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Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy
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A61K48/00
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Parent Industries
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HUMAN NECESSITIES
A61
Medical science
A61K
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
Current Industry
A61K48/00
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases Gene therapy
Sub Industries
A61K48/0008
characterised by an aspect of the 'non-active' part of the composition delivered
A61K48/0016
wherein the nucleic acid is delivered as a 'naked' nucleic acid
A61K48/0025
wherein the non-active part clearly interacts with the delivered nuclic acid
A61K48/0033
the non-active part being non-polymeric
A61K48/0041
the non-active part being polymeric
A61K48/005
characterised by an aspect of the 'active' part of the composition delivered
A61K48/0058
Nucleic acids adapted for tissue specific expression
A61K48/0066
Manipulation of the nucleic acid to modify its expression pattern
A61K48/0075
characterised by an aspect of the delivery route
A61K48/0083
characterised by an aspect of the administration regime
A61K48/0091
Purification or manufacturing processes for gene therapy compositions
Industries
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Patents Grants
last 30 patents
Information
Patent Grant
Adeno-associated virus vector variants for high efficiency genome e...
Patent number
11,965,174
Issue date
Apr 23, 2024
City of Hope
Saswati Chatterjee
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Respiratory syncytial virus (RSV) vaccine
Patent number
11,965,000
Issue date
Apr 23, 2024
CureVac SE
Thomas Kramps
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Compositions and methods for TTR gene editing and treating ATTR amy...
Patent number
11,965,165
Issue date
Apr 23, 2024
Intellia Therapeutics, Inc.
Arti Mahendra Prakash Kanjolia
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Antisense oligonucleotide and composition for prevention or treatme...
Patent number
11,963,974
Issue date
Apr 23, 2024
National Center for Child Health and Development
Go Tajima
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Method for improving retroviral transduction and gene editing in he...
Patent number
11,964,027
Issue date
Apr 23, 2024
Anna Christina Kajaste-Rudnitski
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Targeted DNA demethylation method, fusion protein and application t...
Patent number
11,965,187
Issue date
Apr 23, 2024
GUANGZHOU MEDICAL UNIVERSITY
Xi-Yong Yu
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Gene therapy for neurometabolic disorders
Patent number
11,957,765
Issue date
Apr 16, 2024
Genzyme Corporation
Marco A. Passini
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Gene therapy for tuberous sclerosis
Patent number
11,958,887
Issue date
Apr 16, 2024
The General Hospital Corporation
Xandra Breakefield
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Micro-dystrophins and related methods of use
Patent number
11,958,888
Issue date
Apr 16, 2024
University of Washington
Jeffrey S. Chamberlain
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Methods and compositions for genome editing in non-dividing cells
Patent number
11,959,094
Issue date
Apr 16, 2024
Salk Institute for Biological Studies
Juan Carlos Izpisua Belmonte
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Immunosuppression-reverting oligonucleotides inhibiting the express...
Patent number
11,959,083
Issue date
Apr 16, 2024
Secarna Pharmaceuticals GmbH & Co. KG
Frank Jaschinski
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Compositions and methods for treating cancer using RHOA dominant ne...
Patent number
11,957,739
Issue date
Apr 16, 2024
Dana-Farber Cancer Institute, Inc.
Adam Bass
G01 - MEASURING TESTING
Information
Patent Grant
Lipid nanoparticle compositions and methods for MRNA delivery
Patent number
11,951,180
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
RNA constructs and uses thereof
Patent number
11,951,185
Issue date
Apr 9, 2024
BIONTECH SE
Ugur Sahin
B82 - NANO-TECHNOLOGY
Information
Patent Grant
Diagnostics and therapy for human respiratory syncytial virus
Patent number
11,952,631
Issue date
Apr 9, 2024
Medizinische Hochschule Hannover
Daniel Todt
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Lipid nanoparticle compositions and methods for mRNA delivery
Patent number
11,951,181
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Combination therapy for treatment of thoracic cancer using Ad-REIC/...
Patent number
11,951,182
Issue date
Apr 9, 2024
Momotaro-Gene Inc.
Hiromi Kumon
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Adeno-associated virus compositions for PAH gene transfer and metho...
Patent number
11,951,183
Issue date
Apr 9, 2024
HOMOLOGY MEDICINES, INC.
Albert Barnes Seymour
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Lipid nanoparticle compositions and methods for MRNA delivery
Patent number
11,951,179
Issue date
Apr 9, 2024
Translate Bio, Inc.
