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GENE THERAPY FOR LAMIN A-ASSOCIATED DEFICIENCIES
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Publication number 20250049949
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Publication date Feb 13, 2025
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The Trustees of the University of Pennsylvania
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Christian Hinderer
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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NOVEL PROMOTER AND USE THEREOF
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Publication number 20250051749
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Publication date Feb 13, 2025
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Toolgen Incorporated
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Su Cheong YEOM
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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Lentiviral Vectors
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Publication number 20250034589
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Publication date Jan 30, 2025
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OXFORD BIOMEDICA (UK) LIMITED
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Daniel Farley
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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SELF-REPLICATING RNA AND USES THEREOF
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Publication number 20250018028
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Publication date Jan 16, 2025
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Trustees of Boston University
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Joshua Edward MCGEE
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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GENE THERAPY FOR SPINAL MUSCULAR ATROPHY
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Publication number 20250011812
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Publication date Jan 9, 2025
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University of Massachusetts
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Jun Xie
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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GENE THERAPY FOR GALACTOSEMIA
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Publication number 20250001008
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Publication date Jan 2, 2025
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BridgeBio Gene Therapy Research, Inc.
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Clayton BEARD
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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AAV CAPSID VARIANTS AND USES THEREOF
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Publication number 20250001012
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Publication date Jan 2, 2025
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Mathieu Emmanuel Nonnenmacher
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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RETGC Gene Therapy
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Publication number 20250002936
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Publication date Jan 2, 2025
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MEIRAGTX UK II LIMITED
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Anastasios Georgiadis
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C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
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BCMA CHIMERIC ANTIGEN RECEPTORS
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Publication number 20240417481
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Publication date Dec 19, 2024
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2seventy bio, Inc.
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Richard Morgan
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A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
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