gene therapies for lysosomal disorders
- Patent number 11,993,790
- Issue date May 28, 2024
- Prevail Therapeutics, Inc.
- Asa Abeliovich
- C07 - ORGANIC CHEMISTRY
Information Patent Grant
AADC polynucleotides for the treatment of Parkinson's disease
- Patent number 11,975,056
- Issue date May 7, 2024
- VOYAGER THERAPEUTICS, INC.
- Robert Kotin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy for tuberous sclerosis
- Patent number 11,958,887
- Issue date Apr 16, 2024
- The General Hospital Corporation
- Xandra Breakefield
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods of treating phenylketonuria
- Patent number 11,952,585
- Issue date Apr 9, 2024
- HOMOLOGY MEDICINES, INC.
- Omar L. Francone
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Means and methods for improved regeneration
- Patent number 11,939,586
- Issue date Mar 26, 2024
- VIB VZW
- Lieven De Veylder
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and materials for NT-3 gene therapy
- Patent number 11,926,653
- Issue date Mar 12, 2024
- Research Institute at Nationwide Children's Hospital
- Zarife Sahenk
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Adeno-associated viral vectors for treatment of Niemann-Pick Diseas...
- Patent number 11,905,523
- Issue date Feb 20, 2024
- Ginkgo BioWorks, Inc.
- Daniel McCoy
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Patents Applicationslast 30 patents

Information Patent Application
OPTIMIZED AAV-BASED VACCINE
- Publication number 20250101458
- Publication date Mar 27, 2025
- Massachusetts Eye and Ear Infirmary
- Luc H. Vandenberghe
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS FOR TREATING CANCER
- Publication number 20250099615
- Publication date Mar 27, 2025
- Kelonia Therapeutics, Inc.
- Kevin M. Friedman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...
- Publication number 20250101396
- Publication date Mar 27, 2025
- Spark Therapeutics, Inc.
- Xavier Anguela
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
A NON-HUMAN MAMMAL COMPRISING IN ITS GENOME AT LEAST TWO HUMAN LEUK...
- Publication number 20250098651
- Publication date Mar 27, 2025
- Max-Delbrueck-Centrum für Molekulare Medizin in der Helmholtz-Gemeinschaft
- Arunraj DHAMODARAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTIGEN BINDING POLYPEPTIDES
- Publication number 20250101106
- Publication date Mar 27, 2025
- Kelonia Therapeutics, Inc.
- Kevin M. Friedman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTIGEN BINDING POLYPEPTIDES
- Publication number 20250101122
- Publication date Mar 27, 2025
- Kelonia Therapeutics, Inc.
- Kevin M. Friedman
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR RESTORING PAH GENE FUNCTION...
- Publication number 20250090691
- Publication date Mar 20, 2025
- HOMOLOGY MEDICINES, INC.
- Jason Boke WRIGHT
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
COMPOSITIONS AND METHODS FOR CAPPING RNAS
- Publication number 20250084409
- Publication date Mar 13, 2025
- Verve Therapeutics, Inc.
- Christopher Cheng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
VECTOR CONSTRUCTS FOR DELIVERY OF NUCLEIC ACIDS ENCODING THERAPEUTI...
- Publication number 20250084434
- Publication date Mar 13, 2025
- Kriya Therapeutics, Inc.
- Michele STONE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY METHODS FOR TREATMENT OF DIABETES
- Publication number 20250064978
- Publication date Feb 27, 2025
- Jaguar Gene Therapy, LLC
- Michael Hughes
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
THERAPY
- Publication number 20250064975
- Publication date Feb 27, 2025
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF
- Publication number 20250064981
- Publication date Feb 27, 2025
- THE BROAD INSTITUTE, INC.
- David R. Liu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED POLYNUCLEOTIDES FOR PROTEIN EXPRESSION
- Publication number 20250064986
- Publication date Feb 27, 2025
- PRECISION BIOSCIENCES, INC.
- Jason Richard Harris
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAV GENE THERAPY FOR THE KIDNEY
- Publication number 20250064984
- Publication date Feb 27, 2025
- The University of Bristol
- Moin Ahson Saleem-Uddin
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY
- Publication number 20250066437
- Publication date Feb 27, 2025
- SHANGHAI MYGT BIOPHARMACEUTICAL LLC
- Mengdi YAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACI...
- Publication number 20250049952
- Publication date Feb 13, 2025
- The United States of America,as represented by the Secretary,Department of He...
- Charles P. Venditti
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY
- Publication number 20250049959
- Publication date Feb 13, 2025
- Tenaya Therapeutics, Inc.
- Huanyu ZHOU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES
- Publication number 20250049949
- Publication date Feb 13, 2025
- The Trustees of the University of Pennsylvania
- Christian Hinderer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AADC/GDNF POLYNUCLEOTIDE, AND USE THEREOF IN TREATING PARKINSON'S D...
- Publication number 20250051750
- Publication date Feb 13, 2025
- SHANGHAI REGENELEAD THERAPIES CO., LTD.
- Jun Jiang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL PROMOTER AND USE THEREOF
- Publication number 20250051749
- Publication date Feb 13, 2025
- Toolgen Incorporated
- Su Cheong YEOM
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
DOSING REGIMEN FOR IL-10 ENCODING EXPRESSION CONSTRUCT
- Publication number 20250051412
- Publication date Feb 13, 2025
- Xalud Therapeutics, Inc.
- Jayson Michael Rieger
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF
- Publication number 20250041450
- Publication date Feb 6, 2025
- Insmed Incorporated
- Brian KASPAR
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ANTI-TFR:GAA AND ANTI-CD63:GAA INSERTION FOR TREATMENT OF POMPE DIS...
- Publication number 20250041455
- Publication date Feb 6, 2025
- Regeneron Pharmaceuticals, Inc.
- Andrew Baik
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GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA
- Publication number 20250041445
- Publication date Feb 6, 2025
- The Trustees of the University of Pennsylvania
- Juliette Hordeaux
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Information Patent Application
Lentiviral Vectors
- Publication number 20250034589
- Publication date Jan 30, 2025
- OXFORD BIOMEDICA (UK) LIMITED
- Daniel Farley
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS
- Publication number 20250034556
- Publication date Jan 30, 2025
- THE BROAD INSTITUTE, INC.
- Binhui Zhao
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
IMPROVED CIRCULAR RNA FOR EXPRESSING THERAPEUTIC PROTEINS
- Publication number 20250027108
- Publication date Jan 23, 2025
- CureVac SE
- Dipankar BHANDARI
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING A MUSCULAR DYSTROPHY
- Publication number 20250019721
- Publication date Jan 16, 2025
- ULTRAGENYX PHARMACEUTICAL INC.
- Matthew Scott Fuller
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Information Patent Application
SELF-REPLICATING RNA AND USES THEREOF
- Publication number 20250018028
- Publication date Jan 16, 2025
- Trustees of Boston University
- Joshua Edward MCGEE
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...
- Publication number 20250019409
- Publication date Jan 16, 2025
- ReCode Therapeutics, Inc.
- Mirko Hennig
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