Frank DeRosa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Vector for gene silencing and replacement and methods of use thereof
Patent number
11,951,184
Issue date
Apr 9, 2024
Wisconsin Alumni Research Foundation
Matthew Michael Millette
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Grant
Compositions and methods for treating Huntington's disease
Patent number
11,951,121
Issue date
Apr 9, 2024
VOYAGER THERAPEUTICS, INC.
Dinah Wen-Yee Sah
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Genetically modified probiotics for oral delivery of renin-angioten...
Patent number
11,945,853
Issue date
Apr 2, 2024
University of Florida Research Foundation, Incorporated
Qiuhong Li
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Biologically active compounds
Patent number
11,944,688
Issue date
Apr 2, 2024
SUTURA THERAPEUTICS LTD
Keith Foster
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Compositions of functional mitochondria and uses thereof
Patent number
11,944,642
Issue date
Apr 2, 2024
MINOVIA THERAPEUTICS LTD.
Natalie Yivgi-Ohana
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Engineered chimeric fusion protein compositions and methods of use...
Patent number
11,944,680
Issue date
Apr 2, 2024
Myeloid Therapeutics, Inc.
Daniel Getts
C07 - ORGANIC CHEMISTRY
Information
Patent Grant
Compositions and therapeutic methods of microRNA gene delivery
Patent number
11,946,064
Issue date
Apr 2, 2024
The Brigham & Women's Hospital, Inc.
Pierpaolo Peruzzi
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Modified U6 promoter system for tissue specific expression
Patent number
11,939,579
Issue date
Mar 26, 2024
Research Institute at Nationwide Children's Hospital
Scott Quenton Harper
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Modified cascade ribonucleoproteins and uses thereof
Patent number
11,939,604
Issue date
Mar 26, 2024
Caribou Biosciences, Inc.
Stan Johan Jozef Brouns
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Compositions and methods for treating phenylketonuria
Patent number
11,939,600
Issue date
Mar 26, 2024
Arcturus Therapeutics, Inc.
Kiyoshi Tachikawa
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Grant
Treatment of heart disease by disruption of the anchoring of PP2A
Patent number
11,938,198
Issue date
Mar 26, 2024
University of Miami
Michael S. Kapiloff
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Patents Applications
last 30 patents
Information
Patent Application
INDUCIBLE SINGLE AAV SYSTEM AND USES THEREOF
Publication number
20240123086
Publication date
Apr 18, 2024
University of Massachusetts
Christian Mueller
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
COMPOSITIONS AND METHODS FOR THE TARGETING OF PCSK9
Publication number
20240123089
Publication date
Apr 18, 2024
Scribe Therapeutics Inc.
Jason FERNANDES
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
NOVEL CARBONYL LIPIDS AND LIPID NANOPARTICLE FORMULATIONS FOR DELIV...
Publication number
20240122854
Publication date
Apr 18, 2024
Acuitas Therapeutics, Inc.
Xinyao Du
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
POLYNUCLEOTIDE COMPOSITIONS, RELATED FORMULATIONS, AND METHODS OF U...
Publication number
20240123087
Publication date
Apr 18, 2024
ReCode Therapeutics, Inc.
Daniella Ishimaru
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
HYBRID AAV-ANELLOVECTORS
Publication number
20240123083
Publication date
Apr 18, 2024
FLAGSHIP PIONEERING INNOVATIONS V, INC.
Simon Delagrave
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
FC RECEPTOR BINDING PROTEINS
Publication number
20240124593
Publication date
Apr 18, 2024
Takeda Pharmaceutical Company Limited
Daniel J. Sexton
G01 - MEASURING TESTING
Information
Patent Application
COMPOUNDS AND COMPOSITIONS FOR INTRACELLULAR DELIVERY OF THERAPEUTI...
Publication number
20240124388
Publication date
Apr 18, 2024
ModernaTX, Inc.
Kerry E. BENENATO
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
METHOD FOR PRODUCING DNA-EDITED EUKARYOTIC CELL, AND KIT USED IN TH...
Publication number
20240124898
Publication date
Apr 18, 2024
OSAKA UNIVERSITY
Tomoji MASHIMO
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
CHIMERIC ANTIGEN RECEPTORS (CARs) TARGETING HEMATOLOGIC MALIGNANCIE...
Publication number
20240124547
Publication date
Apr 18, 2024
iCell Gene Therapeuticics LLC
Yupo MA
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR ENHANCING GAMMA DELTA T CELLS IN THE GUT
Publication number
20240123090
Publication date
Apr 18, 2024
King's College London
Adrian HAYDAY
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
COMPOSITIONS AND METHODS FOR THE VECTORED AUGMENTATION OF PROTEIN D...
