Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

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Patents Grantslast 30 patents

Information Patent Grant
Method for delivering RNA to neurons to treat herpes infections
- Patent number 12,156,919
- Issue date Dec 3, 2024
- University of Florida Research Foundation, Incorporated
- David C. Bloom
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for regenerating hair cells and/or support...
- Patent number 12,156,899
- Issue date Dec 3, 2024
- Massachusetts Eye and Ear Infirmary
- Zheng-Yi Chen
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
CRISPR gene therapy of fusion gene related cancers
- Patent number 12,157,905
- Issue date Dec 3, 2024
- Aarhus Universitet
- Christian Kanstrup Holm
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Permanent epigenetic gene silencing
- Patent number 12,152,240
- Issue date Nov 26, 2024
- Ospedale San Raffaele S.r.l.
- Luigi Naldini
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Optimized expression cassettes for gene therapy
- Patent number 12,151,001
- Issue date Nov 26, 2024
- Tenaya Therapeutics, Inc.
- Huanyu Zhou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Methods and compositions for in vivo gene editing based cell-type-s...
- Patent number 12,152,260
- Issue date Nov 26, 2024
- California Institute of Technology
- Yuki Oka
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compounds and compositions for intracellular delivery of therapeuti...
- Patent number 12,151,995
- Issue date Nov 26, 2024
- ModernaTX, Inc.
- Kerry E. Benenato
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods and compositions for car T cell therapy
- Patent number 12,144,850
- Issue date Nov 19, 2024
- Purdue Research Foundation
- Philip Stewart Low
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Stable compositions of MRNA-loaded lipid nanoparticles and processe...
- Patent number 12,144,871
- Issue date Nov 19, 2024
- Translate Bio, Inc.
- Shrirang Karve
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Rescue of central and peripheral neurological phenotype of friedrei...
- Patent number 12,146,150
- Issue date Nov 19, 2024
- VOYAGER THERAPEUTICS, INC.
- Dinah Wen-Yee Sah
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Systems, methods, and compositions for correction of frameshift mut...
- Patent number 12,146,152
- Issue date Nov 19, 2024
- Massachusetts Institute of Technology
- Timothy Lu
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Apparatus for efficient genetic modification of cells
- Patent number 12,139,697
- Issue date Nov 12, 2024
- The Charles Stark Draper Laboratory, Inc.
- Kenneth T. Kotz
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Modulators of chromosome 9 open reading frame 72 gene expression an...
- Patent number 12,139,517
- Issue date Nov 12, 2024
- Sangamo Therapeutics, Inc.
- Joseph F. Nabhan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Chimeric protein and related genic transfer technology
- Patent number 12,138,319
- Issue date Nov 12, 2024
- Lucio Pastore
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Diagnostic and therapeutic methods for EFMR (epilepsy and mental re...
- Patent number 12,139,521
- Issue date Nov 12, 2024
- Central Adelaide Local Health Network Inc.
- Leanne Michelle Dibbens
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dominant active yap, a hippo effector, induces chromatin accessibil...
- Patent number 12,138,284
- Issue date Nov 12, 2024
- Baylor College of Medicine
- Tanner Monroe
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Expression vector for cholesterol 24-hydrolase in therapy of polygl...
- Patent number 12,138,298
- Issue date Nov 12, 2024
- BRAINVECTIS
- Sandro Alves
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Capsid
- Patent number 12,138,318
- Issue date Nov 12, 2024
- UCL BUSINESS LTD
- Amit Nathwani
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Respiratory syncytial virus (RSV) vaccine
- Patent number 12,139,513
- Issue date Nov 12, 2024
- CureVac SE
- Thomas Kramps
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Dry powder composition comprising long-chain RNA
- Patent number 12,138,348
- Issue date Nov 12, 2024
- CureVac SE
- Fabian Johannes Eber
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Methods for treating or alleviating a bone-loss related disease or...
- Patent number 12,133,896
- Issue date Nov 5, 2024
- Kaohsiung Medical University
- Chau-Zen Wang
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Compositions and methods for treatment of GCase related disease states
- Patent number 12,133,880
- Issue date Nov 5, 2024
- Children's Hospital Medical Center
- Ying Sun
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Materials and methods for treatment of hemoglobinopathies
- Patent number 12,134,767
- Issue date Nov 5, 2024
- Vertex Pharmaceuticals Incorporated
- Matthew Hebden Porteus
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Development of optimized recombinant expression construct
- Patent number 12,134,776
- Issue date Nov 5, 2024
- G&P BIOSCIENCE CO., LTD.
- Seong Hyun Ho
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Immunostimulating vector system
- Patent number 12,133,898
- Issue date Nov 5, 2024
- Provecs Medical GmbH
- Frank Schnieders
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Coronavirus vaccine
- Patent number 12,133,899
- Issue date Nov 5, 2024
- BIONTECH SE
- Ugur Sahin
- B82 - NANO-TECHNOLOGY
Information Patent Grant
Compositions and methods for organ specific delivery of nucleic acids
- Patent number 12,133,924
- Issue date Nov 5, 2024
- The Board of Regents of the University of Texas System
- Qiang Cheng
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Grant
Gene therapy delivery of Parkin mutants having increased activity t...
- Patent number 12,133,897
- Issue date Nov 5, 2024
- NysnoBio GT Neurology, LLC
- Jennifer Johnston
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Lipid nanoparticle compositions and uses thereof
- Patent number 12,133,923
- Issue date Nov 5, 2024
- ReCode Therapeutics, Inc.
- Mirko Hennig
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Grant
Materials and methods for treatment of human genetic diseases inclu...
- Patent number 12,129,471
- Issue date Oct 29, 2024
- Vertex Pharmaceuticals Incorporated
- Matthew Hebden Porteus
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE

Patents Applicationslast 30 patents

Information Patent Application
SECRETED SPLICING VARIANT OF MAMMAL KLOTHO AS A MEDICAMENT FOR COGN...
- Publication number 20240398909
- Publication date Dec 5, 2024
- Universitat Autonoma de Barcelona
- Miguel Chillon Rodriguez
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...
- Publication number 20240398983
- Publication date Dec 5, 2024
- ReCode Therapeutics, Inc.
- Vladimir Kharitonov
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
An oncolytic virus vector coding for interleukin-7 (IL-7) polypeptide
- Publication number 20240398986
- Publication date Dec 5, 2024
- TILT Biotherapeutics Oy
- Tatiana Kudling
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS AND COMPOSITIONS FOR DIAGNOSIS AND TREATMENT OF METABOLIC D...
- Publication number 20240398989
- Publication date Dec 5, 2024
- THE BROAD INSTITUTE, INC.
- Melina Claussnitzer
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR TREATING VIRAL INFECTIONS TARGETING TRIM7
- Publication number 20240401007
- Publication date Dec 5, 2024
- The Board of Regents of the University of Texas System
- John W. Schoggins
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MND PROMOTER CHIMERIC ANTIGEN RECEPTORS
- Publication number 20240401080
- Publication date Dec 5, 2024
- 2seventy bio, Inc.
- Richard Morgan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LIPID NANOPARTICLE FORMULATIONS AND COMPOSITIONS
- Publication number 20240398982
- Publication date Dec 5, 2024
- CAPSTAN THERAPEUTICS, INC.
- Priya Prakash Karmali
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NOVEL TRANSCRIPTION FACTORS
- Publication number 20240398985
- Publication date Dec 5, 2024
- Novartis AG
- Keith Everett FERGUSON
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RNAi induced C9ORF72 suppression for the treatment of ALS/FTD
- Publication number 20240398988
- Publication date Dec 5, 2024
- uniQure IP B.V.
- Raygene Michaël MARTIER
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR THE TREATMENT OF AUTOSOMAL DOMINANT PO...
- Publication number 20240400627
- Publication date Dec 5, 2024
- Yale University
- Michael J. Caplan
- C07 - ORGANIC CHEMISTRY
Information Patent Application
COMPOSITIONS AND METHODS FOR PRODUCING OREXIN NEUROPEPTIDE USING NA...
- Publication number 20240398722
- Publication date Dec 5, 2024
- VL Biotech Inc.
- Hsin-Yi LIN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
TREATMENT OF HSV-2 USING A MEGANUCLEASE
- Publication number 20240398984
- Publication date Dec 5, 2024
- Fred Hutchinson Cancer Center
- Keith R. Jerome
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Viral Vectors for Cancer Therapy
- Publication number 20240398994
- Publication date Dec 5, 2024
- Krystal Biotech, Inc.
- Suma KRISHNAN
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID VACCINES
- Publication number 20240398927
- Publication date Dec 5, 2024
- ModernaTX, Inc.
- Giuseppe Ciaramella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEP...
- Publication number 20240398992
- Publication date Dec 5, 2024
- Skyline Therapeutics Limited
- Yanqun SHU
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
SMALL MOLECULE-REGULATED GENE EXPRESSION SYSTEM
- Publication number 20240398993
- Publication date Dec 5, 2024
- Outpace Bio, Inc.
- Glenna FOIGHT
