McIvor (1990), Virol. 176: 652-655. |
Yu et al. (1986) PNAS vol. 83: 3194-3198. |
Miller et al. (1989) BioTechniques vol. 7(9): 980-988. |
Collis et al. (1990) EMBO J vol. 9(1): 233-240. |
Miller et al. (1988) J. Virol. vol. 62(11): 4337-4343. |
Bender, M.A., et al., "A majority of mice show long-term expression of a human .beta.-globin gene after retrovirus transfer into hematopoietic stem cells", Mol. Cell. Biol., 9:1426-1434 (1989). |
Chang, J.C., et al., "A 36-base-pair core sequence of locus control region enhances retrovirally transferred human .beta.-globin gene expression", Proc. Natl. Acad. Sci. USA, 89:3107-3110 (1992). |
Cone, R.D., et al., "Regulated expression of a complete human .beta.-globin gene encoded by a transmissible retrovirus vector", Mol. Cell Biol., 7:887-897 (1987). |
Curtin, P.T., et al., "Human .beta.-globin gene expression in transgenic mice is enhanced by a distant DNase I hypersensitive site", Proc. Natl. Acad. Sci. USA, 86:7082-7086 (1989). |
Danos, O. and R.C. Mulligan, "Safe and efficient generation of recombinant retroviruses with amphotropic and ecotropic host ranges", Proc. Natl. Acad. Sci. USA, 85:6460-6464 (1988). |
Dzierzak, E.A., et al., "Lineage-specific expression of a human .beta.-globin gene in murine bone marrow transplant recipients reconstituted with retrovirus-transduced stem cells", Nature, 331:35-41 (1988). |
Forrester, W.C., et al., "Molecular analysis of the human .beta.-globin locus activation region", Proc. natl. Acad. Sci. USA, 86:5439-5443 (1989). |
Fraser, C.C., et al., "Expansion in vitro of retrovirally marked totipotent hematopoietic stem cells", Blood, 76:1071-1076 (1990). |
Fraser, C.C., et al., "Proliferation of totipotent hematopoietic stem cells in vitro with retention of long-term competitive in vivo reconstituting ability", Proc. Natl. Acad. Sci. USA, 89:1968-1972 (1992). |
Gallie, D.R., et al., "The 5'-leader sequence of tobacco mosaic virus RNA ehances the expression of foreign gene transcripts in vitro and in vivo", Nucleic Acids Res., 15:3257-3273 (1987). |
Grosveld, F., et al., "Position-independent, high-level expression of the human .beta.-globin gene in transgenic mice", Cell, 51:975-985 (1987). |
Hawley, T.S., et al., "Comparative analysis of retroviral vector expression in mouse embryonla carcinoma cells", Plasmid, 22:120-131 (1989). |
Humphries, R.K., et al., "Self-renewal of hemopoietic stem cells during mixed colony formation in vitro", Proc. Natl. Acad. Sci. USA, 78:3629-3633 (1981). |
Karlsson, S., et al., "Expression of the human .beta.-globin gene following retroviral-mediated transfer into multipotential hematopoietic progenitors of mice", Proc. Natl. Acad. Sci. USA 85:6062-6066 (1988). |
Krainer, A.D. and T. Maniatis, (1988) In Hames, B., D., and Glover, D., M. (ed.), "RNA splicing", Transcription and Splicing (IRL Press, Oxford), pp. 131-206. |
Lemischka, I.R., et al., "Developmental potential and dynamic behavior of hematopoietic stem cells", Cell, 45:917-927 91986). |
Nev, P.A., et al., "Tandem AP-1-binding sites within the human .beta.-globin dominant control region function as an inducible enhancer in erythroid cells", Genes Dev., 4:993-1006 (1990). |
Novak, U., et al., "High-level .beta.-globin expression after retroviral transfer of locus activation region-containing human .beta.-globin gene derivatives into murine erythroleukemia cells", Proc. Natl. Acad. Sci. USA, 87:3386-3390 (1990). |
Parkman, B., "The application of bone marrow transplantation to the treatment of genetic diseases", Science, 232:1373-1378 (1986). |
Philipsen, S., et al., "The .beta.-globin dominant control region: hypersensitive site 2", EMBO J., 9:2159-2167 (1990). |
Pruzina, S., et al., "Hypersensitive site 4 of the human .beta.-globin locus control region", Nucleic Acids Res., 19:1413-1419 (1991). |
Ryan, T.M., et al., "A single erythroid-specific DNase I super-hypersensitive site activates high levels of human .beta.-globin gene expression in transgenic mice", Genes Dev., 3:314-323 (1989). |
Talbot, D., et al., "Detailed analysis of the site 3 region of the human .beta.-globin dominant control region", EMBO J., 9:2169-2178 (1990). |
Tuan, D., et al., "The .beta.-like-globin gene domain in human erythroid cells", Proc. Natl. Acad. Sci. USA, 82:6384-6388 (1985). |
Tuan, D.Y.H., et al., "An erythroid-specific, developmental-stage-independent enhancer far upstream of the human .beta.-like globin genes", Proc. Natl. Acad. Sci. USA, 86:2554-2558 (1989). |
Tuan, D. and I.M. London, "Mapping of DNase I-hypersensitive sites in the upstream DNA of human embryonic .epsilon.-globin gene in K562 leukemia cells", Proc. Natl. Acad. Sci. USA, 81:2718-2722 (1984). |
Verma, I.M., "Retroviral vectors for gene transfer", In Microbiology-1985, American Society for Microbiology, pp. 229-232, Washington, 1985. |
Walters, M., et al., "Characterization of a DNA binding activity in DNAse I hypersensitive site 4 of the human globin locus control region", Nucleic Acids Res., 19:5385-5393 (1991). |