Publication number
20240124889
Publication date
Apr 18, 2024
Xiao-Qin Ren
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
VECTORIZED ANTI-CGRP AND ANTI-CGRPR ANTIBODIES AND ADMINISTRATION T...
Publication number
20240124890
Publication date
Apr 18, 2024
Regenxbio Inc.
Jared Smith
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
OPTIMIZED FACTOR VIII GENES
Publication number
20240124555
Publication date
Apr 18, 2024
Bioverativ Therapeutics Inc.
Siyuan TAN
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
RNA CLEAVAGE-INDUCED TRANSCRIPT STABILIZER AND USES THEREOF
Publication number
20240124877
Publication date
Apr 18, 2024
Massachusetts Institute of Technology
Ron Weiss
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
MODIFIED NUCLEOSIDE, NUCLEOTIDE, AND NUCLEIC ACID COMPOSITIONS
Publication number
20240123035
Publication date
Apr 18, 2024
ModernaTX, Inc.
Antonin DE FOUGEROLLES
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
LIVER SPECIFIC DELIVERY OF MESSENGER RNA
Publication number
20240123084
Publication date
Apr 18, 2024
Translate Bio, Inc.
Braydon Charles Guild
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
AAV VECTORS TARGETING T-CELLS
Publication number
20240123085
Publication date
Apr 18, 2024
Ginkgo BioWorks, Inc.
James Kennon Smith
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
USE OF A SPLIT dCAS FUSION PROTEIN SYSTEM FOR EPIGENETIC EDITING
Publication number
20240123088
Publication date
Apr 18, 2024
The Regents of the University of California
Julian Halmai
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
ADENO-ASSOCIATED VIRUS VECTOR
Publication number
20240124894
Publication date
Apr 18, 2024
King's College London
Ralph Michael Linden
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
NUCLEASE-MEDIATED GENOME EDITING OF PRIMARY CELLS AND RELATED KITS
Publication number
20240124895
Publication date
Apr 18, 2024
The Board of Trustees of the Leland Stanford Junior University
Daniel P. Dever
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
COMPOSITIONS AND METHODS FOR TREATMENT OF NIEMANN PICK TYPE A DISEASE
Publication number
20240115733
Publication date
Apr 11, 2024
The Trustees of the University of Pennsylvania
James M. WILSON
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
Method of Increasing the Function of an AAV Vector
Publication number
20240117378
Publication date
Apr 11, 2024
The Trustees of the University of Pennsylvania
Luk VANDENBERGHE
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
Methods for Treatment of Alport Syndrome
Publication number
20240115598
Publication date
Apr 11, 2024
SANOFI
Timothy Wright
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
FUSION PEPTIDES CONTAINING DIMERIC ALPHA-HELICES, PEPTIDE-MOLECULAR...
Publication number
20240116986
Publication date
Apr 11, 2024
Artprobio Co., Ltd.
Yong-Beom LIM
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
LIPID NANOPARTICLE COMPOSITIONS FOR DELIVERING CIRCULAR POLYNUCLEOT...
Publication number
20240116852
Publication date
Apr 11, 2024
Orna Therapeutics, Inc.
Allen T. HORHOTA
A61 - MEDICAL OR VETERINARY SCIENCE HYGIENE
Information
Patent Application
MATERIALS AND METHODS FOR THE TREATMENT OF LYSOSOMAL ACID LIPASE DE...
Publication number
20240115735
Publication date
Apr 11, 2024
Research Institute at Nationwide Children's Hospital
Paul Taylor Martin
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
GENE THERAPY FOR DOPAMINE TRANSPORTER DEFICIENCY SYNDROME
Publication number
20240115737
Publication date
Apr 11, 2024
UCL Business LTD
Joanna NG
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
SYNTHETIC CAS12A FOR ENHANCED MULTIPLEX GENE CONTROL AND EDITING
Publication number
20240115739
Publication date
Apr 11, 2024
The Board of Trustees of the Leland Stanford Junior University
Lei S. QI
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
RAPID DESIGN, BUILD, TEST, AND LEARN TECHNOLOGIES FOR IDENTIFYING A...
Publication number
20240117339
Publication date
Apr 11, 2024
Battelle Memorial Institute
Anthony D. DUONG
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...
Information
Patent Application
SYNTHETIC IMMUNOMODULATION WITH A CRISPR SUPER-REPRESSOR IN VIVO
Publication number
20240117364
Publication date
Apr 11, 2024
Arizona Board of Regents on behalf of Arizona State University
Samira KIANI
C12 - BIOCHEMISTRY BEER SPIRITS WINE VINEGAR MICROBIOLOGY ENZYMOLOGY MUTATION...