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
MRNAS ENCODING CHIMERIC METABOLIC REPROGRAMMING POLYPEPTIDES AND US...
- Publication number 20240401006
- Publication date Dec 5, 2024
- Moderna TX, Inc.
- Laurie Kenney
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS, KITS AND METHODS FOR TREATMENT OF COMPLEMENT-RELATED...
- Publication number 20240398898
- Publication date Dec 5, 2024
- Trustees of Tufts College
- Rajendra Kumar-Singh
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID VACCINES
- Publication number 20240398931
- Publication date Dec 5, 2024
- ModernaTX, Inc.
- Giuseppe Ciaramella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
METHODS FOR THE TEMPORAL REGULATION OF REPROGRAMMING FACTORS IN MAM...
- Publication number 20240398987
- Publication date Dec 5, 2024
- Michael D. West
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LIVER-SPECIFIC EXPRESSION CASSETTES, VECTORS AND USES THEREOF FOR E...
- Publication number 20240398990
- Publication date Dec 5, 2024
- GENERATION BIO CO.
- Jessica Lynn Keenan
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
AAVRH74 PARTICLES FOR GENE THERAPY OF MUSCLE DISEASE
- Publication number 20240398991
- Publication date Dec 5, 2024
- University of Florida Research Foundation, Incorporated
- Arun Srivastava
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
Bacteria-Based Protein Delivery
- Publication number 20240401065
- Publication date Dec 5, 2024
- UNIVERSITAET BASEL
- Cécile Arrieumerlou
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
COMPOSITIONS AND METHODS FOR STIMULATING HAIR GROWTH USING NANOCAPS...
- Publication number 20240398721
- Publication date Dec 5, 2024
- VL Biotech Inc.
- Hsin-Yi LIN
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
IN VIVO DELIVERY OF OLIGONUCLEOTIDES
- Publication number 20240401040
- Publication date Dec 5, 2024
- ONCOIMMUNIN, INC.
- Beverly PACKARD
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ADENO-ASSOCIATED VIRUS VECTORS FOR TREATMENT OF RETT SYNDROME
- Publication number 20240392316
- Publication date Nov 28, 2024
- Sarepta Therapeutics, Inc.
- Colin O'Banion
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
NUCLEIC ACID VACCINES
- Publication number 20240390480
- Publication date Nov 28, 2024
- ModernaTX, Inc.
- Giuseppe Ciaramella
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
ENGINEERED CASX REPRESSOR SYSTEMS
- Publication number 20240392271
- Publication date Nov 28, 2024
- Scribe Therapeutics Inc.
- Jason FERNANDES
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information Patent Application
LIPOCATIONIC DENDRIMERS AND USES THEREOF
- Publication number 20240391869
- Publication date Nov 28, 2024
- The Board of Regents of the University of Texas System
- Daniel J. SIEGWART
- A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information Patent Application
RESPIRATORY SYNCYTIAL VIRUS (RSV) VACCINE
- Publication number 20240391962
- Publication date Nov 28, 2024
- CureVac SE
- Thomas KRAMPS
- C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...

Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy

Industry

Parent Industries

Current Industry

Sub Industries

Patents Grantslast 30 patents

Method for delivering RNA to neurons to treat herpes infections

Methods and compositions for regenerating hair cells and/or support...