regulating RNA stability, not being an intron

Industry

Parent Industries

Current Industry

Patents Grantslast 30 patents

Method to prevent the myelin abnormalites associated with arginase...

Eukaryotic cells comprising adenovirus-associated virus polynucleot...

Adenoviral expression vector and methods and cell lines for production

Methods of treating non-syndromic sensorineural hearing loss

Coronavirus vaccine compositions and methods

Systems and methods for treating hyper-igm syndrome

Compositions and methods for gene editing by targeting transferrin

Factor IX encoding nucleotides

Engineered post-poly A signal RNA and uses thereof

Nucleic acid comprising or coding for a histone stem-loop and a pol...

Lassa virus vaccine

Optimized expression cassettes for gene therapy

CRISPR therapy

Therapy

Self-replicating RNA and uses thereof

Adeno-associated virus vectors for treatment of Rett syndrome

Modified adenoviruses

Codon-optimized acid alpha-glucosidase expression cassettes and met...

Transgene cassettes, AAV vectors and AAV viral vectors for the expr...

Adeno-associated virus compositions for restoring PAH gene function...

Stabilization of poly(A) sequence encoding DNA sequences

Synthetic genetic elements for biomanufacture

BCMA chimeric antigen receptors

Gene therapies for lysosomal disorders

AADC polynucleotides for the treatment of Parkinson's disease

Gene therapy for tuberous sclerosis

Methods of treating phenylketonuria

Means and methods for improved regeneration

Methods and materials for NT-3 gene therapy

Adeno-associated viral vectors for treatment of Niemann-Pick Diseas...

Patents Applicationslast 30 patents

OPTIMIZED AAV-BASED VACCINE

COMPOSITIONS FOR TREATING CANCER

CODON-OPTIMIZED ACID ALPHA-GLUCOSIDASE EXPRESSION CASSETTES AND MET...

A NON-HUMAN MAMMAL COMPRISING IN ITS GENOME AT LEAST TWO HUMAN LEUK...

ANTIGEN BINDING POLYPEPTIDES

ANTIGEN BINDING POLYPEPTIDES

ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR RESTORING PAH GENE FUNCTION...

COMPOSITIONS AND METHODS FOR CAPPING RNAS

VECTOR CONSTRUCTS FOR DELIVERY OF NUCLEIC ACIDS ENCODING THERAPEUTI...

GENE THERAPY METHODS FOR TREATMENT OF DIABETES

THERAPY

AAV VECTORS ENCODING BASE EDITORS AND USES THEREOF

OPTIMIZED POLYNUCLEOTIDES FOR PROTEIN EXPRESSION

AAV GENE THERAPY FOR THE KIDNEY

TRANSGENIC EXPRESSION CASSETTE FOR TREATING MUSCULAR DYSTROPHY

IMPROVED GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACI...

OPTIMIZED EXPRESSION CASSETTES FOR GENE THERAPY

GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES

AADC/GDNF POLYNUCLEOTIDE, AND USE THEREOF IN TREATING PARKINSON'S D...

NOVEL PROMOTER AND USE THEREOF

DOSING REGIMEN FOR IL-10 ENCODING EXPRESSION CONSTRUCT

ADENO-ASSOCIATED VIRUS PARTICLES AND METHODS OF USE THEREOF

ANTI-TFR:GAA AND ANTI-CD63:GAA INSERTION FOR TREATMENT OF POMPE DIS...

GENE THERAPY FOR TREATMENT OF MUCOPOLYSACCHARIDOSIS IIIA

Lentiviral Vectors

COMPOSITIONS AND METHODS FOR SCREENING CIS REGULATORY ELEMENTS

IMPROVED CIRCULAR RNA FOR EXPRESSING THERAPEUTIC PROTEINS

COMPOSITIONS AND METHODS FOR TREATING A MUSCULAR DYSTROPHY

SELF-REPLICATING RNA AND USES THEREOF

POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...