CRISPR gene therapy of fusion gene related cancers

Permanent epigenetic gene silencing

Optimized expression cassettes for gene therapy

Methods and compositions for in vivo gene editing based cell-type-s...

Compounds and compositions for intracellular delivery of therapeuti...

Methods and compositions for car T cell therapy

Stable compositions of MRNA-loaded lipid nanoparticles and processe...

Rescue of central and peripheral neurological phenotype of friedrei...

Systems, methods, and compositions for correction of frameshift mut...

Apparatus for efficient genetic modification of cells

Modulators of chromosome 9 open reading frame 72 gene expression an...

Chimeric protein and related genic transfer technology

Diagnostic and therapeutic methods for EFMR (epilepsy and mental re...

Dominant active yap, a hippo effector, induces chromatin accessibil...

Expression vector for cholesterol 24-hydrolase in therapy of polygl...

Capsid

Respiratory syncytial virus (RSV) vaccine

Dry powder composition comprising long-chain RNA

Methods for treating or alleviating a bone-loss related disease or...

Compositions and methods for treatment of GCase related disease states

Materials and methods for treatment of hemoglobinopathies

Development of optimized recombinant expression construct

Immunostimulating vector system

Coronavirus vaccine

Compositions and methods for organ specific delivery of nucleic acids

Gene therapy delivery of Parkin mutants having increased activity t...

Lipid nanoparticle compositions and uses thereof

Materials and methods for treatment of human genetic diseases inclu...

Patents Applicationslast 30 patents

SECRETED SPLICING VARIANT OF MAMMAL KLOTHO AS A MEDICAMENT FOR COGN...

POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...

An oncolytic virus vector coding for interleukin-7 (IL-7) polypeptide

METHODS AND COMPOSITIONS FOR DIAGNOSIS AND TREATMENT OF METABOLIC D...

COMPOSITIONS AND METHODS FOR TREATING VIRAL INFECTIONS TARGETING TRIM7

MND PROMOTER CHIMERIC ANTIGEN RECEPTORS

LIPID NANOPARTICLE FORMULATIONS AND COMPOSITIONS

NOVEL TRANSCRIPTION FACTORS

RNAi induced C9ORF72 suppression for the treatment of ALS/FTD

COMPOSITIONS AND METHODS FOR THE TREATMENT OF AUTOSOMAL DOMINANT PO...

COMPOSITIONS AND METHODS FOR PRODUCING OREXIN NEUROPEPTIDE USING NA...

TREATMENT OF HSV-2 USING A MEGANUCLEASE

Viral Vectors for Cancer Therapy

NUCLEIC ACID VACCINES

RECOMBINANT ADENO-ASSOCIATED VIRUS WITH MODIFIED AAV CAPSID POLYPEP...

SMALL MOLECULE-REGULATED GENE EXPRESSION SYSTEM

MRNAS ENCODING CHIMERIC METABOLIC REPROGRAMMING POLYPEPTIDES AND US...

COMPOSITIONS, KITS AND METHODS FOR TREATMENT OF COMPLEMENT-RELATED...

NUCLEIC ACID VACCINES

METHODS FOR THE TEMPORAL REGULATION OF REPROGRAMMING FACTORS IN MAM...

LIVER-SPECIFIC EXPRESSION CASSETTES, VECTORS AND USES THEREOF FOR E...

AAVRH74 PARTICLES FOR GENE THERAPY OF MUSCLE DISEASE

Bacteria-Based Protein Delivery

COMPOSITIONS AND METHODS FOR STIMULATING HAIR GROWTH USING NANOCAPS...

IN VIVO DELIVERY OF OLIGONUCLEOTIDES

ADENO-ASSOCIATED VIRUS VECTORS FOR TREATMENT OF RETT SYNDROME

NUCLEIC ACID VACCINES

ENGINEERED CASX REPRESSOR SYSTEMS

LIPOCATIONIC DENDRIMERS AND USES THEREOF

RESPIRATORY SYNCYTIAL VIRUS (RSV) VACCINE